27 October 2025 | Workshop Day
28-29 October 2025 | Conference & Exhibition
RAI Congress Centre, Amsterdam

Strategy, Advocacy & Partnering For
The Global Orphan Drug Industry

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OFFER EXPIRES 9 may

FREE TICKETS FOR PATIENT GROUPS

The World's Largest Rare Disease Event

The World Orphan Drug Congress is the largest and most established orphan drug & rare disease meeting of its kind across the globe.

From cell and gene therapy, genetic testing, and market access, to real world evidence, this one meeting covers the whole orphan drugs value chain where science, government and manufacturers all come together to create groundbreaking progress.

2,000+

Attendees

250+

Speakers

130+

Exhibitors

3

Days

1,500+

1 to 1 Partnering Meetings

15,000+

Networking Connections

Conference

Covering cell & gene therapy, genetic testing, market access, real world evidence, orphan drugs policy and much more

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Exhibition

130+ leading solution providers from across the globe, featuring new ways of thinking and novel partnerships to generate solutions.

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Networking

Networking is at the heart of World Orphan Drug Congress. Our congress allows you to connect directly with thousands of pharma experts across 3 days of built-in 1-2-1 networking

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Early Bird Offer Save €2,100

The Start-to-Finish of Orphan Drugs

From regulation and policy to global pricing and gene therapy

Cell & Gene Therapies

Genetic Testing

Gene Editing

Partnering & Investment

Global Market Access

Expanded Access Programs

Real World Evidence

Global Patient Advocacy

Value Based Pricing & Reimbursement

Epidemiology & Forecasting

Orphan Drugs Policy

Gene Therapy Development

Clinical Trials

Payers, HTA and Pricing

Manufacture

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In Partnership With

Beacon World Orphan Drug Congress 2023 Supporting Partner

Dravet World Orphan Drug Congress 2023 Supporting Partner

EURORDIS World Orphan Drug Congress 2023 Supporting Partner

ERICA World Orphan Drug Congress 2023 Supporting Partner

CataloniaBio & HealthTech World Vaccine Congress Europe 2023 Supporting Partner

EuropaBio World Orphan Drug Congress 2023 Supporting Partner

SEE ALL PARTNERS

Advisory Board

Yann Le Cam
Former CEO
EURORDIS

Daniel O’Connor
Director Regulatory and Early Access Policy
ABPI

Daniel O’Connor at World Orphan Drug Congress

Rick Thompson
CEO
Beacon

Rick Thompson at World Orphan Drug Congress

Durhane Wong-Rieger
President & CEO
Canadian Organization for Rare Disorders

Durhane Wong-Rieger at World Orphan Drug Congress

Toon Digneffe
Head Public Affairs & Public Policy
Takeda

Toon Digneffe World at Orphan Drug Congress

Sheela Upadhyaya
Life Science Advisor in Rare Diseases & Special Advisor
Former FIPRA

Sheela Upadhyaya at World Orphan Drug Congress

Charlotte Chanson
Director, Global Diagnostics & Newborn Screening
Orchard Therapuetics

Charlotte Chanson at World Orphan Drug Congress

Josie Godfrey
Former Associate Director of NICE
Rare Disease, Market Access, JG Zebra Consulting

Josie Godfrey at World Orphan Drug Congress

Anna Bucsics
Project Advisor
MoCA

Anna Bucsics at World Orphan Drug Congress

Dr Alexander Natz
Secretary General
EUCOPE

Dr Alexander Natz at World Orphan Drug Congress

Giorgio Lotti, PhD
Vice President, Global Rare Diseases R&D Pipeline and Portfolio
Chiesi Group

Giorgio Lotti at World Orphan Drug Congress

Samantha Parker
Patient Advocacy and Communication Lead Rare Diseases Europe
Italfarmaco

Samantha Parker at World Orphan Drug Congress

Wills Hughes-Wilson
Head of Patient Access & Commercial Planning
Mereo BioPharma

Wills Hughes-Wilson at World Orphan Drug Congress

Anne-Sophie Chalandon
Head of Global Affairs, Rare Diseases & CGT Policy Speciality Care
Sanofi

Anne-Sophie Chalandon at World Orphan Drug Congress

Marcus Guardian
General Manager
International Horizon Scanning Initiative

Marcus Guardian at World Orphan Drug Congress

Martine Zimmermann
Senior Vice President, Head of Regulatory Affairs, R&D Quality
Ipsen

Martine Zimmermann at World Orphan Drug Congress

Karen Facey
Senior Research Fellow
University of Edinburgh

Karen Facey at World Orphan Drug Congress

Dr Violeta Stoyanova-Beninska
Chair of Committee for Orphan Medicinal Products, EMA
Policy, Regulatory and International Affairs, CBG -MEB

Dr Violeta Stoyanova-Beninska at World Orphan Drug Congress

Fabienne Bartoli
Inspector General for Social Affairs
French Ministry of Health

Fabienne Bartoli at World Orphan Drug Congress

Dr Soraya Bekkali
Senior Vice President, International Commerical Operations
Alexion, AstraZeneca Rare Diseases

Dr Soraya Bekkali at World Orphan Drug Congress

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VIEW 2025 PROSPECTUS

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“Always a great conference, where key players in the rare disease field come together and share ideas, and more importantly, agree on some concrete actions“ – IPSEN

“The leading congress that addresses the subjects most important to patients with rare diseases and treatments by orphan drugs.”
- Alexion, AstraZeneca Rare Disease

“Great access to important colleagues, ability to connect or book time slots on Terrapinn Events App was great, varied sessions and good opportunities to network outside of the sessions”
- Metabolic Support UK

“Great networking opportunities, great panels and discussions!”
- EURORDIS

“Good mix of plenaries and workshops, lots of meeting opportunities, relevant topic selection, very friendly and supportive organizer staff”
- Cerner Enviza

“Excellent organization, very interesting sessions and great networking opportunities.”
- GenCC GmbH

Join the global rare disease community
in Amsterdam

27 - 29 October 2025

Get your ticket now

Strategy, Advocacy & Partnering For
The Global Orphan Drug Industry

The World's Largest Rare Disease Event

2,000+

250+

130+

3

1,500+

15,000+

Early Bird Offer Save €2,100

The Start-to-Finish of Orphan Drugs

From regulation and policy to global pricing and gene therapy

In Partnership With

Advisory Board

Past Sponsors and Exhibitors

Join the global rare disease community
in Amsterdam

27 - 29 October 2025

Get involved at World Orphan Drug Congress Europe 2025

TO SPONSOR

Kieran Duffin
Kieran.Duffin@terrapinn.com

Adam Mayar
Adam.Mayar@terrapinn.com

TO SPEAK

Abdu Kauroo
Abdu.Kauroo@terrapinn.com

MARKETING & PRESS

Jasper Cameron
Jasper.Cameron@terrapinn.com

Stay Up-to-Date

Created by

Strategy, Advocacy & Partnering For The Global Orphan Drug Industry

The World's Largest Rare Disease Event

2,000+

250+

130+

3

1,500+

15,000+

Early Bird Offer Save €2,100

The Start-to-Finish of Orphan Drugs

From regulation and policy to global pricing and gene therapy

In Partnership With

Advisory Board

Past Sponsors and Exhibitors

Join the global rare disease communityin Amsterdam

27 - 29 October 2025

Get involved at World Orphan Drug Congress Europe 2025

TO SPONSOR

Kieran Duffin Kieran.Duffin@terrapinn.com

Adam Mayar Adam.Mayar@terrapinn.com

TO SPEAK

Abdu Kauroo Abdu.Kauroo@terrapinn.com

MARKETING & PRESS

Jasper Cameron Jasper.Cameron@terrapinn.com

Stay Up-to-Date

Created by

Strategy, Advocacy & Partnering For
The Global Orphan Drug Industry

Join the global rare disease community
in Amsterdam

Kieran Duffin
Kieran.Duffin@terrapinn.com

Adam Mayar
Adam.Mayar@terrapinn.com

Abdu Kauroo
Abdu.Kauroo@terrapinn.com

Jasper Cameron
Jasper.Cameron@terrapinn.com