12 - 14 November 2019 | Barcelona
Strategy, advocacy and partnering for the orphan drug industry
500+ Attendees | 275+ Companies | 80% Decision Makers | 150+ Speakers
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What is World Orphan Drug Congress?
World Orphan Drug Congress is Europe's meeting place for the rare disease community. The Conference offers strategic keynote plenaries, themed tracks and dedicated networking sessions, you have the chance to really tailor the event to the needs of your day-to-day role.
Exhibitors have a unique opportunity to put their business products and services in front of potential buyers looking to source the latest technologies in the orphan drugs industry. Meet and listen to biotech start-ups and investors in our Pitch & Partner track where the most promising companies showcase their orphan drug technology and pipeline.
Enjoy discussions on:
Cell & Gene Therapies
Genetic Testing
Gene Editing
Partnering & Investment
Global Market Access
Expanded Access Programs
Real World Evidence
Global Patient Advocacy
Value based pricing & reimbursement
Epidemiology & forecasting
Orphan Drugs Policy
Gene Therapy Development
Together with:
2018 Key Speakers
- Dr Segolene AymeFounder of Orphanet & Rare Disease Expert in ResidenceInsermSophia BrodinDeputy Head of Department, Department of Value Based PricingThe Dental and Pharmaceutical Benefits Agency T.L.V.
- Anna BucsicsProject AdvisorMechanism of Coordinated Access to orphan medicinal products (MoCA)Dr Andreas BuschChief Scientific Officer, Head of Research and DevelopmentShire Pharmaceuticals
- Avril DalyCEORetina InternationalKaren FaceySenior Research FellowUniversity of Edinburgh
- Pamela GavinChief Strategy OfficerNational Organization for Rare DisordersEdmund JessopMedical AdviserNational Health Service
- Dr Greg LarosaSenior Vice President & Head of Scientific Strategy, Rare Disease RUPfizerYann Le CamChief Executive OfficerEURORDIS
- Alastair MackinnonCMOMereo BioPharmaNathalie MollDirector GeneralEFPIA
- Luca SangioriHead of Medical Genetics and Rare Orthopedic DiseasesRizzoli Orthopaedic InstituteAd SchuurmanSenior Advisor International AffairsNational Health Care Institute (ZIN), the Netherlands
- Dr Josep Torrent-FarnellMedicines DepartmentCatalan Health ServiceDr Sander Van DeventerChief Scientific Officer And General ManageruniQure
- Dr Andreas VogelHead of European RegulatoryBluebird BioTill VoigtlanderVice-President of the Board of Members States on ERNsMedical University of Vienna
"It is an important meeting that sheds light on the value patient advocates bring to the development process"
Global Medicines Development Lead - Rare Diseases, Pfizer
Who Attends
AANORA Actelion Pharma Ltd Action Duchenne Addmedica Adelphi Values AGSD (UK) AirLiquide
AKU Society Alcimed Alexion Pharmaceuticals Allaysis LLC Alliance Life Sciences ALS Liga Belgi
Alstrom Syndrome U.K. AMICULUM Anticancer Fund AOP Orphan Pharmaceuticals AG
ArmaGen Technologies, Inc. Atacsia a Fi / Ataxia and Me Ataxia UK aTyr aTyr Pharma
BioBlast Pharma Ltd Biopontis Alliance Blackswan Foundation Brace Pharma Capital
Caligor Rx, Inc. Calypso Biotech SA Capsugel Celgene Centogene AG
Charity Association Neurohereditary Diseases Chiesi Farmaceutici Spa Clear Pharma
Clinart MENA Clinerion Clinigen Global Access Programs Comradis Concenter BioPharma/Silkim Ltd.
Cote Orphan Coulter Partners Covance UK CRF Health CureDuchenne Cures Within Reach
Cydan Development Cytokinetics Daiichi Sankyo Europe GmbH Dipharma SA Diurnal Limited
Dravet Syndrome Foundation Durbin E.C.R.I.N. ECRIN-ERIC ELA Suisse
Emmaus Life Sciences, Inc Ergomed EspeRare Euromedica EuropaBio
European Huntington's Disease Network EURORDIS Euticals Spa EvaluatePharma Ltd
Evidera F.Hoffmann-La Roche Ltd. Facio Therapies BV Federal Joint Committee
F Hoffmann-La Roche French Association Against Friedreich Ataxia Gaucher Disease Russia
Genesis Pharma Genetic Alliance U.K. Genkyotex Innovation Sas Genpharm Genzyme Europe BV
Gerson Lehrman Group Giddi Pharma GlaxoSmithKline Greenovation Biotech GmbH
Grünenthal GmbH GSK Rare Diseases GW Pharmaceuticals Haute Autorite De Sante
Horizon Pharma Inc I.M.S. Health Idis Managed Access Idis Pharma
Imagine - Institut des Maladies génétiques IMS Health INC Research Index Ventures INSERM
Lysogene M3 Pharma S/A Mapi Consultancy Midas Pharma GmbH Minoryx Therapeutics
MPS Society N.O.R.D. National Institute for Health and Care Excellence
National Institutes of Biomedical Innovation, Health and Nutrition
National organisation for rare diseases of Serbia NephCure Kidney International Niemann-Pick UK Novartis
Generate new business
Get your brand, your message and your sales people in front of your customers.
The congress opens doors to fantastic opportunities to form lucrative partnerships and source new ground-breaking solutions.
Join us in Barcelona 12-14 November 2019
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