Mohit Jain is Vice President, Market Access & Pricing, Europe and International at Ascendis Pharma. In this role, he leads market access and pricing strategy across diverse healthcare systems, supporting the development of sustainable pathways for patients to access innovative therapies.
With a focus on the evolving rare-disease landscape, Mohit works at the intersection of evidence generation, value communication, reimbursement, and stakeholder engagement. His perspective is informed by the practical challenges of bringing differentiated treatments to patients across European and international markets, where timely access requires close collaboration among industry, healthcare systems, payers, clinicians, and patient communities.
At the World Orphan Drug Congress 2026, Mohit will contribute to discussions on strategy, advocacy, and partnering in the orphan drug industry, including approaches to advancing equitable and sustainable access for people living with rare diseases.
- What’s in the pipeline and what rare diseases have been targeted?
- How have global launch strategies been impacted by MFN?
- What are the emerging platforms (gene, cell, RNA etc) and novel trial designs for small patient populations?
- How will regulatory pathways accelerate approval, orphan designation and it’s measure overall risk/benefit
- What impacts are new technologies such as AI, Digital Health and medical devices having on the rare disease ecosystem and early diagnosis?
- Have we developed sustainable reimbursement models to fully embrace new these therapies?