The World Orphan Drug Congress is an award-winning event with an exhibition that has grown to become the largest and most established orphan drugs & rare diseases meeting of its kind across the globe.

Now in its 14th annual edition, the World Orphan Drug Congress Europe, together with the co-located Cell & Gene Therapy Congress, will continue to bring experts from the whole value chain under one roof, where you get to meet decision makers in the areas that are most applicable for your business offering.

Covering all the Important Topics

Cell & Gene Therapies
Genetic Testing
Gene Editing
Partnering & Investment 
Global Market Access
Expanded Access Programs
Real World Evidence
Global Patient Advocacy
Value Based Pricing & Reimbursement
Epidemiology & Forecasting
Orphan Drugs Policy
Gene Therapy Development
Clinical Trials
Payers, HTA and Pricing

Conference Tracks




World Orphan Drug Congress 2023
“It's an excellent opportunity to be updated on the most relevant issues for OD and interact with people working in the field.”

- Director Therapeutic Expertise, Rare Disease Laboratorios Biopas
“The program was well balanced and provided many opportunities for exchange on some of the most burning themes.”
- Senior Director Government Relations, Orchard Therapeutics
“Good and relevant topics, smooth organisation of the event, excellent environment to meet peers and stakeholders.
- Head of Government Affairs and Public Policy EMEA & APAC, PTC Therapeutics