The World Orphan Drug Congress is an award-winning event with an exhibition that has grown to become the largest and most established orphan drugs & rare diseases meeting of its kind across the globe.

Now in its 13th annual edition, the World Orphan Drug Congress Europe, together with the co-located Cell & Gene Therapy Congress, will continue to bring experts from the whole value chain under one roof, where you get to meet decision makers in the areas that are most applicable for your business offering.

Covering all the Important Topics

Cell & Gene Therapies
Genetic Testing
Gene Editing
Partnering & Investment 
Global Market Access
Expanded Access Programs
Real World Evidence
Global Patient Advocacy
Value Based Pricing & Reimbursement
Epidemiology & Forecasting
Orphan Drugs Policy
Gene Therapy Development
Clinical Trials
Payers, HTA and Pricing

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“It as a well-organized event and I appreciated the discussions and interesting sessions. Very good to gather both industry and so many patient representatives.”

- President, European Huntington Association
“Good opportunity to get a holistic view of development of the policies in Orphan Drug, and to meet with relevant stakeholders.”

- VP Marketing and Sales, Inceptua Medicines Access
“I attend this event every year and it is the best one to keep updated and network with different stakeholders.“

- Orphan drug policy adviser for Germany


Speaker Hall of Fame