This year’s agenda for the Orphan Drug Congress is filled with comprehensive and future thinking topics. With over 200 speakers and six different streams, this your opportunity to network, discover and initiate life changing discussion.


Learn about new access strategies and negotiations in the Access and Pitching Stream.

Delivery and Manufacture

This year’s Manufacture stream covers industry challenges such as capacity, analytics and regulatory standards.

The Clinical Development stream highlights new innovations in the improvements that are being implemented with the use of biomarkers, within drug discovery and clinical development.

The Cell & Gene congress 2019 highlights the updates within the industry, explores the regulatory challenges and celebrates the innovations discovered throughout the year. 

Precision Medicine

The Precision Medicine Stream is future focused with content AI, machine learning ethics.

Science & Strategy features a variety of case studies from companies such as SOM Biotech and Minoryx. Hear from new companies in our Pitch & Partner sessions.




Enjoy discussions on: 

Cell & Gene Therapies

Genetic Testing

Gene Editing

Partnering & Investment 

Global Market Access

Expanded Access Programs

Real World Evidence

Global Patient Advocacy

Value Based Pricing & Reimbursement

Epidemiology & Forecasting

Orphan Drugs Policy

Gene Therapy Development