2025 Sponsors & Exhibitors

Clinigen is the market leader in Managed Access Programs, enabling pharmaceutical and biotech companies to deliver pre-approval and unlicensed medicines to patients in need worldwide. With more than 35 years’ experience, over 300 active programs...

Parexel is among the world’s largest clinical research organizations (CROs), providing the full range of Phase I to IV clinical development services to help life-saving treatments reach patients faster. Leveraging the breadth of our...

Sanofi is an innovative global healthcare company, driven by one purpose: to chase chasing the miracles of science to improve the health and quality of life of people around the world. Sanofi’extensive geographic footprint, operating  across nearly...

Volv Global is a pioneering AI-driven healthcare intelligence company, delivering unprecedented insights into rare and difficult-to-diagnose diseases. By leveraging population-scale data, Volv helps clinicians and pharmaceutical innovators recognize ...

Worldwide Clinical Trials (Worldwide) is a full-service global contract research organization (CRO) that works in partnership with biotechnology and pharmaceutical companies to create customized solutions that advance new medications – from...

Allucent is on a mission to help bring new therapies to light by solving the distinct challenges of small and mid-sized biotech companies. We’re a global provider of comprehensive drug development solutions, including regulatory consulting, clinical ...

Rare Patient Voice, LLC provides patients and family caregivers an opportunity to participate in all types of healthcare research, including market research, health economics outcomes and real-world evidence, user experience/human factors...

EveryONE Medicines is pioneering a scalable, global framework to design, develop, and manufacture individualized medicines for children with life-threatening neurodegenerative diseases. We are building an integrated, end-to-end system that leverages ...

IQVIA is a leading global provider of clinical research services, commercial insights and healthcare intelligence to the life sciences and healthcare industries. IQVIA’s portfolio of solutions are powered by IQVIA Connected Intelligence™ to deliver...

Sharp Therapeutics is a pre-clinical stage company developing first-choice small-molecule therapeutics for hereditary disorders. The Company's discovery platform combines novel high throughput screening technologies, with compound libraries...

  Regulatory Affairs Advice, Strategy and Support Services for small-medium biopharma and medtech companies. Established in 2006 in the UK to provide a specialist Legal Representative service for non-EU clinical trial sponsors, many of our first...

Medscape Education (medscape.org) is the leading destination for continuous professional development, consisting of more than 30 specialty-focused destinations offering thousands of free CME and CE courses and other educational programs for...

Aixial is a global CRO who have been conducting rare disease and orphan drug clinical trials since 2006.  With deep expertise and a wealth of experience Aixial is well placed to support pharmaceutical and biotech companies by offering a...

The Ataxia Charlevoix-Saguenay Foundation is a federally registered charity founded in 2006 in Montreal by parents of two children affected by Autosomal Recessive Spastic Ataxia of Charlevoix-Saguenay (ARSACS). Its mission is to discover and develop ...

Your global medicines access and clinical trial supplies solution partner. BAP Pharma specialises in providing tailored early and managed access solutions to HCP’s and patients across the globe, the development and production of clinical secondary...

Decisive Consulting Ltd. is a leading consulting firm specializing in providing strategic guidance, advocacy, and partnership opportunities for companies in the orphan drug industry. With a proven track record of success, they offer tailored...

SCN2A is a leading monogenic cause of epilepsy and autism. As in most rare diseases, there is no cure for SCN2A-related disorders. However, recent progress in precision medicine, drug repurposing, and gene therapy are offering hope for treating...

FH Europe Foundation (FHEF) represents the needs of people with familial hyperlipidaemias. Covering both the most common genetic and inherited conditions in the world and the rare conditions, the Foundation acts in the area of advocacy and patient...

Pioneers of Orphan drug access to the global patient community since 2003.  Helping Innovators collect real world data  Helping fund some of the therpaies for those patients who need assitance.  Working to serve the society and not just for...

As the leading kidney research charity in the UK, nothing is going to stop us in our urgent mission to end kidney disease. We’re here to be heard, to make a difference, to change the future. This is a disease that ruins and destroys lives. It must...

Onyx Scientific, the CDMO division of Ipca Laboratories, has specialized in small molecule drug substance development and manufacturing for 25 years. From our MHRA-licensed facilities in the UK, we provide seamless support for early development for...

Proteintech is a leading manufacturer of antibodies, immunoassays, nanobodies, and proteins. With over 300,000 product citations, Proteintech’s comprehensive product portfolio offers antibodies covering 2/3 of the human proteome, all manufactured...

As a business unit of RTI International, we provide global biopharmaceutical companies research and consulting services in health economics, patient-centered outcomes research, market access, and pharmacoepidemiology. As the only...

Volv Global is a pioneering AI-driven healthcare intelligence company, delivering unprecedented insights into rare and difficult-to-diagnose diseases. By leveraging population-scale data, Volv helps clinicians and pharmaceutical innovators recognize ...

Azur Health Science, your premium medical writing and consulting agency, experts in rare disease With a team of expert writers, Azur Health Science offers a full-service regulatory writing consultancy in rare disease and precision...

BioMe, Inc. is a pre-clinical stage biotechnology company dedicated to transforming human healthcare through microbiome-based therapeutics. Leveraging its proprietary SURE™ platform, BioMe establishes clear disease–microbiome connections and...

Cellbyte supports global and local Commercial Pharma teams in the successful launch of new medicines. Its AI-based platform enables users to automate workflows across regulatory data, HTA assessments, and pricing information, or extract targeted...

Phenotypic screening is a versatile and impactful tool in the quest to develop therapies for rare disorders. By leveraging unbiased, functional approaches in disease-relevant cellular systems, this method overcomes many of the limitations of...

Netabolics is a pioneering biotech company specializing in AI-driven biosimulation to decode the complexities of human biology. By integrating computational dynamical modeling with multiomics data, Netabolics enables precise identification and...

NeuroCores, Inc. is a preclinical biotech company that is revolutionizing the treatment of rare pediatric diseases.Our lead asset is KIT-13, a novel oral small molecule drug targeting Rett Syndrome, a rare genetic neurological disorder.NeuroCores is ...

PharmaKrysto is a biopharma company focusd on developing new treatments for patients living with rare kidney disease.  Our lead programme is a small-molecule solution to the frequent formation of kidney stones in people with cystinuria. 

Trialize cuts the biggest operational pain‑points in clinical trials It turns the slowest, most error‑prone parts of trial operations into automated, real‑time workflows — compressing timelines and boosting data quality in one step.   Start‑up...

Unboxed Psychology is a behaviour science consultancy specialising in health psychology and behaviour change principles. Providing strategic services across healthcare working with pharmaceutical and biotech companies to infuse behaviour science...