Sponsors & Exhibitors

HomeNurse4U is a specialized Home Healthcare company offering mobile nursing solutions in clinical trials. They provide high quality care and support to patients in the comfort of their own homes or at any other place which is convenient to the...

Established in 2006 to provide a specialist Legal Representative service for non-EU clinical trial sponsors. Many of our first clients remain working with us today as we have grown alongside them to fit their evolving needs and developed a complete...

Illingworth Research Group are the leading global provider of GCP Research Nurses (RN) to conduct clinical trial visits in the patient’s home, school, or place of work. Our patient focused solutions company also provides a high caliber Patient...

Intexo Società Benefit is a leading Italian company working in Market Access and Regulatory affairs. We design and carry out integrated Patient Access projects. Our goal is to ensure that patients obtain early access to new therapies through a...

Rare Patient Voice, LLC was founded in 2013 by industry veteran Wes Michael to provide patients and family caregivers a chance to be heard through taking part in all types of research. RPV was built on a foundation of direct connections and word of ...

Remap Remap Consulting is a specialist pricing, reimbursement and market access consultancy offering an integrated, evidence-based approach to optimising market access. Our strength lies in our ability to understand the market access challenges from ...

Aptadel Therapeutics is a pre-clinical stage drug development biotech company based on RNA Aptamer technology for the treatment of cancer. Its Aptamer technology is a delivery tool platform for different therapeutic agents...

ASPIRE BIOSCIENCES works relentlessly to find new treatments for unaddressed rare diseases. We use our novel methodology to identify opportunities for treatment development, then create and nurture working partnerships between rare disease patient...

CRISP-HR is a seed-stage therapeutics company that tackles the problem of mutation diversity of heritable human disease by correcting mutations over thousands of basepairs, restoring healthy gene function and allowing us to use a single therapeutic...

At CVGenome we design and execute personalized strategic plans to identify the genetic cause of your disease. We apply our knowledge and expertise to generate highly accurate DNA sequencing and expression data which combined with in-depth analysis...

My name is Claudio from Cure Rare and We are rare disease navigators.When my son Dario was diagnosed with a rare, then incurable disease, a world fell apart. We since then totally changed the perspective of my son – We established therapy...

EveryONE Medicine is working to enable early, precision diagnosis and rapid development of personalized therapies targeting 'N1+' genetic variants causing severe CNS disorders.The term “N1+” encompasses true N-of-1 (1 single patient with a...

Gate2Brain’s technology is based on a technological platform for the transport of drugs to the brain, with the characteristic of being potentially capable of crossing the Blood-Brain Barrier (BBB), which prevents the transport of therapeutic loads...

GeneScape is a pioneering technology company specializing in advanced genomic solutions and data analysis, with a strong focus on drug development for inherited rare or orphan diseases. We support variant calling, patient selection and epidemiology...

Geneial is a secure biomedical data network connecting diverse orphan disease communities with healthcare and biopharma researchers to accelerate research and advance precision care. We offer a privacy- and ownership-preserving patient registry...

Our vision is to devise cancer therapies without side effects. Therefore, GenCC uses the CRISPR/Cas technology to develop a method to quickly and cost-effectively identify and test suitable targets in the DNA of tumor cells. This enables us to...

Jenthera Therapeutics develops a novel and proprietary targeted non-viral gene editing platform that directly addresses the critical limitations of current gene editing systems and aims to unlock transformative therapeutic avenues in drug...

Imagine a pediatric-specific engagement platform, fully co-designed with children and child life specialists. The Little Journey app helps to reduce anxiety before, during and after hospital visits by educating and preparing children and families...

Lyfegen is a global software platform that helps to reduce the cost of drugs by enabling value-based contracting. With the Lyfegen platform, health insurance, governments and pharma companies are able to negotiate, implement and manage value-based...

MDVerse makes advanced cell and gene therapies accessible, revolutionizing the regenerative medicine supply chain with state-of-the-art software, analytics, and AI/ML. We empower CDMOs, pharma, and academic institutions to deliver regenerative...

Medace is committed to bring the (bio)medical innovations (ATMPs, biopharmaceuticals & medical devices) of start-ups and academics to the market and patients faster. By sharing our expertise, infrastructure, Quality Management System (QMS), and...

We help Rare Disease and Advanced Therapies Biotechs to raise funds and secure best-in-class leadership teams. 

Navega Therapeutics, a spin-off out of the University of California San Diego, is a pre-clinical stage developing epigenetic gene therapies with co-lead program in retinitis pigmentosa and chronic pain. Some company highlights: next-generation of...

NEUROSPEAR Co Ltd is a spin-off startup company from Daegu Catholic University School of Medicine, and focused on the development of transcranial electric field treatment (TEFT) as an electroceutical targeting neurotoxic iron deposit associated with ...

Phormulate is a patient-centric healthcare company, dedicated to empowering individuals on their health journey. Our mission is to ensure that every patient has access to the resources they need to enhance their well-being.Through our platform, we...

I would like to introduce you to my start-up Prizm Tx (www.prizmtx.com) a clinical-stage rare disease biotech. Founded the company in late 2020 and is based out of Arizona, USA.  We are developing a platform that comprises of a main asset, SRW101...

REACH is an independent pharmaceutical market research company focused on rare and niche diseases. We are a values-driven team that cares deeply about each other and the partners and customers with whom we work. With decades of experience in...

Our mission at redthread is to help pharma and biotech develop brilliant written communications for payers. Tired of writers who don’t understand how to write for payers? Or consultants who can’t write? Our market access and value communications...

The Salve is a medical affairs consultancy designed to creative positive impact in healthcare through remarkable and purposeful communications. We work with global pharmaceutical and biotechnology companies to support a variety of medical affairs...

TMA Precision Health uses AI driven data and discovery to unlock new therapies for genetic disease. We take a patient-first approach driven by the whole genome, which gives us the ability to explore the nature of complex genetic disease. With our...

Transmineo uses digital technologies to enable the demonstration of real-world value that addresses payer concerns, supporting a smart future proof commercialization model for orphan drugs and other highly personalized treatments.Driven by the...

We are a target discovery platform with the only technology capable to model and validate the key genetic relationships underlying random cell behavior.DescriptionWe are the only technology capable of reproducing the architecture of the...