WHY ATTEND

The World's Largest Rare Disease Event

26-28 October 2026
RAI Convention Center, Amsterdam

Premium Conference

Learn from world KOLs in rare diseases on the latest in diagnosis, AI, NBS, gene therapy, clinical trials and patient access. Ensure that you are equipped with the most recent policy and governmental changes in OMP legislation and EUHTA.

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Busy Exhibition

With a footfall of 1,800+ attendees, exhibitors will get to speak directly to their target market, expand sales leads, strengthen and establish their brand and close deals with customers on-site.

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Limitless Networking

Get access to our dedicated event app (5 weeks before the event), see all of our 1,800+ attendees and set up 1-2-1 meetings* to maximise your ROI in attending the congress.

*A ticket with full app access is required to use all messaging and meeting features

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World Orphan Drug Congress 2026 | Start-up and Biotech Zone

Start-up & Biotech Zone

Meet start-ups or pitch your company at the leading rare disease congress. Meet new companies that can help your business or investors that can take you to the next level.

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Workshops

Host or participate in our pre-congress workshops where we deep dive into topics including AI, early access, patient journey, RD action plan and EU joint clinical assessment with all stakeholders.

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Working Groups

Be part of a NEW format – our working groups. Replacing roundtables, these sessions are intimate discussions and one of the best ways to find out what your target audience wants.

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Patient Zone

Our patient zone provides you with the unique opportunity to engage with Patient Advocacy Groups and ERNs who are at the heart of the rare disease community.

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Media Zone

The media zone will be bustling with all of the biggest names in the rare disease world. Witness live interviews and use our zone to announce press releases and social media outreach to maximise your presence.

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Amsterdam

We’re moving to Amsterdam! The heart of where the EMA, RIVM and ZIN are, as well as some of the strongest ERN networks and biotech hubs. Join us at our newest venue for a state of the art experience.

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Early Bird Tickets - Save up to 60%

Join 1,800 attendees at the world's largest orphan drug and rare disease event.

This is your best opportunity in 2026 to network with professionals in the rare disease industry.

250+ Speakers

Fabienne Bartoli
Inspector General
French National Authority for Health

Stine Bosse
MEP Renew Group Europe
European Parliament
Karen Facey
Chair HTAi Rare Disease Interest Group
University of Edinburgh

Niklas Hedberg
Head Of Pharmacy
Tandvards och Lakemedelsformansverket
Kaja Kantorska
Health and Food Safety Directorate General
European Commission

Yann Le Cam
Advisor
VOZ Advisors
Alexander Natz
Secretary General
EUCOPE - European Confederation of Pharmaceutical Entrepreneurs

Jonathan Neal
Head of Central, South and Eastern Europe Takeda and EFPIA European Markets Committee
Takeda
Francesc Palau
Distinguished Investigator
SJD Barcelona Children's Hospital

Sonia Pulido Sánchez
Co-Chair of the Subgroup for Joint Scientific Consultations of the HTACG
AEMPS
Violeta Stoyanova-Beninska
Senior Scientific Specialist at Human Division EMA, Chair of Regulatory Science Committee, IRDiRC, former Chair of COMP at EMA
EMA

Anne Willemsen
Co-chair JCA Subgroup
Zorginstituut Nederland
P.J. Brooks
Deputy Director, Division of Rare Diseases Research Innovation, Member of IRDiRC Funders Constituent Committee (FCC)
NIH/NCATS

Alexis Arzimanoglou
Coordinator of the European Reference Network for Rare and Complex Epilepsies
EpiCARE
Thomas Butt
Executive Director, Health Economics & Outcomes Research
Biomarin

Matthew Klein
Chief Executive Officer
PTC Therapeutics
Samantha Parker
Patient Engagement Lead Rare Diseases and Vice Chair of IRDiRC
italfarmaco

Durhane Wong-Rieger
President, Chief Executive Officer
Canadian Organisation for Rare Disorder & Rare Diseases International