THE WORLD'S LEADING ORPHAN DRUG EVENT

 

 

What is World Orphan Drug Congress?


The World Orphan Drug Congress is the largest and most established orphan drugs & rare diseases meeting of its kind across the globe.

Conference

Covering cell & gene therapy, genetic testing, market access, real world evidence, orphan drugs policy and much more
 

Exhibition

130+ leading solution providers from across the globe, featuring new ways of thinking and novel partnerships to generate solutions.
 

APPLY TO SPONSOR/EXHIBIT

Networking

Networking is at the heart of World Orphan Drug Congress. Our congress allows you to connect directly with thousands of pharma experts across 3 days of built-in 1-2-1 networking  

GET YOUR TICKET NOW

The Start-to-Finish of Orphan Drugs

From regulation and policy to global pricing and gene therapy

Cell & Gene Therapies
Genetic Testing
Gene Editing
Partnering & Investment 
Global Market Access
Expanded Access Programs
Real World Evidence
Global Patient Advocacy
Value Based Pricing & Reimbursement
Epidemiology & Forecasting
Orphan Drugs Policy
Gene Therapy Development
Clinical Trials
Payers, HTA and Pricing
Manufacture

Early Bird Offer Save €1,500

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2024 Speakers

 

  • Alicia Gil at World Orphan Drug Congress 2024
    Alicia Gil
    CEO&Owner
    Omakase Consulting
    Christopher Rudolf at World Orphan Drug Congress 2024
    Christopher Rudolf
    Founder and Chief Executive Officer
    volv global
  • José Ángel Aibar at World Orphan Drug Congress 2024
    José Ángel Aibar
    President
    Dravet Syndrome Foundation
    Fabienne Bartoli at World Orphan Drug Congress 2024
    Fabienne Bartoli
    Inspector General
    French National Authority for Health
  • Anne-Sophie Chalandon at World Orphan Drug Congress 2024
    Anne-Sophie Chalandon
    Head of Global Public Affairs, Rare Diseases and CGT Policies
    Sanofi
    Charlotte Chanson at World Orphan Drug Congress 2024
    Charlotte Chanson
    Director Global Diagnostics
    Orchard Therapeutics
  • Toon Digneffe at World Orphan Drug Congress 2024
    Toon Digneffe
    Head, Public Affairs & Public Policy, Europe & Canada
    Takeda
    Josie Godfrey at World Orphan Drug Congress 2024
    Josie Godfrey
    Director
    JG Zebra Consulting
  • Alexandra Heumber Perry at World Orphan Drug Congress 2024
    Alexandra Heumber Perry
    Chief Executive Officer
    Rare Diseases International
    Daria Julkowska at World Orphan Drug Congress 2024
    Daria Julkowska
    Assistant Director, Thematic Institute of Genetics, Genomics & Bioinformatics
    EJP RD - IRDiRC
  • Yann Le Cam at World Orphan Drug Congress 2024
    Yann Le Cam
    Founder and past-CEO
    EURORDIS
    Paolo Martini at World Orphan Drug Congress 2024
    Paolo Martini
    Chief Scientific Officer Rare Diseases, Hematology and External R&D
    Moderna, Inc.
  • Lucy Mckay at World Orphan Drug Congress 2024
    Lucy Mckay
    Chief Executive Officer
    Medics4RareDiseases
    Alexander Natz at World Orphan Drug Congress 2024
    Alexander Natz
    Secretary General
    EUCOPE - European Confederation of Pharmaceutical Entrepreneurs
  • Daniel O'Connor at World Orphan Drug Congress 2024
    Daniel O'Connor
    Director, Regulatory Policy & Early Access
    ABPI
    Kacper Rucinski at World Orphan Drug Congress 2024
    Kacper Rucinski
    Executive Committee Member
    SMA Europe
  • Adrien Samson at World Orphan Drug Congress 2024
    Adrien Samson
    Healthcare Policy Senior Manager
    EuropaBio
    Maurizio Scarpa at World Orphan Drug Congress 2024
    Maurizio Scarpa
    Director, Coordinating Center For Rare Diseases
    MetabERN
  • Sophie Schmitz at World Orphan Drug Congress 2024
    Sophie Schmitz
    Managing Partner
    Partners4Access
    Nick Sireau at World Orphan Drug Congress 2024
    Nick Sireau
    Chair and Chief Executive Officer
    AKU Society
  • Claire Skentelbery at World Orphan Drug Congress 2024
    Claire Skentelbery
    Director General
    EuropaBio
    Violeta Stoyanova-Beninska at World Orphan Drug Congress 2024
    Violeta Stoyanova-Beninska
    Chair of Committee for Orphan Medicinal Products
    Medicines Evaluation Board
  • Anton Ussi at World Orphan Drug Congress 2024
    Anton Ussi
    Operations Director
    EATRIS ERIC
    Leon van Wouwe at World Orphan Drug Congress 2024
    Leon van Wouwe
    Clinical Innovation Director
    volv global
  • Mary Wang at World Orphan Drug Congress 2024
    Mary Wang
    Programme Director
    Rare Diseases International
    Durhane Wong-Rieger at World Orphan Drug Congress 2024
    Durhane Wong-Rieger
    President, Chief Executive Officer & Chair
    Canadian Organisation for Rare Disorder & Rare Diseases International
  • Heidi Livingstone at World Orphan Drug Congress 2024
    Heidi Livingstone
    Senior Public Involvement Adviser
    National Institute for Health and Care Excellence
    Martine Zimmermann at World Orphan Drug Congress 2024
    Martine Zimmermann
    Senior Vice President, Head of Global Regulatory Affairs
    Ipsen
  • Wills Hughes-Wilson at World Orphan Drug Congress 2024
    Wills Hughes-Wilson
    Chief Patient Access & Commercial Planning
    Mereo Biopharma
    Enrico Piccinini at World Orphan Drug Congress 2024
    Enrico Piccinini
    Head of Europe Rare Diseases
    Chiesi Group
  • Sheela Upadhyaya at World Orphan Drug Congress 2024
    Sheela Upadhyaya
    Life Sciences Consultant
    Openflex Ltd
    Dennis Akkaya at World Orphan Drug Congress 2024
    Dennis Akkaya
    Chief Commercial Officer
    myTomorrows
  • Stelios Kympouropoulos at World Orphan Drug Congress 2024
    Stelios Kympouropoulos
    MEP
    European Parliament
    Virginie Bros-Facer at World Orphan Drug Congress 2024
    Virginie Bros-Facer
    CEO
    EURORDIS
  • Avril Daly at World Orphan Drug Congress 2024
    Avril Daly
    President
    Eurordis - Rare Diseases Europe
    Judith Fernandez at World Orphan Drug Congress 2024
    Judith Fernandez
    Deputy Director - HTA department
    Haute Aurotité de santé (HAS)
  • Kate Holliday at World Orphan Drug Congress 2024
    Kate Holliday
    Chief Executive
    CCDR/Pathways Telehealth Nurse Service
    Matt Bolz-Johnson at World Orphan Drug Congress 2024
    Matt Bolz-Johnson
    Mental Health Lead & Healthcare Advisor
    EURORDIS
  • Ken Kengatharan at World Orphan Drug Congress 2024
    Ken Kengatharan
    Managing General Partner
    Atheneos Ventures
    Tim Leest at World Orphan Drug Congress 2024
    Tim Leest
    Clinical Assessor Efficacy and Safety
    F.A.M.H.P
  • Frauke Naumann Winter at World Orphan Drug Congress 2024
    Frauke Naumann Winter
    Head of Unit
    BfArM
    Francis Pang at World Orphan Drug Congress 2024
    Francis Pang
    SVP Global Market Access and Geographic Expansion
    Orchard Therapeutics
  • Samantha Parker at World Orphan Drug Congress 2024
    Samantha Parker
    Patient Advocacy and Communication Lead Rare Diseases Europe
    Italfarmaco
    Karen Malone at World Orphan Drug Congress 2024
    Karen Malone
    Chief Executive Officer/Founder
    GeneScape
  • Andrew Mumford at World Orphan Drug Congress 2024
    Andrew Mumford
    Chief Executive Officer
    Initiate Consultancy
    Rachel Smith at World Orphan Drug Congress 2024
    Rachel Smith
    Global Head, Rare Disease
    Parexel
  • Soraya Bekkali at World Orphan Drug Congress 2024
    Soraya Bekkali
    SVP Commercial International
    Alexion Pharmaceuticals
    Stefano Portolano at World Orphan Drug Congress 2024
    Stefano Portolano
    CEO
    Azafaros
  • Lara Bloom at World Orphan Drug Congress 2024
    Lara Bloom
    President and CEO
    The Ehlers-Danlos Society
    Beatriz Carmona-Hidalgo at World Orphan Drug Congress 2024
    Beatriz Carmona-Hidalgo
    Postdoctoral Researcher
    Junta de Andalucía
  • Burcu Eryilmaz at World Orphan Drug Congress 2024
    Burcu Eryilmaz
    Global Rare Diseases Franchise Head
    Sanofi
    Simona Giorgi at World Orphan Drug Congress 2024
    Simona Giorgi
    Scientific Director
    Dravet Syndrome Foundation Spain
  • Vinciane Pirard at World Orphan Drug Congress 2024
    Vinciane Pirard
    Medical - SAI
    Sanofi
    Manuel Carrondo at World Orphan Drug Congress 2024
    Manuel Carrondo
    Professor
    iBET: Instituto de Biologia Experimental e Tecnológica
  • Angela Columbano at World Orphan Drug Congress 2024
    Angela Columbano
    Head Business Development Partnership
    GENETHON
    Jean-Philippe Combal at World Orphan Drug Congress 2024
    Jean-Philippe Combal
    Co-Founder And Chief Executive Officer
    Vivet Therapeutics
  • Emma Eatwell at World Orphan Drug Congress 2024
    Emma Eatwell
    Global Practice Director, Health & Life Sciences
    Global Counsel
    Giorgio Iotti at World Orphan Drug Congress 2024
    Giorgio Iotti
    Head Of Pipeline and Portfolio Leadership, Global Rare Diseases R&D
    Chiesi Farmaceutici SpA
  • David Lyzwa at World Orphan Drug Congress 2024
    David Lyzwa
    Head of Clinical Development
    JJP Biologics
    Paolo Morgese at World Orphan Drug Congress 2024
    Paolo Morgese
    Vice President, Public Affairs, Europe
    Alliance for Regenerative Medicine
  • Jon Neal at World Orphan Drug Congress 2024
    Jon Neal
    Head Pipeline & Portfolio Europe & Canada
    Takeda
    Nicole Verdun at World Orphan Drug Congress 2024
    Nicole Verdun
    Super Office Director
    Food and Drug Administration
  • Elisabetta Zanon at World Orphan Drug Congress 2024
    Elisabetta Zanon
    Director, European Policy and Advocacy
    Alliance for Regenerative Medicine
    Lauren Kopsick at World Orphan Drug Congress 2024
    Lauren Kopsick
    Founder and Executive Director
    The Healthcare Navigation Project
  • Victor Maertens at World Orphan Drug Congress 2024
    Victor Maertens
    Government Affairs Manager
    European Confederation of Pharmaceutical Entrepreneurs
    Camelia Isaic at World Orphan Drug Congress 2024
    Camelia Isaic
    Chairwoman
    HAE Junior patient organization
  • Annabel de Maria at World Orphan Drug Congress 2024
    Annabel de Maria
    Chief Patient Officer
    Alira Health
    Jessica Roberts at World Orphan Drug Congress 2024
    Jessica Roberts
    Director, Pharmacometrics
    Allucent
  • Nicky Wisener at World Orphan Drug Congress 2024
    Nicky Wisener
    Vice-President of Business Development
    Clinigen Group
    Debra Bellon at World Orphan Drug Congress 2024
    Debra Bellon
    Strategic Engagement Manager
    Rare Diseases International
  • Emma James at World Orphan Drug Congress 2024
    Emma James
    Vice President, Medical & Patient Affairs
    Encoded Therapeutics
    Kirsten Johnson at World Orphan Drug Congress 2024
    Kirsten Johnson
    Board Member
    EURORDIS
  • Marisol Montolio at World Orphan Drug Congress 2024
    Marisol Montolio
    Director of Research
    Duchenne Parent Project Spain
    Tom Pulles, MD at World Orphan Drug Congress 2024
    Tom Pulles, MD
    VP, Head of Medical Affairs & Patient Advocacy, Europe
    Acadia Pharmaceuticals Inc.
  • Alicia Granados at World Orphan Drug Congress 2024
    Alicia Granados
    Head, Global Rare Diseases Medical Scientific Advocacy
    SANOFI

 

In Partnership with

Beacon World Orphan Drug Congress 2023 Supporting Partner

Dravet World Orphan Drug Congress 2023 Supporting Partner

EURORDIS World Orphan Drug Congress 2023 Supporting Partner

ERICA World Orphan Drug Congress 2023 Supporting Partner

CataloniaBio & HealthTech World Vaccine Congress Europe 2023 Supporting Partner

EuropaBio World Orphan Drug Congress 2023 Supporting Partner

Title Sponsor

 

 

Alexion

 

2024 Sponsors and Exhibitors

 

  • Title Sponsor

    Alexion – AstraZeneca Rare Disease at World Orphan Drug Congress 2024

    Diamond Sponsor

    Clinigen Group at World Orphan Drug Congress 2024
  • Platinum Sponsor

    Pfizer at World Orphan Drug Congress 2024

    Platinum Sponsor

    Sanofi at World Orphan Drug Congress 2024
  • Platinum Sponsor

    UCB at World Orphan Drug Congress 2024

    Platinum Sponsor

    volv global at World Orphan Drug Congress 2024
  • Gold Sponsor

    Allucent at World Orphan Drug Congress 2024

    Gold Sponsor

    Ascellahealth at World Orphan Drug Congress 2024
  • Gold Sponsor

    Chiesi Global Rare Diseases at World Orphan Drug Congress 2024

    Gold Sponsor

    CRA, Charles River Associates at World Orphan Drug Congress 2024
  • Gold Sponsor

    Partners4Access at World Orphan Drug Congress 2024

    Silver Sponsor

    Initiate at World Orphan Drug Congress 2024
  • Silver Sponsor

    Marken at World Orphan Drug Congress 2024

    Silver Sponsor

    Mendelian at World Orphan Drug Congress 2024
  • Silver Sponsor

    Omakase Consulting at World Orphan Drug Congress 2024

    Silver Sponsor

    Pharma Business Partners at World Orphan Drug Congress 2024
  • Silver Sponsor

    Premier Research at World Orphan Drug Congress 2024

    Silver Sponsor

    Prime at World Orphan Drug Congress 2024
  • Silver Sponsor

    Remap Consulting at World Orphan Drug Congress 2024

    Silver Sponsor

    Veristat at World Orphan Drug Congress 2024
  • Silver Sponsor

    WEP Clinical at World Orphan Drug Congress 2024

    Silver Sponsor

    Worldwide Clinical Trials at World Orphan Drug Congress 2024
  • Bronze Sponsor

    Alira Health at World Orphan Drug Congress 2024

    Bronze Sponsor

    Cascador Health at World Orphan Drug Congress 2024
  • Bronze Sponsor

    GeneScape at World Orphan Drug Congress 2024

    Exhibitor

    Alchemist Consulting Ltd at World Orphan Drug Congress 2024
  • Exhibitor

    BAP Pharma at World Orphan Drug Congress 2024

    Exhibitor

    Centogene at World Orphan Drug Congress 2024
  • Exhibitor

    Dravet Syndrome Foundation at World Orphan Drug Congress 2024

    Exhibitor

    Inserm at World Orphan Drug Congress 2024
  • Exhibitor

    Only Orphans Cote at World Orphan Drug Congress 2024

    Exhibitor

    PDC CRO at World Orphan Drug Congress 2024
  • Exhibitor

    QuickSTAT Global Life Science Logistics at World Orphan Drug Congress 2024

    Exhibitor

    SKC Beratungsgesellschaft at World Orphan Drug Congress 2024
  • Startup

    Ablevia biotech Gmbh at World Orphan Drug Congress 2024

    Startup

    EveryONE Medicines at World Orphan Drug Congress 2024
  • Startup

    Mukherjee-Consultants at World Orphan Drug Congress 2024

    Startup

    Red Thread Market Access Ltd at World Orphan Drug Congress 2024

 

 

 

Remaining marketing opportunities for world-class solution providers are selling fast.
Contact: michael.hodge@terrapinn.com

 

“Always a great conference, where key players in the rare disease field come together and share ideas, and more importantly, agree on some concrete actions“ – IPSEN
“The leading congress that addresses the subjects most important to patients with rare diseases and treatments by orphan drugs.”
- Alexion, AstraZeneca Rare Disease
“Great access to important colleagues, ability to connect or book time slots on Terrapinn Events App was great, varied sessions and good opportunities to network outside of the sessions”
- Metabolic Support UK
“Great networking opportunities, great panels and discussions!”
- EURORDIS
“Good mix of plenaries and workshops, lots of meeting opportunities, relevant topic selection, very friendly and supportive organizer staff”
- Cerner Enviza
“Excellent organization, very interesting sessions and great networking opportunities.”
- GenCC GmbH

 

Join the Global Orphan Drug Community in Barcelona

22 - 25 October 2024, Barcelona
 

 

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