Day 1 - Tuesday 28 October @ 13:00
Start-ups Pitches
13:00: Dr Mona Boyé, CBDO, Ksilink: Automation and high throughput phenotypic screening of patient-based cellular systems for novel treatment options for rare diseases
13:05: Dr Boris Sevarika, Co-Founder & CEO, NanoZymeX: Overcoming Limitations of Current Enzyme Replacement Therapies
13:10: Dr William Jang, Head of Global BD, BioMe
13:15: Dr Sumira Riaz, Founder & Health Psychologist, Unboxed Psychology: Applications of behaviour science: Introducing Unboxed Psychology
13:20: Leonid Stoianov, CEO, Trialize
13:25: Julian Howell, M.D., Founder & CEO, PharmaKrysto: Cystinuria – new approaches to preventing cystine stones – moving to clinical development
13:30: Fabrice Lejeune, CSO, Genvade Therapeutics: Overcoming the Nonsense in Genetic Diseases
13:35: Dr Alistair Irvine, CEO, Scarlet Therapeutics
13:40: Flaminia Macchia, COO, ORPHANET-AISBL
13:45: Vincent Leveque, Co-Founder & CEO, Mirava Bio: Breaking Barriers: Bringing Rare Disease Therapies to Patients in Europe
Sumira Riaz, Founder, Health Psychologist & Patient Engagement Consultant,
Unboxed Psychology

Dr Sumira Riaz (DPsych), Chartered Health Psychologist and Patient Engagement Consultant, Unboxed PsychologyDr Sumira Riaz is a Registered Health Psychologist, Cognitive Behavioural Therapist and Founder of Unboxed Psychology, a behaviour change, patient engagement consultancy. Sumira has 18 years...
William Jang, Managing Director of Global Business Development,
BioMe, Inc.

William Jang is a biotechnology executive specializing in the development and global commercialization of microbiome-based therapeutics. He currently serves as Head of Global Business Development at BioMe, Inc., where he drives strategic partnerships, investment initiatives, and regulatory...
Leonid Stoianov, CEO,
Trialize

CEO of Trialize. Chairman of HL7 UA.
Julian Howell, CEO,
PharmaKrysto Ltd

Julian is the co-founder and leader of PharmaKrysto, a company focused on developing new treatments for people living with rare kidney disease. He has many years of clinical development, translational science and early stage company formation and funding.
Fabrice Lejeune, CSO,
Genvade Therapeutics

Dr. Fabrice Lejeune is the Scientific Advisor & co-Founder of Genvade Therapeutics. He is the author and inventor of the patents for the lead candidate GV-01 and the drug screening platform. He has been a scientific leader in the search for nonsense mutation correctors for over 20 years. He is...
Alistair Irvine, Chief Executive Officer,
Scarlet Therapeutics

Alistair Irvine, PhD, joined Scarlet as Founding CEO in August 2022. He is an experienced biotech and medtech executive who has worked in the industry for >30 years and has broad international executive and R&D experience. Previous to Scarlet, he was Chief Business Officer at Kuros...
Vincent Lévêque, Co-founder & CEO,
Mirava Bio

Vincent Lévêque is a biotech executive with nearly two decades of experience in rare diseases, advanced therapies, and gene therapy commercialization. He has built and led cross-functional organisations across Europe, the Middle East, and Eurasia, with a proven track record of launching...
Flaminia Macchia, Chief Operating Officer,
ORPHANET-AISBL

Flaminia currently serves as the Chief Operating Officer of the Orphanet-AISBL, and as Senior Policy Advisor to different organisations on an independent basis. Flaminia has a broad range of experiences from the patient community, the private sector, as well as the EU institutions. Indeed, Flaminia ...