2017 ATTENDEES

 

 

Organisation
Job Title
  • AbbVie
    Vice President of Global Regulatory Strategy
  • Abeona Therapeutics
    President and CEO
  • Abeona Therapeutics Inc.
    Vice President, Patient Advocacy
  • Action Duchenne
    Director of Research
  • Agility Clinical, Inc.
    EVP Business Operations
  • Agility Clinical, Inc.
    CEO
  • Agility Clinical, Inc.
    EVP PM Clinical Operations
  • Agios Pharmaceuticals
    Senior Director, Rare Genetic Disease Marketing
  • Alexion Pharmaceuticals
    Senior Vice President, Head of Global Regulatory Affairs
  • Alpha 1 UK
    Director of Rare Access and Trustee
  • ALS Liga Belgi
    CEO
  • Amicus Therapeutics
    Head Patient Advocacy - International
  • Amicus Therapeutics Inc
    VP of Global Market Access
  • Armetheon Inc
    Managing Director, Atheneos Capital and Chairman
  • Atacsia a Fi / Ataxia and Me
    Founder
  • Ataxia
    Research Officer
  • Biogen
    Associate Director of Public Policy and Government Affairs
  • Biogen International GmbH
    EU+ Head of Medical Affairs, SMA
  • Biomarin
    Assoc. Dir Development Sciences
  • BioMarin
    Manager Regulatory Affairs
  • Biomedical Systems
    Director BD EU
  • bluebird bio
    Vice President of Clinical Development Operations
  • Braincures
    CEO
  • Braincures
    CEO
  • BresMed
    Senior Insights Analyst
  • Bristol Myers Squibb
    Executive Director, WWHEOR Markets
  • Cambridge Rare Disease Network
    CEO & Founder, Alström Syndrome UK and Chief Executive Officer
  • Caribou Biosciences
    President and Chief Executive Officer
  • CatSalut, Catalunya Health Service
    Director
  • CBG - MEB
    Senior Clinical Assessor
  • Cellectis Therapeutics
    Executive Vice President and Chief Operating Officer
  • Cello Health
    Director
  • Cello Health
    Content & Communications Manager
  • Cello Health Public Affairs
    Managing Partner
  • Chiesi
    Global Pricing & Market Access Specialist
  • CHIESI Farmaceutici Spa
    Project Lead
  • CHIESI FARMACEUTICI SPA
    Global Pricing & Market Access Specialist
  • Clinerion
    Head of Sales
  • Clinigen Group
    Business Development Director
  • Colorado BioScience Association
    Communications and Membership Manager
  • Complete HealthVizion
    Scientific Director
  • Complete HealthVizion
    Head of Operations
  • Complete HealthVizion
    Scientific Director
  • Comradis
    Agency Lead
  • Cote Orphan, a QuintilesIMS Company
    Senior Business Development Representative
  • Cote Orphan, a QuintilesIMS Company
    Senior Business Development Representative
  • Coulter Partners
    Associate Director
  • Croatian Alliance for Rare Diseases
    Project Manager
  • Dolon
    Managing Director
  • Dolon
    Managing Director
  • Dolon
    Director
  • Dracaena Consulting
    Principal
  • Duchenne Parent Project Spain
    Scientific Director
  • Duchenne U.K.
    Co-founder
  • Duchenne U.K.
    Director of Research and patient engagement
  • Eczacibasi
    Director of Business Development
  • Eczacibasi
    In-House Senior Business Development Consultant
  • Emerge Health Pty Ltd
    Head of Commercial Operations
  • Ergomed
    Global Head of Business Development
  • EUCOPE
    Secretary General
  • Euromed
    Corporate Business Development
  • European Medicines Agency
    Chair, Committee for Orphan Medicinal Products (COMP)
  • EURORDIS
    Chief Executive Officer
  • EURORDIS
    Corporate and Foundation Relations Director
  • Facio Therapies BV
    Managing Director
  • Facio Therapies BV
    Managing Director
  • Findacure
    Scientific Officer
  • Fondazione Telethon
    Head of Research Development Office
  • G-BA
    Scientific Advisor
  • Genethon
    Chief Executive Officer
  • Genetic Alliance U.K.
    Ambassador
  • GenSight Biologics
    Project Director
  • Gensight Biologics
    Project Director
  • Georgia Biotech Association
    Marketing
  • GlaxoSmithKline
    Senior Vice President, Head of R&D Rare Diseases
  • GlaxoSmithKline
    Vice President and Head of Gene Therapy Development
  • GlaxoSmithKline Biologicals
    Therapy Area Head of Respiratory Value Evidence and Outcomes
  • Global Genes Project
    President and Founder
  • GlobalCare Clinical Trials
    Vice President
  • Greenovation Biotech GmbH
    CEO
  • GSK
    External Strategy Manager, Gene Therapy
  • GSK
    Director Epidemiology, GSK Fellow, Real World Evidence and Epidemiology
  • GW Pharmaceuticals
    Chief Medical Officer
  • H.R.A. Pharma
    Head of Global Commercial Endocrinology and Rare Diseases
  • H.R.A. Pharma
    Endocrinology and RD Therapeutic Domain Director
  • Health Advances GmbH
    Director
  • Hovid
    Head of Marketing
  • Hygiapharm
    Director
  • IDEA Regulatory
    Regulatory Affairs Manager
  • IDEA Regulatory
    CEO & Co-owner
  • Idis Managed Access
    Head of EU Business Development
  • Ikris Pharma Network Pvt Ltd
    GM - Global Strategic Marketing
  • Imagine Institute
    co-founder
  • Impulsate Foundation
    President
  • INC Research
    Chief Scientific Officer
  • INC Research/inVentiv Health
    Project Director, RWLP Operations, Europe and Asia Pacific
  • INC Research/inVentiv Health
    BD Event Planner
  • INC Research/inVentiv Health
    BD Event Planner
  • Inserm
    Founder of Orphanet & Rare Disease Expert in Residence
  • International Niemann-Pick Disease Aliance
    President
  • Italian Epilepsy Federation
    CSO
  • Komtur Polska
    Managing Director
  • Komtur Polska sp. z.o.o
    Country Manager
  • Latvia Hemophilia Society
  • Lysogene
    SVP patient access
  • M.A. Provider
    MD
  • MAPI Group
    Global Lead Scientific Presentation and Publications
  • Mapi Group
    Vice President, Global Patients Insights and Engagement
  • Mapi Group
    Senior Director of Regulatory Affairs
  • Mapi Group
    Chief Scientific Officer
  • Mapi Group
    Vice President - Strategy and Global Marketing
  • Mapi Group
    Business Development Director
  • Medical Marketing Economics
    President
  • Medical Marketing Economics
    Global President and Chief Executive Officer
  • Medicines Evaluation Board The Netherlands
    Member of the Cross-Committee Task Force on Registries and Senior Clinical Assessor
  • Medicxi Ventures
    Partner
  • Medunik Canada
    Senior Manager of Business Development
  • Merck Serono
    Director for Europe for Global Regulatory and Scientific Policy
  • Merck Sharp and Dohme
    Executive Director, Patient Perspective
  • Minoryx Therapeutics
    CEO
  • Minoryx Therapeutics
    Director of Biology
  • Minoryx Therapeutics S.L.
    Director Clinical operations
  • Montreal Neurological Institute
    Director CRU
  • National Health Service
    Medical Adviser
  • National Institute for Health and Care Excellence
    Director at JG Zebra Consulting, Former Associate Director of HST
  • National Institute For Health and Care Excellence
    Assoc. Director Highly Specialised Technologies
  • National Organization for Rare Disorders
    Director of Membership
  • Netherlands Interstitial Cystitis Patients Organization
    ChairpersonVice-President
  • NORD
    Director of Research Programs
  • Norwegian Medicines Agency
    Senior Adviser
  • Novartis
    Director, Market Access and External Affairs
  • Novartis
    Oncology General Manager. Rare Diseases
  • Novartis Pharma AG
    Director Regulatory and Science Policy
  • Orchard Therapeutics
    Chief Medical Officer and R&D Head
  • Oxford PharmaGenesis
    Commercial Director
  • Partners4Access
    Partner
  • Partners4Access
    Partner
  • Pfizer
    VP Gene Therapy & Head, GMI
  • Philip Chapper & Co
    Marketing Manager
  • Pitt Hopkins UK
    parent
  • Pituitary Community South Africa
    Chairman
  • Portuguese Association for Congenital Disorders of Glycosylation
    patient advocate and volunteer
  • PPi Healthcare Consulting
    Managing Director
  • PRA Health Sciences
    Vice President, Scientific Affairs, Rare Diseases
  • PRA Health Sciences
    Vice President, Scientific Affairs, Rare Diseases
  • Premier Research
    Executive Director, Patient Engagement & Strategic Development
  • Premier Research
    Marketing Specialist
  • ProClinical Executive
    Associate Partner
  • ProClinical Executive
    Managing Partner
  • ProMetic Life Sciences Inc.
    Chief Executive Officer
  • PSR Group
    Business Development Manager
  • Pulse Infoframe Inc
    VP Global Sales for Pulse Infoframe
  • Quintiles
    Vice President, Global Head of Risk Management, Real-World & Late Phase Research
  • Quintiles Inc
    Vice President & Head, Centre of Excellence, Neurology, Therapeutic & Speciality Business Development
  • Quintiles Inc
    Executive Medical Director
  • QuintilesIMS
    Snr Director Project Leadership CNS Rare Diseases
  • QuintilesIMS
    Associate Director, Market Development
  • Rare Disease Foundation Of Iran
    Executive Manager of Liechtenstein
  • Rare Disease Foundation Of Iran
    General Manager
  • Rare Disease Foundation Of Iran
    Division Manager -Pharma
  • RARE Science
    CEO and Founder
  • rareLife solutions
    Founder, EDSers United & Community Engagement Team Leader
  • Raremark
    Founder
  • Raremark
    Co-founder
  • Raremark
    Founder
  • Recursion Pharmaceuticals
    Director of Translational Biology
  • ReGenXBio
    Chief Medical Officer
  • Retrophin
    Vice President and Head of Business Development
  • Roche
    Senior International Payer Strategy Lead
  • Roche
    Head of Rare Disease Discovery
  • Roche
    Head GPMA Neuroscience & Rare Diseases
  • Rodman & Renshaw
    Managing Director, Senior Analyst, Healthcare
  • Sanford Research
    Executive Vice President of Innovation and Research
  • Sant Joan de Deu Barcelona Children's Hospital , Research Foundation
    Clinical Research Unit manager
  • Sant Joan de Déu Children's Hospital
    Patient Advocacy Manager
  • Santhera Pharmaceuticals
    Clinical Trial Leader
  • Santhera Pharmaceuticals
    Clinical Trial Leader
  • Santhera Pharmaceuticals
    Patient Advocacy Manager Europe
  • Sarepta Therapeutics
    Vice President, General Manager and Head of Europe
  • Selecta Biosciences Inc
    Chief Science Officer
  • SERVIER Forschung und Pharma-Entwicklung GmbH
    Project Director Neuropsychiatry
  • SGP
    Scientific Advisor
  • Sirius Healthcare Partners Gmbh
    Managing Partner
  • SKC Beratungsgesellschaft
    Managing Director
  • SKC Beratungsgesellschaft
    Managing Director
  • Sobi
    Senior Vice President, Chief Patient Access Officer
  • Social Medicine Center South - Kaiser-Franz-Josef-Spital
    Cardiologist, Department of Cardiology
  • SOM Biotech
    Founder and Chief Executive Officer
  • SOM Biotech SL
    Founder and Chief Executive Officer
  • Sucampo Pharmaceuticals
    Senior Vice President, Business Development and Licensing
  • Sucampo Pharmaceuticals Inc
    Senior Vice President, Business Development and Licensing
  • Swedish Orphan Biovitrum Ltd
    Business Unit Director of Haemophilia
  • Swiss Biotech Association (SBA)
    Chief Operating Officer
  • T.V.M. Life Science Management Gmbh
    General Partner
  • Takeda Development Centre Europe
    External Asset Lead
  • Takeda Pharmaceuticals International Ltd
    Senior Vice President and Head of C.N.S. Therapeutic Area Unit
  • The Dental and Pharmaceutical Benefits Agency T.L.V.
    Chief Economist
  • The French Foundation for Rare Diseases
  • The French Foundation for Rare Diseases
    Regional Coordinator
  • The National Organization for Rare Disorders
    Director Community Relations and Marketing
  • The Planning Shop International Ltd
    Lead Research Director and Head of Rare Diseases
  • TM3 Therapeutics B.V.
    Head of DMPK, Preclinical Development
  • TranScrip
    Global Business Development Manager
  • UCL
    Senior Research Associate
  • UCL Great Ormond Street Institute of Child Health
    Professor of Paediatrics & Immunology
  • University of Groningen
    PhD Researcher
  • University of Western Ontario
    Research Professor – Health Informatics – Univeristy of Western Ontario
  • University of Wolverhampton
    Industrial Professor
  • University of Wolverhampton
    Senior Innovation Consultant
  • University of Wolverhampton
    Head of Commercialisation
  • University of Wolverhampton
    Professor of Experimental Cancer Therapeutics
  • Venn Life Sciences B.V.
    Business Development Director
  • Vitro Software
    CCO
  • Vitro Software
    CCO
  • WEP Clinical
    EAP Director
  • WEP Clinical
    EAP Director
  • WEP Clinical
    Managing Director EU
  • Wilson Therapeutics
    Vice President Commercial Planning & Launch Strategy
  • Worldwide Clinical Trials
    Chief Medical Officer
  • Worldwide Clinical Trials
    Senior Manager, Global Strategic Marketing
  • Zambon S.p.A.
    Business Development Manager
  • Zambon SpA
    Pipeline Development & Science Intelligence

     

     

     

     

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