Richa Madan Lomash | Therapeutic Development Project Manager
NIH

Richa Madan Lomash, Therapeutic Development Project Manager, NIH

Richa Madan Lomash, Ph.D., is a Therapeutic Development Project Manager at the National Center for Advancing Translational Sciences (NCATS), NIH, where she manages IND-enabling drug development programs for rare diseases across multiple modalities, including AAV gene therapies, peptides, small molecules, and antisense oligonucleotides. She serves as co-lead of the multi-institute Platform Vector Gene Therapy (PaVe-GT) program, advancing innovative gene therapy approaches toward clinical testing, and plays a key role in regulatory strategy, including FDA interactions, IND submissions, and orphan drug designations. Richa has contributed to NIH-wide initiatives such as RARe-SOURCE and i3D-RARE, aimed at accelerating translational science and therapeutic development. She is actively participating in gene therapy strategy groups, international rare disease consortia, and cross-sector collaborations with academia, industry, and patient advocacy organizations. A recipient of multiple NIH and NCATS Director’s Awards, she is also committed to mentorship, scientific dissemination, and advancing collaborative models to improve outcomes for patients with rare diseases. Richa trained as a cell biologist and did her postodoral training at NIH in the field of neurobiology undertsanding brain proteins. 

Appearances:



Pre-Conference Day - World Orphan Drug Congress USA 2026 @ 15:00

Translational Science Initiatives for Advancing Orphan Drug Development

This workshop session covers translational research initiatives that advance drug development for rare diseases.  We will highlight pre-clinical testing strategies, and the tools and technologies that help move promising assets toward the clinic. We will also discuss pre-clinical platforms for AAV gene therapy, stem-cell-derived 3D models, and bioinformatics efforts to consolidate rare disease information. Participants will learn from concrete examples and get familiarized with resources available to advance their own rare disease research and development efforts. 

Session Objectives: 

  • Understand the steps and challenges in the early phases of gene therapy development for rare diseases. 
  • Learn how stem-cell derived 3D disease models can be incorporated into preclinical testing in rare disease drug development. 
  • Explore an integrated bioinformatics resource that aggregates rare disease information for new insights 

 

last published: 13/May/26 12:45 GMT

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