2022 SPEAKERS

 

Faraz Ali, Chief Executive Officer, Tenaya Therapeutics

Faraz Ali | Chief Executive Officer | Tenaya Therapeutics » speaking at Orphan Drug Congress

Paul Aliu, Head Global Governance Office, Novartis Chief Medical Office (CMO), Novartis

Paul Aliu | Head Global Governance Office, Novartis Chief Medical Office (CMO) | Novartis » speaking at Orphan Drug Congress

Alba Ancochea Díaz, Managing Director, Spanish Federation of Rare Disease

Alba Ancochea Díaz | Managing Director | Spanish Federation of Rare Disease » speaking at Orphan Drug Congress

Samer Ansari, Head of Data, Digital & Technology, Takeda Oncology, Takeda

Samer Ansari | Head of Data, Digital & Technology, Takeda Oncology | Takeda » speaking at Orphan Drug Congress

Derek Ansel, Senior Director, Therapeutic Strategy Lead, Rare Diseases, WorldWide Clinical Trials

Derek Ansel | Senior Director, Therapeutic Strategy Lead, Rare Diseases | WorldWide Clinical Trials » speaking at Orphan Drug Congress

Irina Antonijevic, Chief Medical Officer, Head of R&D, Triplet Therapeutics

Irina Antonijevic | Chief Medical Officer, Head of R&D | Triplet Therapeutics » speaking at Orphan Drug Congress

Francis Arickx, Head of the Directorate Reimbursement of Medicines and Pharmaceutical Policy, National Institute for Health and Disability Insurance

Francis Arickx | Head of the Directorate Reimbursement of Medicines and Pharmaceutical Policy | National Institute for Health and Disability Insurance » speaking at Orphan Drug Congress

Ella Balasa, Rare Disease, Patient Advocate

Ella Balasa | Rare Disease | Patient Advocate » speaking at Orphan Drug Congress

Katherine Beaverson, Executive Director and Head of Patient Advocacy and External Engagement, Rare Disease Research Unit,, Pfizer

Katherine Beaverson | Executive Director and Head of Patient Advocacy and External Engagement, Rare Disease Research Unit, | Pfizer » speaking at Orphan Drug Congress

Alon Ben-Noon, Chief Executive Officer, NeuroSense Therapeutics

Alon Ben-Noon | Chief Executive Officer | NeuroSense Therapeutics » speaking at Orphan Drug Congress

Wendy Benson, Chief Strategy and Innovation Officer, Rady Children's Institute for Genomic Medicine

Wendy Benson | Chief Strategy and Innovation Officer | Rady Children's Institute for Genomic Medicine » speaking at Orphan Drug Congress

Terry Jo Bichell, Founder And Director, COMBINEDBrain

Terry Jo Bichell | Founder And Director | COMBINEDBrain » speaking at Orphan Drug Congress

Nicole Boice, Founder & Executive Director, RARE-X

Nicole Boice | Founder & Executive Director | RARE-X » speaking at Orphan Drug Congress

Natasha Bonhomme, Chief Strategy Officer, Genetic Alliance Founder, Expecting Health

Natasha Bonhomme | Chief Strategy Officer, Genetic Alliance Founder | Expecting Health » speaking at Orphan Drug Congress

Larry Bressler, Head of Value and Market Access, Chiesi Global Rare Disease

Larry Bressler | Head of Value and Market Access | Chiesi Global Rare Disease » speaking at Orphan Drug Congress

Phillip Brooks, Acting Director, Office of Rare Diseases Research, NIH - NCATS

Phillip Brooks | Acting Director, Office of Rare Diseases Research | NIH - NCATS » speaking at Orphan Drug Congress

Amy Brower, US National Director, Newborn Screening Translational Research Network (NBSTRN),, American College of Medical Genetics and Genomics

Amy Brower | US National Director, Newborn Screening Translational Research Network (NBSTRN), | American College of Medical Genetics and Genomics » speaking at Orphan Drug Congress

Jackie Brown, Vice President, Rare Diseases, Therapeutic and Device Program Management, Premier Research

Jackie Brown | Vice President, Rare Diseases, Therapeutic and Device Program Management | Premier Research » speaking at Orphan Drug Congress

Jake Caines, Chief Revenue Officer, Curant Health

Jake Caines | Chief Revenue Officer | Curant Health » speaking at Orphan Drug Congress

Jason Cameron, Chief Operating Officer, Orphan Drug Consulting

Jason Cameron | Chief Operating Officer | Orphan Drug Consulting » speaking at Orphan Drug Congress

Elena Cardenal, Scientific Director, Dravet Syndrome Foundation Spain

Elena Cardenal | Scientific Director | Dravet Syndrome Foundation Spain » speaking at Orphan Drug Congress

Vittoria Carraro, Associate Director Government Affairs, European Confederation of Pharmaceutical Entrepreneurs (Belgium)

Vittoria Carraro | Associate Director Government Affairs | European Confederation of Pharmaceutical Entrepreneurs (Belgium) » speaking at Orphan Drug Congress

Nicole Carswell, Executive Director, Patient Engagement and Recruitment,, Premier Research

Nicole Carswell | Executive Director, Patient Engagement and Recruitment, | Premier Research » speaking at Orphan Drug Congress

Grant Castor, Vice President Commercial Operations, Sentynl Therapeutics

Grant Castor | Vice President Commercial Operations | Sentynl Therapeutics » speaking at Orphan Drug Congress

Lynsey Chediak, Head of Partnerships, Rare Base

Lynsey Chediak | Head of Partnerships | Rare Base » speaking at Orphan Drug Congress

Melissa Coloton, EVP, Business Development and Marketing, Scout Clinical

Melissa Coloton | EVP, Business Development and Marketing | Scout Clinical » speaking at Orphan Drug Congress

Graham Dempsey, Chief Scientific Officer, Q-State Biosciences

Graham Dempsey | Chief Scientific Officer | Q-State Biosciences » speaking at Orphan Drug Congress

Lisa Desiderato, Vice President, US Sales and Marketing, Precision Medicine, BAYER

Lisa Desiderato | Vice President, US Sales and Marketing, Precision Medicine | BAYER » speaking at Orphan Drug Congress

Chowdary Dondapati, Executive Director, US Head of Diagnostic Marketing, Precision Medicine, BAYER

Chowdary Dondapati | Executive Director, US Head of Diagnostic Marketing, Precision Medicine | BAYER » speaking at Orphan Drug Congress

Daniel Donovan, Founder & CEO, rareLife solutions

Daniel Donovan | Founder & CEO | rareLife solutions » speaking at Orphan Drug Congress

Marcus Droege, Vice President, Global Value & Market Access, Passage Bio

Marcus Droege | Vice President, Global Value & Market  Access | Passage Bio » speaking at Orphan Drug Congress

Sanjoy Dutta, Chief Scientific Officer, JDRF

Sanjoy Dutta | Chief Scientific Officer | JDRF » speaking at Orphan Drug Congress

Sean Ekins, Founder And Chief Executive Officer, Collaborations Pharmaceuticals

Sean Ekins | Founder And Chief Executive Officer | Collaborations Pharmaceuticals » speaking at Orphan Drug Congress

Matthew Ellinwood, Chief Scientific Officer, National MPS Society

Matthew Ellinwood | Chief Scientific Officer | National MPS Society » speaking at Orphan Drug Congress

Izaskun Elorza, Senior Medical Director,, Parexel

Izaskun Elorza | Senior Medical Director, | Parexel » speaking at Orphan Drug Congress

Wendy Erler, Vice President, Global Head Patient Experience & Insights, Alexion AstraZeneca Rare Disease

Wendy Erler | Vice President, Global Head Patient Experience & Insights | Alexion AstraZeneca Rare Disease » speaking at Orphan Drug Congress

Jorge Faccinetti, Chairman and Chief Executive Officer, Pituitary World News

Jorge Faccinetti | Chairman and Chief Executive Officer | Pituitary World News » speaking at Orphan Drug Congress

Aliza Fink, Director of Research Programs, National Organization for Rare Disorders (NORD)

Aliza Fink | Director of Research Programs | National Organization for Rare Disorders (NORD) » speaking at Orphan Drug Congress

James Fink, Senior Principal Scientist, Q-State Biosciences

James Fink | Senior Principal Scientist | Q-State Biosciences » speaking at Orphan Drug Congress

Daniel Fischer, President and Chief Executive Officer, Tevard Biosciences

Daniel Fischer | President and Chief Executive Officer | Tevard Biosciences » speaking at Orphan Drug Congress

Ryan Fischer, Chief Advocacy Officer, Parent Project Muscular Dystrophy

Ryan Fischer | Chief Advocacy Officer | Parent Project Muscular Dystrophy » speaking at Orphan Drug Congress

Safiyya Gassman, Senior Director, Policy & Public Affairs, Rare Disease & Gene Therapy, Pfizer

Safiyya Gassman | Senior Director, Policy & Public Affairs, Rare Disease & Gene Therapy | Pfizer » speaking at Orphan Drug Congress

Joseph Geraci, Chief Scientific Officer, Nurosene Health Inc.

Joseph Geraci | Chief Scientific Officer | Nurosene Health Inc. » speaking at Orphan Drug Congress

Lev Gerlovin, Vice President, Life Sciences Practice, Charles River Associates

Lev Gerlovin | Vice President, Life Sciences Practice | Charles River Associates » speaking at Orphan Drug Congress

Diego Fernando Gil Cardozo, Executive Director, Federación Colombiana de Enfermedades Raras -FECOER-

Diego Fernando Gil Cardozo | Executive Director | Federación Colombiana de Enfermedades Raras -FECOER- » speaking at Orphan Drug Congress

Christoph Glaetzer, Chief Global Value and Access Officer, Janssen

Christoph Glaetzer | Chief Global Value and Access Officer | Janssen » speaking at Orphan Drug Congress

Sarah Glass, Chief Development Officer, n-Lorem Foundation

Sarah Glass | Chief Development Officer | n-Lorem Foundation » speaking at Orphan Drug Congress

Richard Gliklich, Chief Executive Officer, OM1

Richard Gliklich | Chief Executive Officer | OM1 » speaking at Orphan Drug Congress

Juan Marcos Gonzalez, Associate Professor in Population Health Sciences, Assistant Professor in Medicine, Member, Duke Clinical Research Institute, Duke University School of Medicine

Juan Marcos Gonzalez | Associate Professor in Population Health Sciences, Assistant Professor in Medicine, Member, Duke Clinical Research Institute | Duke University School of Medicine » speaking at Orphan Drug Congress

Scott Gray, Chief Executive Officer, Clincierge

Scott Gray | Chief Executive Officer | Clincierge » speaking at Orphan Drug Congress

Fumie Griego, Deputy Director General And Chief Operating Officer, International Federation of Pharmaceutical Manufacturers and Associations

Fumie Griego | Deputy Director General And Chief Operating Officer | International Federation of Pharmaceutical Manufacturers and Associations » speaking at Orphan Drug Congress

Abhi Gupta, Senior Director, Global Gene Therapy, Pfizer

Abhi Gupta | Senior Director, Global Gene Therapy | Pfizer » speaking at Orphan Drug Congress

Pamela Guthrie, Director, Sales and Marketing, Clincierge

Pamela Guthrie | Director, Sales and Marketing | Clincierge » speaking at Orphan Drug Congress

Elin Haf Davies, Chief Executive Officer, Aparito

Elin Haf Davies | Chief Executive Officer | Aparito » speaking at Orphan Drug Congress

Michael Hamper, Medical/Science Advisory, Kleine-Levin Syndrome Foundation

Michael Hamper | Medical/Science Advisory | Kleine-Levin Syndrome Foundation » speaking at Orphan Drug Congress

Christopher Hamper, Medical Advisory Board Member, Kleine-Levin Syndrome Foundation

Christopher Hamper | Medical Advisory Board Member | Kleine-Levin Syndrome Foundation » speaking at Orphan Drug Congress

Scott Harwood, Director, Check Rare

Scott Harwood | Director | Check Rare » speaking at Orphan Drug Congress

Rachele Hendricks-Sturrup, Research Director, Real World Evidence, Duke Margolis Center for Health Policy

Rachele Hendricks-Sturrup | Research Director, Real World Evidence | Duke Margolis Center for Health Policy » speaking at Orphan Drug Congress

Matthew Hewitt, Executive Director, Scientific Services Cell and Gene Therapy, Charles River

Matthew Hewitt | Executive Director, Scientific Services Cell and Gene Therapy | Charles River » speaking at Orphan Drug Congress

Claudia Hirawat, Owner & Executive Chair, VOZ Advisors

Claudia Hirawat | Owner & Executive Chair | VOZ Advisors » speaking at Orphan Drug Congress

Gwen Hyland, Head of Commercial Excellence, Rare Diseases, AstraZeneca, Alexion Pharmaceuticals

Gwen Hyland | Head of Commercial Excellence, Rare Diseases, AstraZeneca | Alexion Pharmaceuticals » speaking at Orphan Drug Congress

Hearn Jay Cho, Chief Medical Officer, Multiple Myeloma Research Foundation

Hearn Jay Cho | Chief Medical Officer | Multiple Myeloma Research Foundation » speaking at Orphan Drug Congress

Emil Kakkis, Chief Executive Officer, Ultragenyx Pharmaceutical

Emil Kakkis | Chief Executive Officer | Ultragenyx Pharmaceutical » speaking at Orphan Drug Congress

Rashida Karmali, Chief Executive Officer, Tactical Therapeutics Inc

Rashida Karmali | Chief Executive Officer | Tactical Therapeutics Inc » speaking at Orphan Drug Congress

Vikram Karnani, Executive Vice President, President, International, Horizon Therapeutics

Vikram Karnani | Executive Vice President, President, International | Horizon Therapeutics » speaking at Orphan Drug Congress

Lindsay Kehoe, Project Manager, Clinical Trials Transformation Initiative (CTTI)

Lindsay Kehoe | Project Manager | Clinical Trials Transformation Initiative (CTTI) » speaking at Orphan Drug Congress

Ken Kengatharan, Managing General Partner, Atheneos Ventures

Ken Kengatharan | Managing General Partner | Atheneos Ventures » speaking at Orphan Drug Congress

Ms Annie Kennedy, Chief Policy And Advocacy, EveryLife Foundation for Rare Diseases

Ms Annie Kennedy | Chief Policy And Advocacy | EveryLife Foundation for Rare Diseases » speaking at Orphan Drug Congress

Doug Kerr, Chief Medial Officer, Generation Bio

Doug Kerr | Chief Medial Officer | Generation Bio » speaking at Orphan Drug Congress

Maria Kirsch, General Manager, Patient Services, EVERSANA

Maria Kirsch | General Manager, Patient Services | EVERSANA » speaking at Orphan Drug Congress

Matthew Klein, Chief Operating Officer, PTC Therapeutics

Matthew Klein | Chief Operating Officer | PTC Therapeutics » speaking at Orphan Drug Congress

Sarka Kubinova, Medical evaluator, MoCA coordinator, Section of Pricing and Reimbursement Regulation, Czech Republic State Institute for Drug Control

Sarka Kubinova | Medical evaluator, MoCA coordinator, Section of Pricing and Reimbursement Regulation | Czech Republic State Institute for Drug Control » speaking at Orphan Drug Congress

Samarth Kulkarni, Chief Executive Officer, CRISPR Therapeutics

Samarth Kulkarni | Chief Executive Officer | CRISPR Therapeutics » speaking at Orphan Drug Congress

Janet Lynch Lambert, Chief Executive Officer, Alliance for Regenerative Medicine

Janet Lynch Lambert | Chief Executive Officer | Alliance for Regenerative Medicine » speaking at Orphan Drug Congress

David Lapidus, President, Lapidus Data

David Lapidus | President | Lapidus Data » speaking at Orphan Drug Congress

Catherine Lawrence, Head of Rare Disease, Bionical Emas

Catherine Lawrence | Head of Rare Disease | Bionical Emas » speaking at Orphan Drug Congress

Yann Le Cam, Chief Executive Officer, EURORDIS

Yann Le Cam | Chief Executive Officer | EURORDIS » speaking at Orphan Drug Congress

Kimberly LeBlanc, Director, UDN Coordinating Center, Harvard Medical School, Harvard Medical School

Kimberly LeBlanc | Director, UDN Coordinating Center, Harvard Medical School | Harvard Medical School » speaking at Orphan Drug Congress

Seth Lederman, Co-Founder, Chief Executive Officer & Chairman, Tonix Pharmaceuticals

Seth Lederman | Co-Founder, Chief Executive Officer & Chairman | Tonix Pharmaceuticals » speaking at Orphan Drug Congress

Zhiying Li, Director, Life Science and Technology, GemPharmatech

Zhiying Li | Director, Life Science and Technology | GemPharmatech » speaking at Orphan Drug Congress

Naomi Litchfield, Global Patient Advocacy Lead, Bionical Emas

Naomi Litchfield | Global Patient Advocacy Lead | Bionical Emas » speaking at Orphan Drug Congress

Jeff Livingstone, Chief Executive Officer, Igia Pharmaceuticals

Jeff Livingstone | Chief Executive Officer | Igia Pharmaceuticals » speaking at Orphan Drug Congress

Sanjeev Luther, President & Chief Executive Officer, Rafael pharmaceuticals

Sanjeev Luther | President & Chief Executive Officer | Rafael pharmaceuticals » speaking at Orphan Drug Congress

Wolfram Lux, Senior Director, Market Access & Commercial Strategy, Rare Diseases,, Simon-Kucher & Partners

Wolfram Lux | Senior Director, Market Access & Commercial Strategy, Rare Diseases, | Simon-Kucher & Partners » speaking at Orphan Drug Congress

Flaminia Macchia, Executive Director, Rare Diseases International

Flaminia Macchia | Executive Director | Rare Diseases International » speaking at Orphan Drug Congress

Geoff Mackay, President And Chief Executive Officer, AVROBIO

Geoff Mackay | President And Chief Executive Officer | AVROBIO » speaking at Orphan Drug Congress

Natalia Maeva, President, The Bulgarian Society of Patients with Pulmonary Hypertension

Natalia Maeva | President | The Bulgarian Society of Patients with Pulmonary Hypertension » speaking at Orphan Drug Congress

Nitin Mahadev, Vice President, Global Franchise Lead, Rare Disease, Pfizer

Nitin Mahadev | Vice President, Global Franchise Lead, Rare Disease | Pfizer » speaking at Orphan Drug Congress

Will Maier, Vice President, Rare Disease, Drug Development Sciences, ICON plc

Will Maier | Vice President, Rare Disease, Drug Development Sciences | ICON plc » speaking at Orphan Drug Congress

Nick Marchant, Vice President Outcomes & Evidence, Internal Medicine, Pfizer

Nick Marchant | Vice President Outcomes & Evidence, Internal Medicine | Pfizer » speaking at Orphan Drug Congress

Peter Marks, Director, Center For Biologics Evaluation And Research (CBER), U.S. Food and Drug Administration

Peter Marks | Director, Center For Biologics Evaluation And Research (CBER) | U.S. Food and Drug Administration » speaking at Orphan Drug Congress

Brad Martin, Vice President, Market Access, Taysha Gene Therapies

Brad Martin | Vice President, Market Access | Taysha Gene Therapies » speaking at Orphan Drug Congress

Paolo Martini, Chief Scientific Officer, Rare Diseases, Moderna Therapeutics

Paolo Martini | Chief Scientific Officer, Rare Diseases | Moderna Therapeutics » speaking at Orphan Drug Congress

Liz Mascherino, Associate Director of Patient Engagement, Equity and Transparency, Biogen

Liz Mascherino | Associate Director of Patient Engagement, Equity and Transparency | Biogen » speaking at Orphan Drug Congress

Mary McGowan, Chief Executive Officer, Foundation for Sarcoidosis Research

Mary McGowan | Chief Executive Officer | Foundation for Sarcoidosis Research » speaking at Orphan Drug Congress

Kelly McKee, Vice President, Patient Registries and Recruitment, Medidata

Kelly McKee | Vice President, Patient Registries and Recruitment | Medidata » speaking at Orphan Drug Congress

Jennifer McNary, Founder, One Rare

Jennifer McNary | Founder | One Rare » speaking at Orphan Drug Congress

Maureen Menacher, Vice President, Market Access, Enzyvant

Maureen Menacher | Vice President, Market Access | Enzyvant » speaking at Orphan Drug Congress

Wesley Michael, President, Rare Patient Voice, LLC

Wesley Michael | President | Rare Patient Voice, LLC » speaking at Orphan Drug Congress

Christopher Morabito, Chief Medical Officer, Fulcrum Therapeutics

Christopher Morabito | Chief Medical Officer | Fulcrum Therapeutics » speaking at Orphan Drug Congress

Christopher Moxham, Chief Scientific Officer, Rarebase, PBC

Christopher Moxham | Chief Scientific Officer | Rarebase, PBC » speaking at Orphan Drug Congress

Andrew Mumford, Managing Director, Initiate

Andrew Mumford | Managing Director | Initiate » speaking at Orphan Drug Congress

Andy Murphy, U.S Market Lead, Curant Health

Andy Murphy | U.S Market Lead | Curant Health » speaking at Orphan Drug Congress

Michael Murphy, Chief Medical & Scientific Officer, WorldWide Clinical Trials

Michael Murphy | Chief Medical & Scientific Officer | WorldWide Clinical Trials » speaking at Orphan Drug Congress

Paul Nash, Senior Director, Simon-Kucher & Partners

Paul Nash | Senior Director | Simon-Kucher & Partners » speaking at Orphan Drug Congress

Alexander Natz, Secretary General, European Confederation of Pharmaceutical Entrepreneurs (Belgium)

Alexander Natz | Secretary General | European Confederation of Pharmaceutical Entrepreneurs (Belgium) » speaking at Orphan Drug Congress

Indu Navar, Founder and Chief Executive Officer, EverythingALS

Indu Navar | Founder and Chief Executive Officer | EverythingALS » speaking at Orphan Drug Congress

Amy Nicole Nayar, VP US Patient Advocacy and Government Affairs, Novartis Gene Therapies

Amy Nicole Nayar | VP US Patient Advocacy and Government Affairs | Novartis Gene Therapies » speaking at Orphan Drug Congress

Edward Neilan, Chief Medical and Scientific Officer, National Organization for Rare Disorders (NORD)

Edward Neilan | Chief Medical and Scientific Officer | National Organization for Rare Disorders (NORD) » speaking at Orphan Drug Congress

Amanda Nickles Fader, Professor of Gynecology and Obstetrics, Professor of Oncology, Vice-Chair, Gynecologic Surgical Operations,, Johns Hopkins Medical Center

Amanda Nickles Fader | Professor of Gynecology and Obstetrics, Professor of Oncology, Vice-Chair, Gynecologic Surgical Operations, | Johns Hopkins Medical Center » speaking at Orphan Drug Congress

Andrew Obenshain, Chief Executive Officer, Bluebird Bio

Andrew Obenshain | Chief Executive Officer | Bluebird Bio » speaking at Orphan Drug Congress

Asif Paker, VP Clinical Development, SwanBio Therapeutics

Asif Paker | VP Clinical Development | SwanBio Therapeutics » speaking at Orphan Drug Congress

Jim Palma, Executive Director, TargetCancer Foundation

Jim Palma | Executive Director | TargetCancer Foundation » speaking at Orphan Drug Congress

Krina Patel, Director of State Public Policy & Government Affairs, Northeast States, Biogen

Krina Patel | Director of State Public Policy & Government Affairs, Northeast States | Biogen » speaking at Orphan Drug Congress

Bhavesh Patel, Principal, CRA, Charles River Associates

Bhavesh Patel | Principal | CRA, Charles River Associates » speaking at Orphan Drug Congress

Richa Poddar, Chief Commercial Officer, Agios Pharmaceuticals

Richa Poddar | Chief Commercial Officer | Agios Pharmaceuticals » speaking at Orphan Drug Congress

Amy Pott, Division Head of Gene Therapy, Commercial,, Astellas Gene Therapies

Amy Pott | Division Head of Gene Therapy, Commercial, | Astellas Gene Therapies » speaking at Orphan Drug Congress

Ana Puhl, Senior Research Scientist, Collaborations Pharmaceuticals

Ana Puhl | Senior Research Scientist | Collaborations Pharmaceuticals » speaking at Orphan Drug Congress

Pam Rattananont, Director, Customer Strategy and Innovation, Parexel

Pam Rattananont | Director, Customer Strategy and Innovation | Parexel » speaking at Orphan Drug Congress

Shannon Resetich, Global Franchise Head, Rare Diseases, Sanofi Genzyme

Shannon Resetich | Global Franchise Head, Rare Diseases | Sanofi Genzyme » speaking at Orphan Drug Congress

David Ringger, Head of Market Access, Initiate

David Ringger | Head of Market Access | Initiate » speaking at Orphan Drug Congress

David Rose, Business Development, Rare Revolution

David Rose | Business Development | Rare Revolution » speaking at Orphan Drug Congress

Luke Rosen, Founder, KIF1A.ORG

Luke Rosen | Founder | KIF1A.ORG » speaking at Orphan Drug Congress

Ashish Sagrolikar, Chief Operating Officer, Zogenix Inc.

Ashish Sagrolikar | Chief Operating Officer | Zogenix Inc. » speaking at Orphan Drug Congress

Dharmendra Sahay, ZS Associates, Inc.

Dharmendra Sahay |  | ZS Associates, Inc. » speaking at Orphan Drug Congress

Peter Saltonstall, President And Chief Executive Officer, National Organization for Rare Disorders (NORD)

Peter Saltonstall | President And Chief Executive Officer | National Organization for Rare Disorders (NORD) » speaking at Orphan Drug Congress

Denise Schulz, Associate Director of Clinical Operations,, Horizon Therapeutics

Denise Schulz | Associate Director of Clinical Operations, | Horizon Therapeutics » speaking at Orphan Drug Congress

Simone Seiter, Partner, Simon-Kucher & Partners

Simone Seiter | Partner | Simon-Kucher & Partners » speaking at Orphan Drug Congress

Antonino Severino, Head of Clinical Trials & Orphan Drug Production/Packaging, Nextpharma

Antonino Severino | Head of Clinical Trials & Orphan Drug Production/Packaging | Nextpharma » speaking at Orphan Drug Congress

Peter Shadday, Chief Commercial Officer US, Global Head of Marketing Specialties, Board Member,, Zambon

Peter Shadday | Chief Commercial Officer US, Global Head of Marketing Specialties, Board Member, | Zambon » speaking at Orphan Drug Congress

Panna Sharma, Chief Executive Officer, President and Director, Lantern Pharma

Panna Sharma | Chief Executive Officer, President and Director | Lantern Pharma » speaking at Orphan Drug Congress

Tricha Shivas, Chief Strategy Officer, Foundation for Sarcoidosis Research

Tricha Shivas | Chief Strategy Officer | Foundation for Sarcoidosis Research » speaking at Orphan Drug Congress

Fanny Sie, One Roche, Head of Artificial Intelligence and Digital Health, Roche

Fanny Sie | One Roche, Head of Artificial Intelligence and Digital Health | Roche » speaking at Orphan Drug Congress

Stuart Siedman, Head of Patient Advocacy, Chiesi Global Rare Disease

Stuart Siedman | Head of Patient Advocacy | Chiesi Global Rare Disease » speaking at Orphan Drug Congress

Amy Simon, Chief Medical Officer, Beam Therapeutics

Amy Simon | Chief Medical Officer | Beam Therapeutics » speaking at Orphan Drug Congress

Jaswinder Singh Khera, Managing Director, WEP Clinical

Jaswinder Singh Khera | Managing Director | WEP Clinical » speaking at Orphan Drug Congress

Nick Sireau, Chair and Chief Executive Officer, AKU Society

Nick Sireau | Chair and Chief Executive Officer | AKU Society » speaking at Orphan Drug Congress

Scott Snyder, Chief Digital Officer, EVERSANA

Scott Snyder | Chief Digital Officer | EVERSANA » speaking at Orphan Drug Congress

Charlene Son Rigby, Chief Executive Officer, RARE-X

Charlene Son Rigby | Chief Executive Officer | RARE-X » speaking at Orphan Drug Congress

Matt Sowards, Chief Innovation Officer, Scout Clinical

Matt Sowards | Chief Innovation Officer | Scout Clinical » speaking at Orphan Drug Congress

Mark Stenhouse, Chief Operating Officer, Prometheus Biosciences

Mark Stenhouse | Chief Operating Officer | Prometheus Biosciences » speaking at Orphan Drug Congress

Violeta Stoyanova-Beninska, Chair of Committee for Orphan Medicinal Products, Medicines Evaluation Board, Medicines Evaluation Board

Violeta Stoyanova-Beninska | Chair of Committee for Orphan Medicinal Products, Medicines Evaluation Board | Medicines Evaluation Board » speaking at Orphan Drug Congress

Swami Subramanian, Head, US/Global Pricing and Contracting, Regeneron

Swami Subramanian | Head, US/Global Pricing and Contracting | Regeneron » speaking at Orphan Drug Congress

Dean Suhr, President, MLD Foundation

Dean Suhr | President | MLD Foundation » speaking at Orphan Drug Congress

Jamie Sullivan, Director of Public Policy, EveryLife Foundation

Jamie Sullivan | Director of Public Policy | EveryLife Foundation » speaking at Orphan Drug Congress

Lee Sutton, Vice President, Business Development, WEP Clinical

Lee Sutton | Vice President, Business Development | WEP Clinical » speaking at Orphan Drug Congress

Magali Taiel, Chief Medical Officer, GenSight Biologics

Magali Taiel | Chief Medical Officer | GenSight Biologics » speaking at Orphan Drug Congress

Mitra Tavakkoli, VP, Clinical Development, Taysha

Mitra Tavakkoli | VP, Clinical Development | Taysha » speaking at Orphan Drug Congress

Ulrich Thienel, Chief Executive Officer, ReAlta Life Sciences

Ulrich Thienel | Chief Executive Officer | ReAlta Life Sciences » speaking at Orphan Drug Congress

Michael Thomas, Principal, ZS

Michael Thomas | Principal | ZS » speaking at Orphan Drug Congress

Mark Trusheim, Strategic Director, MIT NEWDIGS

Mark Trusheim | Strategic Director | MIT NEWDIGS » speaking at Orphan Drug Congress

Vijesh Unnikrishnan, Principal, ZS Associates, Inc.

Vijesh Unnikrishnan | Principal | ZS Associates, Inc. » speaking at Orphan Drug Congress

Fyodor Urnov, Scientific Director, Innovative Genomics Institute, Professor, Department of Molecular & Cell Biology, University of California, Berkeley

Fyodor Urnov | Scientific Director, Innovative Genomics Institute, Professor, Department of Molecular & Cell Biology | University of California, Berkeley » speaking at Orphan Drug Congress

Zizi Uzezi Imatorbhebhe, Senior Vice President, Global Strategy and Development, Head Rare Disease Innovation Center,, Ergomed

Zizi Uzezi Imatorbhebhe | Senior Vice President, Global Strategy and Development, Head Rare Disease Innovation Center, | Ergomed » speaking at Orphan Drug Congress

Kristin Van Goor, Lead, North America Regulatory Policy, Vertex Pharmaceuticals

Kristin Van Goor | Lead, North America Regulatory Policy | Vertex Pharmaceuticals » speaking at Orphan Drug Congress

Suneet Varma, Global President, Rare Disease Business Unit, Pfizer inc

Suneet Varma | Global President, Rare Disease Business Unit | Pfizer inc » speaking at Orphan Drug Congress

Mary Wang, Science Policy Manager, Rare Diseases International

Mary Wang | Science Policy Manager | Rare Diseases International » speaking at Orphan Drug Congress

Dan Wasserstrom, Senior Director, Business Development, Clinigen Group

Dan Wasserstrom | Senior Director, Business Development | Clinigen Group » speaking at Orphan Drug Congress

Christopher Watson, Director, Consulting, Thread Research

Christopher Watson | Director, Consulting | Thread Research » speaking at Orphan Drug Congress

Kevin Weatherwax, Vice President, Head of Regulatory Affairs, WEP Clinical

Kevin Weatherwax | Vice President, Head of Regulatory Affairs | WEP Clinical » speaking at Orphan Drug Congress

Clive Whitcher, Head of Pharma, Inceptua

Clive Whitcher | Head of Pharma | Inceptua » speaking at Orphan Drug Congress

Toni Williams, Global Business Development Manager, Clinigen Group

Toni Williams | Global Business Development Manager | Clinigen Group » speaking at Orphan Drug Congress

Gareth Williams, President - Sciensus Rare, Sciensus

Gareth Williams | President - Sciensus Rare | Sciensus » speaking at Orphan Drug Congress

Durhane Wong-Rieger, President & Chief Executive Officer, Canadian Organization for Rare Disorders

Durhane Wong-Rieger | President & Chief Executive Officer | Canadian Organization for Rare Disorders » speaking at Orphan Drug Congress

Rachel Yang, Secretary, Council Member, RDI, Head of International Affairs, Chinese Alliance for Rare Diseases (CHARD)

Rachel Yang | Secretary, Council Member, RDI, Head of International Affairs | Chinese Alliance for Rare Diseases (CHARD) » speaking at Orphan Drug Congress

David Young, Chief Executive Officer, Processa Pharmaceuticals, Inc.

David Young | Chief Executive Officer | Processa Pharmaceuticals, Inc. » speaking at Orphan Drug Congress

Christine Yu, Chief Executive Officer, P2P Syncro

Christine Yu | Chief Executive Officer | P2P Syncro » speaking at Orphan Drug Congress

Nancy Yu, Co-Founder & Chief Executive Officer, AllStripes Research

Nancy Yu | Co-Founder & Chief Executive Officer | AllStripes Research » speaking at Orphan Drug Congress

Joseph Zabinski, Senior Director, AI & Precision Medicine, OM1

Joseph Zabinski | Senior Director, AI & Precision Medicine | OM1 » speaking at Orphan Drug Congress

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