Why Attend
June 9 - 11, 2026
Boston Convention & Exhibition Center
Premium Conference
Learn from world KOLs in rare diseases on the latest in AI & digital health, gene therapy, clinical trials, patient access and more. Ensure that you are equipped with the most recent policy and governmental changes in OMP legislation and HTA.
Busy Exhibition
With a footfall of 2,000+ attendees, exhibitors will get to speak directly to their target market, expand sales leads, strengthen and establish their brand and close deals with customers on-site.
Limitless Networking
Get access to our dedicated event app (5 weeks before the event), see all of our 2,000+ attendees and set up 1-2-1 meetings to maximise your ROI in attending the congress.
Innovation Showcase Zone
Meet start-ups or pitch your company at the leading rare disease congress. Meet new companies that can help your business or investors that can take you to the next level.
Workshops
Host or participate in our pre-congress workshops where we deep dive into topics including AI, digital health, patient data, global access & pricing, next gen therapies, and global joint clinical assessment and more with all key stakeholders.
Roundtables
These sessions are intimate discussions and one of the best ways to find out what your target audience wants.
Media Zone
The media zone will be bustling with all of the biggest names in the rare disease world. Witness live interviews and use our zone to announce press releases and social media outreach to maximise your presence.
CPD Accredited
World Orphan Drug Congress USA is proud to announce its recent accreditation by The CPD Group, a globally recognised accreditation body for quality professional development. This accreditation signifies World Orphan Drug Congress USA commitment to delivering high-quality educational experiences that contribute to the professional growth of its attendees.
Boston
We’re in Boston,MA! Boston is the heart of U.S. biotech and rare disease innovation. With top hospitals, research institutions, and a thriving life sciences ecosystem, it's where science turns into breakthrough therapies.
Super Early Bird Tickets - Save up to $3,035
Offer Ends October 10
Join 2,000 attendees at the world's largest orphan drug and rare disease event.
This is your best opportunity in 2026 to network with professionals in the rare disease industry.
280+ Speakers | Subject Matter Experts
Mackenzie Abramson, MPH, BCPAPatient Advocate
Rebecca Ahrens-Nicklas, MD, PhDAssistant Professor of Pediatrics Director, Gene Therapy for Inherited Metabolic Disorders Frontier ProgramChildren's Hospital Of Philadelphia
Lynn AlbizoChief Public Policy OfficerImmune Deficiency Foundation
Annette BakkerCEOChildrens Tumor Foundation
Anny BedardPresidentEgetis Therapeutics US
Hourinaz BehestiFounder & CEOHebbian Bio
Christine BrennanManaging DirectorVertex Ventures HC
P.J. BrooksDeputy Director, Division of Rare Diseases Research InnovationNIH/NCATS
Cynthia CassandroVice President, Patient AdvoacyVigil Neuroscience
James ChambersProfessorTufts Medical Center
Jason ColquittChief Executive OfficerAcross Healthcare
Rumi DesaiDirector, Global Regulatory StrategyAmgen, Inc.
Wendy ErlerSenior Vice President, Patient AffairsSarepta Therapeutics
Djordje FilipovicChief Executive OfficerAB2 Bio Ltd.
Karen FrascelloSenior Director, Medical AffairsAlnylam Pharmaceuticals
Albert FreedmanCounseling Psychologist / Rare DadRarecounseling.com
Chris GarabedianPortfolio Manager, VenturePerceptive Advisors
Federico GoodsaidSVP RegulatoryAriana Pharma
Rachel HarrisonDirector, Expanded Access Programargenx
Neil InhaberHead, Marketed Products, Global MedicalTakeda
Debra JenningsHead of Patient Services Operations, North AmericaKyowa Kirin
Richie KahnCo-Founder & COOCanary Advisors
Patroski LawsonCo-founderThe Just Society
Kimberly LeBlancDirector, UDN Data Management Coordinating Center, Harvard Medical SchoolHarvard Medical School
Julianna LeMieuxDeputy Editor in ChiefGenetic Engineering & Biotechnology News
Robert LongExecutive DirectorUplifting Athletes
Peng LuChief Medical OfficerPharvaris
Fabiana MarzabalSr Director Forecasting, Analytics and InsightsViridian Therapeutics
Maurizio MazziSenior Associate Director, Patient Advocacy & Professional RelationsBöhringer Ingelheim
Jennifer McNaryCo-FounderCanary Advisors
Kiran Musunuru, M.D., Ph.D.Barry J. Gertz Professor for Translational ResearchPerelman School of Medicine University of Pennsylvania
Brian NappiSVP, StrategySaol Therapeutics
Francis PangSVP Global Market Access and International Geographic ExpansionOrchard Therapeutics
Dave PearceChairInternational Rare Diseases Research Consortium (IRDiRC)
Dorian ReadnourVice President, InternationalSarepta Therapeutics
Frank RiveraPresidentStronger Than Sarcoidosis
Luis RojasChief Clinical Development OfficerPolaryx Therapeutics
Devyn SmithCEOArbor Biotechnologies
Frank SorgiPresident and Chief Executive OfficerFLAG Therapeutics
Steve St. OngeSVP - Corporate DevelopmentClarametyx Biosciences
Dionne StallingExecutive DirectorRare And Black
Ying TamChief Scientific OfficerAcuitas Therapeutics
Chelsea TrengroveCEO and CofounderNeoclease
Daniel WainstockResearcher and Rare Disease AdvocatePUC-Rio
Durhane Wong-RiegerPresident, Chief Executive OfficerCanadian Organisation for Rare Disorder & Rare Diseases International
Graeme LaddsCEOPharSafer
Charlene Son RigbyChief Executive OfficerGlobal Genes
Fyodor UrnovScientific Director, Innovative Genomics Institute, Professor, Department of Molecular & Cell BiologyUniversity of California at Berkeley
Jessica CerulloSenior Director, Patient Advocacy & Disease States InitiativesPierre Fabre Pharmaceuticals
Sponsors & Exhibitors | Leading Solution Providers
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