In the Press

Is 'Patient-Centered' enough for medically complex patients & families participating in clinical trials or new treatments?

Article from mejo

Key Takeaways from the World Orphan Drug Congress

Article from Sano Genetics

Insights From an Investor & Ex-payer on the Orphan Drug Market

Article from NAVLIN DAILY

Leveraging the NIH to Develop & Commercialize Products

Article from NAVLIN DAILY

What I Learned at World Orphan Drug Congress 2024

Infographic from ChitChat Digital

Pricing, Reimbursement, & Payer Challenges for Rare Diseases

Article from NAVLIN DAILY

Newborn Screening and Genetic Testing Could Increase the Reach of the Orphan Drug Act

Article from Rare Disease Advisor

Summary – Policy Panel: "360 view: How do we improve access while we continue to promote innovation"

Post from Americas Health Foundation

Highlights – Policy Panel: "360 view: How do we improve access while we continue to promote innovation"

Post from Americas Health Foundation

Prioritizing Clinicians’ Mental Health in Rare Disease Care

Article from Rare Disease Advisor

Accelerating Delivery and Patient Access to Rare Disease Treatments – Highlights from World Orphan Drug Congress

Article from Parexel

Access to Rare Disease Medicines in LMICs

Article from NAVLIN DAILY

Innovation & Access Hurdles in India

Article from NAVLIN DAILY

Alterity Therapeutics Presents New Data Demonstrating Potential of ATH434 to Treat Rare Neurodegenerative Disease Friedreich’s Ataxia

Article from Alterity Therapeutics

Missing Link Between Approval, Access, and Adoption of Rare Disease Treatments Continues to Negatively Impact Patient Care

Article from NAVLIN DAILY

Rare Disease Community Must be "Proactive" When Engaging with State Medicaid Agencies

Article from NAVLIN DAILY

Innovative Payment Models are Key to Payer Coverage of Rare Therapies

Article from NAVLIN DAILY

Legislation Could Improve Access to Specialized Pediatric Health Care

Article from Rare Disease Advisor

A Neglected Health Concern: Rare Diseases in Adults

Article from Rare Disease Advisor

Clinicians Urged to Use Genetic Testing to Expedite Diagnosis

Article from Rare Disease Advisor

The CoRDS Registry: Empowering Patients and Advancing Research

Article from Rare Disease Advisor

Innovative Technologies Could Speed Diagnosis of Rare Diseases

Article from Rare Disease Advisor

Sickle Cell Disease Patient Advocate Calls for Patient-Centered Care

Article from Rare Disease Advisor

To Obtain Reimbursement in Europe, Come Prepared and with Good Evidence

Article from NAVLIN DAILY

Four Takeaways from World Orphan Drug Congress

Article from Real Chemistry

A Call to Action Newborn Screening Now

Presentation from Alice McConnell, CEO & Co-Founder, Speragen

Sciensus hosts a panel at the World Orphan Drug Congress 2024

Article from Sciensus

Unlocking Clinical Trial Recruitment Success: BioNews Presents at World Orphan Drug Congress 2024

Press Release for BioNews Clinical

Joining the Discussion: The Rare Disease Translational Center Attends the 2024 World Orphan Drug Congress

Video from The Jackson Laboratory

FDNA and Genome Medical Improve Access to Critical Diagnostic Services for Children in Medically Underserved Areas

Press Release from FDNA & Genome Medical

The Impact of Rare Diseases on the Experience of Siblings

Article from Pharma 4.0 – Orphan Drugs