SPONSOR THE WORLD ORPHAN DRUG CONGRESS USA 2023

 

 

 

1700+

Attendees

100+

Sponsors & Exhibitors

250+

Speakers

3

Days of Content

13

Themes of Content

 

WHO ATTENDS

Pharma, biotechs

  • VP Clinical Development
  • Chief Medical Officer
  • Chief Scientific Officer
  • Regulatory Affairs
  • President, Head of Rare Diseases

TOPIC AREAS

- Patient centric clinical development

- Clinical trial design

- Real World Evidence in clinical development

- Expanded Access Programs / Managed Access Programs

WHO SHOULD SPONSOR

- Contract Research Organizations (CROs)

- Contract Development and Manufacturing Organizations (CDMOs)

- Clinical Trials Services - Home Clinical Trials

- Patient Recruitment & Identification

- Regulatory Consulting

WHO ATTENDS

Pharma, biotechs

  • Chief Patient Officer
  • VP Patient Advocacy
  • Medical Affairs
  • Patient Engagement

Patient Advocacy Groups

TOPICS AREAS

- Patient Data

- Patient Registries & Patient Reported Outcomes (PROs)

- Evolving role of patient groups in R&D

- Genetic testing & diagnosis

- Advocacy & Policy

- Setting up patient groups

- Industry collaboration

WHO SHOULD SPONSOR

- Pharma & biotechs

- Research Institutions

- Patient Registries

- Patient Engagement Platforms

- Genetic Testing providers

- Genomic Sequencing Platforms

- Diagnostics

WHO ATTENDS

Pharma, biotechs

  • VP Gene Therapy
  • Chief Medical Officer
  • Chief Manufacturing Officer
  • Chief Scientific Officer
  • VP Manufacturing

Technical Operations

TOPICS AREAS

- Gene therapy development

- Cell therapy development

- Translational science and path to clinical trials

- Regulation

WHO SHOULD SPONSOR

- Advanced therapies pharma & biotechs

- Gene Editing biotechs

- Contract Research Organizations (CROs)

- Clinical trial design

WHO ATTENDS

Pharma, biotechs

  • Chief Executive Officer
  • VP, Head of Market Access
  • VP, Head of Pricing and Reimbursement
  • VP of Health Economics/HEOR
  • VP of HTA
  • Head of Value Demonstration
  • VP, Evidence and Data
  • Payers (public and private)
  • Government & Regulatory agencies

TOPICS AREAS

- Advanced therapies pricing & reimbursement

- Real World Evidence

- Health Technology Assessment

- Value Based Assessment

- Next generation pricing and innovative pricing models

WHO SHOULD SPONSOR

- PRO consultancies and PRO technology providers

- Value communication organizations

- Pricing & Reimbursement consulting firms

- HEOR service providers

- Patient registries and database providers

WHO ATTENDS

Pharma, biotechs

  • Chief Data Officer
  • Chief Technology Officer
  • Chief Operating Officer
  • VP, Analytics
  • Head of Innovation
  • Head of Digital

Hospitals and healthcare centers

Payers

TOPICS AREAS

- AI in drug discovery

- Patient identification

- Data analytics

- Data collection through wearables and applications

WHO SHOULD SPONSOR

- Artificial Intelligence platforms

- Patient identification solutions

- Machine learning

- Data analytics

- Wearable technology

- Digital Health Apps

- Patient registries

WHO ATTENDS

Pharma, biotechs

  • CEO
  • Presidents
  • Chief Business Officer
  • VP Business Development
  • VP External Innovation
  • VP R&D

Venture Capital Firms

Grant Agencies (Public and Private)

Licensing pharma

TOPICS AREAS

- Advanced therapies investment

- Risk assessment

- Partnering and co-development opportunities

- Funding

- Accelerating orphan drug development

- Successful case studies

WHO SHOULD SPONSOR

- Advanced therapies investment

- Risk assessment

- Partnering and co-development opportunities

- Funders

WHO ATTENDS

Pharma, biotechs

  • Chief Commercial Officer
  • VP Commercial Operations
  • VP of Marketing
  • VP Medical Affairs

TOPIC AREAS

- Business models

- Forecasting and Epidemiology

- Global expansion and internationalization

- Business development

WHO SHOULD SPONSOR

- Specialty Pharmacy

- Logistics, Supply Chain, 3PL

- Strategic Consulting

- Real World Evidence

- Forecasting and Epidemiology

- Marketing, Communications Agency

WHO ATTENDS

Pharma, biotechs

  • Presidents & Heads of Patient Diagnosis Programs
  • R&D Strategic Alliance

Rare Disease advocacy organizations

  • Newborn Screening

TOPIC AREAS

- Genetic counselling

- Industry partnerships

- Genomics

- Newborn Screening

- Access & Reimbursement of testing

WHO SHOULD SPONSOR

- Genetic testing companies

- Genetic counselling consulting

- Genomics companies

- Newborn screening providers

WHO ATTENDS

Pharma, biotechs

  • Chief Operating Officer
  • Chief Manufacturing & Technology Officer
  • VP Technical Operations
  • VP of CMC
  • VP Manufacturing
  • VP of Process Development
  • VP of Quality Control

TOPIC AREAS

- Process development

- Outsourcing

- Viral vector development

- Manufacturing efficiency and capacity

- Analytical development

- Quality Control

WHO SHOULD SPONSOR

- Process development

- Outsourcing

- Viral vector development

- Manufacturing efficiency and capacity

- Analytical development

WHO ATTENDS

Pharma, biotechs

  • VP Market Access
  • Pricing and Reimbursement
  • Chief Commercial Officer
  • International Business

Regulators

Government

  • Ministry of Health
  • Policy makers

TOPIC AREAS

- Market entry strategies

- Stakeholder collaboration for market access

- Real World Evidence

- Improving access

- International regulation

WHO SHOULD SPONSOR

- Market entry strategies

- Stakeholder collaboration for market access

- Real World Evidence

- Improving access

- International regulation

WHO ATTENDS

Pharma, biotechs

  • Heads of Discovery
  • VP Clinical Development
  • Chief Medical Officer
  • Chief Scientific Officer
  • Regulatory Affairs
  • President, Head of Rare Diseases

TOPIC AREAS

- Discovery platforms

- Artificial Intelligence & Machine Learning applications

- Small molecule development

- Scientific innovations

- Collaborations

WHO SHOULD SPONSOR

- Drug discovery companies

- Artificial Intelligence and Machine Learning applications

- Predictive analytics platforms

- Contract Research Organizations (CROs)

WHO ATTENDS

Pharma, biotechs

  • VP Cell Therapy
  • Head of Oncology
  • Head of Immunotherapy 
  • Chief Medical Officer

TOPIC AREAS

- Diagnosis

- Biomarker R&D

- CAR-T development

- Advocacy and patient voice

- Clinical development and commercialization

WHO SHOULD SPONSOR

- Immunoncology pharma and biotechs

- Contract Manufacturing Organizations (CMOs)

- Contract Research Organizations (CROs)

- Genomic/DNA sequencing

 

PAYERS SEMINAR

On this seminar, payers from around the world will discuss approaches and strategies to improve pricing & reimbursement in rare diseases, including innovative pricing schemes and optimization of value-based assessments.

NEXT GEN THERAPIES SEMINAR

Learn about novel pipelines, approaches and candidates on the Next Generation Therapies Seminar, where someday these technologies and therapies could be the common place to treat rare diseases.

PATIENT DATA SEMINAR

When developing therapies for rare and ultra-rare diseases the value of patient data is immensurable. Though patients and their families are usually willing to share their data to advance research being their individual causes, issues with data privacy, ownership, consent and handling are still a big hurdle impeding the progress of utilizing data to identify patients, shorten the time for an accurate diagnosis, build disease knowledge, expedite R&D, and enhance access to available therapies. assessments.

2023 SPONSORS & EXHIBITORS

  • Title Sponsor

    Sanofi at World Orphan Drug Congress USA 2023

    Platinum Sponsor

    Clinigen Group at World Orphan Drug Congress USA 2023

    Platinum Sponsor

    GeneDx at World Orphan Drug Congress USA 2023
  • Platinum Sponsor

    Pfizer at World Orphan Drug Congress USA 2023

    Platinum Sponsor

    Premier Research at World Orphan Drug Congress USA 2023

    Platinum Sponsor

    volv global at World Orphan Drug Congress USA 2023
  • Diamond Sponsor

    Alexion at World Orphan Drug Congress USA 2023

    Diamond Sponsor

    EVERSANA at World Orphan Drug Congress USA 2023

    Diamond Sponsor

    IPM.ai at World Orphan Drug Congress USA 2023
  • Diamond Sponsor

    Janssen (J&J) at World Orphan Drug Congress USA 2023

    Diamond Sponsor

    Parexel at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Allucent at World Orphan Drug Congress USA 2023
  • Gold Sponsor

    BlueDil International Ltd at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Uniphar/Durbin at World Orphan Drug Congress USA 2023

    Gold Sponsor

    H4B-Boston at World Orphan Drug Congress USA 2023
  • Gold Sponsor

    ICON plc at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Invitae at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Emmes at World Orphan Drug Congress USA 2023
  • Gold Sponsor

    P2P Syncro at World Orphan Drug Congress USA 2023

    Gold Sponsor

    PCM Trials at World Orphan Drug Congress USA 2023

    Gold Sponsor

    PPD, part of Thermo Fisher Scientific at World Orphan Drug Congress USA 2023
  • Gold Sponsor

    ProPharma at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Red Nucleus at World Orphan Drug Congress USA 2023

    Gold Sponsor

    TREND Community at World Orphan Drug Congress USA 2023
  • Gold Sponsor

    UCB at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Worldwide Clinical Trials at World Orphan Drug Congress USA 2023

    Silver Sponsor

    Anovo at World Orphan Drug Congress USA 2023
  • Silver Sponsor

    Arthur D. Little at World Orphan Drug Congress USA 2023

    Silver Sponsor

    Bionical Emas at World Orphan Drug Congress USA 2023

    Silver Sponsor

    BluePrint Orphan at World Orphan Drug Congress USA 2023
  • Silver Sponsor

    Inozyme at World Orphan Drug Congress USA 2023

    Silver Sponsor

    Magnolia Innovation at World Orphan Drug Congress USA 2023

    Silver Sponsor

    myTomorrows at World Orphan Drug Congress USA 2023
  • Silver Sponsor

    PDC CRO at World Orphan Drug Congress USA 2023

    Silver Sponsor

    Pharma BP DMCC at World Orphan Drug Congress USA 2023

    Silver Sponsor

    Resilience at World Orphan Drug Congress USA 2023
  • Silver Sponsor

    Simon-Kucher at World Orphan Drug Congress USA 2023

    Silver Sponsor

    WEP Clinical at World Orphan Drug Congress USA 2023

    Exhibitor

    Rare Diseases International at World Orphan Drug Congress USA 2023
  •  

    Check Rare at World Orphan Drug Congress USA 2023

    Exhibitor

    National Organization for Rare Disorders at World Orphan Drug Congress USA 2023

    Exhibitor

    Lubrizol Life Science - Health at World Orphan Drug Congress USA 2023
  • Exhibitor

    ActiGraph Inc at World Orphan Drug Congress USA 2023

    Exhibitor

    Biorasi at World Orphan Drug Congress USA 2023

    Exhibitor

    Carbogen Amcis Switzerland at World Orphan Drug Congress USA 2023
  • Exhibitor

    Ergomed at World Orphan Drug Congress USA 2023

    Exhibitor

    Fighting for Kaiden Foundation, Inc. at World Orphan Drug Congress USA 2023

    Exhibitor

    Genome Medical at World Orphan Drug Congress USA 2023
  • Exhibitor

    Genomenon at World Orphan Drug Congress USA 2023

    Exhibitor

    Innomar Strategies at World Orphan Drug Congress USA 2023

    Exhibitor

    n-Lorem Foundation at World Orphan Drug Congress USA 2023
  • Exhibitor

    Only Orphans Cote at World Orphan Drug Congress USA 2023

    Exhibitor

    P3 Technology at World Orphan Drug Congress USA 2023

    Exhibitor

    PerkinElmer at World Orphan Drug Congress USA 2023
  • Exhibitor

    Pharmaceutics International Inc. at World Orphan Drug Congress USA 2023

    Exhibitor

    Rare Disease Research at World Orphan Drug Congress USA 2023

    Exhibitor

    Rare Patient Voice, LLC at World Orphan Drug Congress USA 2023
  • Exhibitor

    Scout Clinical at World Orphan Drug Congress USA 2023

    Exhibitor

    Sequegenics at World Orphan Drug Congress USA 2023

    Exhibitor

    Specialty Scripts RX at World Orphan Drug Congress USA 2023
  • Exhibitor

    TMC Pharma at World Orphan Drug Congress USA 2023

    Poster

    Across Healthcare at World Orphan Drug Congress USA 2023

    Poster

    Adcum - association of urea and metabolic cycle disorders Peru at World Orphan Drug Congress USA 2023
  • Poster

    aggamin at World Orphan Drug Congress USA 2023

    Poster

    Americas Health Foundation at World Orphan Drug Congress USA 2023

    Poster

    Amneal Pharmaceuticals at World Orphan Drug Congress USA 2023
  • Poster

    Aspire Biosciences at World Orphan Drug Congress USA 2023

    Poster

    August Care at World Orphan Drug Congress USA 2023

    Poster

    AVLT/Eurordis at World Orphan Drug Congress USA 2023
  • Poster

    Biohaven at World Orphan Drug Congress USA 2023

    Poster

    Biostrategies at World Orphan Drug Congress USA 2023

    Poster

    Catailyst Inc at World Orphan Drug Congress USA 2023
  • Poster

    Chronic Disease Coalition at World Orphan Drug Congress USA 2023

    Poster

    Critical Path Institute at World Orphan Drug Congress USA 2023

    Poster

    Collaborations Pharmaceuticals at World Orphan Drug Congress USA 2023
  • Poster

    Cure AP-4 at World Orphan Drug Congress USA 2023

    Poster

    Dreamsickle Kids Foundation at World Orphan Drug Congress USA 2023

    Poster

    ECP at World Orphan Drug Congress USA 2023
  • Poster

    EverythingALS at World Orphan Drug Congress USA 2023

    Poster

    Fibrous Dysplasia Foundation at World Orphan Drug Congress USA 2023

    Poster

    Fshd Society at World Orphan Drug Congress USA 2023
  • Poster

    GeneScape at World Orphan Drug Congress USA 2023

    Poster

    Pulse Infoframe at World Orphan Drug Congress USA 2023

    Poster

    Histiocytosis Association at World Orphan Drug Congress USA 2023
  • Poster

    Indo US Organization for Rare Diseases (IndoUSrare) at World Orphan Drug Congress USA 2023

    Poster

    KBG Foundation at World Orphan Drug Congress USA 2023

    Poster

    Moderna at World Orphan Drug Congress USA 2023
  • Poster

    Patient expert at World Orphan Drug Congress USA 2023

    Poster

    Principia Health Sciences at World Orphan Drug Congress USA 2023

    Poster

    PUC-Rio at World Orphan Drug Congress USA 2023
  • Poster

    Rare Disorders Kenya at World Orphan Drug Congress USA 2023

    Poster

    RetireSafe at World Orphan Drug Congress USA 2023

    Poster

    SATB2 Gene Foundation at World Orphan Drug Congress USA 2023
  • Poster

    Scleroderma Foundation Inc at World Orphan Drug Congress USA 2023

    Poster

    Southern Nevada Black Nurse Association at World Orphan Drug Congress USA 2023

    Poster

    Sprout Health Solutions at World Orphan Drug Congress USA 2023
  • Poster

    Systemic JIA Foundation at World Orphan Drug Congress USA 2023

    Poster

    TESS Research Foundation at World Orphan Drug Congress USA 2023

    Poster

    Tenaya Therapeutics at World Orphan Drug Congress USA 2023
  • Poster

    The Sturge-Weber Foundation at World Orphan Drug Congress USA 2023

    Poster

    TBRS community at World Orphan Drug Congress USA 2023

    Poster

    University of Maryland School of Medicine at World Orphan Drug Congress USA 2023
  • Poster

    Unravel Biosciences at World Orphan Drug Congress USA 2023

    Poster

    Usher III Initiative at World Orphan Drug Congress USA 2023

Get Involved At World Orphan Drug Congress USA

 

To Sponsor Or Exhibit

 
 

Justin Franks
justin.franks@terrapinn.com
t/ +1 914 819 3506

 

 

 

To Speak

 
 

Claire Murphy
claire.murphy@terrapinn.com
t/ +1 646 619 1784

 

 

 

Marketing & Press Opportunities

 
 

Taylor Post
taylor.post@terrapinn.com
t/ +1 646 619 1785