EVERSANA® is the leading provider of global commercial services to the life sciences industry. Our integrated solutions are rooted in the patient experience and span all stages of the product life cycle to deliver long-term, sustainable value for...
Diamond Sponsor
Diamond Sponsor
Parexel - Diamond Sponsor
Parexel is among the world’s largest clinical research organizations (CROs), providing the full range of Phase I to IV clinical development services to help life-saving treatments reach patients faster. Leveraging the breadth of our...
Diamond Sponsor
Sciensus - Diamond Sponsor
Sciensus is a global network dedicated to getting rare medicines to hard-to-reach patients worldwide. For over 30 years, we’ve delivered on every aspect of this vital transaction; from early access all the way to full commercialisation, including...
Diamond Sponsor
Havas Life Rare - Platinum Sponsor
Havas Life Rare is the premier commercialization and marketing partner for orphan drugs and rare disease markets.
In a setting where natural history, diagnosis, care pathways, awareness, and access are almost always underdeveloped, it takes...
Platinum Sponsor
Platinum Sponsor
Premier Research - Platinum Sponsor
Premier Research, the clinical research company that’s Built for Biotech℠, is dedicated to helping biotech, specialty pharma, and device innovators transform life-changing ideas and breakthrough science into new medical treatments. As a global...
Platinum Sponsor
Red Nucleus - Platinum Sponsor
We are your global strategic partner trusted to deliver transformative solutions across the entire life sciences product life cycle. By connecting our full suite of products and services, we are the “red thread” to lead you through transformational...
Platinum Sponsor
volv global - Platinum Sponsor
Volv Global utilizes advanced data science to identify undiagnosed patients with hard-to-diagnose diseases, prioritizing innovation, data security, and efficient solutions. Based in Switzerland, we aim to reduce healthcare costs and enhance global...
Platinum Sponsor
Ada Health - Gold Sponsor
Ada Health is a global digital health company created by doctors to improve human health by transforming knowledge into better outcomes.With our medical-AI-based symptom assessment and care navigation solutions, we help millions of people with...
Gold Sponsor
Gold Sponsor
Allucent - Gold Sponsor
Allucent, is a global clinical services organization uniquely positioned to serve small and mid-sized biotech companies. With more than 30 years of experience in over 60 countries, we have supported over 210 rare and orphan disease clinical studies...
Gold Sponsor
GeneDx - Gold Sponsor
At GeneDx, we believe that everyone deserves personalized, targeted medical care—and that it all begins with a genetic diagnosis. Fueled by one of the world’s largest rare disease data sets, our exome and genome tests translate complex genomic data...
Gold Sponsor
ICON PLC - Gold Sponsor
ICON is the world’s leading clinical research organisation, powered by healthcare intelligence. From molecule to medicine, we advance clinical research providing a comprehensive suite of outsourced development and commercialisation services to...
Gold Sponsor
Gold Sponsor
Gold Sponsor
Halloran Consulting Group - Gold Sponsor
Halloran Consulting Group is a life science consulting firm providing strategic development, regulatory, quality, clinical, and organizational support to industry leaders in the pharmaceutical, biotechnology, and medical device sectors. Our...
Gold Sponsor
Real Chemistry - Gold Sponsor
Real Chemistry’s mission is to transform what healthcare is to what it should be by leveraging the industry’s most advanced AI-powered insights, diverse expertise and customer-centric ideas. We help the healthcare industry better understand, reach...
Gold Sponsor
Lannett CDMO - Gold Sponsor
Founded in 1942, Lannett Company, Inc., is a long-established manufacturer of unique pharmaceutical indications with over 100 product families currently in distribution. Our deep industry knowledge of end-to-end solutions can be customized to our...
Gold Sponsor
P2P Syncro - Gold Sponsor
P2P Syncro is at the forefront of rare disease education. We recognized that the educational approach used in disorders commonly seen may not apply to rare diseases. We adopted innovative strategies in conducting campaigns and delivering programs to ...
Gold Sponsor
PCM Trials - Gold Sponsor
PCM Trials is leading the way in mobile research and decentralized clinical trials. Since 2008, PCM Trials has led the way in mobile research. Our Certified Mobile Research Nurses (CMRNs) are driving the shift to patient-centric, decentralized...
Gold Sponsor
Gold Sponsor
Gold Sponsor
Uniphar - Gold Sponsor
Uniphar is a dynamic global healthcare company with more than 3,500 employees worldwide and active in 160 countries. We are a trusted global partner to pharma and Medtech manufacturers, working to unlock access to innovative therapies and optimise...
Gold Sponsor
Worldwide Clinical Trials - Gold Sponsor
Worldwide Clinical Trials (Worldwide) is a leading global contract research organization (CRO) that works in partnership with biotechnology and pharmaceutical companies to create customized solutions that advance new medications, from discovery to...
Gold Sponsor
York Health Economics Consortium - Gold Sponsor
York Health Economics Consortium is a health economics consulting company owned by the University of York. It provides a range of services, including economic modelling, literature searching, systematic reviews, network...
Gold Sponsor
Akrolyth - Silver Sponsor
Akrolyth Advisory provides expert commercial strategy and business planning, opportunity evaluation and acquisition/licensing support, valuation, modeling and forecasting, analytical, and market research services with a focus on Life Sciences – for...
Silver Sponsor
Alethium Health - Silver Sponsor
Alethium Health transforms protocols into working trials. We are debuting our newest eCOA, Consent, and telehealth solution. Built on decades of industry experience, our exquisite UI and innovative features foster security, prevent...
Silver Sponsor
AnovoRx - Silver Sponsor
Dedicated. Exclusive. Unique.
Every orphan product requires its own solution, and only Anovo is built from the ground up to develop and deliver the optimal solution, every time.
Our business is entirely dedicated to supporting orphan...
Silver Sponsor
BlueGene Search - Silver Sponsor
BlueGene Search is your one-stop shop for life science and specialty biotech recruiting. With a focus on startups and rare disease, we're passionate about creating the right talent fit to build teams that deliver on their promise to patients. We ...
Silver Sponsor
Silver Sponsor
Costello Medical - Silver Sponsor
Costello Medical provides scientific and health economic support in the analysis and interpretation of clinical and economic data
Silver Sponsor
Silver Sponsor
myTomorrows - Silver Sponsor
myTomorrows' mission is to enable earlier and better access to all possible treatment options. We aim to break barriers for eligible patients to receive information on and enroll in clinical trials and expanded access programs by providing a...
Silver Sponsor
Silver Sponsor
PharmaBlue - Silver Sponsor
Welcome to PharmaBlue
A Partner for Innovative Pharmaceutical CompaniesWe are your Medium/Long term partner to get and run your Early Access Program in France.
We provide Exploitant services to our clients for rapidly marketing their approved...
Silver Sponsor
Scout - Silver Sponsor
Scout empowers the life sciences industry with people-first solutions: Scout Meetings, Scout Clinical, and Scout Academy. We specialize in face-to-face, virtual, and hybrid clinical meeting planning, patient payment, travel, and logistics...
Silver Sponsor
Silver Sponsor
EpidStrategies - Silver Sponsor
ToxStrategies is a multidisciplinary scientific consulting firm that strives to develop innovative solutions to address the scientific, technical, and regulatory challenges confronting our clients. We have a reputation for applying sound science and ...
Silver Sponsor
Veristat - Silver Sponsor
Veristat is The Science-First CRO™, integrating full service clinical trial execution, regulatory consulting, and strategic planning to rapidly advance the development, approval, and commercialization of your revolutionary therapies around the...
Silver Sponsor
Avance - Exhibitor
Avance Clinical is a full-service CRO for biotechs with a proven track-record for delivering clinical excellence in Australia, New Zealand, and North America. As the largest premium full-service CRO in Australia and North America, Avance Clinical...
Exhibitor
Berkshire Sterile Manufacturing - Exhibitor
Berkshire Sterile Manufacturing (BSM), located in Lee, Massachusetts, specializes as a contract development and manufacturing organization (CDMO) focused on aseptic filling. Our expertise extends to vials, syringes, and cartridges, equipped with...
Exhibitor
Bio Insight Group - Exhibitor
Video and Animation Specialists
At Bio Insight Group, we focus on helping companies elevate the impact of their life-saving therapies. We deliver on this focus by leveraging our direct pharma/biotech brand leadership experience with award-winning...
Exhibitor
Caidya - Exhibitor
Caidya is a multi-therapeutic clinical research organization (CRO) serving innovators worldwide. Focused on delivery excellence and an elevated customer experience, Caidya offers a wide range of clinical services and vast therapeutic...
Exhibitor
Centogene - Exhibitor
CENTOGENE’s mission is to provide data-driven, life-changing answers to patients, physicians, and pharma companies for rare and neurodegenerative diseases. We integrate multiomic technologies with the CENTOGENE Biodatabank – providing dimensional...
Exhibitor
Dendrite Clinical Systems - Exhibitor
Dendrite Clinical Systems is a specialist supplier of clinical database software, consultancy and publishing services for the international healthcare sector. With over 30 years’ experience, the company’s global user base extends across hundreds of...
Exhibitor
Exhibitor
ExperTrials - Exhibitor
We are a full-service CRO for Biotech and Medtech companies.Founded in 2011 and based in France, we are proud to be experts in offering niche services which span the entire lifecycle of your product.From clinical development to marketing...
Exhibitor
Genome Medical - Exhibitor
Genome Medical is enabling a world where everyone’s health is informed by genetics. As the nation’s leading telehealth genetics provider, we make genetic care easily accessible and actionable for any patient that needs it. We partner with health...
Exhibitor
Greenphire Inc - Exhibitor
Greenphire is a Thoma Bravo-backed software company specializing in providing comprehensive solutions for streamlining clinical trials. With a focus on optimizing patient experiences, Greenphire offers innovative software for travel and logistics...
Exhibitor
Exhibitor
Exhibitor
PDC CRO - Exhibitor
PDC CRO is a full-Service CRO serving the MEA region and specialized in providing a full range of clinical trial services to the pharmaceutical, biotechnology, and medical device industries. With a focus on quality, efficiency, and...
Exhibitor
Rare Disease Research, LLC - Exhibitor
RDR is an independent clinical research site network, 100% dedicated to conducting clinical research, accelerating the development of safe and effective treatments for rare diseases, and providing access to innovative investigational therapies to...
Exhibitor
Rare Patient Voice, LLC - Exhibitor
Rare Patient Voice, LLC provides patients and family caregivers an opportunity to participate in all types of research including market research, health economics outcomes and real-world evidence, user experience/human factors studies, and clinical...
Exhibitor
TMC Pharma - Exhibitor
TMC is a global clinical research organisation dedicated to supporting the progression of life-saving treatment solutions for orphan, rare and oncology diseases.
With over two decades of experience, we’re a specialised, full-service CRO providing...
Exhibitor
Start-Up
Start-Up
Exhibiting Partner
jCyte Inc - Start-Up
jCyte, Inc. is a clinical-stage biotech company focused on developing its first-in-class allogeneic cell therapy, jCell, for retinitis pigmentosa (RP) and other retinal degenerative disorders. The treatment has received FDA Regenerative Medicine...
Start-Up
Exhibiting Partner
Project Alive - Exhibiting Partner
We exist to find a cure for Hunter syndrome through research and advocacy, and providing education and resources to the Hunter syndrome community. We are here to give a voice to the families and children touched by Hunter syndrome.
Project Alive is ...
Exhibiting Partner
Start-Up
Undiagnosed Diseases Network Foundation - Exhibiting Partner
The UDNF aims to foster collaboration among patients, clinicians, and scientists to enhance the quality of life of undiagnosed and ultra-rare disease patients. We do this by mitigating barriers to equity and access in healthcare; setting standards...
Exhibiting Partner
Varient - Start-Up
Varient is a scalable digital health platform to create touch points with, and collect real-world evidence from, patients living with genetic and rare disease. Varient creates a win-win scenario for all stakeholders: the patients receive off-label...
Start-Up
Supporting Partner
Patient Advocacy Partner
Undiagnosed Diseases Network Foundation - Patient Advocacy Partner
The UDNF aims to foster collaboration among patients, clinicians, and scientists to enhance the quality of life of undiagnosed and ultra-rare disease patients. We do this by mitigating barriers to equity and access in healthcare; setting standards...
Patient Advocacy Partner
Alliance for Regenerative Medicine - Media Partner
ARM is the leading international advocacy organization championing the benefits of engineered cell therapies and genetic medicines for patients, healthcare systems, and society. As a community, ARM builds the future of medicine by convening the...
Media Partner
Media Partner
Americas Health Foundation - Media Partner
Americas Health Foundation is a 501 (c)(3), non-profit foundation. We are a unique bridge between the industry and governments. We strive to create multi-stakeholder collaboration for the future of healthcare. Although specialized in the Latin...
Media Partner
Media Partner
BioNews Clinical - Media Partner
BioNews is a health media company focused on rare diseases and rare patient experiences. BioNews provides an insider’s view into disease and treatment news, condition management information, and community across more than 60+ diseases.A fierce...
Media Partner
Check Rare - Media Partner
CheckRare is a website and learning platform for health care professionals and patients. Our platform allows users to gain insight and learn about rare diseases, current and emerging therapies, clinical trials, and the BioPharma companies behind...
Media Partner
Cushing's Support & Research Foundation - Media Partner
Cushing's Support and Research Foundation (CSRF) is a US 501c3 non-profit organization that will celebrate its 30th anniversary in 2025. Patient-led from inception, CSRF's focus has support, education, and quality of life research at its...
Media Partner
Enterprise Viewpoint - Media Partner
Enterprise Viewpoint (EV) creates high-quality content to improve businesses. Our platform offers unique insights and valuable networks to support the growth of young and ambitious entrepreneurs. Our special edition features stories of successful...
Media Partner
ERCAL Enfermedades raras del Caribe y América Latina - Media Partner
ERCAL is a multi-stakeholder Foundation in Latin America and the Caribbean (LAC) consisting of expert individuals and organizations that promote and work to improve the lives of people living with rare diseases and their families.Formed by experts...
Media Partner
Gene Therapy Net - Media Partner
Gene Therapy Net is the information resource for basic and clinical research in gene therapy, and the site serves as a network for the exchange of gene therapy information and breaking news items. Visitors can keep track of the latest scientific...
Media Partner
Icon Outlook - Media Partner
ICON Outlook Magazine is a hub for businesses around the world using technology to transform our world. Our seasoned researchers, analysts, and writers spot global trends and the latest tech marvels poised for disruption. As a team with the most...
Media Partner
Media Partner
Medhealth Outlook - Media Partner
Medhealth Outlook offers insights into the latest technologies and trends in the healthcare, pharma, and medical industries. Our publication provides a balanced perspective through an inside/outside approach, showcasing interviews, features, and...
Media Partner
Media Planet - Media Partner
Mediaplanet delivers best-in-class content marketing campaigns for more than 8,000 clients around the globe. We make branding easy for our clients by taking care of the entire value chain – from concept to production and distribution, and by...
Media Partner
Media Partner
NAVLIN Daily by Eversana - Media Partner
Global pricing and market access news without all of the noise. NAVLIN Daily connects the dots on how the day’s biggest stories affect your business and keeps you up-to-date and informed, so you can make better, smarter decisions. We provide...
Media Partner
n-Lorem Foundation - Media Partner
n-Lorem Foundation is a non-profit organization established to apply the efficiency, versatility and specificity of antisense technology to charitably discover, develop, and provide personalized experimental antisense oligonucleotide (ASO) medicines ...
Media Partner
Patient Worthy - Media Partner
Since 2015, Patient Worthy has been helping rare disease patients around the world to tell their stories. Whether it’s the latest in rare disease news, courageous patient profiles or heartfelt interviews on our award-winning podcast, Patient Worthy...
Media Partner
Personalize My Medicine - Media Partner
Personalize my Medicine is a platform for medical innovation. We keep you informed about the latest advancements in medical innovation with a focus on personalized and precision medicine approaches to healthcare. PMM aims to place people and...
Media Partner
Pharma Tech Outlook - Media Partner
Pharma Tech Outlook is a monthly publication that has been a pioneer in bringing forth real-world solutions, news, product trends, solutions, and many more to subscribers. The unique learn-from-peers approach is creating a difference since the...
Media Partner
Media Partner
Rare Access Action Project - Media Partner
RAAP, the Rare Access Action Project, is a coalition of life sciences and patient stakeholders that explore creative policy solutions to address structural issues in access and coverage. Our priority is to help ensure rare disease patients have...
Media Partner
Rare Disease Advisor - Media Partner
Rare Disease Advisor is a leading online resource for healthcare providers who treat rare diseases. RDA publishes timely news, exclusive features, expert opinions, and valuable resources across 40+ rare disease areas with the goal of helping reduce...
Media Partner
Rare Revolution - Media Partner
RARE Revolution Magazine is an independent not-for-profit publication dedicated to elevating the voice of the rare disease community through its website, digital magazine, patient engagement services and RARE Youth Revolution. It produces...
Media Partner
TREAT-NMD - Media Partner
TREAT-NMD works in partnership with organisations and individuals globally to transform diagnosis, treatment and care for people living with neuromuscular diseases.
Media Partner
Start-Up
Start-Up
Exhibiting Partner
jCyte Inc - Start-Up
jCyte, Inc. is a clinical-stage biotech company focused on developing its first-in-class allogeneic cell therapy, jCell, for retinitis pigmentosa (RP) and other retinal degenerative disorders. The treatment has received FDA Regenerative Medicine...
Start-Up
Exhibiting Partner
Project Alive - Exhibiting Partner
We exist to find a cure for Hunter syndrome through research and advocacy, and providing education and resources to the Hunter syndrome community. We are here to give a voice to the families and children touched by Hunter syndrome.
Project Alive is ...
Exhibiting Partner
Start-Up
Undiagnosed Diseases Network Foundation - Exhibiting Partner
The UDNF aims to foster collaboration among patients, clinicians, and scientists to enhance the quality of life of undiagnosed and ultra-rare disease patients. We do this by mitigating barriers to equity and access in healthcare; setting standards...
Exhibiting Partner
Varient - Start-Up
Varient is a scalable digital health platform to create touch points with, and collect real-world evidence from, patients living with genetic and rare disease. Varient creates a win-win scenario for all stakeholders: the patients receive off-label...
Start-Up
Undiagnosed Diseases Network Foundation - Patient Advocacy Partner
The UDNF aims to foster collaboration among patients, clinicians, and scientists to enhance the quality of life of undiagnosed and ultra-rare disease patients. We do this by mitigating barriers to equity and access in healthcare; setting standards...
Patient Advocacy Partner
Media Partner
Check Rare - Media Partner
CheckRare is a website and learning platform for health care professionals and patients. Our platform allows users to gain insight and learn about rare diseases, current and emerging therapies, clinical trials, and the BioPharma companies behind...
Media Partner
Cushing's Support & Research Foundation - Media Partner
Cushing's Support and Research Foundation (CSRF) is a US 501c3 non-profit organization that will celebrate its 30th anniversary in 2025. Patient-led from inception, CSRF's focus has support, education, and quality of life research at its...
Media Partner
Media Partner
Rare Disease Advisor - Media Partner
Rare Disease Advisor is a leading online resource for healthcare providers who treat rare diseases. RDA publishes timely news, exclusive features, expert opinions, and valuable resources across 40+ rare disease areas with the goal of helping reduce...
Media Partner
Rare Revolution - Media Partner
RARE Revolution Magazine is an independent not-for-profit publication dedicated to elevating the voice of the rare disease community through its website, digital magazine, patient engagement services and RARE Youth Revolution. It produces...