I proudly earned my medical degree from the Universidad de Buenos Aires, which set the foundation for my journey in pediatrics. My residency at Hospital Interzonal Agudos Especializado en Pediatría Sor María Ludovica in La Plata, Argentina, deepened my commitment to caring for children in need. Driven by a passion for advancing pediatric care, I pursued two Master's Degrees: one in Pediatric Neurology and Neurodevelopment from Universidad Cardenal Herrera in Spain, and another in Inherited Metabolic Disease from Universidad Santiago de Compostela. My clinical experience at Hospital Sor María Ludovica, working with patients affected by Inborn Metabolic Diseases, has only fueled my dedication to this field. Since 2019, I’ve had the privilege of serving as a Lead Clinical Research Associate at Connecticut Children’s, where I strive to make a meaningful impact. In addition, I am honored to be an Assistant Professor in the Department of Pediatrics at the University of Connecticut, where I can inspire the next generation of healthcare professionals. I am deeply passionate about the rare disease community and actively contribute to various global associations dedicated to different conditions. I am a member of the Society of Clinical Research Associates and a Certified Clinical Research Professional, underscoring my dedication to excellence in the field. I am passionately committed to advancing research and enhancing patients' quality of life through innovative solutions and compassionate care.
Recruitment and retention in rare disease clinical trials demand thoughtful planning, strong cross-disciplinary collaboration, and adaptable study designs. This presentation highlights practical, actionable strategies for coordinators and investigators to identify eligible participants, simplify screening procedures, and sustain participant engagement throughout the study lifecycle. Key topics include regulatory considerations, optimizing site-level workflows, and partnering with patient advocacy organizations to support recruitment. Attendees will leave with concrete tools and proven approaches to boost enrollment efficiency while upholding ethical and patient-centered research standards