Brandon Michael Henry | Medical Director, Cell and Gene Therapy
IQVIA

Brandon Michael Henry, Medical Director, Cell and Gene Therapy, IQVIA

Brandon Michael Henry, MD is a physician-scientist and Medical Director of the Cell and Gene Therapy Center of Excellence at IQVIA, where he leads medical strategy for rare disease programs across cell, gene, and RNA therapeutic modalities. He is internationally recognized for his contributions to rare disease research and clinical development, with over 400 peer-reviewed publications and recognition among the world’s top 2% of scientists (Stanford University, 2021–2024) and Clarivate’s Highly Cited Researchers list (2024). Dr. Henry brings 12+ years of experience spanning basic, translational, and clinical research across cell, gene, and RNA therapy, with deep expertise in biomarker-driven trials, adaptive trial design, and mitigating risks of immunogenicity. His work focuses on accelerating the development of novel therapeutics for rare diseases through innovative, data-driven approaches to trial design and execution. He serves as a scientific and medical advisor to both internal and sponsor teams and is an appointed member of multiple international professional body committees and journal editorial boards.  At the World Orphan Drug Congress USA 2025, Dr. Henry will share insights on clinical strategy and development innovation for long term follow-up in rare diseases, drawing from his experience at the intersection of cutting-edge science and global trial execution.

Appearances:



Day 1- World Orphan Drug Congress USA 2025 @ 15:30

Fireside chat: Cell and gene therapy long term follow-up: Innovative technology & data to support delivery for rare disease populations

We will discuss unique needs and challenges associated with the design and delivery of LTFU studies in rare disease. We will focus on how we can address these challenges by bringing together digital tools, with behavioral science, with instrument science / Patient Experience Data, and decentralized operations to drive long-term engagement and retention. We will review case studies, which provide lessons learned, and illuminate the possibilities of what can be achieved when you bring together these unique disciplines and deploy them through digital tools

Sposnored by IQVIA.

last published: 24/Apr/25 11:35 GMT

back to speakers

Get Involved At World Orphan Drug Congress USA

 

Connect with us

 
 
 
 

 

To Sponsor Or Exhibit

 
 

Justin Franks
justin.franks@terrapinn.com
t/ +1 914 819 3506

 

 

 

To Speak

 
 

Kaylee Nguyen
kaylee.nguyen@terrapinn.com
 

 

 

 

Marketing & Press

 
 

Kaylie Brogan
kaylie.brogan@terrapinn.com