Advanced Therapies


Advanced Therapies, Thursday 25 April 2024

Sheila Mikhail
Advanced Therapies

Manufacturing improvements for gene therapy for orphan drugs

Sheila Mikhail, Executive Director, Columbus Children's Foundation
Irina Antonijevic
Advanced Therapies

Individualized medicines for rare diseases – Opportunities and challenges

Irina Antonijevic, Chief Medical Officer, EveryONE Medicines
Carole Cramer
Advanced Therapies

Advances in treating the multisystemic manifestations of metabolic diseases – delivering enzyme everywhere it is needed

last published: 20/Apr/24 16:35




Get Involved At World Orphan Drug Congress USA


To Sponsor Or Exhibit


Justin Franks
t/ +1 914 819 3506




To Speak


Gina McHugh
t/ +1 646 619 1775




Marketing & Press Opportunities


Kaylie Brogan