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    World Orphan Drug Congress USA 2023

     

    May 23-25, 2023
    Gaylord National Resort & Convention Center Washington, D.C.

     

    Riverview Ballroom

    Tuesday, May 23 | Registration: 12pm, Pre-Conference 1-5pm

     

    Prince George Exhibit Halls C & D - Atrium Level

    Wednesday, May 24 | Registration: 8am, Expo hall: 8am-5:30pm, Conference: 8:30-6pm, Cocktail Party: 6-7pm 

    Thursday, May 25: Registration: 8am, Expo hall: 8am-3pm, Conference: 9am-4pm

     

    The World’s Most Important Orphan Drug
    and Rare Disease Event

     

1,200+

Attendees

100+

Sponsors & Exhibitors

250+

Speakers

3

Days of Content

13

Themes of Content

 
 

Title Sponsor

Breaking down silos and fostering collaboration to help rare disease patients

The World Orphan Drug Congress brings together leading pharmaceutical and biotech companies, government and regulatory authorities, patient advocacy groups, payers, investors and solution providers. The conference is a place to meet and brainstorm ways to advance orphan drug development and improve access to life-saving therapies.


Join us for three days in Washington for the most comprehensive program and inclusive gathering of rare disease stakeholders.

2023 Speakers

 

2023 Speakers

 

 

 

Companies that attend World Orphan Drug Congress USA

 

 

2023 Sponsors & Exhibitors
 

 

  • Title Sponsor

    Sanofi at World Orphan Drug Congress USA 2023

    Platinum Sponsor

    Clinigen Group at World Orphan Drug Congress USA 2023

    Platinum Sponsor

    GeneDx at World Orphan Drug Congress USA 2023
  • Platinum Sponsor

    Pfizer at World Orphan Drug Congress USA 2023

    Platinum Sponsor

    Premier Research at World Orphan Drug Congress USA 2023

    Platinum Sponsor

    volv global at World Orphan Drug Congress USA 2023
  • Diamond Sponsor

    Alexion at World Orphan Drug Congress USA 2023

    Diamond Sponsor

    EVERSANA at World Orphan Drug Congress USA 2023

    Diamond Sponsor

    IPM.ai at World Orphan Drug Congress USA 2023
  • Diamond Sponsor

    Janssen (J&J) at World Orphan Drug Congress USA 2023

    Diamond Sponsor

    Parexel at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Allucent at World Orphan Drug Congress USA 2023
  • Gold Sponsor

    BlueDil International Ltd at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Uniphar/Durbin at World Orphan Drug Congress USA 2023

    Gold Sponsor

    H4B-Boston at World Orphan Drug Congress USA 2023
  • Gold Sponsor

    ICON plc at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Invitae at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Emmes at World Orphan Drug Congress USA 2023
  • Gold Sponsor

    P2P Syncro at World Orphan Drug Congress USA 2023

    Gold Sponsor

    PCM Trials at World Orphan Drug Congress USA 2023

    Gold Sponsor

    PPD, part of Thermo Fisher Scientific at World Orphan Drug Congress USA 2023
  • Gold Sponsor

    ProPharma at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Red Nucleus at World Orphan Drug Congress USA 2023

    Gold Sponsor

    TREND Community at World Orphan Drug Congress USA 2023
  • Gold Sponsor

    UCB at World Orphan Drug Congress USA 2023

    Gold Sponsor

    Worldwide Clinical Trials at World Orphan Drug Congress USA 2023

    Silver Sponsor

    Anovo at World Orphan Drug Congress USA 2023
  • Silver Sponsor

    Arthur D. Little at World Orphan Drug Congress USA 2023

    Silver Sponsor

    Bionical Emas at World Orphan Drug Congress USA 2023

    Silver Sponsor

    BluePrint Orphan at World Orphan Drug Congress USA 2023
  • Silver Sponsor

    Inozyme at World Orphan Drug Congress USA 2023

    Silver Sponsor

    Magnolia Innovation at World Orphan Drug Congress USA 2023

    Silver Sponsor

    myTomorrows at World Orphan Drug Congress USA 2023
  • Silver Sponsor

    PDC CRO at World Orphan Drug Congress USA 2023

    Silver Sponsor

    Pharma BP DMCC at World Orphan Drug Congress USA 2023

    Silver Sponsor

    Resilience at World Orphan Drug Congress USA 2023
  • Silver Sponsor

    Simon-Kucher at World Orphan Drug Congress USA 2023

    Silver Sponsor

    WEP Clinical at World Orphan Drug Congress USA 2023

    Exhibitor

    Rare Diseases International at World Orphan Drug Congress USA 2023
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    Check Rare at World Orphan Drug Congress USA 2023

    Exhibitor

    National Organization for Rare Disorders at World Orphan Drug Congress USA 2023

    Exhibitor

    Lubrizol Life Science - Health at World Orphan Drug Congress USA 2023
  • Exhibitor

    ActiGraph Inc at World Orphan Drug Congress USA 2023

    Exhibitor

    Biorasi at World Orphan Drug Congress USA 2023

    Exhibitor

    Carbogen Amcis Switzerland at World Orphan Drug Congress USA 2023
  • Exhibitor

    Ergomed at World Orphan Drug Congress USA 2023

    Exhibitor

    Fighting for Kaiden Foundation, Inc. at World Orphan Drug Congress USA 2023

    Exhibitor

    Genome Medical at World Orphan Drug Congress USA 2023
  • Exhibitor

    Genomenon at World Orphan Drug Congress USA 2023

    Exhibitor

    Innomar Strategies at World Orphan Drug Congress USA 2023

    Exhibitor

    n-Lorem Foundation at World Orphan Drug Congress USA 2023
  • Exhibitor

    Only Orphans Cote at World Orphan Drug Congress USA 2023

    Exhibitor

    P3 Technology at World Orphan Drug Congress USA 2023

    Exhibitor

    PerkinElmer at World Orphan Drug Congress USA 2023
  • Exhibitor

    Pharmaceutics International Inc. at World Orphan Drug Congress USA 2023

    Exhibitor

    Rare Disease Research at World Orphan Drug Congress USA 2023

    Exhibitor

    Rare Patient Voice, LLC at World Orphan Drug Congress USA 2023
  • Exhibitor

    Scout Clinical at World Orphan Drug Congress USA 2023

    Exhibitor

    Sequegenics at World Orphan Drug Congress USA 2023

    Exhibitor

    Specialty Scripts RX at World Orphan Drug Congress USA 2023
  • Exhibitor

    TMC Pharma at World Orphan Drug Congress USA 2023

    Poster

    Across Healthcare at World Orphan Drug Congress USA 2023

    Poster

    Adcum - association of urea and metabolic cycle disorders Peru at World Orphan Drug Congress USA 2023
  • Poster

    aggamin at World Orphan Drug Congress USA 2023

    Poster

    Americas Health Foundation at World Orphan Drug Congress USA 2023

    Poster

    Amneal Pharmaceuticals at World Orphan Drug Congress USA 2023
  • Poster

    Aspire Biosciences at World Orphan Drug Congress USA 2023

    Poster

    August Care at World Orphan Drug Congress USA 2023

    Poster

    AVLT/Eurordis at World Orphan Drug Congress USA 2023
  • Poster

    Biohaven at World Orphan Drug Congress USA 2023

    Poster

    Biostrategies at World Orphan Drug Congress USA 2023

    Poster

    Catailyst Inc at World Orphan Drug Congress USA 2023
  • Poster

    Chronic Disease Coalition at World Orphan Drug Congress USA 2023

    Poster

    Critical Path Institute at World Orphan Drug Congress USA 2023

    Poster

    Collaborations Pharmaceuticals at World Orphan Drug Congress USA 2023
  • Poster

    Cure AP-4 at World Orphan Drug Congress USA 2023

    Poster

    Dreamsickle Kids Foundation at World Orphan Drug Congress USA 2023

    Poster

    ECP at World Orphan Drug Congress USA 2023
  • Poster

    EverythingALS at World Orphan Drug Congress USA 2023

    Poster

    Fibrous Dysplasia Foundation at World Orphan Drug Congress USA 2023

    Poster

    Fshd Society at World Orphan Drug Congress USA 2023
  • Poster

    GeneScape at World Orphan Drug Congress USA 2023

    Poster

    Pulse Infoframe at World Orphan Drug Congress USA 2023

    Poster

    Histiocytosis Association at World Orphan Drug Congress USA 2023
  • Poster

    Indo US Organization for Rare Diseases (IndoUSrare) at World Orphan Drug Congress USA 2023

    Poster

    KBG Foundation at World Orphan Drug Congress USA 2023

    Poster

    Moderna at World Orphan Drug Congress USA 2023
  • Poster

    Patient expert at World Orphan Drug Congress USA 2023

    Poster

    Principia Health Sciences at World Orphan Drug Congress USA 2023

    Poster

    PUC-Rio at World Orphan Drug Congress USA 2023
  • Poster

    Rare Disorders Kenya at World Orphan Drug Congress USA 2023

    Poster

    RetireSafe at World Orphan Drug Congress USA 2023

    Poster

    SATB2 Gene Foundation at World Orphan Drug Congress USA 2023
  • Poster

    Scleroderma Foundation Inc at World Orphan Drug Congress USA 2023

    Poster

    Southern Nevada Black Nurse Association at World Orphan Drug Congress USA 2023

    Poster

    Sprout Health Solutions at World Orphan Drug Congress USA 2023
  • Poster

    Systemic JIA Foundation at World Orphan Drug Congress USA 2023

    Poster

    TESS Research Foundation at World Orphan Drug Congress USA 2023

    Poster

    Tenaya Therapeutics at World Orphan Drug Congress USA 2023
  • Poster

    The Sturge-Weber Foundation at World Orphan Drug Congress USA 2023

    Poster

    TBRS community at World Orphan Drug Congress USA 2023

    Poster

    University of Maryland School of Medicine at World Orphan Drug Congress USA 2023
  • Poster

    Unravel Biosciences at World Orphan Drug Congress USA 2023

    Poster

    Usher III Initiative at World Orphan Drug Congress USA 2023

 


NETWORKING IS OUR SWEET SPOT

By App. By Facilitated Meetings. By RoundTables. By Hangin’ Out.


So you can: Exchange ideas, Build brand, Form friendships and partnerships, Grow your professional network, Explore the future, Uncover new opportunities.
 

Our World-Class Conference Features The Following Themes

 

patient data

PATIENT DATA

With so few patients, patient data/real-world-data (RWD/RWE) is the key element to advancing the rare disease space. What are best practices right now for data collection, ownership and sharing to benefit rare disease diagnosis, drug development and access.

next generation therapies

NEXT GENERATION THERAPIES

The rare disease space is a breeding ground for innovative approaches in drug development and platform technologies. What are the products and approaches that will be making headlines in 5-10 years from now?

payers

PAYERS

US-based insurers and single payer agencies around the world have a lot of impact of access and reimbursement for orphan products. Hear from top US and international payers on their strategies for orphan drugs.

clinical development & regulatory

CLINICAL DEVELOPMENT & REGULATORY

Understanding the regulatory and clinical landscape for rare disease drug development. How can companies, regulators and patient advocates work together to further patient voice, real world evidence, and decentralized clinical trials.

commercial

COMMERCIAL

What are the best commercial strategies for orphan products? How can companies bring products to new markets, build more efficient commercial operations, and develop effective launch strategies?

rare disease advocacy world

RARE DISEASE ADVOCACY WORLD

It all starts and ends with patients. So what are the challenges facing rare disease patients and patient organizations today? How can rare disease patient groups rethink funding strategies, partnerships with industry and advance policies around access?

global marketing & patient access

GLOBAL MARKET & PATIENT ACCESS

Access is often the crucial and challenges last step for rare disease patients and developers. How can all stakeholders work together to ensure rare disease patients have access to appropriate treatments globally.

pricing & reimbursement

PRICING & REIMBURSEMENT

Pricing orphan products, especially one-time treatments, is complex and a key element to ensuring timely access for rare disease patients. What are the current best practices for pricing orphan products, negotiating innovative contracts and working with payers around the world?

pitch & partner

PITCH & PARTNER

The orphan drug space is booming with innovation, M&A activity and partnerships. We play match maker for up and coming biotechs in the rare space and investors & pharma partners looking for their next blockbuster.

advanced therapies manufacturing

ADVANCED THERAPIES - MANUFACTURING

What are the current roadblocks in manufacturing cell and gene therapies and how can companies efficiently scale-up for commercial production?

advanced therapies clinical development

ADVANCED THERAPIES - CLINICAL DEVELOPMENT

The regulatory and clinical development landscape is ever evolving for cell and gene therapies. How are companies ensuring continued development of these potentially transformative products and what clinical hurdles remain?

rare oncology

RARE ONCOLOGY

As the rare cancer field evolves and diagnosis becomes more precise, how can all stakeholders work together to advance drug development for rare cancer patients?

advanced therapies commercialization

ADVANCED THERAPIES - COMMERCIALIZATION

Rare disease patients are uniquely positioned to benefit from the advancements of cell and gene therapies. What are the best strategies for commercializing these innovative products and how do health systems need to evolve to accommodate patient access and reimbursement?

digital health & artificial intelligence

DIGITAL HEALTH & ARTIFICIAL INTELLIGENCE

Approaches in AI and digital health span the full development life cycle of drug development and commercialization. What are the best approaches to implementing these technologies in patient finding, clinical development and commercialization for rare diseases?

diagonis

DIAGNOSIS

It takes an average of seven years for an accurate diagnosis. How can all stakeholders broaden access to Newborn Screening, Whole Genome Sequencing and Genetic testing to shorten the diagnostic odyssey for rare disease patients?

discovery

DISCOVERY

Technologies and processes are ever. How is the growing access to data, and use of AI and machine learning impacting drug discovery in the rare disease space?
 

Sponsor the World Orphan Drug Congress USA

 

 

Get your product or solution in front of the leaders in the rare disease industry — from pharma, biotechs, governments, payers, investors and patient/patient advocates.

The World Orphan Drug Congress USA is a place where innovation and expertise is showcased, solutions are found and learning is done.

 

DOWNLOAD PROSPECTUS

pharma, biotechs, governments, payers, investors and patient patient advocates.

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Get Involved At World Orphan Drug Congress USA

 

To Sponsor Or Exhibit

 
 

Justin Franks
justin.franks@terrapinn.com
t/ +1 914 819 3506

 

 

 

To Speak

 
 

Claire Murphy
claire.murphy@terrapinn.com
t/ +1 646 619 1784

 

 

 

Marketing & Press Opportunities

 
 

Taylor Post
taylor.post@terrapinn.com
t/ +1 646 619 1785