World Orphan Drug Congress USA 2022

 

July 11-13, 2022
Hynes Center, Boston, MA

 

The World’s Most Important Orphan Drug
and Rare Disease Event

 

Featuring

 

 

TITLE SPONSOR


1,700+

Attendees

100+

Sponsors & Exhibitors

250+

Speakers

3

Days of Content

13

Themes of Content

 
 

Breaking down silos and fostering collaboration to help rare disease patients

The World Orphan Drug Congress brings together leading pharmaceutical and biotech companies, government and regulatory authorities, patient advocacy groups, payers, investors and solution providers. The conference is a place to meet and brainstorm ways to advance orphan drug development and improve access to life-saving therapies.


Join us for three days in Boston for the most comprehensive program and inclusive gathering of rare disease stakeholders.

2022 Speakers

Our World-Class Conference Features The Following Themes

 

patient data

PATIENT DATA

With so few patients, patient data/real-world-data (RWD/RWE) is the key element to advancing the rare disease space. What are best practices right now for data collection, ownership and sharing to benefit rare disease diagnosis, drug development and access.    

next generation therapies

NEXT GENERATION THERAPIES

The rare disease space is a breeding ground for innovative approaches in drug development and platform technologies. What are the products and approaches  that will be making headlines in 5-10 years from now?  

payers

PAYERS

US-based insurers and single payer agencies around the world have a lot of impact of access and reimbursement for orphan products. Hear from top US and international payers on their strategies for orphan drugs.   

clinical development & regulatory

CLINICAL DEVELOPMENT & REGULATORY

Understanding the regulatory and clinical landscape for rare disease drug development. How can companies, regulators and patient advocates work together to further patient voice, real world evidence, and decentralized clinical trials.   

commercial

COMMERCIAL

What are the best commercial strategies for orphan products? How can companies bring products to new markets, build more efficient commercial operations, and develop effective launch strategies?   

rare disease advocacy world

RARE DISEASE ADVOCACY WORLD

It all starts and ends with patients. So what are the challenges facing rare disease patients and patient organizations today? How can rare disease patient groups rethink funding strategies, partnerships with industry and advance policies around access?  

global marketing & patient access

GLOBAL MARKET & PATIENT ACCESS

Access is often the crucial and challenges last step for rare disease patients and developers. How can all stakeholders work together to ensure rare disease patients have access to appropriate treatments globally.   

pricing & reimbursement

PRICING & REIMBURSEMENT

Pricing orphan products, especially one-time treatments, is complex and a key element to ensuring timely access for rare disease patients. What are the current best practices for pricing orphan products, negotiating innovative contracts and working with payers around the world?  

pitch & partner

PITCH & PARTNER

The orphan drug space is booming with innovation, M&A activity and partnerships. We play match maker for up and coming biotechs in the rare space and investors & pharma partners looking for their next blockbuster.   

advanced therapies manufacturing

ADVANCED THERAPIES - MANUFACTURING

What are the current roadblocks in manufacturing cell and gene therapies and how can companies efficiently scale-up for commercial production?  

advanced therapies clinical development

ADVANCED THERAPIES - CLINICAL DEVELOPMENT

The regulatory and clinical development landscape is ever evolving for cell and gene therapies. How are companies ensuring continued development of these potentially transformative products and what clinical hurdles remain?  

rare oncology

RARE ONCOLOGY

As the rare cancer field evolves and diagnosis becomes more precise, how can all stakeholders work together to advance drug development for rare cancer patients?  
 

advanced therapies commercialization

ADVANCED THERAPIES - COMMERCIALIZATION

Rare disease patients are uniquely positioned to benefit from the advancements of cell and gene therapies. What are the best strategies for commercializing these innovative products and how do health systems need to evolve to accommodate patient access and reimbursement?   
 

digital health & artificial intelligence

DIGITAL HEALTH & ARTIFICIAL INTELLIGENCE

Approaches in AI and digital health span the full development life cycle of drug development and commercialization. What are the best approaches to implementing these technologies in patient finding, clinical development and commercialization for rare diseases?  
 

diagonis

DIAGNOSIS

It takes an average of seven years for an accurate diagnosis. How can all stakeholders broaden access to Newborn Screening, Whole Genome Sequencing and Genetic testing to shorten the diagnostic odyssey for rare disease patients?  
 

discovery

DISCOVERY

Technologies and processes are ever. How is the growing access to data, and use of AI and machine learning impacting drug discovery in the rare disease space?  
 

2022 Sponsors & Exhibitors
 

  • Title Sponsorship

    Sanofi Genzyme at World Orphan Drug Congress USA 2022

    Diamond Sponsor

    Eversana at World Orphan Drug Congress USA 2022
  • Diamond Sponsor

    Komodo Health at World Orphan Drug Congress USA 2022

    Platinum Sponsor

    Pfizer at World Orphan Drug Congress USA 2022
  • Platinum Sponsor

    AllStripes Research Inc. at World Orphan Drug Congress USA 2022

    Platinum Sponsor

    Premier Research at World Orphan Drug Congress USA 2022
  • Platinum Sponsor

    Cardinal Health at World Orphan Drug Congress USA 2022

    Diamond Sponsor

    Parexel at World Orphan Drug Congress USA 2022
  • Platinum Sponsor

    ZS Associates, Inc. at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Ada Health at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    Aparito at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Charles River Laboratories at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    Clincierge at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Clinigen Group at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    CRA, Charles River Associates at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Ergomed at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    GemPharmatech at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Icon at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    iTakeControl, a Red Nucleus Company at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Lumanity at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    Medidata at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Nextpharma at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    OM1 at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Orphan Drug Consulting at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    PPD, part of Thermo Fisher Scientific at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Rady Children's Institute for Genomic Medicine at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    rareLife solutions at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Sciensus at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    The Emmes Company, LLC at World Orphan Drug Congress USA 2022

    Gold Sponsor

    Thread Research.com at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    volv global at World Orphan Drug Congress USA 2022

    Gold Sponsor

    VOZ Advisors at World Orphan Drug Congress USA 2022
  • Gold Sponsor

    WorldWide Clinical Trials at World Orphan Drug Congress USA 2022

    Silver Sponsor

    Bionical Emas at World Orphan Drug Congress USA 2022
  • Silver Sponsor

    Elligo Health Research at World Orphan Drug Congress USA 2022

    Silver Sponsor

    CTI Clinical Trial and Consulting at World Orphan Drug Congress USA 2022
  • Silver Sponsor

    Curant Health at World Orphan Drug Congress USA 2022

    Silver Sponsor

    Durbin- part of Uniphar Group at World Orphan Drug Congress USA 2022
  • Silver Sponsor

    Lapidus Data at World Orphan Drug Congress USA 2022

    Silver Sponsor

    Pharm-Olam International at World Orphan Drug Congress USA 2022
  • Silver Sponsor

    P2P Syncro at World Orphan Drug Congress USA 2022

    Silver Sponsor

    Scout Clinical at World Orphan Drug Congress USA 2022
  • Silver Sponsor

    Simon-Kucher & Partners at World Orphan Drug Congress USA 2022

    Silver Sponsor

    WEP Clinical at World Orphan Drug Congress USA 2022
  • Exhibitor

    Medpace at World Orphan Drug Congress USA 2022

    Exhibitor

    Aristea Therapeutics, Inc. at World Orphan Drug Congress USA 2022
  • Exhibitor

    Argonaut Manufacturing Services at World Orphan Drug Congress USA 2022

    Exhibitor

    Advanced Clinical at World Orphan Drug Congress USA 2022
  • Exhibitor

    BlueDil International Ltd at World Orphan Drug Congress USA 2022

    Exhibitor

    Certara - Raleigh, NC at World Orphan Drug Congress USA 2022
  • Exhibitor

    Fulcrum Research Group at World Orphan Drug Congress USA 2022

    Exhibitor

    Grand River Aseptic Manufacturing at World Orphan Drug Congress USA 2022
  • Exhibitor

    IDEA Regulatory at World Orphan Drug Congress USA 2022

    Exhibitor

    Invitae at World Orphan Drug Congress USA 2022
  • Exhibitor

    IQVIA at World Orphan Drug Congress USA 2022

    Exhibitor

    Medpace at World Orphan Drug Congress USA 2022
  • Exhibitor

    PCM Trials at World Orphan Drug Congress USA 2022

    Exhibitor

    Pharmaceutics International at World Orphan Drug Congress USA 2022
  • Exhibitor

    Precision for Medicine at World Orphan Drug Congress USA 2022

    Exhibitor

    SVA Consulting at World Orphan Drug Congress USA 2022

Companies that attend World Orphan Drug Congress USA

 

 

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Sponsor the World Orphan Drug Congress USA

 

 

Get your product or solution in front of the leaders in the rare disease industry — from pharma, biotechs, governments, payers, investors and patient/patient advocates.

The World Orphan Drug Congress USA is a place where innovation and expertise is showcased, solutions are found and learning is done.

 

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pharma, biotechs, governments, payers, investors and patient patient advocates.

Get Involved At World Orphan Drug Congress USA

 

To Sponsor Or Exhibit

 
 

Justin Franks
justin.franks@terrapinn.com
t/ +1 914 819 3506

 

 

 

To Speak

 
 

Claire Murphy
claire.murphy@terrapinn.com
t/ +1 646 619 1784

 

 

 

Marketing & Press Opportunities

 
 

Taylor Post 
taylor.post@terrapinn.com
t/ +1 646 619 1785