World Orphan Drug Congress USA 2020


Wednesday, April 29 - Friday, May 1 2020
Gaylord National Harbor Hotel, Oxon Hill, Maryland USA

 

THE GLOBAL ORPHAN DRUG CONFERENCE AND EXPO

 
 
1,500+
Attendees
50+
Countries
350+
Speakers
100+
Exhibitors
260+
Sessions

What is the World Orphan Drug Congress USA?

 

World Orphan Drug Congress USA focuses on the most pressing challenges and opportunities to bring rare disease therapies to patients faster.
 

Bringing together a global gathering of 1,500 leaders in orphan drugs from 50 countries, World Orphan Drug Congress USA will feature over 260 presentations covering all aspects of orphan drug development and rare disease research.

 

Register Now

Sign Up for Event Updates

Meet our first 200 speakers.
We're adding more every week.

 
Emil Kakkis at World Orphan Drug Congress USA
Emil Kakkis
President & Chief Executive Officer
Ultragenyx Pharmaceutical
Janet Woodcock at World Orphan Drug Congress USA
Janet Woodcock
Director, Center for Drug Evaluation and Research (CDER)
U.S. Food & Drug Administration
David Lennon at World Orphan Drug Congress USA
David Lennon
President
AveXis
Sara (Saraswathy) Nochur at World Orphan Drug Congress USA
Sara (Saraswathy) Nochur
Chief Regulatory Officer, Regulatory Affairs
Alnylam Pharmaceuticals
Yann Le Cam at World Orphan Drug Congress USA
Yann Le Cam
Chief Executive Officer
EURORDIS — Rare Diseases Europe
Mayo Pujols at World Orphan Drug Congress USA
Mayo Pujols
VP, Head of Global Cell & Gene Technical Development & Manufacturing
Novartis
Dianne Berry at World Orphan Drug Congress USA
Dianne Berry
Senior Vice President, Global Health Policy and Government and Patient Affairs
Sarepta Therapeutics
Shannon Baumann at World Orphan Drug Congress USA
Shannon Baumann
Senior director, Access Value and Evidence Strategy
bluebird bio
Bob Smith at World Orphan Drug Congress USA
Bob Smith
Senior Vice President, Global Gene Therapy Business
Pfizer
Nuriya Musina at World Orphan Drug Congress USA
Nuriya Musina
Head Of Development, Federal State Budgetary Institution, the Center for Healthcare Quality Assessment and Control
Ministry of Health Russian Federation
Paolo Martini at World Orphan Drug Congress USA
Paolo Martini
Chief Scientific Officer, Rare Diseases
Moderna Inc.
Linn Parrish at World Orphan Drug Congress USA
Linn Parrish
Head of CSR Innovation and Stakeholder Engagement, Corporate Communications & Public Affairs
Takeda Pharmaceutical Company Limited
Peter Marks at World Orphan Drug Congress USA
Peter Marks
Director, Center for Biologics Evaluation and Research (CBER)
U.S. Food and Drug Administration
Mark Rothera at World Orphan Drug Congress USA
Mark Rothera
President & Chief Executive Officer
Orchard Therapeutics
Peter Saltonstall at World Orphan Drug Congress USA
Peter Saltonstall
Chief Executive Officer
NORD

 

VIEW ALL SPEAKERS

2020 topics areas

CLINICAL DEVELOPMENT/ REGULATORY

COMMERCIALIZATION

RARE DISEASE ADVOCACY WORLD

GLOBAL PATIENT AND MARKET ACCESS

PRICING & REIMBURSEMENT

RARE ONCOLOGY

ADVANCED THERAPIES CLINICAL DEVELOPMENT

ADVANCED THERAPIES MANUFACTURING

ADVANCED THERAPIES COMMERCIALIZATION (NEW)

DIGITAL HEALTH AND ARTIFICIAL INTELLIGENCE (NEW)

DIAGNOSIS (NEW)

PITCH & PARTNER

REGISTER NOW

DOWNLOAD BROCHURE

 

Featuring

2020 Sponsors & Exhibitors

 

  • Diamond Sponsor

    Orchard Therapeutics at World Orphan Drug Congress USA 2020

    Platinum Sponsor

    volv global at World Orphan Drug Congress USA 2020

    Platinum Sponsor

    EVERSANA at World Orphan Drug Congress USA 2020

  • Platinum Sponsor

    Oxford Biomedica at World Orphan Drug Congress USA 2020

    Gold Sponsor

    Aeglea Biotherapeutics at World Orphan Drug Congress USA 2020

    Gold Sponsor

    Catalent Pharma Solutions at World Orphan Drug Congress USA 2020

  • Gold Sponsor

    Charles River Associates at World Orphan Drug Congress USA 2020

    Gold Sponsor

    CVS Health at World Orphan Drug Congress USA 2020

    Gold Sponsor

    Genentech at World Orphan Drug Congress USA 2020

  • Gold Sponsor

    HVH Precision Analytics at World Orphan Drug Congress USA 2020

    Gold Sponsor

    Optum at World Orphan Drug Congress USA 2020

    Gold Sponsor

    PAREXEL International at World Orphan Drug Congress USA 2020

  • Gold Sponsor

    Partners4Access at World Orphan Drug Congress USA 2020

    Gold Sponsor

    Premier Research at World Orphan Drug Congress USA 2020

    Gold Sponsor

    Simon-Kucher & Partners at World Orphan Drug Congress USA 2020

  • Patient Advocacy Sponsor

    EURORDIS at World Orphan Drug Congress USA 2020

    Patient Advocacy Sponsor

    National Organization for Rare Disorders (NORD) at World Orphan Drug Congress USA 2020

    Silver Sponsor

    Ambry Genetics at World Orphan Drug Congress USA 2020

  • Silver Sponsor

    CENTOGENE US, LLC at World Orphan Drug Congress USA 2020

    Silver Sponsor

    Clincierge at World Orphan Drug Congress USA 2020

    Silver Sponsor

    Huron Consulting Group at World Orphan Drug Congress USA 2020

  • Silver Sponsor

    ICRC-Weyer GmbH at World Orphan Drug Congress USA 2020

    Silver Sponsor

    Innoplexus at World Orphan Drug Congress USA 2020

    Silver Sponsor

    IPM.ai at World Orphan Drug Congress USA 2020

  • Silver Sponsor

    McKesson Specialty Health at World Orphan Drug Congress USA 2020

    Silver Sponsor

    OPEN Health at World Orphan Drug Congress USA 2020

    Silver Sponsor

    Pfizer at World Orphan Drug Congress USA 2020

  • Silver Sponsor

    PRA Health Sciences at World Orphan Drug Congress USA 2020

    Silver Sponsor

    Synteract at World Orphan Drug Congress USA 2020

    Silver Sponsor

    Worldwide Clinical Trials at World Orphan Drug Congress USA 2020

  • Bronze Sponsor

    Aldevron at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    AssistRx Patient Solutions at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    BluePrint Orphan at World Orphan Drug Congress USA 2020

  • Bronze Sponsor

    Camargo Pharmaceutical Services at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    ClinEdge at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    Covance at World Orphan Drug Congress USA 2020

  • Bronze Sponsor

    Dolon at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    Early Access Care at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    EpidStrategies, A Division of ToxStrategies at World Orphan Drug Congress USA 2020

  • Bronze Sponsor

    Global Data Support at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    Inceptua LTD at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    Lapidus Data at World Orphan Drug Congress USA 2020

  • Bronze Sponsor

    Medidata, a Dassault Systèmes company at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    MME at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    PharmaCord at World Orphan Drug Congress USA 2020

  • Bronze Sponsor

    Rho, Inc at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    Rubius Therapeutics at World Orphan Drug Congress USA 2020

    Bronze Sponsor

    VOZ Advisors at World Orphan Drug Congress USA 2020

  • Exhibitor

    Alcami at World Orphan Drug Congress USA 2020

    Exhibitor

    Anovo at World Orphan Drug Congress USA 2020

    Exhibitor

    Bio Insight Group at World Orphan Drug Congress USA 2020

  • Exhibitor

    Cello Health at World Orphan Drug Congress USA 2020

    Exhibitor

    Clinart MENA at World Orphan Drug Congress USA 2020

    Exhibitor

    Cobra Biologics at World Orphan Drug Congress USA 2020

  • Exhibitor

    CSI Specialty Group at World Orphan Drug Congress USA 2020

    Exhibitor

    Ergomed / PSR at World Orphan Drug Congress USA 2020

    Exhibitor

    Firma Clinical Research at World Orphan Drug Congress USA 2020

  • Exhibitor

    Fulcrum Research Group at World Orphan Drug Congress USA 2020

    Exhibitor

    Grifols Recombinant Protein CDMO at World Orphan Drug Congress USA 2020

    Exhibitor

    Healthcare at Home at World Orphan Drug Congress USA 2020

  • Exhibitor

    Illingworth Research at World Orphan Drug Congress USA 2020

    Exhibitor

    Invitae at World Orphan Drug Congress USA 2020

    Exhibitor

    IQVIA Biotech at World Orphan Drug Congress USA 2020

  • Exhibitor

    PerkinElmer at World Orphan Drug Congress USA 2020

    Exhibitor

    Pharmaceutics International at World Orphan Drug Congress USA 2020

    Exhibitor

    Pharm-Olam International at World Orphan Drug Congress USA 2020

  • Exhibitor

    Precision For Medicine, Oncology and Rare Disease at World Orphan Drug Congress USA 2020

    Exhibitor

    rareLife solutions at World Orphan Drug Congress USA 2020

    Exhibitor

    Scout Clinical at World Orphan Drug Congress USA 2020

  • Exhibitor

    TMC Pharma services at World Orphan Drug Congress USA 2020

    Exhibitor

    TransPerfect at World Orphan Drug Congress USA 2020

    Exhibitor

    Treximo at World Orphan Drug Congress USA 2020

  • Exhibitor

    Unither Pharmaceuticals at World Orphan Drug Congress USA 2020

    Exhibitor

    Verasci at World Orphan Drug Congress USA 2020

    Exhibitor

    WEP Clinical at World Orphan Drug Congress USA 2020

  • Rare Technology Zone

    ArborMetrix at World Orphan Drug Congress USA 2020

    Rare Technology Zone

    RDMD Inc. at World Orphan Drug Congress USA 2020

 

 

SPONSORSHIP OPPORTUNITIES

1,500 Attendees Including Representatives From:

THE GLOBAL GATHERING FOR ORPHAN DRUGS

EUROPE

 

FINLAND

FINLAND

DENMARK

DENMARK

SWEDEN

SWEDEN

UNITEDKINGDOM

UNITED KINGDOM

BULGARIA

BULGARIA

IRELAND

IRELAND

ITALY

ITALY

PORTUGAL

PORTUGAL

SWITZERLAND

SWITZERLAND

CROATIA

CROATIA

RUSSIA

RUSSIA

AUSTRIA

AUSTRIA

BELGIUM

BELGIUM

FRANCE

FRANCE

GERMANY

GERMANY

CZECH REPUBLIC

CZECH REPUBLIC

HUNGARY

HUNGARY

ICELAND

ICELAND

NETHERLANDS

NETHERLANDS

NORWAY

NORWAY

POLAND

POLAND

SLOVENIA

SLOVENIA

SPAIN

SPAIN

MALTA

MALTA

AMERICAS

 

USA

USA

CANADA

CANADA

COLOMBIA

COLOMBIA

BRAZIL

BRAZIL

MEXICO

MEXICO

PANAMA

PANAMA

 

ASIA & AUSTRALASIA

 

INDIA

INDIA

CHINA

CHINA

JAPAN

JAPAN

MALAYSIA

MALAYSIA

AUSTRALIA

AUSTRALIA

NEW ZEALAND

NEW ZEALAND

PHILIPPINES

PHILIPPINES

SOUTH KOREA

SOUTH KOREA

SINGAPORE

SINGAPORE

TAIWAN

TAIWAN

THAILAND

THAILAND

AFRICA & MIDDLE EAST

 

SOUTH AFRICA

SOUTH AFRICA

ISRAEL

ISRAEL

UNITED ARABEMIRATES

UNITED ARAB EMIRATES

TURKEY

TURKEY