Unlocking Insights: How decentralized clinical trials and advanced therapies are revolutionizing pediatric rare disease research
This session will explore solutions to challenges in pediatric rare disease research, specifically in consideration of decentralized clinical trials (DCT) and cell and gene therapy development. You will learn:
The complexities of executing cell and gene therapy programs in pediatric populations
Key considerations for instituting a DCT approach for cell and gene therapy programs in a pediatric population
Strategies for seamless operationalization of DCTs
Ruth Rostron,Director of Program Management, Uniphar
Day 1 - World Orphan Drug Congress USA 2024 15:20, Advanced Therapies Clinical Development
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