World Orphan Drug Congress USA 2017

 

 

THE GLOBAL ORPHAN DRUG
CONFERENCE AND EXPO

 

19 - 21 April 2017

1,000  High-level attendees

50+ Sponsors and exhibitors

150+  Expert Speakers

Possibilities:  UNLIMITED

WHAT IS THE WORLD ORPHAN DRUG CONGRESS USA?  


3 Conferences. 3 Days. 1 Event.

At the World Orphan Drug Congress USA in April 2017, we are bringing together more than 150 elite speakers to educate and inspire our 1,000 attendees from big pharma, biotech, payers, patient groups, academics and government bodies. In 2017, World Orphan Drug Congress USA is bringing together the worlds of Scientific Innovation and Commercialization, with 2 tracks in the main conference. 

By exploring trends in Digital Health, Biosimilars, Gene Therapy, and more, we will uncover the next scientific breakthrough. Examinations of Mergers, Commercialization, Marketing and the Regional Markets will provide insight into this billion-dollar business. That's not all with Rare Disease Advocacy World and Pitch and Partner 2017, there are 4 tracks of content for you and your team to enjoy. 

Enjoy discussions on: 

FUTURE OF ORPHAN DRUGS

PRICING & REIMBURSEMENT

APPROVAL & ACCESS

M&A AND COMMERCIALIZATION

PATIENT-CENTRIC RESEARCH

REAL-WORLD EVIDENCE

MARKETING & COMPETITIVENESS

GENE THERAPY

SCIENTIFIC INNOVATION

REGIONAL MARKET ANALYSIS

BIOSIMILARS

ROUNDTABLES

Click on these logos for more information on: 

Rare Disease Advocacy World USA at World Orphan Drug Congress

Pitch and Partner at World Orphan Drug Congress USA 2017

 

Download the World Orphan Drug Congress USA 2017 prospectus

The largest global orphan drug industry event

The World Orphan Drug Congress USA is a place where innovation and expertise is showcased, solutions are found and learning is done.

 

If you offer a solution or product in the orphan drug space, the World Orphan Drug Congress USA is definitely the right place to do this.

 

DOWNLOAD BROCHURE


 

2017 SPEAKERS INCLUDE

 

  • Karen Aiach at World Orphan Drug Congress USA 2017
    Karen Aiach
    Founder and Chief Executive Officer
    Lysogene
    Einar Andreassen at World Orphan Drug Congress USA 2017
    Einar Andreassen
    Senior Adviser
    Norwegian Medicines Agency
  • Donna Armentano at World Orphan Drug Congress USA 2017
    Donna Armentano
    Executive Director, Global Head Gene Therapy External R&D Innovation
    Pfizer, Inc
    Alison Bateman House at World Orphan Drug Congress USA 2017
    Alison Bateman House
    Postdoctoral Fellow, Division of Medical Ethics,
    New York University Langone Medical Center
  • Ms Soraya Bekkali at World Orphan Drug Congress USA 2017
    Ms Soraya Bekkali
    Senior Vice President and Chief Medical Officer
    Lysogene
    Stella Blackburn at World Orphan Drug Congress USA 2017
    Stella Blackburn
    Vice President, Global Head of Risk Management, Real-World Insights
    QuintilesIMS
  • Paul Bolno at World Orphan Drug Congress USA 2017
    Paul Bolno
    President and Chief Executive Officer
    WaVe Life Sciences
    Mr Max Bronstein at World Orphan Drug Congress USA 2017
    Mr Max Bronstein
    Senior Director, Public and Government Relations
    EveryLife Foundation for Rare Diseases
  • Angela Chaves at World Orphan Drug Congress USA 2017
    Angela Chaves
    President
    FEDERACION COLOMBIANA DE ENFERMEDADES RARAS
    Ms Leah Christl at World Orphan Drug Congress USA 2017
    Ms Leah Christl
    Associate Director for Therapeutic Biologics and Biosimilars
    Office of New Drugs C.D.E.R. F.D.A.
  • Margaret Collins at World Orphan Drug Congress USA 2017
    Margaret Collins
    Pathologist, Consortium of Eosinophilic Gastrointestinal Disease Researchers (CEGIR). Professor of Pediatrics,
    Cincinnati Childrens Hospital
    Francesca Cook at World Orphan Drug Congress USA 2017
    Francesca Cook
    Director, Pricing and Market Access
    RegenxBio
  • Gregory Daniel at World Orphan Drug Congress USA 2017
    Gregory Daniel
    Deputy Director
    Duke University
    Peter Dehnel at World Orphan Drug Congress USA 2017
    Peter Dehnel
    Medical Director
    Blue Cross and Blue Shield of Minnesota
  • Keith DeMatteo at World Orphan Drug Congress USA 2017
    Keith DeMatteo
    Director, Global Procurement Center of Excellence
    Bristol Myers Squibb
    Kelly Du Plessis at World Orphan Drug Congress USA 2017
    Kelly Du Plessis
    Chief Executive Officer
    Rare Disease Society of South Africa
  • Glyn Edwards at World Orphan Drug Congress USA 2017
    Glyn Edwards
    Chief Executive Officer
    Summit Therapeutics
    Mary Frances Harmon at World Orphan Drug Congress USA 2017
    Mary Frances Harmon
    Head of Global Patient Advocacy
    PTC Therapeutics
  • Ms Pat Furlong at World Orphan Drug Congress USA 2017
    Ms Pat Furlong
    Founding President and Chief Executive Officer
    Parent Project Muscular Dystrophy
    Vignesh Ganapathy at World Orphan Drug Congress USA 2017
    Vignesh Ganapathy
    Associate Director of Advocacy & Government Relations
    EveryLife Foundation for Rare Diseases
  • Chris Garabedian at World Orphan Drug Congress USA 2017
    Chris Garabedian
    Former President and Chief Executive Officer
    Sarepta Therapeutics
    Jayne Gershkowitz at World Orphan Drug Congress USA 2017
    Jayne Gershkowitz
    Senior Vice President and Chief Patient Advocate
    Amicus Therapeutics Inc
  • Jonathan Goldsmith at World Orphan Drug Congress USA 2017
    Jonathan Goldsmith
    Associate Director Rare Diseases Program
    Food And Drug Administration
    Rashmi Gopal-Srivastava at World Orphan Drug Congress USA 2017
    Rashmi Gopal-Srivastava
    Director, Extramural Research Program, Office Rare Diseases Research, National Cnter for Advancing Translational Sciences(NCATS)
    National Institutes of Health
  • Scott Gray at World Orphan Drug Congress USA 2017
    Scott Gray
    Chief Executive Officer
    Clincierge
    Mr James Greenwood at World Orphan Drug Congress USA 2017
    Mr James Greenwood
    Chief Executive Officer
    Biotechnology Industry Organization
  • Sascha Haverfield at World Orphan Drug Congress USA 2017
    Sascha Haverfield
    Senior Vice President, Science and Regulatory Advocacy
    Pharmaceutical Research and Manufacturers of America
    Colin Hayward at World Orphan Drug Congress USA 2017
    Colin Hayward
    Chief Medical Officer
    Premier Research
  • Jonathan Heller at World Orphan Drug Congress USA 2017
    Jonathan Heller
    Executive Director and Global Head, External R&D Innovation, Rare Diseases
    Pfizer, Inc
    Mrs Claudia Hirawat at World Orphan Drug Congress USA 2017
    Mrs Claudia Hirawat
    Chair
    EURORDIS
  • Kenneth Hobby at World Orphan Drug Congress USA 2017
    Kenneth Hobby
    President
    Cure SMA
    Angus Hogg at World Orphan Drug Congress USA 2017
    Angus Hogg
    Vice President Hunters (MPSII) Franchise
    Shire Pharmaceuticals Ltd
  • Kay Holcombe at World Orphan Drug Congress USA 2017
    Kay Holcombe
    Senior Vice President for Science Policy
    Biotechnology Industry Organization (BIO)
    Wills Hughes-Wilson at World Orphan Drug Congress USA 2017
    Wills Hughes-Wilson
    Senior Vice President, Chief Patient Access Officer
    Sobi
  • Cynthia Jackson at World Orphan Drug Congress USA 2017
    Cynthia Jackson
    Vice President and Head, Pediatric and Rare Disease Centers of Excellence
    QuintilesIMS
    Donald Johns at World Orphan Drug Congress USA 2017
    Donald Johns
    Vice President, Head ALS Neuroscience Discovery & Development SMA Clinical Development, Vice-Chair, Clinical Trial Review Board
    Biogen
  • Matt Kapusta at World Orphan Drug Congress USA 2017
    Matt Kapusta
    Chief Executive Officer
    uniQure
    Petra Kaufmann at World Orphan Drug Congress USA 2017
    Petra Kaufmann
    Director, Office of Rare Diseases Research and Division of Clinical Innovation
    National Institutes of Health
  • Sven Kili at World Orphan Drug Congress USA 2017
    Sven Kili
    Vice President and Head of Gene Therapy Development
    GSK
    Yann Le Cam at World Orphan Drug Congress USA 2017
    Yann Le Cam
    Chief Executive Officer
    EURORDIS
  • Nadea Leavitt at World Orphan Drug Congress USA 2017
    Nadea Leavitt
    Engagement Manager, Predictive Analytics, Real World Insights
    QuintilesIMS
    Nick Leschly at World Orphan Drug Congress USA 2017
    Nick Leschly
    President and Chief Executive Officer
    bluebird bio
  • Terrie Livingston at World Orphan Drug Congress USA 2017
    Terrie Livingston
    Senior Director, US Medical
    Biogen
    Aoife M Brennan at World Orphan Drug Congress USA 2017
    Aoife M Brennan
    Chief Medical Officer
    Synlogic Therapeutics
  • Jeffrey D. Marrazzo at World Orphan Drug Congress USA 2017
    Jeffrey D. Marrazzo
    Co Founder and Chief Executive Officer
    Spark Therapeutics
    Howard Mayer at World Orphan Drug Congress USA 2017
    Howard Mayer
    Senior Vice President & Head of Global Clinical Development
    Shire Pharmaceuticals Inc
  • Andrew McFayden at World Orphan Drug Congress USA 2017
    Andrew McFayden
    Executive Director
    The Isaac Foundation
    Paul Melmeyer at World Orphan Drug Congress USA 2017
    Paul Melmeyer
    Associate Director of Public Policy
    National Organization for Rare Disorders
  • Christopher Missling at World Orphan Drug Congress USA 2017
    Christopher Missling
    President and Chief Executive Officer
    Anavex Life Sciences
    Kenneth Moch at World Orphan Drug Congress USA 2017
    Kenneth Moch
    Former Chief Executive Officer
    Chimerix
  • Richard Moscicki at World Orphan Drug Congress USA 2017
    Richard Moscicki
    Deputy Director for Science Operations, CDER
    FDA
    Michael Murphy at World Orphan Drug Congress USA 2017
    Michael Murphy
    Chief Medical & Scientific Officer
    Worldwide Clinical Trials
  • Francois Nader at World Orphan Drug Congress USA 2017
    Francois Nader
    Board Chairman, Acceleron Pharma (XLRN), Former President & CEO
    NPS Pharmaceuticals
    Yukiko Nishimura at World Orphan Drug Congress USA 2017
    Yukiko Nishimura
    Chief Secretariat of International Relations
    Japan Patients Association, ASrid
  • Letitia O'dwyer at World Orphan Drug Congress USA 2017
    Letitia O'dwyer
    Chief Executive Officer
    New Zealand Organisation For Rare Disorders
    Luca Pani at World Orphan Drug Congress USA 2017
    Luca Pani
    Director General
    Italian Medicines Agency A.I.F.A.
  • Eric Pauwels at World Orphan Drug Congress USA 2017
    Eric Pauwels
    Senior Vice President and General Manager, The Americas
    PTC Therapeutics
    Edmund Pezalla at World Orphan Drug Congress USA 2017
    Edmund Pezalla
    Fomer Vice President of National Medical Director of Pharmaceutical Policy and Strategy
    Aetna
  • Mr Andreas Pleil at World Orphan Drug Congress USA 2017
    Mr Andreas Pleil
    Senior Director, Team Lead, Outcomes & Evidence Hematology Global Health & Value
    Pfizer Inc
    Sy Pretorius at World Orphan Drug Congress USA 2017
    Sy Pretorius
    Senior Vice President and Chief Scientific Officer
    PAREXEL International
  • Ms Harsha Rajasimha at World Orphan Drug Congress USA 2017
    Ms Harsha Rajasimha
    Co Founder
    Indian Organization For Rare Diseases
    Gayatri Rao JD., MD, at World Orphan Drug Congress USA 2017
    Gayatri Rao JD., MD,
    Director, Orphan Products Development
    FDA
  • Jens Renstrup at World Orphan Drug Congress USA 2017
    Jens Renstrup
    SVP, Head of Global Medical Affairs
    Alexion Pharmaceuticals
    Scott Rocklage at World Orphan Drug Congress USA 2017
    Scott Rocklage
    Former CEO, Epirus Biosciences, Managing Partner
    5AM Ventures
  • Mark Rothera at World Orphan Drug Congress USA 2017
    Mark Rothera
    Chief Commercial Officer
    PTC Therapeutics
    Peter Saltonstall at World Orphan Drug Congress USA 2017
    Peter Saltonstall
    CEO
    National Organization For Rare Disorders
  • Scott Schliebner at World Orphan Drug Congress USA 2017
    Scott Schliebner
    Vice President of Rare Diseases and Scientific Affairs
    PRA Health Sciences
    Ana Maria Serrato Navas at World Orphan Drug Congress USA 2017
    Ana Maria Serrato Navas
    Country Manager, Colombia
    Aegerion Pharmaceuticals
  • Mr Thomas Sproat at World Orphan Drug Congress USA 2017
    Mr Thomas Sproat
    Senior Vice President, Scientific Services
    ClinicalMind
    Mary Szela at World Orphan Drug Congress USA 2017
    Mary Szela
    Chief Executive Officer
    Aegerion Pharmaceuticals
  • Mr Timothy Walbert at World Orphan Drug Congress USA 2017
    Mr Timothy Walbert
    Chairman, President, and Chief Executive Officer
    Horizon Pharma
    Diane White at World Orphan Drug Congress USA 2017
    Diane White
    Assoc. Director Development Sciences Project Management
    Biomarin
  • Barbara Wuebbels at World Orphan Drug Congress USA 2017
    Barbara Wuebbels
    Vice President of Patient Advocacy
    Audentes Therapeutics
    Andrea Chiesi at World Orphan Drug Congress USA 2017
    Andrea Chiesi
    Director of Research and Development and Portfolio Management
    Chiesi
  • Hazel Gorham at World Orphan Drug Congress USA 2017
    Hazel Gorham
    Director of Biosimilars Development
    P.R.A. Health Sciences
    Valerie Duquet at World Orphan Drug Congress USA 2017
    Valerie Duquet
    Clinical Team Manager
    PRA Health Sciences
  • Birgitte Volck at World Orphan Drug Congress USA 2017
    Birgitte Volck
    Senior Vice President, Head of R&D Rare Diseases
    GSK
    Eric Gascho at World Orphan Drug Congress USA 2017
    Eric Gascho
    Vice President of Government Affairs
    National Health Council
  • Ms Deborah Geraghty at World Orphan Drug Congress USA 2017
    Ms Deborah Geraghty
    Head of Commercial and Portfolio Strategy
    Dimension Therapeutics
    Michael Goettler at World Orphan Drug Congress USA 2017
    Michael Goettler
    Global President
    Pfizer Rare Disease
  • Marc Martinell at World Orphan Drug Congress USA 2017
    Marc Martinell
    Chief Executive Officer
    Minoryx Therapeutics
    Nancy Parsons at World Orphan Drug Congress USA 2017
    Nancy Parsons
    Vice President Commercial Operations, Pharmaceutical Products
    SigmaTau Pharmaceuticals

 

SEE ALL 2017 SPEAKERS

WHO ATTENDS?

Here's a glimpse of who attends World Orphan Drug Congress USA

 

AccessPharmaCon,LLC Aegerion Pharmaceuticals  Aetna Pharmacy Management  Alexion Pharmaceuticals  Andarix Pharmaceuticals  ArmaGen Technologies, Inc.  Ashfield Healthcare   Asklepion Pharmaceuticals LLC  Ax-S Pharma  B.D.C. Venture Capital  BioBlast Pharma Ltd  Biomarin Pharmaceutical Inc.  BioPontis Alliance for Rare Disease Brace Pharma Capital   Brazilian Federal Council of Medicine  Bristol-Myers Squibb  CatalentPharma Solutions   CatalystPharmaceutical Partners  CDER FDA  Clear Pharma  Clementia Pharmaceuticals Inc.   Clinuvel Pharmaceuticals Ltd  Dicerna Pharmaceuticals  DrugDev  EvaluatePharma Ltd   Genoa Pharmaceuticals   Genpharm  GenSight Biologics  Genzyme Corp  Giddi Pharma Co., Ltd.   Idera Pharmeceuticals  IDIS Pharma   Iptechex Pharmalicensing  Jazz Pharmaceuticals, Inc  Juice Pharma Worldwide   KBI Biopharma Inc   Lumos Pharma   M3 Pharma  Marathon Pharmaceuticals LLC   Marinus Pharmaceuticals  Momenta Pharmaceuticals Inc  Opsona Therapeutics Ltd  Optio Biopharma Solutions LLC  Orpharma  Pfizer, Inc  Pharmaceutics International In  Pharmaessentia Corp   Pharnext   Portola Pharmaceuticals , Inc.  Provectus PharmaceuticalsInc   QuayPharma  Quintiles Inc  Raptor Pharmaceuticals Corp  Reata Pharmaceuticals   Recordati S.p.A  Recursion Pharmaceuticals  Retrophin   Sanofi   Savara Pharmaceuticals  Seattle Children's Research Institute   Shire Pharmaceuticals Inc  Taiba Pharma LLC Teva  Threshold Pharmaceuticals Inc   Tolero Pharmaceuticals   Ultragenyx Pharmaceutical Inc.  Valley Fever Solutions   Vanda Pharmaceuticals Inc   Vertex Pharmaceuticals 

 

FIND OUT MORE

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Choose your package

Prices increase after 6th January – book now to get these prices

 

2 DAY CONFERENCE


Individual Pass

USD $2,380

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Group Booking of 3 or more

USD $2,025

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3 DAY CONFERENCE


Individual Pass

USD $2,910

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Group Booking of 3 or more

USD $2,470

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World Orphan Drug Congress USAWorld Orphan Drug Congress USAWorld Orphan Drug Congress USAWorld Orphan Drug Congress USAWorld Orphan Drug Congress USAWorld Orphan Drug Congress USAWorld Orphan Drug Congress USAWorld Orphan Drug Congress USAWorld Orphan Drug Congress USAWorld Orphan Drug Congress USAWorld Orphan Drug Congress USAWorld Orphan Drug Congress USA

Sponsor World Orphan Drug Congress USA

Get Involved

Your customers are here continuously looking for new strategies and technologies to expedite orphan drugs to patients.

 

If you offer a solution or product in the orphan drug space, then you need to be here

 

DOWNLOAD PROSPECTUS


 

OUR SPONSORS & EXHIBITORS

 

  • Platinum Sponsor

    Premier Research at World Orphan Drug Congress USA 2017

    Platinum Sponsor

    PTC Therapeutics at World Orphan Drug Congress USA 2017

    Gold Sponsor

    AmerisourceBergen at World Orphan Drug Congress USA 2017
  • Gold Sponsor

    Cello Health at World Orphan Drug Congress USA 2017

    Gold Sponsor

    GlaxoSmithKline at World Orphan Drug Congress USA 2017

    Gold Sponsor

    Parexel at World Orphan Drug Congress USA 2017
  • Silver Sponsor

    Clincierge at World Orphan Drug Congress USA 2017

    Silver Sponsor

    ClinicalMind at World Orphan Drug Congress USA 2017

    Silver Sponsor

    onevoice at World Orphan Drug Congress USA 2017
  • Silver Sponsor

    Pfizer at World Orphan Drug Congress USA 2017

    Silver Sponsor

    PRA Health Sciences at World Orphan Drug Congress USA 2017

    Silver Sponsor

    QuintilesIMS at World Orphan Drug Congress USA 2017
  • Silver Sponsor

    WEP Clinical at World Orphan Drug Congress USA 2017

    Bronze Sponsor

    Lapidus Data at World Orphan Drug Congress USA 2017

    Bronze Sponsor

    Marken at World Orphan Drug Congress USA 2017
  • Bronze Sponsor

    McKesson Canada at World Orphan Drug Congress USA 2017

    Bronze Sponsor

    Medicom Innovation Partner a/s at World Orphan Drug Congress USA 2017

    Bronze Sponsor

    MME at World Orphan Drug Congress USA 2017
  • Bronze Sponsor

    Worldwide Clinical Trials at World Orphan Drug Congress USA 2017

    Exhibitor

    AnovaFill at World Orphan Drug Congress USA 2017

    Exhibitor

    APL at World Orphan Drug Congress USA 2017
  • Exhibitor

    Cardinal Health at World Orphan Drug Congress USA 2017

    Exhibitor

    Clinart MENA at World Orphan Drug Congress USA 2017

    Exhibitor

    CORAM Clinical Trials at World Orphan Drug Congress USA 2017
  • Exhibitor

    Illingworth Research Ltd at World Orphan Drug Congress USA 2017

    Exhibitor

    INC Research at World Orphan Drug Congress USA 2017

    Exhibitor

    Omnicare Inc at World Orphan Drug Congress USA 2017
  • Exhibitor

    Paragon Enterprises Inc at World Orphan Drug Congress USA 2017

    Exhibitor

    Pharmaceutics International at World Orphan Drug Congress USA 2017

    Exhibitor

    PSR-Agility at World Orphan Drug Congress USA 2017
  • Exhibitor

    Rare Patient Voice, LLC at World Orphan Drug Congress USA 2017
 

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