Karen Frascello | Senior Director, Medical Affairs
Alnylam Pharmaceuticals

Day 1 - World Orphan Drug Congress USA 2026 @ 12:10

Streamlining U.S. Expanded Access for Small Biotechs

This session will explore practical strategies for designing and executing Rare Disease US Expanded Access Programs that are both compliant and manageable for small biotech organizations with limited resources. Session will further discuss common operational challenges and share scalable solutions that help maintain efficiency without compromising patient access or regulatory expectations.