• April 25 - 27, 2018
    Gaylord National Harbor Hotel, Oxon Hill, MD
     

    The 8 th Global Orphan Drug Conference and Expo

    Strategy, Regulation and Opportunity for Pharma, Biotech and Investors in Rare Diseases

     


  • April 25 - 27, 2018
    Gaylord National Harbor Hotel, Oxon Hill, MD
     

    The 8 th Global Orphan Drug Conference and Expo

    Strategy, Regulation and Opportunity for Pharma, Biotech and Investors in Rare Diseases

     


  • April 25 - 27, 2018
    Gaylord National Harbor Hotel, Oxon Hill, MD
     

    The 8 th Global Orphan Drug Conference and Expo

    Strategy, Regulation and Opportunity for Pharma, Biotech and Investors in Rare Diseases 

     


  • April 25 - 27, 2018
    Gaylord National Harbor Hotel, Oxon Hill, MD
     

    The 8 th Global Orphan Drug Conference and Expo

    Strategy, Regulation and Opportunity for Pharma, Biotech and Investors in Rare Diseases 

     


  • April 25 - 27, 2018
    Gaylord National Harbor Hotel, Oxon Hill, MD
     

    The 8 th Global Orphan Drug Conference and Expo

    Strategy, Regulation and Opportunity for Pharma, Biotech and Investors in Rare Diseases

     


  • April 25 - 27, 2018
    Gaylord National Harbor Hotel, Oxon Hill, MD
     

    The 8 th Global Orphan Drug Conference and Expo

    Strategy, Regulation and Opportunity for Pharma, Biotech and Investors in Rare Diseases

     


  • April 25 - 27, 2018
    Gaylord National Harbor Hotel, Oxon Hill, MD
     

    The 8 th Global Orphan Drug Conference and Expo

    Strategy, Regulation and Opportunity for Pharma, Biotech and Investors in Rare Diseases

     


  • April 25 - 27, 2018
    Gaylord National Harbor Hotel, Oxon Hill, MD
     

    The 8 th Global Orphan Drug Conference and Expo

    Strategy, Regulation and Opportunity for Pharma, Biotech and Investors in Rare Diseases

     

 



Excellent gathering of stakeholders in rare diseases
 



From discussions on rare diseases to the sustainability of our health systems



Leaders from every sector of rare diseases
 

What is World Orphan Drug Congress USA?

 

World Orphan Drug Congress USA focusses on the most pressing challenges and opportunities to bring rare disease therapies to patients faster.
 

World Orphan Drug Congress USA has evolved from a one track conference focused on regulatory pathways, policy and incentives, to a global gathering of 1,000 leaders in orphan drugs from 38 countries, and over 135 presentations covering all aspects of orphan drug development and rare disease research.
 

Enjoy discussions on: 

Cell & Gene Therapies

Genetic Testing

Gene Editing

Partnering & Investment 

Global Market Access

Expanded Access Programs

Real World Evidence

Global Patient Advocacy

Value based pricing & reimbursement

Epidemiology & forecasting

Orphan Drugs Policy

Gene Therapy Development 

 

Together with: 

Rare Disease Advocacy World USA 2018

Pitch & Partner 2018

 

Meet our first 100 Speakers

We've more to announce

 

 

  • Jacqueline Corrigan-Curay at World Orphan Drug Congress USA 2018
    Jacqueline Corrigan-Curay
    Director, Office of Medical Policy, Center for Drug Evaluation and Research
    F.D.A
    Tim Miller at World Orphan Drug Congress USA 2018
    Tim Miller
    President and Chief Executive Officer
    Abeona Therapeutics
    Mark Rothera at World Orphan Drug Congress USA 2018
    Mark Rothera
    President and Chief Executive Officer
    Orchard Therapeutics
  • Amrit Ray at World Orphan Drug Congress USA 2018
    Amrit Ray
    Senior Vice President, Science & Medicine
    Johnson & Johnson
    Sandy Macrae at World Orphan Drug Congress USA 2018
    Sandy Macrae
    President and Chief Executive Officer
    Sangamo BioSciences, Inc
    Katrine Bosley at World Orphan Drug Congress USA 2018
    Katrine Bosley
    Chief Executive Officer
    Editas Medicine
  • Rodger Novak at World Orphan Drug Congress USA 2018
    Rodger Novak
    Chief Executive Officer and Founder
    CRISPR Therapeutics
    Makoto Suematsu at World Orphan Drug Congress USA 2018
    Makoto Suematsu
    Founding President
    Japan Agency for Medical Research and Development
    Rick Chapman at World Orphan Drug Congress USA 2018
    Rick Chapman
    Director of Health Economics
    Institute for Clinical and Economic Review
  • Catherine Stehman Breen at World Orphan Drug Congress USA 2018
    Catherine Stehman Breen
    Chief Medical Officer
    Sarepta Therapeutics
    Yann Le Cam at World Orphan Drug Congress USA 2018
    Yann Le Cam
    Chief Executive Officer
    EURORDIS
    Ron Bartek at World Orphan Drug Congress USA 2018
    Ron Bartek
    Co-Founder/Founding President
    Friedreich's Ataxia Research Alliance
  • Edmund Jessop at World Orphan Drug Congress USA 2018
    Edmund Jessop
    Medical Adviser
    National Health Service
    Katri Asikainen at World Orphan Drug Congress USA 2018
    Katri Asikainen
    Chairperson
    Finnish Rare Diseases and Disabilities Organization (HARSO)
    Saira Bates at World Orphan Drug Congress USA 2018
    Saira Bates
    Co Founder and Chief Executive Officer
    Escend Pharmaceuticals Inc
  • Carole Ben Maimon at World Orphan Drug Congress USA 2018
    Carole Ben Maimon
    Chief Executive Officer
    Chondrial Therapeutics
    Laxminarayan Bhat at World Orphan Drug Congress USA 2018
    Laxminarayan Bhat
    Founder and Chief Executive Officer
    Reviva Pharmaceuticals Inc
    Preston Campbell at World Orphan Drug Congress USA 2018
    Preston Campbell
    President and Chief Executive Officer
    Cystic Fibrosis Foundation
  • Denis Belyakov at World Orphan Drug Congress USA 2018
    Denis Belyakov
    CEO
    Union of Patients’ And Patients’ Organizations With Rare Diseases
    Olivier Danos at World Orphan Drug Congress USA 2018
    Olivier Danos
    Chief Scientific Officer
    Regenxbio Inc
    Rylan Hanks at World Orphan Drug Congress USA 2018
    Rylan Hanks
    Director, Regulatory and R&D Policy
    Amgen Inc
  • Katherine High at World Orphan Drug Congress USA 2018
    Katherine High
    President and Head, Research & Development
    Spark Therapeutics
    Douglas Ingram at World Orphan Drug Congress USA 2018
    Douglas Ingram
    Chief Executive Officer
    Sarepta Therapeutics
    Cristina Klafehn at World Orphan Drug Congress USA 2018
    Cristina Klafehn
    Associate Director,Development Sciences Patient Advocacy
    BioMarin Pharmaceutical Inc.
  • Ken Mills at World Orphan Drug Congress USA 2018
    Ken Mills
    Chief Executive Officer
    ReGenX Biosciences Llc
    Lara Sullivan at World Orphan Drug Congress USA 2018
    Lara Sullivan
    President and Founder
    SpringWorks Therapeutics
    Yvette Venable at World Orphan Drug Congress USA 2018
    Yvette Venable
    International Public Affairs Lead
    Kyowa Kirin International
  • Sue Washer at World Orphan Drug Congress USA 2018
    Sue Washer
    President/CEO
    AGTC
    Barbara Wuebbels at World Orphan Drug Congress USA 2018
    Barbara Wuebbels
    Vice President of Patient Advocacy
    Audentes Therapeutics
    Mark Baglin at World Orphan Drug Congress USA 2018
    Mark Baglin
    Vice President of Global Marketing
    Alnylam Pharmaceuticals
  • Jeanne Barnett at World Orphan Drug Congress USA 2018
    Jeanne Barnett
    Founder and President
    Cysticfibrosis.com
    Alison Bateman House at World Orphan Drug Congress USA 2018
    Alison Bateman House
    Assistant Professor, Division of Medical Ethics
    New York University Langone Medical Center
    Dawn Bir at World Orphan Drug Congress USA 2018
    Dawn Bir
    Chief Commercial Officer
    Reata Pharmaceuticals
  • Philip J. Brooks at World Orphan Drug Congress USA 2018
    Philip J. Brooks
    Program Director, Office of Rare Diseases Research
    NCATS, NIH
    Angela Chavez at World Orphan Drug Congress USA 2018
    Angela Chavez
    President
    Colombia Rare Disorders Society
    Francesca Cook at World Orphan Drug Congress USA 2018
    Francesca Cook
    Director, Pricing and Market Access
    RegenxBio
  • Kelly Du Plessis at World Orphan Drug Congress USA 2018
    Kelly Du Plessis
    Chief Executive Officer
    Rare Diseases South Africa
    Beata Ferencz at World Orphan Drug Congress USA 2018
    Beata Ferencz
    Project Manager
    Rare Diseases Sweden
    Stephen Franklin at World Orphan Drug Congress USA 2018
    Stephen Franklin
    Chief Executive
    Evgen Pharma
  • Pat Furlong at World Orphan Drug Congress USA 2018
    Pat Furlong
    Founding President and Chief Executive Officer
    Parent Project Muscular Dystrophy
    Pamela Gavin at World Orphan Drug Congress USA 2018
    Pamela Gavin
    Chief Operating Officer
    National Organization for Rare Disorders
    Jayne Gershkowitz at World Orphan Drug Congress USA 2018
    Jayne Gershkowitz
    Chief Patient Advocate
    Amicus Therapeutics
  • Scott Gray at World Orphan Drug Congress USA 2018
    Scott Gray
    Chief Executive Officer
    Clincierge
    Philippe Guedat at World Orphan Drug Congress USA 2018
    Philippe Guedat
    Managing Director
    In Flectis Bio Science
    Colin Hayward at World Orphan Drug Congress USA 2018
    Colin Hayward
    Chief Medical Officer
    Premier Research
  • Kenneth Hobby at World Orphan Drug Congress USA 2018
    Kenneth Hobby
    President
    Cure SMA
    Birthe Byskov Holm at World Orphan Drug Congress USA 2018
    Birthe Byskov Holm
    President
    Rare Diseases Denmark
    Kevin Huang at World Orphan Drug Congress USA 2018
    Kevin Huang
    President
    Chinese Organization for Rare Disorders
  • Steven Kaminsky at World Orphan Drug Congress USA 2018
    Steven Kaminsky
    Chief Science Officer
    International Rett Syndrome Foundation
    Alastair Kent OBE at World Orphan Drug Congress USA 2018
    Alastair Kent OBE
    Ambassador
    Genetic Alliance U.K.
    David Lapidus at World Orphan Drug Congress USA 2018
    David Lapidus
    President
    Lapidus Data
  • Edmund Lim at World Orphan Drug Congress USA 2018
    Edmund Lim
    Co-founder
    We CARE Journey
    Igor Lokot at World Orphan Drug Congress USA 2018
    Igor Lokot
    Chief Executive Officer
    Double Bond Pharmaceutical A.B.
    Alastair Macdonald at World Orphan Drug Congress USA 2018
    Alastair Macdonald
    Exec Director, RWLP Strategy, Global
    INC Research/inVentiv Health
  • Jay Madan at World Orphan Drug Congress USA 2018
    Jay Madan
    President
    Innovate Biopharmaceuticals Inc
    Andrew McFadyen at World Orphan Drug Congress USA 2018
    Andrew McFadyen
    Executive Director
    The Isaac Foundation
    Donnie McGrath at World Orphan Drug Congress USA 2018
    Donnie McGrath
    Head of Corporate Strategy & Business Development
    Biohaven Pharmaceuticals
  • Christopher Missling at World Orphan Drug Congress USA 2018
    Christopher Missling
    President and CEO
    Anavex Life Sciences
    Leslie Morgan at World Orphan Drug Congress USA 2018
    Leslie Morgan
    Managing Director
    Durbin
    Juliet Moritz at World Orphan Drug Congress USA 2018
    Juliet Moritz
    Executive Director, Patient Engagement & Strategic Development
    Premier Research
  • Tricia Mullins at World Orphan Drug Congress USA 2018
    Tricia Mullins
    Senior Director of Global Patient Advocacy
    Horizon Pharma
    Michael Murphy at World Orphan Drug Congress USA 2018
    Michael Murphy
    Chief Medical & Scientific Officer
    Worldwide Clinical Trials
    Francois Nader at World Orphan Drug Congress USA 2018
    Francois Nader
    Chairman
    Acceleron Pharma
  • Yukiko Nishimura at World Orphan Drug Congress USA 2018
    Yukiko Nishimura
    President, NPO
    Japan Patients Association, ASrid
    Ayse Deniz Ozger at World Orphan Drug Congress USA 2018
    Ayse Deniz Ozger
    Vice President, Healthcare Division
    Eczacibasi Healthcare
    Carmencita D Padilla at World Orphan Drug Congress USA 2018
    Carmencita D Padilla
    Founding Chairman
    Philippine Society for Orphan Disorders
  • Harsha Rajasimha at World Orphan Drug Congress USA 2018
    Harsha Rajasimha
    Co Founder
    Organization for Rare Diseases India
    Luiz Fernando Lima Reis at World Orphan Drug Congress USA 2018
    Luiz Fernando Lima Reis
    Director of Education and Research
    Hospital Sirio-Libanes
    Trevor Richter at World Orphan Drug Congress USA 2018
    Trevor Richter
    Director, Common Drug Review and Optimal Use
    CADTH
  • Alan Robertson at World Orphan Drug Congress USA 2018
    Alan Robertson
    Chief Executive Officer and Managing Director
    Alsonex
    Chandler Robinson at World Orphan Drug Congress USA 2018
    Chandler Robinson
    CEO
    Monopar Therapeutics
    Christer Rosén at World Orphan Drug Congress USA 2018
    Christer Rosén
    Chairman & CEO
    Jupiter Orphan Therapeutics, Inc.
  • Peter Saltonstall at World Orphan Drug Congress USA 2018
    Peter Saltonstall
    CEO
    National Organization for Rare Disorders
    Gustavo San Martin at World Orphan Drug Congress USA 2018
    Gustavo San Martin
    AME - Amigos Múltiplos pela Esclerose
    Lukas Scheibler at World Orphan Drug Congress USA 2018
    Lukas Scheibler
    Executive Vice President of Research and Development
    Acucela
  • Scott Schliebner at World Orphan Drug Congress USA 2018
    Scott Schliebner
    Vice President, Scientific Affairs, Rare Diseases
    PRA Health Sciences
    Ray Takigiku at World Orphan Drug Congress USA 2018
    Ray Takigiku
    President and Chief Executive Officer
    Bexion Pharmaceuticals Llc
    Pamela Tenaerts at World Orphan Drug Congress USA 2018
    Pamela Tenaerts
    Director
    Clinical Trials Transformation Initiative
  • Vladimir Tomov at World Orphan Drug Congress USA 2018
    Vladimir Tomov
    Chairman
    National Alliance of People with Rare Diseases - Bulgaria
    Martin Welschof at World Orphan Drug Congress USA 2018
    Martin Welschof
    Chief Executive Officer
    Opsona Therapeutics Ltd
    Durhane Wong-Rieger at World Orphan Drug Congress USA 2018
    Durhane Wong-Rieger
    President and Chief Executive Officer
    Canadian Organization For Rare Disorders
  • Jude Samulski at World Orphan Drug Congress USA 2018
    Jude Samulski
    Vice President, Gene Therapy
    Pfizer
    David Cory at World Orphan Drug Congress USA 2018
    David Cory
    President, Chief Executive Officer
    Eiger Biopharmaceuticals

 

SEE MORE SPEAKERS

 

2018 Sponsors & Exhibitors

 

  • Platinum Sponsor

    INC Research at World Orphan Drug Congress USA 2018

    Platinum Sponsor

    Premier Research at World Orphan Drug Congress USA 2018

    Patient Advocacy Sponsor

    National Organization for Rare Disorders at World Orphan Drug Congress USA 2018
  • Patient Advocacy Sponsor

    EURORDIS at World Orphan Drug Congress USA 2018

    Gold Sponsor

    Invitae at World Orphan Drug Congress USA 2018

    Gold Sponsor

    ICON at World Orphan Drug Congress USA 2018
  • Gold Sponsor

    McKesson Canada at World Orphan Drug Congress USA 2018

    Gold Sponsor

    Parexel International Corp at World Orphan Drug Congress USA 2018

    Silver Sponsor

    Atlantic Research Group Inc at World Orphan Drug Congress USA 2018
  • Silver Sponsor

    Clincierge at World Orphan Drug Congress USA 2018

    Silver Sponsor

    IQVIA at World Orphan Drug Congress USA 2018

    Silver Sponsor

    Leadiant Biosciences at World Orphan Drug Congress USA 2018
  • Silver Sponsor

    Pfizer at World Orphan Drug Congress USA 2018

    Silver Sponsor

    Boston Healthcare Associates Inc at World Orphan Drug Congress USA 2018

    Silver Sponsor

    PPD at World Orphan Drug Congress USA 2018
  • Silver Sponsor

    PRA Health Sciences at World Orphan Drug Congress USA 2018

    Silver Sponsor

    rareLife solutions at World Orphan Drug Congress USA 2018

    Silver Sponsor

    WEP Clinical at World Orphan Drug Congress USA 2018
  • Associate Sponsor

    Durbin at World Orphan Drug Congress USA 2018

    Associate Sponsor

    Lapidus Data at World Orphan Drug Congress USA 2018

    Associate Sponsor

    BluePrint Orphan at World Orphan Drug Congress USA 2018
  • Associate Sponsor

    Covance at World Orphan Drug Congress USA 2018

    Associate Sponsor

    Dolon at World Orphan Drug Congress USA 2018

    Associate Sponsor

    Enzyvant at World Orphan Drug Congress USA 2018
  • Associate Sponsor

    Medical Marketing Economics at World Orphan Drug Congress USA 2018

    Associate Sponsor

    National Center for Advancing Translational Sciences - NCATS at World Orphan Drug Congress USA 2018

    Associate Sponsor

    Sucampo Pharmaceuticals Inc at World Orphan Drug Congress USA 2018
  • Associate Sponsor

    Worldwide Clinical Trials at World Orphan Drug Congress USA 2018

    Exhibitor

    Illingworth Research at World Orphan Drug Congress USA 2018

    Exhibitor

    Cello Health at World Orphan Drug Congress USA 2018
  • Exhibitor

    Clinart MENA at World Orphan Drug Congress USA 2018

    Exhibitor

    Fulcrum Research Group at World Orphan Drug Congress USA 2018

    Exhibitor

    Ergomed plc at World Orphan Drug Congress USA 2018
  • Exhibitor

    Euromed srl at World Orphan Drug Congress USA 2018

    Exhibitor

    Paragon Bioservices, Inc. at World Orphan Drug Congress USA 2018

    Exhibitor

    Chapper Healthcare at World Orphan Drug Congress USA 2018
  • Exhibitor

    Pharmaceutics International at World Orphan Drug Congress USA 2018

    Exhibitor

    UBC at World Orphan Drug Congress USA 2018

 

 

SPONSORSHIP OPPORTUNITIES


Sponsor World Orphan Drug Congress USA

Interested in selling to the Orphan Drug sector?


Your customers are here continuously looking for new strategies and technologies to expedite orphan drugs to patients.
 

Find out how World Orphan Drug Congress USA can solve all your sales and marketing needs.

 

DOWNLOAD PROSPECTUS


 

Apply to Speak at Pitch & Partner 2018

 

Are you a rare disease biotech who's looking for funding or partnership/co-development/licensing opportunities? 

Applications for Pitch & Partner 2018 are now open and only 30 biotechs will be selected to present to prospective investors and partners!

 

DOWNLOAD APPLICATION KIT

 

WHO ATTENDS?

Here's a glimpse of who attends World Orphan Drug Congress USA

 

AccessPharmaCon,LLC Aegerion Pharmaceuticals  Aetna Pharmacy Management  Alexion Pharmaceuticals  Andarix Pharmaceuticals  ArmaGen Technologies, Inc.  Ashfield Healthcare   Asklepion Pharmaceuticals LLC  Ax-S Pharma  B.D.C. Venture Capital  BioBlast Pharma Ltd  Biomarin Pharmaceutical Inc.  BioPontis Alliance for Rare Disease Brace Pharma Capital   Brazilian Federal Council of Medicine  Bristol-Myers Squibb  CatalentPharma Solutions   CatalystPharmaceutical Partners  CDER FDA  Clear Pharma  Clementia Pharmaceuticals Inc.   Clinuvel Pharmaceuticals Ltd  Dicerna Pharmaceuticals  DrugDev  EvaluatePharma Ltd   Genoa Pharmaceuticals   Genpharm  GenSight Biologics  Genzyme Corp  Giddi Pharma Co., Ltd.   Idera Pharmeceuticals  IDIS Pharma   Iptechex Pharmalicensing  Jazz Pharmaceuticals, Inc  Juice Pharma Worldwide   KBI Biopharma Inc   Lumos Pharma   M3 Pharma  Marathon Pharmaceuticals LLC   Marinus Pharmaceuticals  Momenta Pharmaceuticals Inc  Opsona Therapeutics Ltd  Optio Biopharma Solutions LLC  Orpharma  Pfizer, Inc  Pharmaceutics International In  Pharmaessentia Corp   Pharnext   Portola Pharmaceuticals , Inc.  Provectus PharmaceuticalsInc   QuayPharma  Quintiles Inc  Raptor Pharmaceuticals Corp  Reata Pharmaceuticals   Recordati S.p.A  Recursion Pharmaceuticals  Retrophin   Sanofi   Savara Pharmaceuticals  Seattle Children's Research Institute   Shire Pharmaceuticals Inc  Taiba Pharma LLC Teva  Threshold Pharmaceuticals Inc   Tolero Pharmaceuticals   Ultragenyx Pharmaceutical Inc.  Valley Fever Solutions   Vanda Pharmaceuticals Inc   Vertex Pharmaceuticals 

 

FIND OUT MORE

GET YOUR PASS NOW

Choose your package

Prices increase after January 31st – book now to get these prices

2 DAY CONFERENCE


Individual Pass

USD $2,550

BOOK NOW

 

Group Booking of 3 or more

USD $2,295

BOOK NOW

3 DAY CONFERENCE


Individual Pass

USD $3,115

BOOK NOW

 

Group Booking of 3 or more

USD $2,805

BOOK NOW

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Get Involved At World Orphan Drug Congress USA

 

To Sponsor Or Exhibit

 
 

Andre Singer
andre.singer@terrapinn.com
t/ +1 646 619 1797

 

 

 

To Speak

 
 

Katerina Leon
katerina.leon@terrapinn.com
t/ +1 646 619 1786

 

 

 

To Register

 
 

William Horgan
william.horgan@terrapinn.com
t/ +1 212 379 6320