World Orphan Drug Congress USA

The Global Orphan Drug Conference & Expo

Bringing together pharma, biotech, patient groups, academia, regulators, payers and investors gather to talk about strategies to expedite orphan drug development.

 

 

 

World Orphan Drug Congress USA is the largest global orphan drug industry event.

 

 

This event is dedicated to fostering partnerships and collaboration amongst industry, governments, payers, investors and patients. It is about expediting orphan drug development and articulating its value, from discovery to patient access, so that manufacturers are guaranteed full and speedy reimbursement. 

 

 

Grow your orphan drug business in 2016

If you wish to educate:

Publish your white paper on our dedicated Total Orphan Drugs blog, monthly newsletter 
Dedicated email blast to targeted job titles and profiles 
20-minute plenary keynote or case study
3-hour workshop/seminar

If you wish to establish thought leadership and credibility: 

Chair a whole day at the main conference, Rare Disease Advocacy World or Pitch & Partner 
20-minute plenary keynote 
Moderate a round table discussion 

If you wish to establish rapport and introduce your brand: 

Host a cocktail hour 
Throw a dinner party 
Sponsor breakfast, coffee breaks or lunch   

If you wish to showcase your product or service:

Book either a 60, 120 or 240 square feet space 
Wrap your brand around a column at the World Orphan Drug Congress USA Exhibit Hall 

 

DOWNLOAD THE SPONSORSHIP PROSPECTUS

 

"The World Orphan Drug Congress USA – the UN of Orphan Drugs.”

- 2015 Conference Attendee

 

Meet key industry leaders 

Showcase your expertise by joining our impressive speaker line-up.

In 2015 we were joined by: 

  • Chris Adams at World Orphan Drug Congress USA 2016
    Chris Adams
    CEO
    Andarix Pharmaceuticals
    Zohar Argov at World Orphan Drug Congress USA 2016
    Zohar Argov
    Chief Medical Officer
    BioBlast Pharma Ltd
  • Dr Leone Atkinson at World Orphan Drug Congress USA 2016
    Dr Leone Atkinson
    Senior Medical Director
    Covance
    Sonja L. Banks at World Orphan Drug Congress USA 2016
    Sonja L. Banks
    President and Chief Operating Officer
    Sickle Cell Disease Association of America, Inc.
  • Ms Nicole Boice at World Orphan Drug Congress USA 2016
    Ms Nicole Boice
    President and Founder
    Global Genes Project
    Max Bronstein at World Orphan Drug Congress USA 2016
    Max Bronstein
    Senior Director, Public and Government Relations
    EveryLife Foundation for Rare Diseases
  • Mr Kyle Brown at World Orphan Drug Congress USA 2016
    Mr Kyle Brown
    Chief Executive Officer and Founder
    PatientCrossroads
    Mary E. Brown at World Orphan Drug Congress USA 2016
    Mary E. Brown
    President and Chief Executive Officer
    Sickle Cell Disease Association of California
  • Mr Yann LE Cam at World Orphan Drug Congress USA 2016
    Mr Yann LE Cam
    Chief Executive Officer
    EURORDIS
    Shawn Carbonell at World Orphan Drug Congress USA 2016
    Shawn Carbonell
    Co-Founder, President & CEO
    OncoSynergy
  • Christopher Cashman at World Orphan Drug Congress USA 2016
    Christopher Cashman
    Chairman and CEO
    Marinus Pharmaceuticals
    Keya Chiang at World Orphan Drug Congress USA 2016
    Keya Chiang
    Corporate Sales Director
    Giddi Pharma
  • Mr Jean-Philippe Combal at World Orphan Drug Congress USA 2016
    Mr Jean-Philippe Combal
    COO
    GenSight Biologics
    Ms Kathleen Coolidge at World Orphan Drug Congress USA 2016
    Ms Kathleen Coolidge
    Director for U.S. Patient Advocacy
    Genzyme
  • Mr Mark Corbett at World Orphan Drug Congress USA 2016
    Mr Mark Corbett
    Senior Vice President
    Clinigen Global Access Programs
    Antoine Daher at World Orphan Drug Congress USA 2016
    Antoine Daher
    President
    Casa Hunter
  • Nach Dave at World Orphan Drug Congress USA 2016
    Nach Dave
    Director, Regulatory Affairs
    Premier Research
    Jeff Davis at World Orphan Drug Congress USA 2016
    Jeff Davis
    Head of Corporate Development
    Acer Therapeutics
  • Mr David Drutz at World Orphan Drug Congress USA 2016
    Mr David Drutz
    Chief Executive Officer
    D.A.R.A. BioSciences Inc
    Alistair Duncan at World Orphan Drug Congress USA 2016
    Alistair Duncan
    President and Chief Executive Officer
    Vida Therapeutics Inc
  • Jamie Eckman at World Orphan Drug Congress USA 2016
    Jamie Eckman
    President
    The Menkes Foundation
    Celia Economides at World Orphan Drug Congress USA 2016
    Celia Economides
    Director, Patient Advocacy
    Biomarin Pharmaceutical Inc.
  • Neal M. Farber at World Orphan Drug Congress USA 2016
    Neal M. Farber
    Chief Executive Officer
    Neurohealing Pharmaceuticals Inc
    Kelly Franchetti at World Orphan Drug Congress USA 2016
    Kelly Franchetti
    Executive Director, Global Patients Insights and Engagement
    MAPI
  • Mr Michael French at World Orphan Drug Congress USA 2016
    Mr Michael French
    President & CEO
    Marina Biotech Inc
    Patricia Furlong at World Orphan Drug Congress USA 2016
    Patricia Furlong
    President and CEO
    Parent Project Muscular Dystrophy
  • Thomas Gegeny at World Orphan Drug Congress USA 2016
    Thomas Gegeny
    Stakeholder Engagement Leader
    Clear Pharma
    Dr Jeff Gerschwind at World Orphan Drug Congress USA 2016
    Dr Jeff Gerschwind
    Founder and Chief Executive Officer
    PreScience Labs
  • Dr Chris Gibson at World Orphan Drug Congress USA 2016
    Dr Chris Gibson
    Chief Executive Officer
    Recursion Pharmaceuticals
    Mr Alan Gilstrap at World Orphan Drug Congress USA 2016
    Mr Alan Gilstrap
    Director
    Genzyme
  • Nancy Goodman at World Orphan Drug Congress USA 2016
    Nancy Goodman
    Founder and Executive Director
    Kids v Cancer
    Mr. Greg Gorgas at World Orphan Drug Congress USA 2016
    Mr. Greg Gorgas
    Senior Vice President, Commercial
    Mast Therapeutics Inc
  • Ms Kate Holland at World Orphan Drug Congress USA 2016
    Ms Kate Holland
    VP, Commercial
    Vanda Pharmaceuticals Inc
    Sangeetha Iyer at World Orphan Drug Congress USA 2016
    Sangeetha Iyer
    Scientist
    Perlstein Labs
  • Mr Derek Kelaita at World Orphan Drug Congress USA 2016
    Mr Derek Kelaita
    VP Business Development
    ArmaGen Technologies, Inc.
    David Larwood at World Orphan Drug Congress USA 2016
    David Larwood
    CEO and Founder
    Valley Fever Solutions
  • Mr Pierre Laurin at World Orphan Drug Congress USA 2016
    Mr Pierre Laurin
    Chief Executive Officer
    ProMetic Life Sciences Inc.
    Margaret Lee at World Orphan Drug Congress USA 2016
    Margaret Lee
    Vice President, Product Leadership and Biology
    Karyopharm
  • Antonio Lee at World Orphan Drug Congress USA 2016
    Antonio Lee
    Chief Executive Officer & Managing Director
    MEDIPOST America, Inc.
    Ms Teresa Leezer at World Orphan Drug Congress USA 2016
    Ms Teresa Leezer
    COO
    Rhinocyte Inc
  • Wendi LeVigne at World Orphan Drug Congress USA 2016
    Wendi LeVigne
    Vice President Manufacturer Relations
    Oneworld
    Stacie Lindsey at World Orphan Drug Congress USA 2016
    Stacie Lindsey
    President
    The Cholangiocarcinoma Foundation
  • Malcolm MacKenzie at World Orphan Drug Congress USA 2016
    Malcolm MacKenzie
    SVP, Strategic Planning & Customer Insights
    Juice Pharma Worldwide
    Mr John Maki at World Orphan Drug Congress USA 2016
    Mr John Maki
    Chief Executive Officer
    Vicus Therapeutics , LLC
  • Charles Makin at World Orphan Drug Congress USA 2016
    Charles Makin
    Vice President, HEOR and Strategic Market Access
    MAPI
    John Maslowski at World Orphan Drug Congress USA 2016
    John Maslowski
    Vice President, Scientific Affairs
    Fibrocell Science Inc
  • Dr Pierre Miniou at World Orphan Drug Congress USA 2016
    Dr Pierre Miniou
    Co-Founder
    Inflectis Bioscience
    Christopher Missling at World Orphan Drug Congress USA 2016
    Christopher Missling
    President and Chief Executive Officer
    Anavex Life Sciences Corp
  • Matthew Mollan at World Orphan Drug Congress USA 2016
    Matthew Mollan
    General Manager, Development and Analytical Solutions
    Catalent Pharma Solutions
    Allison Moore at World Orphan Drug Congress USA 2016
    Allison Moore
    Director
    Hereditary Neuropathy Foundation
  • Dr Richard Moscicki at World Orphan Drug Congress USA 2016
    Dr Richard Moscicki
    Deputy Center Director for Science Operations
    CDER FDA
    Jordan Muller at World Orphan Drug Congress USA 2016
    Jordan Muller
    Founder
    KAT6A Foundation
  • Nicoletta Muner at World Orphan Drug Congress USA 2016
    Nicoletta Muner
    Director, Global Regulatory Affairs
    Clinuvel Pharmaceuticals Ltd
    Mr Ramaiah Muthyala at World Orphan Drug Congress USA 2016
    Mr Ramaiah Muthyala
    Associate Director, Center for Orphan Drug Development
    University of Minnesota
  • Jeff Myers at World Orphan Drug Congress USA 2016
    Jeff Myers
    President and Chief Executive Officer
    Medicaid Health Plans of America
    Rob Neville at World Orphan Drug Congress USA 2016
    Rob Neville
    Chief Executive Officer
    Savara Pharmaceutical
  • Jan Nielsen at World Orphan Drug Congress USA 2016
    Jan Nielsen
    Division President of Access and Patient Support
    Sonexus Health
    Mr Jean Nordstrom at World Orphan Drug Congress USA 2016
    Mr Jean Nordstrom
    Chairman & CEO
    Sixera Pharma Ab
  • Stephanie Okey at World Orphan Drug Congress USA 2016
    Stephanie Okey
    Senior Vice President Head of North America
    Genzyme, A Sanofi Company
    Tuyen Ong at World Orphan Drug Congress USA 2016
    Tuyen Ong
    Senior Vice President, Head of Clinical Development and Translational Research
    PTC Therapeutics
  • Dr May Orfali at World Orphan Drug Congress USA 2016
    Dr May Orfali
    Global Medicines Development Lead- Rare Diseases
    Pfizer
    Xavier Paoli at World Orphan Drug Congress USA 2016
    Xavier Paoli
    Commercialization Strategy Director
    Pharnext
  • Ms Rekha Patel at World Orphan Drug Congress USA 2016
    Ms Rekha Patel
    Director
    Catalent Pharma Solutions
    Eric Pauwels at World Orphan Drug Congress USA 2016
    Eric Pauwels
    Senior Vice President and General Manager, The Americas
    PTC Therapeutics
  • Mr Edmund Pezalla at World Orphan Drug Congress USA 2016
    Mr Edmund Pezalla
    National Medical Director of Pharmacy Policy and Strategy
    Aetna Pharmacy Management
    Renato Porto at World Orphan Drug Congress USA 2016
    Renato Porto
    Director
    ANVISA - Agência Nacional de Vigilância Sanitária
  • Jess Rabourn at World Orphan Drug Congress USA 2016
    Jess Rabourn
    Chief Executive Officer
    Ax-S Pharma
    Dr Gayatri Rao at World Orphan Drug Congress USA 2016
    Dr Gayatri Rao
    Director, Orphan Products Development
    FDA
  • Angi Robinson at World Orphan Drug Congress USA 2016
    Angi Robinson
    Executive Director, Scientific Account Leader
    Premier Research
    Danielle Rollmann at World Orphan Drug Congress USA 2016
    Danielle Rollmann
    Head, International Policy within Pfizer Corporate Affairs
    Pfizer, Inc
  • Jan Rosenbaum at World Orphan Drug Congress USA 2016
    Jan Rosenbaum
    Chief Scientific Officer
    Airway Therapeutics
    Mr Mark Rothera at World Orphan Drug Congress USA 2016
    Mr Mark Rothera
    Chief Commercial Officer
    PTC Therapeutics, Inc.
  • Yaffa Rubinstein at World Orphan Drug Congress USA 2016
    Yaffa Rubinstein
    Director, Patient Resources for Clinical and Translational Research
    NIH / NCATS / Office of Rare Diseases Research
    Peter Saltonstall at World Orphan Drug Congress USA 2016
    Peter Saltonstall
    Chief Executive Officer
    National Organization For Rare Disorders
  • Lisa Schill at World Orphan Drug Congress USA 2016
    Lisa Schill
    Vice President
    RASopathies Network USA
    Peggy Schorr at World Orphan Drug Congress USA 2016
    Peggy Schorr
    VP, US Operations
    OrphanReach
  • Dr Joerg Seebeck at World Orphan Drug Congress USA 2016
    Dr Joerg Seebeck
    Chief Medical Officer
    Primevigilance
    Chander Seghal at World Orphan Drug Congress USA 2016
    Chander Seghal
    Director, Common Drug Review (CDR) and Optimal Use of Drugs
    CADTH
  • Raghuram “Ram” Selvaraju at World Orphan Drug Congress USA 2016
    Raghuram “Ram” Selvaraju
    Managing Director, Equity Research - Healthcare
    MLV & Co.
    Alvin Shih at World Orphan Drug Congress USA 2016
    Alvin Shih
    EVP, Head of R&D
    Retrophin
  • Charles Stark at World Orphan Drug Congress USA 2016
    Charles Stark
    Sr. Vice President
    Emmaus Life Sciences, Inc
    Julie Stoss at World Orphan Drug Congress USA 2016
    Julie Stoss
    Vice President, Government Relations
    Kaiser Permanente
  • Emily Stube at World Orphan Drug Congress USA 2016
    Emily Stube
    Director, Medical Writing Product Development and Client Relations
    Premier Research
    Paolo Tagliaferri at World Orphan Drug Congress USA 2016
    Paolo Tagliaferri
    Consultant
    M3 Pharma
  • Mr Henri Termeer at World Orphan Drug Congress USA 2016
    Mr Henri Termeer
    Chief Executive Officer, Former
    Genzyme
    Santa Tumminia at World Orphan Drug Congress USA 2016
    Santa Tumminia
    Special Assistant To The Director
    National Eye Institute N.I.H.
  • Mr Mark Varney at World Orphan Drug Congress USA 2016
    Mr Mark Varney
    Chief Executive Officer
    Neurolixis
    Mark Vineis at World Orphan Drug Congress USA 2016
    Mark Vineis
    VP, Cardinal Health Specialty Pharmacy
    Cardinal Health
  • Tom Watson at World Orphan Drug Congress USA 2016
    Tom Watson
    Business Development Director
    Clinigen Global Access Programs
    Keith Watts at World Orphan Drug Congress USA 2016
    Keith Watts
    Executive Vice President Strategic Services at One-World
    Oneworld
  • Mr Martin Welschof at World Orphan Drug Congress USA 2016
    Mr Martin Welschof
    Chief Executive Officer
    Opsona Therapeutics Ltd
    Ms Elizabeth White at World Orphan Drug Congress USA 2016
    Ms Elizabeth White
    Assistant Vice President, Rare Disease Commercial Development
    Pfizer

 

SPONSORSHIP PROSPECTUS

Are you looking to meet CEOs, VPs and Directors working in R&D, Business Development, Regulatory Access, Market Access, Commercial, Marketing and Brand/Product from pharma and biotech?

Then you need to join our sponsors at World Orphan Drug Congress USA 2016.

 


  • Platinum Sponsor

    Premier Research at World Orphan Drug Congress USA 2016
  • Silver Sponsor

    Lapidus Data at World Orphan Drug Congress USA 2016
  • Silver Sponsor

    Quintiles at World Orphan Drug Congress USA 2016
  • Bronze Sponsor

    Clear Pharma at World Orphan Drug Congress USA 2016
  • Bronze Sponsor

    Patient Crossroads at World Orphan Drug Congress USA 2016
  • Bronze Sponsor

    Medical Marketing Economics at World Orphan Drug Congress USA 2016
  • Bronze Sponsor

    One-World, inc at World Orphan Drug Congress USA 2016
  • Bronze Sponsor

    PRA International at World Orphan Drug Congress USA 2016
  • Exhibitor

    Clinart MENA at World Orphan Drug Congress USA 2016
  • Exhibitor

    Cote Orphan at World Orphan Drug Congress USA 2016
  • Exhibitor

    Dohmen Life Science Services at World Orphan Drug Congress USA 2016
  • Exhibitor

    Pharmaceutics International Inc at World Orphan Drug Congress USA 2016
  • Exhibitor

    PSR-Agility at World Orphan Drug Congress USA 2016

 

JOIN THEM TODAY

 

Take a look at the sponsorship prospectus

It helps explain how you can get involved with World Orphan Drug Congress USA Congress USA 2015.  

GET YOUR COPY HERE

 

World Orphan Drug Congress USA

"The most comprehensive event I've attended in the past few years. It was the perfect opportunity for learning all the latest important information in the rare disease space."   

Patricia Weltin, Executive Director and Founder, Rare Disease United Foundation 

World Orphan Drug Congress USA

"The congress was extremely stimulating and productive for us: If there was a prize for phenomenal energy, good vibes, and flawless execution, you and your folks would win it, hands down."  

Florian Brey, Medical Director, JUICE Pharma Worldwide 

World Orphan Drug Congress USA

"Amazing collaborative environment and networking. Great Orphan 360-degree perspective. Very informative compact event."  

Oksana Komarova, Business Development Director, Big Arrow Group

 

Register Now

THIS CONFERENCE WILL SELL OUT!
Early registration and partner discounts available.
Click below for the full list of ticket options...

REGISTER NOW

 

 
ChristopherMisslingPresImage

“Potential Applications of Sigma-1 Receptors in Orphan Indications: Spinocerebellar Ataxia (SCA)”

Christopher Missling of Anavex Life Sciences Corp.  joined us for World Orphan Drug Congress USA 2015 to present about ‘ Potential Applications of Sigma-1 Receptors in Orphan ...

The post “Potential Applications of Sigma-1 Receptors in Orphan Indications: Spinocerebellar Ataxia (SCA)” appeared first on Orphan Drugs.

AlistairDuncanPresImage

“viDA Therapeutics Inc. ”

Alistair Duncan of viDA Therapeutics Inc.  joined us for World Orphan Drug Congress USA 2015 to present about ‘ viDA Therapeutics Inc.’  Download the presentation now to learn ...

The post “viDA Therapeutics Inc. ” appeared first on Orphan Drugs.

GjaltHuismanPresImage

“Oral Biological Candidate for the Treatment of PKU”

Gjalt Huisman of Codexis  joined us for World Orphan Drug Congress USA 2015 to present about ‘ Oral Biological Candidate for the Treatment of PKU’  Download the presentation ...

The post “Oral Biological Candidate for the Treatment of PKU” appeared first on Orphan Drugs.

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