• World Orphan Drug Congress USA 2017

     

    THE GLOBAL ORPHAN DRUG
    CONFERENCE AND EXPO

     

    19 - 21 April 2017

  • Bringing stakeholders from across the world together to spearhead orphan drug development

     

    APPLY TO SPEAK

  • The place to be for leaders in the rare disease community

    Hans Schikan, CEO, Prosensa Therapeutics Bv

  • Fostering partnerships and collaboration amongst industry, governments, payers, investors and patients

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This is the largest global orphan drug industry event

CONFERENCE

Agenda at World Orphan Drug Congress USA

With keynotes, interactive discussions, workshops and roundtables, this event is designed to tackle the most important challenges facing the orphan drug and rare disease industry.

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EXHIBITION

Exhibit at World Orphan Drug Congress USA

This is the perfect platform to generate new leads, create brand awareness and launch new products. No other marketing gets you in a room with so many potential customers looking for suppliers.

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NETWORKING

Network at World Orphan Drug Congress USA

We offer a variety of networking opportunities from Speed Networking to 1-2-1 Partnering sessions to ensure that you meet as many other attendees as possible in 2 days.

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Together with:

WHAT'S NEW IN 2017

 

In 2017 we're looking to the future...

What, for instance, happens when a global orphan drug biopharma goes into Korea, India and Brazil – places where generics is king?

Or how commercially acceptable is an even-higher priced, potentially one-time treatment gene therapy?

Is the regulatory and reimbursement pathway more or less the same as other orphan drugs?

 

Whats new at the World Orphan Drug Congress USA 2017

World Orphan Drug Congress USA 2017 will have a whole day seminar on these forward-looking environments:
 

NextGen Therapies
featuring Gene Therapy, Biosimilars, Immunotherapy and other up-and-coming biologics...

Alongside a separate whole-day session on Personalized Medicine.
 

 

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The largest global orphan drug industry event

The World Orphan Drug Congress USA is a place where innovation and expertise is showcased, solutions are found and learning is done.

 

If you offer a solution or product in the orphan drug space, the World Orphan Drug Congress USA is definitely the right place to do this.

 

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2016 KEYNOTE SPEAKERS INCLUDED

 

  • Dr Richard Moscicki at World Orphan Drug Congress USA 2015
    Dr Richard Moscicki
    Deputy Center Director for Science Operations
    CDER FDA
    Jeff Myers at World Orphan Drug Congress USA 2015
    Jeff Myers
    President and Chief Executive Officer
    Medicaid Health Plans of America
    Mr Edmund Pezalla at World Orphan Drug Congress USA 2015
    Mr Edmund Pezalla
    National Medical Director of Pharmacy Policy and Strategy
    Aetna Pharmacy Management
  • Dr Nick Sireau at World Orphan Drug Congress USA 2015
    Dr Nick Sireau
    Chairman
    AKU Society
    Patricia Furlong at World Orphan Drug Congress USA 2015
    Patricia Furlong
    President and CEO
    Parent Project Muscular Dystrophy
    Stephen Groft at World Orphan Drug Congress USA 2015
    Stephen Groft
    Director Of Office Of Rare Diseases Research
    N.I.H
  • Celia Economides at World Orphan Drug Congress USA 2015
    Celia Economides
    Director, Patient Advocacy
    Biomarin Pharmaceutical Inc.
    Ms Wills Hughes-Wilson at World Orphan Drug Congress USA 2015
    Ms Wills Hughes-Wilson
    Senior Vice President, Chief Patient Access Officer
    Sobi
    Daniel Anderson at World Orphan Drug Congress USA 2015
    Daniel Anderson
    Samuel A. Goldblith Professor of Applied Biology
    Institute For Medical Engineering and Science Harvard M.I.T. Division of Health Sciences and Technology
  • Eric Hoffman at World Orphan Drug Congress USA 2015
    Eric Hoffman
    Director, Research Center for Genetic Medicine
    The George Washington University Children's Hospital National Medical Center
    Nancy Goodman at World Orphan Drug Congress USA 2015
    Nancy Goodman
    Founder and Executive Director
    Kids v Cancer
    Chander Seghal at World Orphan Drug Congress USA 2015
    Chander Seghal
    Director, Common Drug Review (CDR) and Optimal Use of Drugs
    CADTH
  • Zohar Argov at World Orphan Drug Congress USA 2015
    Zohar Argov
    Chief Medical Officer
    BioBlast Pharma Ltd
    Dr Leone Atkinson at World Orphan Drug Congress USA 2015
    Dr Leone Atkinson
    Senior Medical Director
    Covance
    Max Bronstein at World Orphan Drug Congress USA 2015
    Max Bronstein
    Senior Director, Public and Government Relations
    EveryLife Foundation for Rare Diseases
  • Mr Kyle Brown at World Orphan Drug Congress USA 2015
    Mr Kyle Brown
    Chief Executive Officer and Founder
    PatientCrossroads
    Mary E. Brown at World Orphan Drug Congress USA 2015
    Mary E. Brown
    President and Chief Executive Officer
    Sickle Cell Disease Association of California
    Christopher Cashman at World Orphan Drug Congress USA 2015
    Christopher Cashman
    Chairman and CEO
    Marinus Pharmaceuticals
  • Keya Chiang at World Orphan Drug Congress USA 2015
    Keya Chiang
    Corporate Sales Director
    Giddi Pharma
    Mr Jean-Philippe Combal at World Orphan Drug Congress USA 2015
    Mr Jean-Philippe Combal
    COO
    GenSight Biologics
    Ms Kathleen Coolidge at World Orphan Drug Congress USA 2015
    Ms Kathleen Coolidge
    Director for U.S. Patient Advocacy
    Genzyme
  • Mr Mark Corbett at World Orphan Drug Congress USA 2015
    Mr Mark Corbett
    Senior Vice President
    Clinigen Global Access Programs
    Antoine Daher at World Orphan Drug Congress USA 2015
    Antoine Daher
    President
    Casa Hunter
    Nach Dave at World Orphan Drug Congress USA 2015
    Nach Dave
    Director, Regulatory Affairs
    Premier Research
  • Mr Danko Dominis at World Orphan Drug Congress USA 2015
    Mr Danko Dominis
    Head of Business Development
    Ergomed
    Alistair Duncan at World Orphan Drug Congress USA 2015
    Alistair Duncan
    President and Chief Executive Officer
    Vida Therapeutics Inc
    Jamie Eckman at World Orphan Drug Congress USA 2015
    Jamie Eckman
    President
    The Menkes Foundation
  • Kelly Franchetti at World Orphan Drug Congress USA 2015
    Kelly Franchetti
    Executive Director, Global Patients Insights and Engagement
    MAPI
    Mr Michael French at World Orphan Drug Congress USA 2015
    Mr Michael French
    President & CEO
    Marina Biotech Inc
    Thomas Gegeny at World Orphan Drug Congress USA 2015
    Thomas Gegeny
    Stakeholder Engagement Leader
    Clear Pharma
  • Dr Chris Gibson at World Orphan Drug Congress USA 2015
    Dr Chris Gibson
    Chief Executive Officer
    Recursion Pharmaceuticals
    Mr Alan Gilstrap at World Orphan Drug Congress USA 2015
    Mr Alan Gilstrap
    Director
    Genzyme
    Mr Rob Gustines at World Orphan Drug Congress USA 2015
    Mr Rob Gustines
    Director, Biologics
    Catalent Pharma Solutions
  • Robert Haws at World Orphan Drug Congress USA 2015
    Robert Haws
    Doctor of Pediatric Nephrology
    Marshfield Clinic
    Marc Hedrick at World Orphan Drug Congress USA 2015
    Marc Hedrick
    President and CEO
    Cytori Therapeutics Inc
    Sangeetha Iyer at World Orphan Drug Congress USA 2015
    Sangeetha Iyer
    Scientist
    Perlstein Labs
  • Mr Derek Kelaita at World Orphan Drug Congress USA 2015
    Mr Derek Kelaita
    VP Business Development
    ArmaGen Technologies, Inc.
    Mr Pierre Laurin at World Orphan Drug Congress USA 2015
    Mr Pierre Laurin
    Chief Executive Officer
    ProMetic Life Sciences Inc.
    Antonio Lee at World Orphan Drug Congress USA 2015
    Antonio Lee
    Chief Executive Officer & Managing Director
    MEDIPOST America, Inc.
  • Margaret Lee at World Orphan Drug Congress USA 2015
    Margaret Lee
    Vice President, Product Leadership and Biology
    Karyopharm
    Wendi LeVigne at World Orphan Drug Congress USA 2015
    Wendi LeVigne
    Vice President Manufacturer Relations
    Oneworld
    Malcolm MacKenzie at World Orphan Drug Congress USA 2015
    Malcolm MacKenzie
    SVP, Strategic Planning & Customer Insights
    Juice Pharma Worldwide
  • John Maki at World Orphan Drug Congress USA 2015
    John Maki
    Chief Executive Officer
    Vicus Therapeutics , LLC
    Charles Makin at World Orphan Drug Congress USA 2015
    Charles Makin
    Vice President, HEOR and Strategic Market Access
    MAPI
    John Maslowski at World Orphan Drug Congress USA 2015
    John Maslowski
    Vice President, Scientific Affairs
    Fibrocell Science Inc
  • Dr Pierre Miniou at World Orphan Drug Congress USA 2015
    Dr Pierre Miniou
    Co-Founder
    Inflectis Bioscience
    Christopher Missling at World Orphan Drug Congress USA 2015
    Christopher Missling
    President and Chief Executive Officer
    Anavex Life Sciences Corp
    Matthew Mollan at World Orphan Drug Congress USA 2015
    Matthew Mollan
    General Manager, Development and Analytical Solutions
    Catalent Pharma Solutions
  • Jordan Muller at World Orphan Drug Congress USA 2015
    Jordan Muller
    Founder
    KAT6A Foundation
    Nicoletta Muner at World Orphan Drug Congress USA 2015
    Nicoletta Muner
    Director, Global Regulatory Affairs
    Clinuvel Pharmaceuticals Ltd
    Mr Ramaiah Muthyala at World Orphan Drug Congress USA 2015
    Mr Ramaiah Muthyala
    Associate Director, Center for Orphan Drug Development
    University of Minnesota
  • Rob Neville at World Orphan Drug Congress USA 2015
    Rob Neville
    Chief Executive Officer
    Savara Pharmaceutical
    Mr Jean Nordstrom at World Orphan Drug Congress USA 2015
    Mr Jean Nordstrom
    Chairman & CEO
    Sixera Pharma Ab
    Tuyen Ong at World Orphan Drug Congress USA 2015
    Tuyen Ong
    Senior Vice President, Head of Clinical Development and Translational Research
    PTC Therapeutics
  • Dr May Orfali at World Orphan Drug Congress USA 2015
    Dr May Orfali
    Global Medicines Development Lead- Rare Diseases
    Pfizer
    Xavier Paoli at World Orphan Drug Congress USA 2015
    Xavier Paoli
    Commercialization Strategy Director
    Pharnext
    Ms Rekha Patel at World Orphan Drug Congress USA 2015
    Ms Rekha Patel
    Director
    Catalent Pharma Solutions
  • Eric Pauwels at World Orphan Drug Congress USA 2015
    Eric Pauwels
    Senior Vice President and General Manager, The Americas
    PTC Therapeutics
    Renato Porto at World Orphan Drug Congress USA 2015
    Renato Porto
    Director
    ANVISA - Agência Nacional de Vigilância Sanitária
    Jess Rabourn at World Orphan Drug Congress USA 2015
    Jess Rabourn
    Chief Executive Officer
    Ax-S Pharma
  • Dr Gayatri Rao at World Orphan Drug Congress USA 2015
    Dr Gayatri Rao
    Director, Orphan Products Development
    FDA
    Danielle Rollmann at World Orphan Drug Congress USA 2015
    Danielle Rollmann
    Head, International Policy within Pfizer Corporate Affairs
    Pfizer, Inc
    Jan Rosenbaum at World Orphan Drug Congress USA 2015
    Jan Rosenbaum
    Chief Scientific Officer
    Airway Therapeutics
  • Mr Mark Rothera at World Orphan Drug Congress USA 2015
    Mr Mark Rothera
    Chief Commercial Officer
    PTC Therapeutics, Inc.
    Peter Saltonstall at World Orphan Drug Congress USA 2015
    Peter Saltonstall
    Chief Executive Officer
    National Organization For Rare Disorders
    Lisa Schill at World Orphan Drug Congress USA 2015
    Lisa Schill
    Vice President
    RASopathies Network USA
  • Dr Joerg Seebeck at World Orphan Drug Congress USA 2015
    Dr Joerg Seebeck
    Chief Medical Officer
    Primevigilance
    Alvin Shih at World Orphan Drug Congress USA 2015
    Alvin Shih
    EVP, Head of R&D
    Retrophin
    Charles Stark at World Orphan Drug Congress USA 2015
    Charles Stark
    Sr. Vice President
    Emmaus Life Sciences, Inc
  • Julie Stoss at World Orphan Drug Congress USA 2015
    Julie Stoss
    Vice President, Government Relations
    Kaiser Permanente
    Emily Stube at World Orphan Drug Congress USA 2015
    Emily Stube
    Director, Medical Writing Product Development and Client Relations
    Premier Research
    Paolo Tagliaferri at World Orphan Drug Congress USA 2015
    Paolo Tagliaferri
    Consultant
    M3 Pharma
  • Mr Henri Termeer at World Orphan Drug Congress USA 2015
    Mr Henri Termeer
    Chief Executive Officer, Former
    Genzyme
    Santa Tumminia at World Orphan Drug Congress USA 2015
    Santa Tumminia
    Special Assistant To The Director
    National Eye Institute N.I.H.
    Mark Vineis at World Orphan Drug Congress USA 2015
    Mark Vineis
    VP, Cardinal Health Specialty Pharmacy
    Cardinal Health
  • Tom Watson at World Orphan Drug Congress USA 2015
    Tom Watson
    Business Development Director
    Clinigen Global Access Programs
    Keith Watts at World Orphan Drug Congress USA 2015
    Keith Watts
    Executive Vice President Strategic Services at One-World
    Oneworld
    Ms Elizabeth White at World Orphan Drug Congress USA 2015
    Ms Elizabeth White
    Assistant Vice President, Rare Disease Commercial Development
    Pfizer
  • Megan O'Boyle at World Orphan Drug Congress USA 2015
    Megan O'Boyle
    Board Member
    Phelan-McDermid Syndrome Foundation
    Chris Adams at World Orphan Drug Congress USA 2015
    Chris Adams
    CEO
    Andarix Pharmaceuticals
    Jan Nielsen at World Orphan Drug Congress USA 2015
    Jan Nielsen
    Division President of Access and Patient Support
    Sonexus Health
  • Ms Nicole Boice at World Orphan Drug Congress USA 2015
    Ms Nicole Boice
    President and Founder
    Global Genes Project
    Sonja L. Banks at World Orphan Drug Congress USA 2015
    Sonja L. Banks
    President and Chief Operating Officer
    Sickle Cell Disease Association of America, Inc.
    Mr Yann LE Cam at World Orphan Drug Congress USA 2015
    Mr Yann LE Cam
    Chief Executive Officer
    EURORDIS
  • Shawn Carbonell at World Orphan Drug Congress USA 2015
    Shawn Carbonell
    Co-Founder, President & CEO
    OncoSynergy
    Jeff Davis at World Orphan Drug Congress USA 2015
    Jeff Davis
    Head of Corporate Development
    Acer Therapeutics
    Mr David Drutz at World Orphan Drug Congress USA 2015
    Mr David Drutz
    Chief Executive Officer
    D.A.R.A. BioSciences Inc
  • Neal M. Farber at World Orphan Drug Congress USA 2015
    Neal M. Farber
    Chief Executive Officer
    Neurohealing Pharmaceuticals Inc
    Dr Jeff Gerschwind at World Orphan Drug Congress USA 2015
    Dr Jeff Gerschwind
    Founder and Chief Executive Officer
    PreScience Labs
    Mr. Greg Gorgas at World Orphan Drug Congress USA 2015
    Mr. Greg Gorgas
    Senior Vice President, Commercial
    Mast Therapeutics Inc
  • Ms Kate Holland at World Orphan Drug Congress USA 2015
    Ms Kate Holland
    VP, Commercial
    Vanda Pharmaceuticals Inc
    David Larwood at World Orphan Drug Congress USA 2015
    David Larwood
    CEO and Founder
    Valley Fever Solutions
    Ms Teresa Leezer at World Orphan Drug Congress USA 2015
    Ms Teresa Leezer
    COO
    Rhinocyte Inc
  • Stacie Lindsey at World Orphan Drug Congress USA 2015
    Stacie Lindsey
    President
    The Cholangiocarcinoma Foundation
    Matt Might at World Orphan Drug Congress USA 2015
    Matt Might
    Associate Professor
    University of Utah
    Allison Moore at World Orphan Drug Congress USA 2015
    Allison Moore
    Director
    Hereditary Neuropathy Foundation
  • Christoffer Nellaker at World Orphan Drug Congress USA 2015
    Christoffer Nellaker
    Group Leader in MRC Functional Genomics Unit
    University of Oxford
    Angi Robinson at World Orphan Drug Congress USA 2015
    Angi Robinson
    Executive Director, Scientific Account Leader
    Premier Research
    Yaffa Rubinstein at World Orphan Drug Congress USA 2015
    Yaffa Rubinstein
    Director, Patient Resources for Clinical and Translational Research
    NIH / NCATS / Office of Rare Diseases Research
  • Peggy Schorr at World Orphan Drug Congress USA 2015
    Peggy Schorr
    VP, US Operations
    OrphanReach
    Ann Tsukamoto at World Orphan Drug Congress USA 2015
    Ann Tsukamoto
    Executive Vice President of Research and Development
    Stemcells Inc
    Mr Mark Varney at World Orphan Drug Congress USA 2015
    Mr Mark Varney
    Chief Executive Officer
    Neurolixis
  • Mr Martin Welschof at World Orphan Drug Congress USA 2015
    Mr Martin Welschof
    Chief Executive Officer
    Opsona Therapeutics Ltd

 

SEE ALL 2016 SPEAKERS

WHO ATTENDS?

Here's a glimpse of who attends World Orphan Drug Congress USA

 

AccessPharmaCon,LLC Aegerion Pharmaceuticals  Aetna Pharmacy Management  Alexion Pharmaceuticals  Andarix Pharmaceuticals  ArmaGen Technologies, Inc.  Ashfield Healthcare   Asklepion Pharmaceuticals LLC  Ax-S Pharma  B.D.C. Venture Capital  BioBlast Pharma Ltd  Biomarin Pharmaceutical Inc.  BioPontis Alliance for Rare Disease Brace Pharma Capital   Brazilian Federal Council of Medicine  Bristol-Myers Squibb  CatalentPharma Solutions   CatalystPharmaceutical Partners  CDER FDA  Clear Pharma  Clementia Pharmaceuticals Inc.   Clinuvel Pharmaceuticals Ltd  Dicerna Pharmaceuticals  DrugDev  EvaluatePharma Ltd   Genoa Pharmaceuticals   Genpharm  GenSight Biologics  Genzyme Corp  Giddi Pharma Co., Ltd.   Idera Pharmeceuticals  IDIS Pharma   Iptechex Pharmalicensing  Jazz Pharmaceuticals, Inc  Juice Pharma Worldwide   KBI Biopharma Inc   Lumos Pharma   M3 Pharma  Marathon Pharmaceuticals LLC   Marinus Pharmaceuticals  Momenta Pharmaceuticals Inc  Opsona Therapeutics Ltd  Optio Biopharma Solutions LLC  Orpharma  Pfizer, Inc  Pharmaceutics International In  Pharmaessentia Corp   Pharnext   Portola Pharmaceuticals , Inc.  Provectus PharmaceuticalsInc   QuayPharma  Quintiles Inc  Raptor Pharmaceuticals Corp  Reata Pharmaceuticals   Recordati S.p.A  Recursion Pharmaceuticals  Retrophin   Sanofi   Savara Pharmaceuticals  Seattle Children's Research Institute   Shire Pharmaceuticals Inc  Taiba Pharma LLC Teva  Threshold Pharmaceuticals Inc   Tolero Pharmaceuticals   Ultragenyx Pharmaceutical Inc.  Valley Fever Solutions   Vanda Pharmaceuticals Inc   Vertex Pharmaceuticals 

 

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2016 Sponsors & Exhibitors

 

Are you looking to meet CEOs, VPs and Directors working in R&D, Business Development, Regulatory Access,
Market Access, Commercial, Marketing and Brand/Product from pharma and biotech?

Then you need to join us at World Orphan Drug Congress USA 2017.

 

 

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SPONSOR OR EXHIBIT NOW

Get Involved

Your customers are here continuously looking for new strategies and technologies to expedite orphan drugs to patients.

 

If you offer a solution or product in the orphan drug space, then you need to be here

 

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