RARE DISEASE DAY AGENDA

Join us for a one-day event featuring:

Patient innovative Technology

One year one from COVID-19, what technologies has shaped the way the RD community has continued to persevere?

o Artificial intelligence, patient platforms, remote monitoring, wearables, Telehealth & digital health

o How to make RD patients more self-sufficient, including use of digital technology

o How do we collect, store and translate this data to compliment drug approval?

Real World Evidence

Continuing from the huge attention gained from November

o Session will involve HTA, payers, industry and patients

Gene Therapy

Key panels on “improving clinical trial design,” “overcoming the hurdles that are impacting patient access to gene therapies” and “ensuring commercial readiness”.