Samantha Parker | Patient Engagement Lead Rare Diseases and Vice Chair of IRDiRC
italfarmaco

Day 2 @ 09:45

Keynote Panel: How are patients involved in every step of the orphan drug development and global access?

-       Patient led solutions to orphan drug development and access bottlenecks

-       How to solve the issue of small patient populations through statistical innovation, regulatory flexibility and patient-centricity

-       Utilising Real-World Data and natural history studies

-       Creating meaningful endpoints that improves patients’ quality of life

Moderator: Samantha Parker, Patient Engagement Lead Rare Diseases and Vice Chair of IRDiRC, italfarmaco

Francesc Palau, Distinguished Investigator, SJD Barcelona Children's Hospital

×

Francesc Palau / Keynote Panel: How are patients involved in every step of the orphan drug development and global access?

Francesc Palau, Distinguished Investigator,
SJD Barcelona Children's Hospital

I am a trained physician with an MD degree from 1982 and a PhD in human genetics from the University of Valencia, completed in 1989. From 1985 to 1988, I underwent pediatric training at the Children's Hospital of the La Fe University Hospital in Valencia, Spain, where I also specialized in...

CloseMore

Frauke Naumann-Winter, Head of Unit, BfArM