The 8th annual World Orphan Drug Congress is the marketplace for orphan drug professionals looking at the complete value chain of orphan drug development, from clinical development and R&D to corporate development and market access.

Being Europe’s largest Orphan Drug Congress, this event will provide a platform for you to showcase your thought leadership and expertise pharma, biotechs, payers, regulators and patient advocates.





Keynote Conference

The Conference offers strategic keynote plenaries, themed tracks and dedicated networking sessions, you have the chance to really tailor the event to the needs of your day-to-day role.

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The Exhibitors have a unique opportunity to put their business products and services in front of potential buyers looking to source the latest technologies in the orphan drugs industry. 

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The pre-congress workshops will offer insights into Pricing, Reimbursement and Market Access Challenges and Accelerating Commercialization of Rare Disease Treatments in the afternoon. 

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Pitch & Partner

Meet and listen to biotech start-ups and investors in our Pitch & Partner track where the most promising companies showcase their orphan drug technology and pipeline.

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  • Mr Henri Termeer at World Orphan Drug Congress
    Mr Henri Termeer
    Chief Executive Officer, Former
  • Rito Bergemann at World Orphan Drug Congress
    Rito Bergemann
    Director, Value Evidence Lead Rare Diseases
  • David Jakouloff at World Orphan Drug Congress
    David Jakouloff
    Global Market Access Director of Oncology and Orphan Disease
  • Hans Schikan at World Orphan Drug Congress
    Hans Schikan
    Former CEO
  • Segolene Ayme at World Orphan Drug Congress
    Segolene Ayme
    Coordinator, Scientific Secretariat
    International Rare Diseases Research Consortium (IRDiRC)
  • Dr Ana Mingorance at World Orphan Drug Congress
    Dr Ana Mingorance
    Scientific Director
    Dravet Syndrome Foundation
  • Mrs Debra Miller at World Orphan Drug Congress
    Mrs Debra Miller
  • Mr Bruce Bloom at World Orphan Drug Congress
    Mr Bruce Bloom
    Cures Within Reach
  • Mr Francois Meyer at World Orphan Drug Congress
    Mr Francois Meyer
    Advisor To The President
    Haute Autorite De Sante
  • Dr Cesar Hernandez at World Orphan Drug Congress
    Dr Cesar Hernandez
    Head of Department of Medicines for Human Use
    Spanish Agency of Medicines and Medical Devices



"It is an important meeting that sheds light on the value patient advocates bring to the development process!"

Global Medicines Development Lead - Rare Diseases, Pfizer




  • Gold Sponsor

    INC Research at World Orphan Drug Congress
  • Platinum Sponsor

    Mapi Group at World Orphan Drug Congress
  • Silver Sponsor

    Medical Marketing Economics at World Orphan Drug Congress
  • Gold Sponsor

    QuintilesIMS at World Orphan Drug Congress
  • Gold Sponsor

    Premier Research at World Orphan Drug Congress
  • Bronze Sponsor

    Komtur Polska sp. z.o.o at World Orphan Drug Congress
  • Bronze Sponsor

    SKC Beratungsgesellschaft at World Orphan Drug Congress


"The information provided was really helpful, I will use it in my daily work. The networking was also great!" 


Director, Value Evidence Lead Rare Diseases, GSK



AANORA Actelion Pharma Ltd Action Duchenne Addmedica Adelphi Values AGSD (UK) AirLiquide AKU Society Alcimed Alexion Pharmaceuticals Allaysis LLC Alliance Life Sciences ALS Liga Belgi Alstrom Syndrome U.K. AMICULUM Anticancer Fund AOP Orphan Pharmaceuticals   AG ArmaGen Technologies, Inc. Atacsia a Fi / Ataxia and Me Ataxia UK aTyr aTyr Pharma  BioBlast Pharma Ltd Biopontis Alliance Blackswan Foundation Brace Pharma Capital Caligor Rx, Inc. Calypso Biotech SA  Capsugel Celgene Centogene AG Charity Association Neurohereditary Diseases Chiesi Farmaceutici Spa Clear Pharma Clinart MENA Clinerion Clinigen Global Access Programs Comradis Concenter BioPharma/Silkim Ltd. Cote Orphan Coulter Partners   Covance UK CRF Health CureDuchenne Cures Within Reach Cydan Development  Cytokinetics Daiichi Sankyo Europe GmbH Dipharma SA Diurnal Limited Dravet Syndrome Foundation Durbin E.C.R.I.N. ECRIN-ERIC ELA Suisse Emmaus Life Sciences, Inc Ergomed EspeRare Euromedica EuropaBio European Huntington's Disease Network EURORDIS  Euticals Spa EvaluatePharma Ltd Evidera F.Hoffmann-La Roche Ltd. Facio Therapies BV Federal Joint Committee F Hoffmann-La Roche French Association Against Friedreich Ataxia Gaucher Disease Russia Genesis Pharma Genetic Alliance U.K. Genkyotex Innovation Sas Genpharm Genzyme Europe BV Gerson Lehrman Group Giddi Pharma GlaxoSmithKline  Greenovation Biotech GmbH Grünenthal GmbH GSK Rare Diseases GW Pharmaceuticals   Haute Autorite De Sante Horizon Pharma Inc I.M.S. Health Idis Managed Access Idis Pharma  Imagine - Institut des Maladies génétiques IMS Health INC Research Index Ventures INSERM  Lysogene M3 Pharma S/A Mapi Consultancy Midas Pharma GmbH Minoryx Therapeutics   MPS Society N.O.R.D. National Institute for Health and Care Excellence National Institutes of Biomedical Innovation, Health and Nutrition National organisation for rare diseases of Serbia  NephCure Kidney International Niemann-Pick UK Novartis