Download: The top 25 most researched rare diseases (PPC)

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Find out which rare diseases have the most advanced clinical trials

This report highlights the top 25 most researched rare diseases.

Diseases were elected based on the following criteria:

Phase 2b or Phase 3 trials – nearest to market
Studies with data updates in 2013
Trials being conducted under FDA surveillance and review
Sponsored by any types of organizations (NIH, Industry, Research Institutions, Government, Academia, Grants Programs, etc.

Want to find out which diseases made the list? Download the report now.