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Download: The top 25 most researched rare diseases (PPC)

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Find out which rare diseases have the most advanced clinical trials

This report highlights the top 25 most researched rare diseases.

Diseases were elected based on the following criteria:

  • Phase 2b or Phase 3 trials – nearest to market
  • Studies with data updates in 2013
  • Trials being conducted under FDA surveillance and review
  • Sponsored by any types of organizations (NIH, Industry, Research Institutions,  Government, Academia, Grants Programs, etc.

Want to find out which diseases made the list? Download the report now.