Developing a mutant protein-stabilizing platform based on a small molecule for orphan diseases
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Developing a mutant protein-stabilizing platform based on a small molecule for orphan diseases

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Zohar Argov of BioBlast Pharma  joined us for World Orphan Drug Congress USA 2015 to present about ' Developing a mutant protein-stabilizing platform based on a small molecule for orphan diseases'
 
Download the presentation now to learn about:
  • Trehalose as a known protein stabilizer and autophagy enhancer
  • Proof of Concept: Trehalose in OPMD
  • Current human studies of Cabaletta

...and much more!

 

Get your copy here ! 

 
To learn more about developing a mutant protein-stabilizing platform , attend  World Orphan Drug Congress USA 2016 September 2-3  in Washington, DC.