Drishti Discoveries


Drishti Discoveries is an early-stage gene therapy company building a platform to develop disease-modifying treatments for rare diseases. Using bioinformatics and machine learning tools we are identifying novel targets and developing drug candidates using our RNA modulator technology against these targets.

Using this approach, we are developing a novel multi-drug gene therapy programme to treat Amyotrophic Lateral Sclerosis. We are also working on a ‘silence and replace’ gene therapy programme to develop mutation independent gene therapy for autosomal dominant Retinitis Pigmentosa.


Get involved with Advanced Therapies Congress


To speak

Jessica Robinson
+44 208 164 3086



To sponsor or exhibit

Ashlea Foster
+44 208 164 3032