2017 Speakers

 

Catherine Acquadro, Global Lead Scientific Presentation and Publications, Mapi Group

Catherine Acquadro at World Orphan Drug Congress

Gail Adinamis, CEO, GlobalCare Clinical Trials

Gail Adinamis at World Orphan Drug Congress

Omar Ali, Former NHS Pharmacy Payer NICE, N.I.C.E. National Institute for Health and Clinical Excellence

Omar Ali at World Orphan Drug Congress

Einar Andreassen, Senior Adviser, Norwegian Medicines Agency

Einar Andreassen at World Orphan Drug Congress

Diego Ardigo, Project Lead, CHIESI Farmaceutici Spa

Diego Ardigo at World Orphan Drug Congress

Dr Segolene Ayme, Founder of Orphanet & Rare Disease Expert in Residence, Inserm

Dr Segolene Ayme at World Orphan Drug Congress

Nuno Barata, SMA Medical Lead for Spain and Portugal, Biogen

Nuno Barata at World Orphan Drug Congress

Michelle Berg, Vice President, Patient Advocacy, Abeona Therapeutics Inc.

Michelle Berg at World Orphan Drug Congress

Stella Blackburn, Vice President, Global Head of Risk Management, Real-World & Late Phase Research, Quintiles

Stella Blackburn at World Orphan Drug Congress

Dr Jane Blyth, Scientific Director, Complete HealthVizion

Dr Jane Blyth at World Orphan Drug Congress

Nadia Bodkin, Founder, EDSers United & VP of Special Markets, MAXIFYLIFE

Nadia Bodkin at World Orphan Drug Congress

Nicole Boice, President and Founder, Global Genes Project

Nicole Boice at World Orphan Drug Congress

Vanessa Boulanger, Director of Research Programs, NORD

Vanessa Boulanger at World Orphan Drug Congress

Michale Bouskila-Chubb, Head of Business Development, Healx Limited

Michale Bouskila-Chubb at World Orphan Drug Congress

Dr Woody Bryan, Senior Vice President, Business Development and Licensing, Sucampo Pharmaceuticals Inc

Dr Woody Bryan at World Orphan Drug Congress

Ivana Cattaneo, Director, Market Access and External Affairs, Novartis

Ivana Cattaneo at World Orphan Drug Congress

Fleur Chandler, Therapy Area Head of Respiratory Value Evidence and Outcomes, GlaxoSmithKline Biologicals

Fleur Chandler at World Orphan Drug Congress

Janis Clayton, Vice President and General Manager for United Kingdom and Ireland, PTC Therapeutics

Janis Clayton at World Orphan Drug Congress

Emily Crossley, Co-founder, Duchenne U.K.

Emily Crossley at World Orphan Drug Congress

Emily Culme-Seymour, External Strategy Manager, Gene Therapy, GSK

Emily Culme-Seymour at World Orphan Drug Congress

David Dasberg, Managing Director, Facio Therapies BV

David Dasberg at World Orphan Drug Congress

Dr Renato Dellamano, President, Medical Marketing Economics

Dr Renato Dellamano at World Orphan Drug Congress

Robert Donnell, Director of Business Development, Durbin

Robert Donnell at World Orphan Drug Congress

Debbie Drell, Director of Membership, National Organization for Rare Disorders

Debbie Drell at World Orphan Drug Congress

Begonya Nafria Escalera, Patient Advocacy Manager, Sant Joan de Déu Children's Hospital

Begonya Nafria Escalera at World Orphan Drug Congress

Lucia Faccio, Head of Research Development Office, Fondazione Telethon

Lucia Faccio at World Orphan Drug Congress

Davide Finocchiaro, Global Pricing & Market Access Specialist, Chiesi

Davide Finocchiaro at World Orphan Drug Congress

Lindsey Foulkes, Marketing Director, ProMetic BioSciences

Lindsey Foulkes at World Orphan Drug Congress

Rob Fox, Head of EU Business Development, IDIS, a Clinigen Company

Rob Fox at World Orphan Drug Congress

Kelly Franchetti, Vice President, Global Patients Insights and Engagement, Mapi Group

Kelly Franchetti at World Orphan Drug Congress

Pedro Franco, Director for Europe for Global Regulatory and Scientific Policy, Merck Serono

Pedro Franco at World Orphan Drug Congress

Ben Gannon, Head of International Government Affairs, Public Policy & Patient Engagement, Vertex Pharmaceuticals

Ben Gannon at World Orphan Drug Congress

Prof. Bobby Gaspar, Professor of Paediatrics & Immunology, UCL Great Ormond Street Institute of Child Health

Prof. Bobby Gaspar at World Orphan Drug Congress

Josie Godfrey, Director at JG Zebra Consulting, Former Associate Director of HST, National Institute for Health and Care Excellence

Josie Godfrey at World Orphan Drug Congress

Rory Graham, Senior Director of Regulatory Affairs, Mapi Group

Rory Graham at World Orphan Drug Congress

Jim Green, President, International Niemann-Pick Disease Aliance

Jim Green at World Orphan Drug Congress

Rachel Haurwitz, President and Chief Executive Officer, Caribou Biosciences

Rachel Haurwitz at World Orphan Drug Congress

Patrick Hopkinson, Executive Director, WWHEOR Markets, Bristol Myers Squibb

Patrick Hopkinson at World Orphan Drug Congress

Dr Jemila Houacine, Associate, Medicxi Ventures

Dr Jemila Houacine at World Orphan Drug Congress

Lynne Hughes, Vice President & Head, Centre of Excellence, Neurology, Therapeutic & Speciality Business Development, IQVIA

Lynne Hughes at World Orphan Drug Congress

Wills Hughes-Wilson, Senior Vice President, Chief Patient Access Officer, Sobi

Wills Hughes-Wilson at World Orphan Drug Congress

Adam Hutchings, Managing Director, Dolon

Adam Hutchings at World Orphan Drug Congress

Williams Hywel, Senior Research Associate, UCL

Williams Hywel at World Orphan Drug Congress

Raul Insa, Founder and Chief Executive Officer, SOM Biotech SL

Raul Insa at World Orphan Drug Congress

Edmund Jessop, Medical Adviser, National Health Service

Edmund Jessop at World Orphan Drug Congress

Edmund Jessop, Medical Adviser, National Health Service

Edmund Jessop at World Orphan Drug Congress

M Ken Kengatharan, Managing Director, Atheneos Capital and Chairman, Armetheon Inc

M Ken Kengatharan at World Orphan Drug Congress

Alastair Kent OBE, Ambassador, Genetic Alliance U.K.

Alastair Kent OBE at World Orphan Drug Congress

Takashi Kei Kishimoto, Chief Science Officer, Selecta Biosciences Inc

Takashi Kei Kishimoto at World Orphan Drug Congress

Maryna Kolochavina, Project Director, Real World & Late Phase, INC Research/inVentiv Health

Maryna Kolochavina at World Orphan Drug Congress

Yann Le Cam, Chief Executive Officer, EURORDIS

Yann Le Cam at World Orphan Drug Congress

Douglas Lundin, Chief Economist, The Dental and Pharmaceutical Benefits Agency T.L.V.

Douglas Lundin at World Orphan Drug Congress

Tiziana Magni, Global Pricing & Market Access Specialist, CHIESI FARMACEUTICI SPA

Tiziana Magni at World Orphan Drug Congress

Dr Will Maier, Chief Scientific Officer, Mapi Group

Dr Will Maier at World Orphan Drug Congress

Ana Mingorance, Principal, Dracaena Consulting

Ana Mingorance at World Orphan Drug Congress

Juliet Moritz, Executive Director, Patient Engagement & Strategic Development, Premier Research

Juliet Moritz at World Orphan Drug Congress

Dr Michael Murphy, Chief Medical & Scientific Officer, Worldwide Clinical Trials

Dr Michael Murphy at World Orphan Drug Congress

Dr Alexander Natz, Secretary General, EUCOPE

Dr Alexander Natz at World Orphan Drug Congress

Sandra Nestler-Parr., Director of Rare Access and Trustee, Alpha 1 UK

Sandra Nestler-Parr. at World Orphan Drug Congress

Judith Ng-Cashin, Chief Scientific Officer, INC Research/inVentiv Health

Judith Ng-Cashin at World Orphan Drug Congress

Mauro Ninci, Head of Medical Affairs for Europe, Genzyme, A Sanofi Company

Mauro Ninci at World Orphan Drug Congress

Alan Nolan, Patient Advocacy, Associate Director, IQVIA

Alan Nolan at World Orphan Drug Congress

Dr Jane Nunn, Head of Operations, Complete HealthVizion

Dr Jane Nunn at World Orphan Drug Congress

Tara Omeara, Vice President of Clinical Development Operations, bluebird bio

Tara Omeara at World Orphan Drug Congress

Mareike Ostertag, Director Regulatory and Science Policy, Novartis Pharma AG

Mareike Ostertag at World Orphan Drug Congress

Francis Pang, VP of Global Market Access, Amicus Therapeutics Inc

Francis Pang at World Orphan Drug Congress

Samantha Parker, SVP patient access, Lysogene

Samantha Parker at World Orphan Drug Congress

Kay Parkinson, CEO & Founder, Alström Syndrome UK and Chief Executive Officer, Cambridge Rare Disease Network

Kay Parkinson at World Orphan Drug Congress

Doug Paul, partner, Medical Marketing Economics

Doug Paul at World Orphan Drug Congress

David Pearce, Executive Vice President of Innovation and Research, Sanford Research

David Pearce at World Orphan Drug Congress

Scott L Pescatore, Oncology General Manager. Rare Diseases, Novartis

Scott L Pescatore at World Orphan Drug Congress

Marco Petschulies, Scientific Advisor, G-BA

Marco Petschulies at World Orphan Drug Congress

Dr Mathew Pletcher, Head of Rare Disease Discovery, Roche

Dr Mathew Pletcher at World Orphan Drug Congress

Krzysztof Potempa, CEO, Braincures

Krzysztof Potempa at World Orphan Drug Congress

Emiliangelo Ratti, Senior Vice President and Head of C.N.S. Therapeutic Area Unit, Takeda Pharmaceuticals International Ltd

Emiliangelo Ratti at World Orphan Drug Congress

Frederic Revah, Chief Executive Officer, Genethon

Frederic Revah at World Orphan Drug Congress

George Reynolds, CCO, Vitro Software

George Reynolds at World Orphan Drug Congress

Diana Ribeiro, Director of Research, Action Duchenne

Diana Ribeiro at World Orphan Drug Congress

Marc Riviere, General Partner, T.V.M. Life Science Management Gmbh

Marc Riviere at World Orphan Drug Congress

Dr Paul Robinson, Executive Director, Patient Perspective, Merck Sharp and Dohme

Dr Paul Robinson at World Orphan Drug Congress

Subhasis Roy, Managing Partner, Sirius Healthcare Partners Gmbh

Subhasis Roy at World Orphan Drug Congress

Dr Juan Ruiz, Chief Medical Officer, Abeona Therapeutics Inc.

Dr Juan Ruiz at World Orphan Drug Congress

Dr Carina Schey, PhD Researcher, University of Groningen

Dr Carina Schey at World Orphan Drug Congress

Scott Schliebner, Vice President, Scientific Affairs, Rare Diseases, PRA Health Sciences

Scott Schliebner at World Orphan Drug Congress

Sophie Schmitz, Partner, Partners4Access

Sophie Schmitz at World Orphan Drug Congress

Matthias P. Schönermark, M.D., Ph.D., Managing Director, SKC Beratungsgesellschaft

Matthias P. Schönermark, M.D., Ph.D. at World Orphan Drug Congress

Raghuram Selvaraju, M.B.A., Managing Director, Senior Analyst, Healthcare, Rodman & Renshaw

Raghuram Selvaraju, M.B.A. at World Orphan Drug Congress

Dr Bruno Sepodes, Chair, Committee for Orphan Medicinal Products (COMP), European Medicines Agency

Dr Bruno Sepodes at World Orphan Drug Congress

Mathieu Simon, Executive Vice President and Chief Operating Officer, Cellectis Therapeutics

Mathieu Simon at World Orphan Drug Congress

Jan Span, Member of the Cross-Committee Task Force on Registries and Senior Clinical Assessor, Medicines Evaluation Board The Netherlands

Jan Span at World Orphan Drug Congress

Dr Andrea Spezzi, Chief Medical Officer and R&D Head, Orchard Therapeutics

Dr Andrea Spezzi at World Orphan Drug Congress

Heide Stirnadel-Farrant, Director Epidemiology, GSK Fellow, Real World Evidence and Epidemiology, GSK

Heide Stirnadel-Farrant at World Orphan Drug Congress

Rick Thompson, Scientific Officer, Findacure

Rick Thompson at World Orphan Drug Congress

Dr Josep Torrent-Farnell, Medicines Department, Catalan Health Service

Dr Josep Torrent-Farnell at World Orphan Drug Congress

Marie Trad, Executive Medical Director, IQVIA

Marie Trad at World Orphan Drug Congress

Sheela Upadhyaya, Assoc. Director Highly Specialised Technologies, National Institute For Health and Care Excellence

Sheela Upadhyaya at World Orphan Drug Congress

Birgitte Volck, Senior Vice President, Head of R&D Rare Diseases, GlaxoSmithKline

Birgitte Volck at World Orphan Drug Congress

Julie Walters, Founder, Raremark

Julie Walters at World Orphan Drug Congress

Rob Walton, Managing Partner, Cello Health Public Affairs

Rob Walton at World Orphan Drug Congress

Christina Waters, CEO and Founder, RARE Science

Christina Waters at World Orphan Drug Congress

Dr Keith Watson, Director of Global Regulatory Affairs and Biologics Strategic Development, AbbVie

Dr Keith Watson at World Orphan Drug Congress

Diane White, Assoc. Dir Development Sciences, Biomarin

Diane White at World Orphan Drug Congress

Pawel Wozniak, Managing Director, Komtur Polska

Pawel Wozniak at World Orphan Drug Congress

Dr Stephen Wright, Chief Medical Officer, GW Pharmaceuticals

Dr Stephen Wright at World Orphan Drug Congress

Stephen Yoo, Chief Medical Officer, ReGenXBio

Stephen Yoo at World Orphan Drug Congress

Martine Zimmermann, Senior Vice President, Head of Global Regulatory Affairs, Alexion Pharmaceuticals

Martine Zimmermann at World Orphan Drug Congress

 

 

 

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Get Involved At World Orphan Drug Congress 2018

 

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Andrew Mears
andrew.mears@terrapinn.com
t/ +44 20 7092 1228

 

 

 

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Wing-Yun Cheung
wing-yun.cheung@terrapinn.com
t/ +44 20 7092 1172

 

 

 

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Issa Mauthoor
issa.mauthoor@terrapinn.com
t/ +44 20 7092 1257