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IQVIA: Orphan Medicines Launch Excellence


Medidata: Rare Disease Clinical Development: Novel Approaches to Overcoming Operational Challenges

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OPEN Health: Succeeding with Star Wars medicine: Translating the science and value of gene therapy to key stakeholders

McKesson: The Key to Commercializing Revolutionary Gene Therapies and Other Orphan Drugs


Optum: Maximize clinical trial enrollment using precision patient finding


 EpidStrategies: Critical Insights into Nonclinical Toxicology and Real World Evidence Essential for a Successful Rare Disease Product Launch

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Precision for Medicine: Optimizing Successful Development of Viral Vector Gene Therapies, Gene Therapy Trials, and Companion Diagnostics

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Centogene: Biomarker Development: CENTOGENE’s approach for rare diseases

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EVERSANA: The Evolving World of Artificial Intelligence: Rare Disease Impact


Parexel: A multi-pronged and customized approach to rare disease clinical trial patient identification and recruitment

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