At our center, we conduct clinical trials for patients with rare diseases, whom otherwise would not have the opportunity to receive any treatment or therapy. There are currently nearly 7000 rare diseases and less than 400 treatments approved by the FDA. With the advent of molecular understanding and discovery, we now have a unique opportunity to identify potential treatment through clinical research.
Our multidisciplinary team is well equipped with years of clinical research experience to carry clinical trials in rare diseases. Our goal is to improve access to investigational therapies for patients with rare diseases.