Keynote Fireside-chat: State of global rare ecosystem – leveraging public private partnerships to further shape the future or rare diseases around the world
Keynote Panel: Advancing cell and gene therapies for rare diseases: What challenges face developers in pre-commercialization and how can all stakeholders work to get therapies to rare patients faster?
Data & Innovation Keynote Panel: Use of Real World Data & AI for rare diseases - where are key areas of opportunity in product development, patient access and commercialization?