Rare Oncology

 

REGISTER NOW
 

Rare Oncology, Monday 11 July 2022

last published: 20/May/22 23:45
BOOK NOW
 

Rare Oncology, Tuesday 12 July 2022

08:30

Organizer Opening Remarks

08:35

Chair Opening Remarks

Emil Kakkis
08:40

Keynote Address: Drug Development in the 21st Century - The use of primary disease activity biomarkers to establish efficacy

Keynote speaker to be announced
Emil Kakkis, Chief Executive Officer, Ultragenyx Pharmaceutical
Shannon Resetich
09:00

Keynote Fireside-chat: State of global rare ecosystem – leveraging public private partnerships to further shape the future or rare diseases around the world

Shannon Resetich, Global Franchise Head, Rare Diseases, Sanofi Genzyme
Fumie Griego, Deputy Director General And Chief Operating Officer, International Federation of Pharmaceutical Manufacturers and Associations
Durhane Wong-Rieger, President & Chief Executive Officer, Canadian Organization for Rare Disorders
09:35

Keynote Address: Reserved for FDA Commissioner

Panel discussion
09:45

Keynote Panel: Advancing cell and gene therapies for rare diseases: What challenges face developers in pre-commercialization and how can all stakeholders work to get therapies to rare patients faster?

Moderator: Izaskun Elorza, Senior Medical Director,, Parexel
Janet Lynch Lambert, Chief Executive Officer, Alliance for Regenerative Medicine
Samarth Kulkarni, Chief Executive Officer, CRISPR Therapeutics
Edward Neilan, Chief Medical and Scientific Officer, National Organization for Rare Disorders (NORD)
Peter Marks, Director, Center For Biologics Evaluation And Research (CBER), U.S. Food and Drug Administration
Paolo Martini, Chief Scientific Officer, Rare Diseases, Moderna Therapeutics
Zhiying Li
Rare Oncology
11:35

Session title to be announced

Zhiying Li, Director, Life Science and Technology, GemPharmatech
Rare Oncology
11:55

Session title to be announced

Sponsored by EMMES
Chowdary Dondapati
Rare Oncology
15:15

Session title to be announced

Chowdary Dondapati, Executive Director, US Head of Diagnostic Marketing, Precision Medicine, BAYER
Panel discussion
Rare Oncology
15:55

PANEL: Leveraging and managing relationships within the rare cancer space

Amanda Nickles Fader, Professor of Gynecology and Obstetrics, Professor of Oncology, Vice-Chair, Gynecologic Surgical Operations,, Johns Hopkins Medical Center
Sanjeev Luther, President & Chief Executive Officer, Rafael pharmaceuticals
Jim Palma, Executive Director, TargetCancer Foundation
Panel discussion
16:50

Data & Innovation Keynote Panel: Use of Real World Data & AI for rare diseases - where are key areas of opportunity in product development, patient access and commercialization?

Sponsored by EVERSANA
Moderator: Rachele Hendricks-Sturrup, Research Director, Real World Evidence, Duke Margolis Center for Health Policy
Christopher Moxham, Chief Scientific Officer, Rarebase, PBC
Samer Ansari, Head of Data, Digital & Technology, Takeda Oncology, Takeda
Scott Snyder, Chief Digital Officer, EVERSANA
last published: 20/May/22 23:45
BOOK NOW

 

 

Get Involved At World Orphan Drug Congress USA

 

To Sponsor Or Exhibit

 
 

Justin Franks
justin.franks@terrapinn.com
t/ +1 914 819 3506

 

 

 

To Speak

 
 

Claire Murphy
claire.murphy@terrapinn.com
t/ +1 646 619 1784

 

 

 

Marketing & Press Opportunities

 
 

Taylor Post 
taylor.post@terrapinn.com
t/ +1 646 619 1785