Rare Disease Advocacy World

 

Rare Disease Advocacy World, Monday 11 July 2022

last published: 20/May/22 23:45
 

Rare Disease Advocacy World, Tuesday 12 July 2022

08:30

Organizer Opening Remarks

08:35

Chair Opening Remarks

Emil Kakkis
08:40

Keynote Address: Drug Development in the 21st Century - The use of primary disease activity biomarkers to establish efficacy

Keynote speaker to be announced
09:35

Keynote Address: Reserved for FDA Commissioner

Flaminia Macchia
Rare Disease Advocacy World
11:15

Persons living with a rare disease, universal health coverage and the promise of health for all

Nick Sireau
Rare Disease Advocacy World
11:55

Public-Private Partnerships to fund ultra-rare disease drug development: case studies and future outlook of innovative funding models

Mary McGowan
Rare Disease Advocacy World
12:15

Ignore No More: Catalyzing action for DEI in advocacy

Natalia Maeva
Rare Disease Advocacy World
15:15

Eastern Europe and the rare disease patient journey

Speaker to be announced
Rare Disease Advocacy World
15:35

Fireside chat: Session title to be announced

Sponsored by PCM Trials
Rare Disease Advocacy World
15:55

PANEL: Session title to be announced

Sanofi Sponsored Panel
last published: 20/May/22 23:45

 

 

Get Involved At World Orphan Drug Congress USA

 

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Justin Franks
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t/ +1 914 819 3506

 

 

 

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Claire Murphy
claire.murphy@terrapinn.com
t/ +1 646 619 1784

 

 

 

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