Pre-Conference Workshops  

The workshops will be showcasing successful case studies, solutions, technologies and platforms that are supporting
pharma, biotechs, and patient groups to achieve commercial, therapeutics success while raising the bar of the standard of
care for rare diseases.
Workshop attendance is restricted to specific profiles, such as pharmaceutical and biotechnology companies,
patient advocacy groups, government and payers.
Your registration may be subject to approval if your organization
does not fit within these profiles.
For questions about workshop attendence, please contact Joseph McManus at 646-619-1774 or
To register for a 3 day pass to attend the workshops, click here >>

Morning Workshops 9AM- 12PM




Workshop 1

Community stewardship -  building a digital home

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Workshop 2

Identifying & engaging patients & clinicians in the rare disease space

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Afternoon Workshops 1PM-5PM

Workshop A 

Predicting and influencing the market potential of orphan drugs and gene therapies

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Workshop B

The expanded access to commercialization journey: operational considerations, interdependencies, strategy & assessment framework

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Contact Joseph McManus at 646-619-1774 or