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World Orphan Drug Congress USA 2024
23 - 25 April
Boston Convention and Exhibition Center,
Boston, MA
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Drug Discovery
Drug Discovery, Wednesday 24 April 2024
last published: 27/Mar/24 15:36
BOOK NOW
Drug Discovery, Thursday 25 April 2024
Drug Discovery
12:00
CureAP-4 drug discovery for ultra-rare CNS disease
Kasey Edwards,
Co-Founder, Community Relations Specialist,
Cure AP-4
Lauren Dougherty,
Chief Operating Officer,
TREND Community
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Day 2 - World Orphan Drug Congress USA 2024 12:00, Drug Discovery
CureAP-4 drug discovery for ultra-rare CNS disease
Kasey Edwards,
Co-Founder, Community Relations Specialist,
Cure AP-4
Lauren Dougherty,
Chief Operating Officer,
TREND Community
Drug Discovery
12:40
In-house drug development for patient advocacy groups
Julia Taravella,
Exececutive Director,
Rare Trait Hope Fund
Drug Discovery
13:00
Interactive Discussion: A new data frontier: Harnessing AI to unlock rare disease insights from social media conversations
Colton Flowers,
NLP Engineer,
TREND Community
Max Flurie,
Senior Data Scientist,
TREND Community
×
Day 2 - World Orphan Drug Congress USA 2024 13:00, Drug Discovery
Interactive Discussion: A new data frontier: Harnessing AI to unlock rare disease insights from social media conversations
Colton Flowers,
NLP Engineer,
TREND Community
Max Flurie,
Senior Data Scientist,
TREND Community
Drug Discovery
15:15
Accelerate and advance drug development: From Patients to approvals
Priya S Chockalingam,
Vice President, Head of Clinical Bioanalytics & Translational Sciences,
Beam Therapeutics
Sarah Gheuens,
Chief Medical Officer, Head of R&D,
Agios Pharmaceuticals
×
Day 2 - World Orphan Drug Congress USA 2024 15:15, Drug Discovery
Accelerate and advance drug development: From Patients to approvals
Priya S Chockalingam,
Vice President, Head of Clinical Bioanalytics & Translational Sciences,
Beam Therapeutics
Sarah Gheuens,
Chief Medical Officer, Head of R&D,
Agios Pharmaceuticals
Drug Discovery
15:35
How caregiver and patient driven medical discoveries impact rare diseases
Patricia Weltin,
Chief Executive Officer,
Beyond the Diagnosis
Annette Maughan,
CEO/Co-Founder,
KBG Foundation
×
Day 2 - World Orphan Drug Congress USA 2024 15:35, Drug Discovery
How caregiver and patient driven medical discoveries impact rare diseases
Patricia Weltin,
Chief Executive Officer,
Beyond the Diagnosis
Annette Maughan,
CEO/Co-Founder,
KBG Foundation
Drug Discovery
15:55
Drug discovery for treating rare disease patients
Moderator:
Justin Yang,
Co-Founder,
Kaibab Health & DMV Bio
Tricha Shivas,
Chief Strategy Officer,
Foundation for Sarcoidosis Research
Cathleen Lutz,
Vice President of the Rare Disease Translational Center,
Jackson Laboratory
Sarah Gheuens,
Chief Medical Officer, Head of R&D,
Agios Pharmaceuticals
Alicia Fiscus,
Head of Global Regulatory Affairs and QA,
Rhythm Pharmaceuticals
×
Day 2 - World Orphan Drug Congress USA 2024 15:55, Drug Discovery
Drug discovery for treating rare disease patients
Moderator:
Justin Yang,
Co-Founder,
Kaibab Health & DMV Bio
Tricha Shivas,
Chief Strategy Officer,
Foundation for Sarcoidosis Research
Cathleen Lutz,
Vice President of the Rare Disease Translational Center,
Jackson Laboratory
Sarah Gheuens,
Chief Medical Officer, Head of R&D,
Agios Pharmaceuticals
Alicia Fiscus,
Head of Global Regulatory Affairs and QA,
Rhythm Pharmaceuticals
last published: 27/Mar/24 15:36
BOOK NOW
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