Diagnosis

 

Diagnosis, Wednesday 24 April 2024

last published: 27/Mar/24 15:36

Diagnosis, Thursday 25 April 2024

Alice McConnell
Diagnosis
12:00

Call to action: Update newborn screening

Panel discussion
Diagnosis
12:20

Newborn screening, sequencing, and the future

Moderator: Christopher Porter, Vice President, Government Affairs and Policy, Travere Therapeutics
Natasha Bonhomme, Chief Strategy Officer, Genetic Alliance, Founder, Expecting Health
Nicole Miller, Vice President, Molecular Diagnostics, Global Medical Affairs, Ultragenyx
Kate Donigan, Senior Director, Science & Regulatory Policy, Global Policy, Government, & Patient Affairs, Sarepta Therapeutics
Tom Defay, Deputy Head Diagnostics Strategy & Development, Alexion Pharmaceuticals
Mary Wang
Diagnosis
15:15

Global collaboration to support timely diagnosis and care for persons living with a rare disease

Mary Wang, Programme Director, Rare Diseases International
Diagnosis
15:35

The Global Commission, a partnership to end the diagnostic odyssey for children with rare diseases

Sponsored by Sanofi

last published: 27/Mar/24 15:36

 

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