Premier Research, a clinical research company, is dedicated to helping biotech, specialty pharma, and device innovators transform life-changing ideas and breakthrough science into new medical treatments. As a global company, Premier Research...
Platinum Sponsor
Platinum Sponsor
Alexion - Diamond Sponsor
Alexion, AstraZeneca Rare Disease, is the group within AstraZeneca focused on rare diseases, created following the 2021 acquisition of Alexion Pharmaceuticals, Inc. As a leader in rare diseases for 30 years, Alexion is focused on serving patients...
Diamond Sponsor
Diamond Sponsor
IPM.ai - Diamond Sponsor
IPM.ai (www.ipm.ai), a part of Real Chemistry, is an Insights as a Service (IaaS) provider that empowers the world’s leading life sciences companies to better understand and improve the lives of patients through the commercialization of precision...
Diamond Sponsor
Diamond Sponsor
Gold Sponsor
Gold Sponsor
Gold Sponsor
Gold Sponsor
Gold Sponsor
Gold Sponsor
Gold Sponsor
Gold Sponsor
Gold Sponsor
ProPharma Group - Gold Sponsor
For the past 20 years, ProPharma has improved the health and wellness of patients by providing advice and expertise that empowers biotech, med device, and pharmaceutical organizations of all sizes to confidently advance scientific breakthroughs and...
Gold Sponsor
Red Nucleus - Gold Sponsor
We provide trusted guidance and long-term partnership to life science clients worldwide by applying in-depth ingenuity coupled with domain knowledge to solve strategic and operational challenges. Our proprietary methodologies, toolkits, and products ...
Gold Sponsor
Gold Sponsor
Gold Sponsor
Gold Sponsor
Silver Sponsor
Bionical Emas - Silver Sponsor
Bionical Emas is the only Contract Research Organization (CRO) to combine Clinical Development, Clinical Trial Supply (CTS) and Early Access Programs (EAP) bringing life-changing medicines to patients around the world.
Their unique integrated...
Silver Sponsor
Silver Sponsor
Silver Sponsor
Silver Sponsor
Silver Sponsor
WEP Clinical - Silver Sponsor
WEP Clinical is a specialist services company that works with sponsors to help patients and physicians gain early access to medicines when no other treatment options are available. We do this by working with companies to set up and manage Expanded...
Silver Sponsor
ActiGraph Inc - Exhibitor
ActiGraph is pioneering the digital transformation of clinical research. We provide end-to-end digital health technology (DHT) solutions by integrating and operationalizing the best hardware, software, and algorithms to generate reliable evidence...
Exhibitor
Exhibitor
Carbogen Amcis Innovations AG - Exhibitor
CARBOGEN AMCIS leverages its world-class chemistry skills to provide seamless drug substance, drug products development and commercialization services for leading pharmaceutical and biopharmaceutical companies. We help customers create a better...
Exhibitor
Exhibitor
Exhibitor
Exhibitor
n-Lorem Foundation - Exhibitor
n-Lorem Foundation is a non-profit established to apply the efficiency, versatility, and specificity of antisense technology to provide experimental antisense oligonucleotide (ASO) medicines to treat nano-rare patients for free, for life. Nano-rare ...
Exhibitor
Exhibitor
Exhibitor
Exhibitor
Rare Disease Research - Exhibitor
As an independent clinical research site, we are 100% dedicated to conducting clinical research, accelerating the development of safe and effective treatments, and providing rare disease patients with access to innovative investigational...
Exhibitor
Rare Patient Voice, LLC - Exhibitor
Rare Patient Voice, LLC provides patients and family caregivers with opportunities to participate in all types of research including market research, health economics outcomes and real-world evidence, user experience/human factors studies, and...
Exhibitor
Exhibitor
Exhibitor
Exhibitor
Exhibitor
Poster
Poster
Poster
Poster
Poster
Poster
Poster
Poster
Poster
Personalize My Medicine - Media Partner
Personalize My Medicine was created to address the growing need for a platform for medical innovation that places people and patients at the center. Our aim is to integrate disciplines and to research, inform, and facilitate advancements in...
Media Partner
Gene Therapy Net - Media Partner
Gene Therapy Net is the information resource for basic and clinical research in gene therapy, and the site serves as a network for the exchange of gene therapy information and breaking news items. Visitors can keep track of the latest scientific...
Media Partner
Pharma Tech Outlook - Media Partner
Pharma Tech Outlook is a monthly publication that has been a pioneer in bringing forth real-world solutions, news, product trends, solutions, and many more to subscribers. The unique learn-from-peers approach is creating a difference since the...
Media Partner
Sanofi - Title Sponsorship
We are an innovative global healthcare company, driven by one purpose: we chase the miracles of science to improve peoples’ lives. For more than 40 years, we have been a pioneer and innovator in rare genetic diseases with high unmet need. Focusing...