Catherine Nester, Senior Vice President HCP and Patient Engagement, Inozyme Pharma
Galina Nesterova, Executive Medical Director- Rare Diseases & Pediatrics, PPD, part of Thermo Fisher Scientific
Victoria Niklas, Chief Medical Officer, Oak Hill Bio
Megan O'Boyle, Patient Engagement Lead, Global Genes, RARE-X
Phillip Okwo, Patient, Sickle Beta Zero Thalassemia
Curtis Oltmans, Chief Legal Officer, Fulcrum
Elizabeth Ottinger, Project Management Group Leader, NIH/NCATS
Lisa Padilla, Chief Executive Officer, Beryl Therapeutics Inc
Jennifer Panagoulias, Chief Regulatory and Compliance Officer, Mahzi Therapeutics
Maria Pandolfo, Senior Vice President, Patient Services, Catalyst Pharmaceutical Partners
Kinnari Patel, President & COO, Rocket Pharma
Alana Paull, Director of Associate, Genentech
Melissa Penn, Director Patient Engagement Research & Development, Bayer
Marissa Penrod, Founder and CEO, Rare Disease Advocate, Mom to son with Duchenne Muscular Dystrophy, Team Joseph
Sue Peschin, President and Chief Executive Officer, Alliance for Aging Research
Steven Peskin, President and Chief Executive Officer, Formerly Executive Medical Director Population Health at Horizon Blue Cross Blue Shield o, SRP Advisors, LLC