2021 Speakers

 

Alba Ancochea Díaz, Chief Executive Officer, Spanish Federation of Rare Disease

Alba Ancochea Díaz | Chief Executive Officer | Spanish Federation of Rare Disease » speaking at Orphan USA

Francis Arickx, Head Of The Directorate Reimbursement Of Medicines And Pharmaceutical Policy, Riziv-Inami

Francis Arickx | Head Of The Directorate Reimbursement Of Medicines And Pharmaceutical Policy | Riziv-Inami » speaking at Orphan USA

Amira Awada, Director, Financial And Legal, Instituto Vidas Raras

Amira Awada | Director, Financial And Legal | Instituto Vidas Raras » speaking at Orphan USA

Luc Boileau, Chairman And Chief Executive Officer, INESSS

Luc Boileau | Chairman And Chief Executive Officer | INESSS » speaking at Orphan USA

Philip J Brooks, Program Director, National Center For Advancing Translational Sciences - Ncats, National Institutes of Health (NIH)

Philip J Brooks | Program Director, National Center For Advancing Translational Sciences - Ncats | National Institutes of Health (NIH) » speaking at Orphan USA

Frederic Chereau, Chief Executive Officer, LogicBio Therapeutics

Frederic Chereau | Chief Executive Officer | LogicBio Therapeutics » speaking at Orphan USA

Nimi Chhina, Head, Global R&D and Regulatory Policy, BioMarin Pharmaceutical Inc.

Nimi Chhina | Head, Global R&D and Regulatory Policy | BioMarin Pharmaceutical Inc. » speaking at Orphan USA

Alexander Cole, Executive Director, Global Head Epidemiology, Alexion

Alexander Cole | Executive Director, Global Head Epidemiology | Alexion » speaking at Orphan USA

Avril Daly, Chief Executive Officer, Retina International

Avril Daly | Chief Executive Officer | Retina International » speaking at Orphan USA

Graham Dempsey, Chief Scientific Officer, Q-State Biosciences

Graham Dempsey | Chief Scientific Officer | Q-State Biosciences » speaking at Orphan USA

Scott Dorfman, CEO, Odylia Therapeutics

Scott Dorfman | CEO | Odylia Therapeutics » speaking at Orphan USA

Sonja Durinck, President, Canadian Pituitary Patient Network

Sonja Durinck | President | Canadian Pituitary Patient Network » speaking at Orphan USA

Stacey Frisk, Global Policy, Government & Patient Affairs, Sarepta Therapeutics

Stacey Frisk | Global Policy, Government & Patient Affairs | Sarepta Therapeutics » speaking at Orphan USA

Simon Frost, CEO, Tiber Capital

Simon Frost | CEO | Tiber Capital » speaking at Orphan USA

Melissa Haendel, Director, Center for Data to Health, Professor, Medical Informatics & Clinical Epidemiology, Translational Data Science, Oregon Health & Science University

Melissa Haendel | Director, Center for Data to Health, Professor, Medical Informatics & Clinical Epidemiology, Translational Data Science | Oregon Health & Science University » speaking at Orphan USA

Christina Hartman, Senior Director of Advocacy, The Assistance Fund

Christina Hartman | Senior Director of Advocacy | The Assistance Fund » speaking at Orphan USA

Rachele Hendricks-Sturrup, Health Policy Counsel, Future of Privacy Fprum

Rachele Hendricks-Sturrup | Health Policy Counsel | Future of Privacy Fprum » speaking at Orphan USA

Vikram Karnani, Executive Vice President, President, International, Horizon Therapeutics

Vikram Karnani | Executive Vice President, President, International | Horizon Therapeutics » speaking at Orphan USA

Doug Kerr, Chief Medial Officer, Generation Bio

Doug Kerr | Chief Medial Officer | Generation Bio » speaking at Orphan USA

Sean Khozin, Global Head Of Data Strategy, Johnson & Johnson

Sean Khozin | Global Head Of Data Strategy | Johnson & Johnson » speaking at Orphan USA

Augusta Elizabeth Koroma, Chief Executive Officer, Sickle Cell Intervention U.K

Augusta Elizabeth Koroma | Chief Executive Officer | Sickle Cell Intervention U.K » speaking at Orphan USA

David Lennon, President, Novartis Gene Therapies

David Lennon | President | Novartis Gene Therapies » speaking at Orphan USA

Clement Leong, Chief Executive Officer And Managing Director, Stamford Pharmaceuticals

Clement Leong | Chief Executive Officer And Managing Director | Stamford Pharmaceuticals » speaking at Orphan USA

Nanxin (Nick) Li, Senior Director and Head, Health Economics and Outcomes Research (HEOR), uniQure

Nanxin (Nick) Li | Senior Director and Head, Health Economics and Outcomes Research (HEOR) | uniQure » speaking at Orphan USA

Andrew Lo, Charles E. and Susan T. Harris Professor, Massachusetts Institute of Technology (MIT)

Andrew Lo | Charles E. and Susan T. Harris Professor | Massachusetts Institute of Technology (MIT) » speaking at Orphan USA

Geoff Mackay, President And Chief Executive Officer, AVROBIO

Geoff Mackay | President And Chief Executive Officer | AVROBIO » speaking at Orphan USA

Craig Malzahn, VP of Manufacturing and Supply, REGENX Bioscience

Craig Malzahn | VP of Manufacturing and Supply | REGENX Bioscience » speaking at Orphan USA

Peter Marks, Director, Center For Biologics Evaluation And Research (CBER), U.S. Food and Drug Administration

Peter Marks | Director, Center For Biologics Evaluation And Research (CBER) | U.S. Food and Drug Administration » speaking at Orphan USA

Nancy Mendelson, Chief Medical Officer, Complex Health Solutions, UnitedHealthcare

Nancy Mendelson | Chief Medical Officer, Complex Health Solutions | UnitedHealthcare » speaking at Orphan USA

Amanda Moore, Chief Executive Officer, Angelman Syndrome Foundation

Amanda Moore | Chief Executive Officer | Angelman Syndrome Foundation » speaking at Orphan USA

Alexander Natz, Secretary General, European Confederation of Pharmaceutical Entrepreneurs (Belgium)

Alexander Natz | Secretary General | European Confederation of Pharmaceutical Entrepreneurs (Belgium) » speaking at Orphan USA

Steven Peskin, Executive Medical Director Population Health, Horizon Blue Cross Blue Shield - New Jersey

Steven Peskin | Executive Medical Director Population Health | Horizon Blue Cross Blue Shield - New Jersey » speaking at Orphan USA

Avital Pushett, Head of ALS Clinical Program, NeuroSense Therapeutics

Avital Pushett | Head of ALS Clinical Program | NeuroSense Therapeutics » speaking at Orphan USA

Sanuj Ravindran, Chief Executive Officer, PellePharm, Inc.

Sanuj Ravindran | Chief Executive Officer | PellePharm, Inc. » speaking at Orphan USA

Tamanna Roshan Lal, Co-Director, Lysosomal Storage and Treatment Program, Metabolic Geneticist,, Rare Disease Institut, Childrens National Medical Center

Tamanna Roshan Lal | Co-Director, Lysosomal Storage and Treatment Program, Metabolic Geneticist, | Rare Disease Institut, Childrens National Medical Center » speaking at Orphan USA

Ashish Sagrolikar, Chief Commercial Officer, Zogenix Inc.

Ashish Sagrolikar | Chief Commercial Officer | Zogenix Inc. » speaking at Orphan USA

Joel Schneider, Chief Technology Officer, Solid Biosciences

Joel Schneider | Chief Technology Officer | Solid Biosciences » speaking at Orphan USA

Panna Sharma, President And Chief Executive Officer, Lantern Pharma

Panna Sharma | President And Chief Executive Officer | Lantern Pharma » speaking at Orphan USA

German Suarez, Chief Executive Officer and President, GENBIE SAS

German Suarez | Chief Executive Officer and President | GENBIE SAS » speaking at Orphan USA

Ulrich Thienel, Chief Executive Officer, ReAlta Life Sciences

Ulrich Thienel | Chief Executive Officer | ReAlta Life Sciences » speaking at Orphan USA

Bryce Waldman, Manager, Strategy And Market Development, Rady Children's Institute for Genomic Medicine

Bryce Waldman | Manager, Strategy And Market Development | Rady Children's Institute for Genomic Medicine » speaking at Orphan USA

John Walter, Chief Executive Officer, Foundation For Prader Willi Research

John Walter | Chief Executive Officer | Foundation For Prader Willi Research » speaking at Orphan USA

Brian Wamhoff, Chief Operating Officer, HemoShear Therapeutics LLC

Brian Wamhoff | Chief Operating Officer | HemoShear Therapeutics LLC » speaking at Orphan USA

David Young, Chief Executive Officer, Processa Pharmaceuticals, Inc.

David Young | Chief Executive Officer | Processa Pharmaceuticals, Inc. » speaking at Orphan USA

 

 

 

 

Get Involved At World Orphan Drug Congress USA

 

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