2021 Speakers

 

Derek Adams, Chief Operating Officer, PlateletBio

Derek Adams | Chief Operating Officer | PlateletBio » speaking at Orphan USA

Karen Aiach, Chief Executive Officer, Lysogene

Karen Aiach | Chief Executive Officer | Lysogene » speaking at Orphan USA

Bonnie Albright, Director Portfolio Oversight, Labcorp Drug Development

Bonnie Albright | Director Portfolio Oversight | Labcorp Drug Development » speaking at Orphan USA

Paul Aliu, Head Global Governance Office, Novartis Chief Medical Office (CMO), Novartis

Paul Aliu | Head Global Governance Office, Novartis Chief Medical Office (CMO) | Novartis » speaking at Orphan USA

Alba Ancochea Díaz, Chief Executive Officer, Spanish Federation of Rare Disease

Alba Ancochea Díaz | Chief Executive Officer | Spanish Federation of Rare Disease » speaking at Orphan USA

Francis Arickx, Head Of The Directorate Reimbursement Of Medicines And Pharmaceutical Policy, Riziv-Inami

Francis Arickx | Head Of The Directorate Reimbursement Of Medicines And Pharmaceutical Policy | Riziv-Inami » speaking at Orphan USA

Georgianne Arnold, Professor of Pediatrics, University of Pittsburgh, President, Society for Inherited Metabolic Disorders, Society for Inherited Metabolic Disorders

Georgianne Arnold | Professor of Pediatrics, University of Pittsburgh, President, Society for Inherited Metabolic Disorders | Society for Inherited Metabolic Disorders » speaking at Orphan USA

Amira Awada, Director, Financial And Legal, Instituto Vidas Raras

Amira Awada | Director, Financial And Legal | Instituto Vidas Raras » speaking at Orphan USA

Shirley Bachman, Vice President Of Market Access, Alnylam Pharmaceuticals

Shirley Bachman | Vice President Of Market Access | Alnylam Pharmaceuticals » speaking at Orphan USA

Lakiea Bailey, Chief Executive Officer, Sickle Cell Consortium

Lakiea Bailey | Chief Executive Officer | Sickle Cell Consortium » speaking at Orphan USA

Alison Bateman-House, Assistant Professor, Division of Medical Ethics,, NYU Grossman School of Medicine

Alison Bateman-House | Assistant Professor, Division of Medical Ethics, | NYU Grossman School of Medicine » speaking at Orphan USA

Peter Bauer, Chief Genomic Officer, CENTOGENE

Peter Bauer | Chief Genomic Officer | CENTOGENE » speaking at Orphan USA

Wendy Benson, Vice President Of Strategic Initiatives, Rady Children's Institute for Genomic Medicine

Wendy Benson | Vice President Of Strategic Initiatives | Rady Children's Institute for Genomic Medicine » speaking at Orphan USA

Michelle Berg, President, Aldevron

Michelle Berg | President | Aldevron » speaking at Orphan USA

Scott Bergeron, Partner, iTakeControl, a Red Nucleus Company

Scott Bergeron | Partner | iTakeControl, a Red Nucleus Company » speaking at Orphan USA

David Bettoun, Vice President Discovery and Non-Clinical R&D, Larimar Therapeutics

David Bettoun | Vice President Discovery and Non-Clinical R&D | Larimar Therapeutics » speaking at Orphan USA

Heidi Bjornson-Pennell, Patient Engagement Strategist, Chan Zuckerberg Initiative

Heidi Bjornson-Pennell | Patient Engagement Strategist | Chan Zuckerberg Initiative » speaking at Orphan USA

Nadia Bodkin, OLM DEI Expert, Rare Advocacy Movement

Nadia Bodkin | OLM DEI Expert | Rare Advocacy Movement » speaking at Orphan USA

Luc Boileau, Chief Executive Officer, INESSS

Luc Boileau | Chief Executive Officer | INESSS » speaking at Orphan USA

Pablo Botas, Head Of Science, Foundation 29

Pablo Botas | Head Of Science | Foundation 29 » speaking at Orphan USA

Lisa Boyette, Senior Director of Medical Affairs, Recursion

Lisa Boyette | Senior Director of Medical Affairs | Recursion » speaking at Orphan USA

Michael Boyle, President and Chief Executive Officer, Cystic Fibrosis Foundation

Michael Boyle | President and Chief Executive Officer | Cystic Fibrosis Foundation » speaking at Orphan USA

Jennifer Braswell, Executive Director, ARM Foundation for Cell and Gene Medicine

Jennifer Braswell | Executive Director | ARM Foundation for Cell and Gene Medicine » speaking at Orphan USA

Philip J Brooks, Program Director, National Center For Advancing Translational Sciences - Ncats, National Institutes of Health (NIH)

Philip J Brooks | Program Director, National Center For Advancing Translational Sciences - Ncats | National Institutes of Health (NIH) » speaking at Orphan USA

Rob Brown, Vice President, PharmaCord

Rob Brown | Vice President | PharmaCord » speaking at Orphan USA

Stephanie Brown, Senior Vice President and Business Unit Head, Rare Disease – North America, Ipsen

Stephanie Brown | Senior Vice President and Business Unit Head, Rare Disease – North America | Ipsen » speaking at Orphan USA

Anna Bucsics, Project Advisor, Mechanism of Coordinated Access to orphan medicinal products (MoCA)

Anna Bucsics | Project Advisor | Mechanism of Coordinated Access to orphan medicinal products (MoCA) » speaking at Orphan USA

Jessica Carmen, US Business Development Advisor, Oxford Biomedica

Jessica Carmen | US Business Development Advisor | Oxford Biomedica » speaking at Orphan USA

Lovena Chaput, SVP, Americas, Commercial, Audentes

Lovena Chaput | SVP, Americas, Commercial | Audentes » speaking at Orphan USA

Frederic Chereau, Chief Executive Officer, LogicBio Therapeutics

Frederic Chereau | Chief Executive Officer | LogicBio Therapeutics » speaking at Orphan USA

Nimi Chhina, Head, Global R&D and Regulatory Policy, BioMarin Pharmaceutical Inc.

Nimi Chhina | Head, Global R&D and Regulatory Policy | BioMarin Pharmaceutical Inc. » speaking at Orphan USA

Susan Chittooran, Patient Enagement Project Coordinator, U.S. Food and Drug Administration

Susan Chittooran | Patient Enagement Project Coordinator | U.S. Food and Drug Administration » speaking at Orphan USA

Christopher Chute, Professor Of Health Informatics, Johns Hopkins University

Christopher Chute | Professor Of Health Informatics | Johns Hopkins University » speaking at Orphan USA

Alexander Cole, Executive Director, Global Head Epidemiology, alexion

Alexander Cole | Executive Director, Global Head Epidemiology | alexion » speaking at Orphan USA

Jess Conicelli, Executive Director, Strategic Development, Rare, Orphan, & Pediatric Diseases, Synteract

Jess Conicelli | Executive Director, Strategic Development, Rare, Orphan, & Pediatric Diseases | Synteract » speaking at Orphan USA

Anne Cropp, Chief Scientific Officer, Early Access Care

Anne Cropp | Chief Scientific Officer | Early Access Care » speaking at Orphan USA

John F. Crowley, Chairman and Chief Executive Officer, Amicus Therapeutics Inc

John F. Crowley | Chairman and Chief Executive Officer | Amicus Therapeutics Inc » speaking at Orphan USA

Steven Cummings, Executive Director, San Francisco Coordinating Center, California Pacific Medical Center Research Institute

Steven Cummings | Executive Director, San Francisco Coordinating Center | California Pacific Medical Center Research Institute » speaking at Orphan USA

Daniel Curran, Head, Rare Genetics & Hematology Therapeutic Area, Takeda

Daniel Curran | Head, Rare Genetics & Hematology Therapeutic Area | Takeda » speaking at Orphan USA

Avril Daly, Chief Executive Officer, Retina International

Avril Daly | Chief Executive Officer | Retina International » speaking at Orphan USA

Eric Michael David, Chief Executive Officer, BridgeBio-Gene Therapy

Eric Michael David | Chief Executive Officer | BridgeBio-Gene Therapy » speaking at Orphan USA

Graham Dempsey, Chief Scientific Officer, Q-State Biosciences

Graham Dempsey | Chief Scientific Officer | Q-State Biosciences » speaking at Orphan USA

Rebecca Derwin, Director, Portfolio And Commercial Analytics, Regenxbio Inc

Rebecca Derwin | Director, Portfolio And Commercial Analytics | Regenxbio Inc » speaking at Orphan USA

Dan Donovan, Founder & CEO, rareLife solutions

Dan Donovan | Founder & CEO | rareLife solutions » speaking at Orphan USA

Scott Dorfman, CEO, Odylia Therapeutics

Scott Dorfman | CEO | Odylia Therapeutics » speaking at Orphan USA

Debbie Drell, Director Of Membership, National Organization for Rare Disorders (NORD)

Debbie Drell | Director Of Membership | National Organization for Rare Disorders (NORD) » speaking at Orphan USA

Rafael Escandon, PGTME Member, Clinical Development Consultant, Former Senior VP Medical Affairs, Policy and Patient Engagement, BridgeBio-Gene Therapy

Rafael Escandon | PGTME Member, Clinical Development Consultant,  Former Senior VP Medical Affairs, Policy and Patient Engagement | BridgeBio-Gene Therapy » speaking at Orphan USA

Elizabeth Evans, COO, Vaccinex

Elizabeth Evans | COO | Vaccinex » speaking at Orphan USA

Jorge Faccinetti, Chairman and Chief Executive Officer, Pituitary World News

Jorge Faccinetti | Chairman and Chief Executive Officer | Pituitary World News » speaking at Orphan USA

Amanda Finlayson, Director of Patient Strategy, ClinEdge

Amanda Finlayson | Director of Patient Strategy | ClinEdge » speaking at Orphan USA

Chad Forinash, Senior Director, Pharmacy, PharmaCord

Chad Forinash | Senior Director, Pharmacy | PharmaCord » speaking at Orphan USA

Anthony Frangie, Vice President, US LSD-ENDO Franchise Head, Takeda

Anthony Frangie | Vice President, US LSD-ENDO Franchise Head | Takeda » speaking at Orphan USA

Stacey Frisk, Global Policy, Government & Patient Affairs, Sarepta Therapeutics

Stacey Frisk | Global Policy, Government & Patient Affairs | Sarepta Therapeutics » speaking at Orphan USA

Simon Frost, CEO, Tiber Capital

Simon Frost | CEO | Tiber Capital » speaking at Orphan USA

Michela Gabaldo, Head Of Alliance Management, Fondazione Telethon

Michela Gabaldo | Head Of Alliance Management | Fondazione Telethon » speaking at Orphan USA

Kristin Gabor, Research Scientist, Rho, Inc

Kristin Gabor | Research Scientist | Rho, Inc » speaking at Orphan USA

Pushkal Garg, Chief Medical Officer, Alnylam Pharmaceuticals

Pushkal Garg | Chief Medical Officer | Alnylam Pharmaceuticals » speaking at Orphan USA

Pamela Gavin, Chief Strategy Officer, National Organization for Rare Disorders (NORD)

Pamela Gavin | Chief Strategy Officer | National Organization for Rare Disorders (NORD) » speaking at Orphan USA

Azadeh Golipour, SVP, CMC and Manufacturing, AVROBIO

Azadeh Golipour | SVP, CMC and Manufacturing | AVROBIO » speaking at Orphan USA

Scott Gray, CEO, Clincierge

Scott Gray | CEO | Clincierge » speaking at Orphan USA

Suzanne Greenwood, CCO, EVERSANA

Suzanne Greenwood | CCO | EVERSANA » speaking at Orphan USA

Russell Griffith, DCT Manager, Syneos Health

Russell Griffith | DCT Manager | Syneos Health » speaking at Orphan USA

Melissa Haendel, Director, Center for Data to Health, Professor, Medical Informatics & Clinical Epidemiology, Translational Data Science, Oregon Health & Science University

Melissa Haendel | Director, Center for Data to Health, Professor, Medical Informatics & Clinical Epidemiology, Translational Data Science | Oregon Health & Science University » speaking at Orphan USA

Alix Hall, Managing Director, Policy, Patient Support, and Industry Liaison, The Isaac Foundation

Alix Hall | Managing Director, Policy, Patient Support, and Industry Liaison | The Isaac Foundation » speaking at Orphan USA

Christina Hartman, Senior Director of Advocacy, The Assistance Fund

Christina Hartman | Senior Director of Advocacy | The Assistance Fund » speaking at Orphan USA

Shane Hegarty, Chief Scientific Officer & Co-Founder, AXONIS Therapeutics

Shane Hegarty | Chief Scientific Officer & Co-Founder | AXONIS Therapeutics » speaking at Orphan USA

Mo Heidaran, Vice President, Regulatory Consulting,, Parexel International

Mo Heidaran | Vice President, Regulatory Consulting, | Parexel International » speaking at Orphan USA

Rachele Hendricks-Sturrup, Research Director, Real World Evidence, Duke Margolis Center for Health Policy

Rachele Hendricks-Sturrup | Research Director, Real World Evidence | Duke Margolis Center for Health Policy » speaking at Orphan USA

Andy Holt, Vice President Of Business Development and Manufacturing, Asklepios BioPharmaceutical Inc

Andy Holt | Vice President Of Business Development and Manufacturing | Asklepios BioPharmaceutical Inc » speaking at Orphan USA

Gillian Hooker, Past-President,, National Society of Genetic Counselors

Gillian Hooker | Past-President, | National Society of Genetic Counselors » speaking at Orphan USA

Amy Hutnik, General Manager, Agency, Advisory & Evidence Services,, EVERSANA

Amy Hutnik | General Manager, Agency, Advisory & Evidence Services, | EVERSANA » speaking at Orphan USA

Rachelle Jacques, Chief Executive Officer, Enzyvant

Rachelle Jacques | Chief Executive Officer | Enzyvant » speaking at Orphan USA

Amanda Jezek, Senior Vice President, Public Policy And Government Relations, Infectious Diseases Society of America

Amanda Jezek | Senior Vice President, Public Policy And Government Relations | Infectious Diseases Society of America » speaking at Orphan USA

Audrey Jia, President, Children's Rare Disease Organization

Audrey Jia | President | Children's Rare Disease Organization » speaking at Orphan USA

Chris Jones, Partner, iTakeControl, a Red Nucleus Company

Chris Jones | Partner | iTakeControl, a Red Nucleus Company » speaking at Orphan USA

Gurdyal Kalsi, Chief Medical Officer, Asklepion Pharmaceuticals

Gurdyal Kalsi | Chief Medical Officer | Asklepion Pharmaceuticals » speaking at Orphan USA

Rashida Karmali, CEO, Tactical Therapeutics Inc

Rashida Karmali | CEO | Tactical Therapeutics Inc » speaking at Orphan USA

Vikram Karnani, Executive Vice President, President, International, Horizon Therapeutics

Vikram Karnani | Executive Vice President, President, International | Horizon Therapeutics » speaking at Orphan USA

Lucas Kempf, Vice President, Technical, Parexel

Lucas Kempf | Vice President, Technical | Parexel » speaking at Orphan USA

Ken Kengatharan, Managing Partner, Atheneos Ventures

Ken Kengatharan | Managing Partner | Atheneos Ventures » speaking at Orphan USA

Annie Kennedy, Chief Policy And Advocacy, EveryLife Foundation for Rare Diseases

Annie Kennedy | Chief Policy And Advocacy | EveryLife Foundation for Rare Diseases » speaking at Orphan USA

Doug Kerr, Chief Medial Officer, Generation Bio

Doug Kerr | Chief Medial Officer | Generation Bio » speaking at Orphan USA

Faisal Khan, Executive Director Of Advanced Analytics And Artificial Intelligence, AstraZeneca

Faisal Khan | Executive Director Of Advanced Analytics And Artificial Intelligence | AstraZeneca » speaking at Orphan USA

Sean Khozin, Global Head Of Data Strategy, Johnson & Johnson

Sean Khozin | Global Head Of Data Strategy | Johnson & Johnson » speaking at Orphan USA

Maria Kirsch, SR VP & Head of Patient Services Operations, EVERSANA

Maria Kirsch | SR VP & Head of Patient Services Operations | EVERSANA » speaking at Orphan USA

Augusta Elizabeth Koroma, Chief Executive Officer, Sickle Cell Intervention U.K

Augusta Elizabeth Koroma | Chief Executive Officer | Sickle Cell Intervention U.K » speaking at Orphan USA

Karen Kozarsky, Chief Scientific Officer, SwanBio Therapeutics

Karen Kozarsky | Chief Scientific Officer | SwanBio Therapeutics » speaking at Orphan USA

Katherine Krieger, Director, Client Services, VOZ Advisors

Katherine Krieger | Director, Client Services | VOZ Advisors » speaking at Orphan USA

Akshay Kumar, Partner, Partners4Access

Akshay Kumar | Partner | Partners4Access » speaking at Orphan USA

Janet Lynch Lambert, Chief Executive Officer, Alliance for Regenerative Medicine

Janet Lynch Lambert | Chief Executive Officer | Alliance for Regenerative Medicine » speaking at Orphan USA

David Lapidus, President, Lapidus Data

David Lapidus | President | Lapidus Data » speaking at Orphan USA

Yann Le Cam, Chief Executive Officer, EURORDIS

Yann Le Cam | Chief Executive Officer | EURORDIS » speaking at Orphan USA

Michael Lehmicke, Sr. Director, Science and Industry Affairs, Alliance for Regenerative Medicine

Michael Lehmicke | Sr. Director, Science and Industry Affairs | Alliance for Regenerative Medicine » speaking at Orphan USA

Clement Leong, Chief Executive Officer And Managing Director, Stamford Pharmaceuticals

Clement Leong | Chief Executive Officer And Managing Director | Stamford Pharmaceuticals » speaking at Orphan USA

Jeremy Levin, Chairman and Chief Executive Officer, Chairman, BIO, Ovid Therapeutics

Jeremy Levin | Chairman and Chief Executive Officer, Chairman, BIO | Ovid Therapeutics » speaking at Orphan USA

Jaclyn Lizotte, VP, PCM TRIALS

Jaclyn Lizotte | VP | PCM TRIALS » speaking at Orphan USA

Sanjeev Luther, President & CEO, Rafael Pharmaceuticals

Sanjeev Luther | President & CEO | Rafael Pharmaceuticals » speaking at Orphan USA

Flaminia Macchia, Executive Director, Rare Diseases International

Flaminia Macchia | Executive Director | Rare Diseases International » speaking at Orphan USA

Geoff Mackay, President And Chief Executive Officer, AVROBIO

Geoff Mackay | President And Chief Executive Officer | AVROBIO » speaking at Orphan USA

Jack Mahler, Chief Investment Officer, Cystic Fibrosis Foundation

Jack Mahler | Chief Investment Officer | Cystic Fibrosis Foundation » speaking at Orphan USA

Craig Malzahn, VP of Manufacturing and Supply, REGENX Bioscience

Craig Malzahn | VP of Manufacturing and Supply | REGENX Bioscience » speaking at Orphan USA

Peter Marks, Director, Center For Biologics Evaluation And Research (CBER), U.S. Food and Drug Administration

Peter Marks | Director, Center For Biologics Evaluation And Research (CBER) | U.S. Food and Drug Administration » speaking at Orphan USA

Janet Maynard, Director, Food and Drug Administration

Janet Maynard | Director | Food and Drug Administration » speaking at Orphan USA

Sean McAuliffe, Chief Commercial Officer, Taysha Gene Therapies

Sean McAuliffe | Chief Commercial Officer | Taysha Gene Therapies » speaking at Orphan USA

Mike Mcbrierty, Director, State Public Policy And Government Affairs, Biogen

Mike Mcbrierty | Director, State Public Policy And Government Affairs | Biogen » speaking at Orphan USA

Emily McGinnis, Chief Patient Officer and Head of Government Affairs, Taysha Gene Therapies

Emily McGinnis | Chief Patient Officer and Head of Government Affairs | Taysha Gene Therapies » speaking at Orphan USA

Jenn Mcnary, Founder, One Rare

Jenn Mcnary | Founder | One Rare » speaking at Orphan USA

Nancy Mendelson, Chief Medical Officer, Complex Health Solutions, UnitedHealthcare

Nancy Mendelson | Chief Medical Officer, Complex Health Solutions | UnitedHealthcare » speaking at Orphan USA

Timothy Miller, President, CEO, and Co-Founder, Forge Biologics

Timothy Miller | President, CEO, and Co-Founder | Forge Biologics » speaking at Orphan USA

Boris Minev, President, Medical & Scientific Affairs,, Calidi Biotherapeutics

Boris Minev | President, Medical & Scientific Affairs, | Calidi Biotherapeutics » speaking at Orphan USA

Ali Mohamadi, Executive Director, Patient and Medical Alliances, Vertex Pharmaceuticals

Ali Mohamadi | Executive Director, Patient and Medical Alliances | Vertex Pharmaceuticals » speaking at Orphan USA

Amanda Moore, CEO, Angelman Syndrome Foundation

Amanda Moore | CEO | Angelman Syndrome Foundation » speaking at Orphan USA

Shephard Mpofu, Chief Medical Officer, Novartis Gene Therapies

Shephard Mpofu | Chief Medical Officer | Novartis Gene Therapies » speaking at Orphan USA

James Mullen, Chairman, President, Chief Executive Officer,, Editas Medicine

James Mullen | Chairman, President, Chief Executive Officer, | Editas Medicine » speaking at Orphan USA

Claire Murphy, Production Director, Terrapinn

Claire Murphy | Production Director | Terrapinn » speaking at Orphan USA

Alexander Natz, Secretary General, European Confederation of Pharmaceutical Entrepreneurs (Belgium)

Alexander Natz | Secretary General | European Confederation of Pharmaceutical Entrepreneurs (Belgium) » speaking at Orphan USA

Amy Nicole Nayar, VP US Patient Advocacy and Government Affairs, Novartis Gene Therapies

Amy Nicole Nayar | VP US Patient Advocacy and Government Affairs | Novartis Gene Therapies » speaking at Orphan USA

Edward Neilan, Chief Medical and Scientific Officer, National Organization for Rare Disorders (NORD)

Edward Neilan | Chief Medical and Scientific Officer | National Organization for Rare Disorders (NORD) » speaking at Orphan USA

Lesli Nordstrom, Director of Marketing and Communications, National Organization for Rare Disorders (NORD)

Lesli Nordstrom | Director of Marketing and Communications | National Organization for Rare Disorders (NORD) » speaking at Orphan USA

Phung Osborn, Exec Director US Payers Cell Therapy, Iovance

Phung Osborn | Exec Director US Payers Cell Therapy | Iovance » speaking at Orphan USA

Jeff Parish, Head of North America, Partners4Access

Jeff Parish | Head of North America | Partners4Access » speaking at Orphan USA

Lili Peng, Associate Director, External Innovation Data Sciences, Biogen

Lili Peng | Associate Director, External Innovation Data Sciences | Biogen » speaking at Orphan USA

Steven Peskin, Executive Medical Director Population Health, Horizon Blue Cross Blue Shield - New Jersey

Steven Peskin | Executive Medical Director Population Health | Horizon Blue Cross Blue Shield - New Jersey » speaking at Orphan USA

Stacy Pike-Langenfeld, Co-Founder And President, KrabbeConnect

Stacy Pike-Langenfeld | Co-Founder And President | KrabbeConnect » speaking at Orphan USA

Gianluca Pirozzi, Senior Vice President, Head of Clinical Development and Translational Sciences,, Alexion Pharmaceticals

Gianluca Pirozzi | Senior Vice President, Head of Clinical Development and Translational Sciences, | Alexion Pharmaceticals » speaking at Orphan USA

Stuart Portman, Health Policy Advisor, United States Senate Committee On Finance

Stuart Portman | Health Policy Advisor | United States Senate Committee On Finance » speaking at Orphan USA

Isabella Presch, Senior Medical Director Rare and Pediatrics Team, Labcorp Drug Development

Isabella Presch | Senior Medical Director Rare and Pediatrics Team | Labcorp Drug Development » speaking at Orphan USA

Amy Price, Director, Client Services, VOZ Advisors

Amy Price | Director, Client Services | VOZ Advisors » speaking at Orphan USA

Amy Raymond, Director of Therapeutic Expertise, Center for Rare Diseases, ICON

Amy Raymond | Director of Therapeutic Expertise, Center for Rare Diseases | ICON » speaking at Orphan USA

Shannon Resetich, Global Franchise Head, Rare Diseases, Sanofi Genzyme

Shannon Resetich | Global Franchise Head, Rare Diseases | Sanofi Genzyme » speaking at Orphan USA

Marisa Ricci, Vice President, Global Head, Pipeline Programs Market Development, Patient Diagnosis Programs, Ultragenyx Pharmaceutical

Marisa Ricci | Vice President, Global Head, Pipeline Programs Market Development,  Patient Diagnosis Programs | Ultragenyx Pharmaceutical » speaking at Orphan USA

Destrey Roberson, Executive Director, Program Strategy, Premier Research

Destrey Roberson | Executive Director, Program Strategy | Premier Research » speaking at Orphan USA

Kay-Diene Robinson, OLM DEI Expert, Rare Advocacy Movement

Kay-Diene Robinson | OLM DEI Expert | Rare Advocacy Movement » speaking at Orphan USA

Traceann Rose, Director, Patient Engagament, Children's Tumor Foundation

Traceann Rose | Director, Patient Engagament | Children's Tumor Foundation » speaking at Orphan USA

Tamanna Roshan Lal, Co-Director, Lysosomal Storage and Treatment Program, Metabolic Geneticist,, Rare Disease Institut, Childrens National Medical Center

Tamanna Roshan Lal | Co-Director, Lysosomal Storage and Treatment Program, Metabolic Geneticist, | Rare Disease Institut, Childrens National Medical Center » speaking at Orphan USA

Ashish Sagrolikar, Chief Commercial Officer, Zogenix Inc.

Ashish Sagrolikar | Chief Commercial Officer | Zogenix Inc. » speaking at Orphan USA

Mary Schaheen, President, Prevail Partners

Mary Schaheen | President | Prevail Partners » speaking at Orphan USA

Scott Schliebner, SVP, Scientific Affairs and Therapeutic Expertise, ICON

Scott Schliebner | SVP, Scientific Affairs and Therapeutic Expertise | ICON » speaking at Orphan USA

Joel Schneider, Chief Technology Officer, Solid Biosciences

Joel Schneider | Chief Technology Officer | Solid Biosciences » speaking at Orphan USA

Denise Scots Knight, Chief Executive Officer, Mereo Biopharma

Denise Scots Knight | Chief Executive Officer | Mereo Biopharma » speaking at Orphan USA

Simone Seiter, Partner, Simon-Kucher & Partners

Simone Seiter | Partner | Simon-Kucher & Partners » speaking at Orphan USA

Gaurav Shah, Chief Executive Officer And President, Rocket Pharmaceuticals

Gaurav Shah | Chief Executive Officer And President | Rocket Pharmaceuticals » speaking at Orphan USA

Panna Sharma, President And Chief Executive Officer, Lantern Pharma

Panna Sharma | President And Chief Executive Officer | Lantern Pharma » speaking at Orphan USA

Amy Shea, Director, Diagnostics & Strategic Initiatives, Ionis Pharmaceuticals

Amy Shea | Director, Diagnostics & Strategic Initiatives | Ionis Pharmaceuticals » speaking at Orphan USA

Conor Sheehey, Health Policy Advisor, United States Senate Committee On Finance

Conor Sheehey | Health Policy Advisor | United States Senate Committee On Finance » speaking at Orphan USA

Fanny Sie, One Roche, Head of Artificial Intelligence and Digital Health, Roche

Fanny Sie | One Roche, Head of Artificial Intelligence and Digital Health | Roche » speaking at Orphan USA

Dylan Simon, Newborn Screening and Diagnostics Policy Manager, EveryLife Foundation for Rare Diseases

Dylan Simon | Newborn Screening and Diagnostics Policy Manager | EveryLife Foundation for Rare Diseases » speaking at Orphan USA

Manny Simons, Founder And Chief Executive Officer, Akouos

Manny Simons | Founder And Chief Executive Officer | Akouos » speaking at Orphan USA

Alison Skrinar, VP, Clinical Outcomes Research and Evaluation, Ultragenyx Pharmaceutical

Alison Skrinar | VP, Clinical Outcomes Research and Evaluation | Ultragenyx Pharmaceutical » speaking at Orphan USA

Matt Slabbert, Global Lead – Public Affairs, Cell & Gene Therapy, Bayer

Matt Slabbert | Global Lead – Public Affairs, Cell & Gene Therapy | Bayer » speaking at Orphan USA

Jason Slingsby, Chief Business Officer, Oxford Biomedica

Jason Slingsby | Chief Business Officer | Oxford Biomedica » speaking at Orphan USA

Charlie Small, Associate Director of Integrated Trial Solutions,, ClinEgde

Charlie Small | Associate Director of Integrated Trial Solutions, | ClinEgde » speaking at Orphan USA

Patroula Smpokou, Deputy Director, Office of Rare Diseases, Pediatrics, Urologic, and Reproductive Medicine, FDA

Patroula Smpokou | Deputy Director, Office of Rare Diseases, Pediatrics, Urologic, and Reproductive Medicine | FDA » speaking at Orphan USA

Kim Stephens, President, Project Alive

Kim Stephens | President | Project Alive » speaking at Orphan USA

Violeta Stoyanova-Beninska, Chair of Committee for Orphan Medicinal Productsof EMA, Medicines Evaluation Board

Violeta Stoyanova-Beninska | Chair of Committee for Orphan Medicinal Productsof EMA | Medicines Evaluation Board » speaking at Orphan USA

Jeffrey Strovel, Chief Executive Officer, Veralox Therapeutics

Jeffrey Strovel | Chief Executive Officer | Veralox Therapeutics » speaking at Orphan USA

German Suarez, Chief Executive Officer and President, GENBIE SAS

German Suarez | Chief Executive Officer and President | GENBIE SAS » speaking at Orphan USA

Romesh Subramanian, Chief Scientific Officer, Dyne Therapeutics

Romesh Subramanian | Chief Scientific Officer | Dyne Therapeutics » speaking at Orphan USA

Jason Tardio, Chief Operating Officer, Ovid Therapeutics

Jason Tardio | Chief Operating Officer | Ovid Therapeutics » speaking at Orphan USA

Ulrich Thienel, Chief Executive Officer, ReAlta Life Sciences

Ulrich Thienel | Chief Executive Officer | ReAlta Life Sciences » speaking at Orphan USA

Brigette Tippin Davis, Chief Scientific Officer,, Ambry Genetics

Brigette Tippin Davis | Chief Scientific Officer, | Ambry Genetics » speaking at Orphan USA

Mark Trusheim, Strategic Director, MIT NEWDIGS

Mark Trusheim | Strategic Director | MIT NEWDIGS » speaking at Orphan USA

Andrew Udell, President of North America, Commercial, Calliditas Therapeutics

Andrew Udell | President of North America, Commercial | Calliditas Therapeutics » speaking at Orphan USA

Julian Upton, European and Online Editor, Pharmaceutical Executive, MJH Life Sciences

Julian Upton | European and Online Editor, Pharmaceutical Executive | MJH Life Sciences » speaking at Orphan USA

Suneet Varma, Global President, Rare Disease Business Unit, Pfizer Inc

Suneet Varma | Global President, Rare Disease Business Unit | Pfizer Inc » speaking at Orphan USA

Denise Von Dohren, Vice President, PharmaCord

Denise Von Dohren | Vice President | PharmaCord » speaking at Orphan USA

Pavle Vukojevic, Chief Medical Officer, Pharm-Olam

Pavle Vukojevic | Chief Medical Officer | Pharm-Olam » speaking at Orphan USA

John Walter, Chief Executive Officer, Foundation for Prader-Willi Research

John Walter | Chief Executive Officer | Foundation for Prader-Willi Research » speaking at Orphan USA

Brian Wamhoff, Chief Operating Officer, HemoShear Therapeutics LLC

Brian Wamhoff | Chief Operating Officer | HemoShear Therapeutics LLC » speaking at Orphan USA

Joseph Watson, Associate Director, Regulatory Strategy, Rho, Inc

Joseph Watson | Associate Director, Regulatory Strategy | Rho, Inc » speaking at Orphan USA

Ellen Weiss, Vice President Of Business Development, PCM TRIALS

Ellen Weiss | Vice President Of Business Development | PCM TRIALS » speaking at Orphan USA

Monica Weldon, President and CEO, Syngap1 Foundation

Monica Weldon | President and CEO | Syngap1 Foundation » speaking at Orphan USA

Jessica Wessel, Clinical Strategy Liaison, Center for Rare Diseases, PRA Health Sciences

Jessica Wessel | Clinical Strategy Liaison, Center for Rare Diseases | PRA Health Sciences » speaking at Orphan USA

Melissa Williams, Director of Patient Diagnosis Programs, Ultragenyx Pharmaceutical

Melissa Williams | Director of Patient Diagnosis Programs | Ultragenyx Pharmaceutical » speaking at Orphan USA

Scott Williams, Head, Global Public Affairs Rare Diseases and Rare Blood Disorders, Sanofi Genzyme

Scott Williams | Head, Global Public Affairs Rare Diseases and Rare Blood Disorders | Sanofi Genzyme » speaking at Orphan USA

Toni Williams, Global Business Development Manager, Clinigen Group

Toni Williams | Global Business Development Manager | Clinigen Group » speaking at Orphan USA

Durhane Wong-Rieger, President And Chief Executive Officer, Canadian Organization For Rare Disorders

Durhane Wong-Rieger | President And Chief Executive Officer | Canadian Organization For Rare Disorders » speaking at Orphan USA

Janet Woodcock, Acting Commissioner, Food and Drug Administration (FDA)

Janet Woodcock | Acting Commissioner | Food and Drug Administration (FDA) » speaking at Orphan USA

David Young, Chief Executive Officer, Processa Pharmaceuticals, Inc.

David Young | Chief Executive Officer | Processa Pharmaceuticals, Inc. » speaking at Orphan USA

Nancy Yu, Co-Founder & CEO, AllStripes Research

Nancy Yu | Co-Founder & CEO | AllStripes Research » speaking at Orphan USA

Joseph Zabinski, Senior Director, AI & Precision Medicine, OM1

Joseph Zabinski | Senior Director, AI & Precision Medicine | OM1 » speaking at Orphan USA

Shiran Zimri, Head of Scientific Program, NeuroSense Therapeutics

Shiran Zimri | Head of Scientific Program | NeuroSense Therapeutics » speaking at Orphan USA

 

 

 

 

Get Involved At World Orphan Drug Congress USA

 

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