Janet Lynch Lambert, Chief Executive Officer, Alliance for Regenerative Medicine
Jim Lang, Chief Executive Officer, EVERSANA
David Lapidus, President, Lapidus Data
Leanne Larson, Corporate Vice President and WW Head, Real-World Evidence, Parexel
Yann Le Cam, Chief Executive Officer, EURORDIS
Kimberly Leblanc, Associate Director Of Research Operations Undiagnosed Diseases Network Coordinating Center, Harvard Medical School
Joseph Lee, Executive Director, PTC Therapeutics
Michael Lehmicke, Director, Science and Industry Affairs, Alliance for Regenerative Medicine
Clement Leong, Chief Executive Officer And Managing Director, Stamford Pharmaceuticals
Friedhelm Leverkus, Director Health Technology Assessment And Outcomes Research, Pfizer
Paul Levesque, Global President, Rare Disease, Pfizer
Jeremy Levin, Chairman and Chief Executive Officer, Chairman, BIO, Ovid Therapeutics
Edmund Lim, Abc, We CARE Journey
Marius George Linguraru, Principal Investigator at Children’s National Health System, Professor of Radiology, Pediatrics and Biomedical Engineering, The George Washington University
Donald Lo, Director, Therapeutic Development Branch, Division Of Pre-Clinical Innovation, National Center for Advancing Translational Sciences - NCATS
Robert Lodder, President, Biospherics
Brian Loew, CEO, Inspire
Robert Long, Executive Director, Uplifting Athletes
Jarrod Longcor, Chief Business Officer, Cellectar Biosciences Inc
Annastasiah Mudiwa Mhaka, Co-Founder, Convenor, President, Alliance for Artificial Intelligence in Healthcare
Sheila Mikhail, President And Co-Founder, Asklepios BioPharmaceutical Inc
Randy Milby, Chief Executive Officer, Hillstream Biopharma
Timothy Miller, Co-Founder, President And Chief Scientific Officer, Abeona Therapeutics
Debra Miller, CEO & Founder, CureDuchenne
James Miskin, Chief Technical Officer, Oxford Biomedica
Hubert Misztela, Machine Learning Expert At Novartis, Lecturer At Dublin Business School, Novartis
Ali Mohamadi, Executive Director, BioMarin Pharmaceutical Inc.
Samarendra Mohanty, Founder And President, NanoScope Technologies
Michael Murphy, Chief Medical & Scientific Officer, Worldwide Clinical Trials
Michelle Muscat, Co-Founder And President, National Alliance for Rare Diseases Support - Malta
Nuriya Musina, Head Of Development, Federal State Budgetary Institution, The Center For Healthcare Quality Assessme, Ministry of Health Russian Federation
Joseph Musumeci, President, BluePrint Orphan
Alexander Natz, Secretary General, European Confederation of Pharmaceutical Entrepreneurs (Belgium)
Lauren Neighbours, VP, Regulatory Affairs & Program Management, Optum
Brian Newkirk, Market Access Director, Alnylam Pharmaceuticals
Jay Newman, Senior Vice President and General Manager, Head Of Us Commercial, Spark Therapeutics
Scott Nickerson, Senior Vice President, Global Quality, Moderna Therapeutics
Jan Nielsen, Division President, Patient Solutions, AssistRx Patient Solutions
Yukiko Nishimura, President, ASrid Japan
Neena Nizar, President, The Jansens Foundation
Sara Nochur, Senior Vice President Regulatory Affairs, Alnylam Pharmaceuticals
Mukund Nori, Director, Medical Affairs & Principal Med, rareLife solutions
Wolfram Nothaft, Chief Medical Officer, Takeda
Lynn O'Connor Vos, Chief Executive Officer, Muscular Dystrophy Association
Daniel O'Mahony, Partner, Seroba Life Sciences
Lianna Orlando, Senior Director Of Research, CureDuchenne
Nick Page, Chief Operations Officer, Oxford Biomedica
Palani Palaniappan, CTO, Aruvant
Jim Palma, Executive Director, TargetCancer Foundation
Francis Pang, Vice President Global Market Access, Orchard Therapeutics
Art Pappas, Managing Partner, Pappas Capital
Bhash Parasuraman, Vice President Of Business Unit Lead, Rare Disease, Patient And Health Impact, Pfizer
Andrew Parece, Vice President, Charles River Associates
Anne Pariser, Director, Office Of Rare Diseases Research, National Center For Advancing Translational Sciences - Ncats, National Institutes of Health (NIH)
Detlev Parow, Head Pharmaceutical Department, D.A.K.
Linn Parrish, Global Patient & Scientific Affairs, Chief Medical Office,, Takeda
Doug Paul, Vice President And Partner, MME
Peter Payne, Vice President, Head of the Digital Research Network, Optum
Steven Peskin, Associate Clinical Professor Of Medicine, Rutgers Rwj Medical School, Executive Medical Director Population Health And Transform, Horizon Blue Cross Blue Shield - New Jersey
Dmitry Petrov, Head Of Medical Writing And Pharmacovigilance, ICRC-Weyer GmbH
Areejit Phukan, Director, Analytics And Forecasting, Insmed Inc
Andres Pichon-Riviere, Executive Director Of The Institute For Clinical Effectiveness And Health Policy (Iecs), Director Of The Health Technology, University Of Buenos Aires
Oresta Piniazhko, Director, Hta Department, Ministry of Health of Ukraine
Sarah Pitluck, Head, Global Pricing And Reimbursement, Spark Therapeutics
Leslie Powell, Director Of Policy And Advocacy, Cystic Fibrosis Foundation
Mayo Pujols, Vice President, Head Of Global Cell And Gene Technical Development And Manufacturing, Novartis
Anthony Quinn, President And Chief Executive Officer, Aeglea BioTherapeutics
Harsha Rajasimha, Founder And Chairman, IndoUSrare
Shankar Ramaswamy, Chief Business Officer, Axovant
Kyle Rasbach, Partner, Pappas Ventures
Karlyne Reilly, Senior Associate Scientist And Section Head, National Cancer Institute
Frederic Revah, Chief Executive Officer, Genethon
John Reynders, Vice President, Data Sciences, Genomics, And Bioinformatics, Alexion Pharmaceticals
Marisa Ricci, Vice President Patient Diagnosis Programs And U.S. Field Medical Engagement, Ultragenyx Pharmaceutical
Dara Richardson-Heron, Chief Patient Officer, Pfizer
Will Richmond, Lead, Value And Access, Sanofi Genzyme
Trevor Richter, Director, Common Drug Review And Optimal Use, CADTH
Juan Roman, Head Of Market Access And Pricing, Acceleron Pharmaceuticals, Inc.
Kieran Rooney, Vice President, Strategic Alliances And Licensing, Amryt Pharmaceuticals
Luke Rosen, Vice President, Accelerated Development & Patient Engagement, Ovid Therapeutics
Ruth Rostron, Vice President Of Project Management, Inceptua Medicines Access
Seth Rotberg, Co Founder And President, Our Odyssey
John Rother, Chief Executive Officer, National Coalition On Health Care
Delphine Roulland, Director Government Affairs And Public Policy, European Confederation of Pharmaceutical Entrepreneurs (Belgium)
Kacper Rucinski, Executive Committee Member, SMA Europe
Christopher Rudolf, Founder And Chief Executive Officer, volv global
David Russell, Head Of External Innovation, Actelion-Janssen
Leo Russo, Senior Director, Epidemiology Worldwide Safety And Regulatory, Pfizer
Susan S, Advocate, Patient Advocate
Peter Saltonstall, Chief Executive Officer, National Organization for Rare Disorders (NORD)
Abby Sandler, Executive Director, Mypart, Center For Cancer Research,, National Institutes of Health
Scott Schliebner, SVP, Scientific Affairs, PRA Health Sciences
Sophie Schmitz, Managing Partner, Partners4Access
Dana Schoknecht, Life Sciences Manager, MUV People
Jeffrey Schwartz, Managing Director, Bain Capital Life Sciences
Denise Scots Knight, Chief Executive Officer And Co-Founder, Mereo BioPharma
Jessica Scott, Head of R&D Patient Engagement Office,, Takeda Pharmaceuticals
Joanna Segieth, CEO, Biosynetix
Simone Seiter, Partner, Simon-Kucher & Partners
Jim Shaffer, Cbo, Eiger Biopharmaceuticals
Lesha Shah, Co-Chair, Pediatric Gene Therapy And Medical Ethics Working Group, Assistant Professor Of Psychiatry, Icahn School Of Medicine, The Mount Sinai Hospital
Avinash Shanbhag, Director, Nationwide Health Information Network Division, U.S. Department of Health & Human Services
Nataliya Shandarovska, patient, patient advocate, senior staff nurse, National Alliance for Rare Diseases Support - Malta
Panna Sharma, President And Chief Executive Officer, Lantern Pharma
Adam Shaywitz, Chief Medical Officer, Rare Disease Drug Development, BridgeBio Pharma
Rachel Sher, Vice President Policy And Regulatory Affairs, NORD
Alex Sherman, Director, Center For Innovation And Bioinformatics, Harvard Medical School
Gerard Short, svp medical science, Freeline Therapeutics
Oodaye Shukla, Chief Data Officer, HVH Precision Analytics, now EVERSANA
Anna Shurshalina, Global Safety Lead, Safety Physician, Oncology. Benefit Risk Management, Pharmacovigilance, Bayer Pharmaceuticals
Alison Skrinar, Vice President, Clinical Outcomes Research And Evaluation, Ultragenyx Pharmaceutical
Andrew Slugg, Senior Vice President Of Regulatory Affairs, Alnylam Pharmaceuticals
Kristin Smedley, President, Curing Retinal Blindness Foundation
Bob Smith, Senior Vice President, Global Gene Therapy Business, Pfizer
Peter Snyder, Medical and Scientific Publications, rareLife solutions
Nancy Spinner, Chief of the Division of Genomic Diagnostics, The Children's Hospital of Philadelphia
Meagan Spychala, Assistant Vice President Of Patient Engagement And Program Strategy, Rho, Inc
Alicia Staley, Senior Director, Patient Engagement, Medidata, a Dassault Systèmes company
Cornell Stamoran, Vice President of Corporate Strategy, Catalent Pharma Solutions
Kim Stephens, President, Project Alive
Dean Suhr, President, MLD Foundation
Jamie Sullivan, Director Of Public Policy, EveryLife Foundation for Rare Diseases
Marshall Summar, Division Chief Of Genetics And Metabolism, Children's National Medical Center
Weiyong Sun, Senior Director, Specialty Medicine Search, Evaluation And Global Business Development, Daiichi Sankyo Co Ltd
Thayer Surette, Deputy Director, Partnership to Improve Patient Care (PIPC)
Jodie Vento, Chair, Access Committee, National Society Of Genetic Counselors, Manager, Center For Rare Disease Therapy, Childrens Hospital of Pittsburgh
Terry Jo Vetters Bichell, Founder And Director, COMBINEDBrain
Craig Wakeford, Director, Global Value And Access, Biogen
Kim Warren, Head Of Operations, Avrobio
Melissa Wasserstein, Chief, Division Of Pediatric Genetic Medicine, Department Of Pediatrics,, Montefiore Medical Center
Christina Waters, Chief Executive Officer And Founder, RARE Science
Allison Watson, Co founder/Secretary, Ring20 Research and Support UK
Monica Weldon, President/CEO, Bridge The Gap Syngap Education And Research Foundation
Bjorn Wester, Global Client Services Manager, Clincierge
Samuel Agyei Wiafe, Executive Director, Rare Disease Ghana Initiative
Terry Wilcox, Co-Founder And Executive Director, Patients Rising & Patients Rising
Laurie Witherwax, Sr Vice President, Site Activation, Worldwide Clinical Trials
Durhane Wong-Rieger, President And Chief Executive Officer, Canadian Organization For Rare Disorders
Marcie Wood, Senior Managing Scientist, Practice Director, Biopharmaceutical/Pharmaceutical, ToxStrategies
Janet Woodcock, Director Of Drug Evaluation And Research Center, Food and Drug Administration (FDA)
Jonathan Woodring, Executive Vice President And General Manager, IPM.ai
Laura Wuerth, Vice President, rareLife solutions
Loukas Xaplanteris, Director Eu+ Value And Market Acces, Biogen
William Xiang, Director, Strategy And Operations, XW Laboratories
Richard R Yang, Chief Executive Officer And Founder, Reflection Biotechnologies
Zheng Yang, Head Of Technology And Data Innovation, Customer Value, Boehringer Ingelheim
Dimitar Yonchev, Patient Advocate Representative, Pro Retina Deutschland e.V.
David Young, Chief Executive Officer, Processa Pharmaceuticals, Inc.
Timothy Yu, Attending Physician, Investigator, Division Of Genetics And Genomics, Boston Children's Hospital
Wyatt Yue, Principal Investigator, Associate Professor, Lead Scientist, Rare Disease Research, Oxford University Structural Genomics Consortium
Martin Zagari, Vice President Global Health Economics, Amgen Inc
Shuyang Zhang, Department Of Cardiology, Peking Union Medical College
Ran Zheng, Chief Technology Officer, Orchard Therapeutics
Sameer Zuberi, Consultant Paediatric Neurologist, President, European Paediatric Neurology Society, Royal Hospital for Children,, National Health Service