Prof. Bobby Gaspar | Professor of Paediatrics & Immunology
UCL Great Ormond Street Institute of Child Health

Prof. Bobby Gaspar, Professor of Paediatrics & Immunology, UCL Great Ormond Street Institute of Child Health

Professor Bobby Gaspar is Professor of Paediatrics and Immunology at UCL Great Ormond Street Institute of Child Health and Honorary Consultant Paediatric Immunologist at Great Ormond Street Hospital for Children NHS Foundation Trust.   He initially trained in paediatrics and then became interested in primary immunodeficiencies at an early stage in his career and undertook a PhD at the Molecular Immunology Unit at ICH. From there he has continued his academic and clinical career. His interests are in many different aspects of primary immunodeficiency including understanding the molecular and cellular defects and disease pathogenesis, bone marrow transplantation for severe immunodeficiencies and the development of gene and cell therapy for these conditions. Over the last decade, his team have conducted clinical trials that have shown that gene therapy can successfully correct the immune defect in specific immunodeficiency conditions. He is leading UK and European initiatives for newborn screening for severe combined immunodeficiency. He is also Director Designate of the Zayed Centre for Research into Rare Diseases in Children (ZCRRDC), the new academic and clinical facility that will open at Great Ormond Street in 2018.


Day 1 Orphan 14th Nov @ 14:15

Chair opening remarks

Day 1 Orphan 14th Nov @ 14:20

Ex vivo gene therapy for monogenic bone marrow disorders

  • Sharing GSK’s journey in treating ADA-SCID through gene therapy: perspectives on regulation, facing challenging communities and the reputable high price

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