12 - 14 November 2019 | Barcelona
Strategy, advocacy and partnering for the orphan drug industry
500+ Attendees | 275+ Companies | 80% Decision Makers | 150+ Speakers
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What is World Orphan Drug Congress?
World Orphan Drug Congress is Europe's meeting place for the rare disease community. The Conference offers strategic keynote plenaries, themed tracks and dedicated networking sessions, you have the chance to really tailor the event to the needs of your day-to-day role.
Exhibitors have a unique opportunity to put their business products and services in front of potential buyers looking to source the latest technologies in the orphan drugs industry. Meet and listen to biotech start-ups and investors in our Pitch & Partner track where the most promising companies showcase their orphan drug technology and pipeline.
Enjoy discussions on:
Cell & Gene Therapies
Genetic Testing
Gene Editing
Partnering & Investment
Global Market Access
Expanded Access Programs
Real World Evidence
Global Patient Advocacy
Value based pricing & reimbursement
Epidemiology & forecasting
Orphan Drugs Policy
Gene Therapy Development
Together with:
Supported by:
Advisory Board
Wills Hughes-Wilson
Head of Patient Access & Commercial Planning
Mereo Biopharma
Professor Michael Linden
Former VP Gene Therapy & Head, GMI
Pfizer
Yann Le Cam
Chief Executive Officer
EURORDIS
Dr Ségolène Aymé
Founder of Orphanet, Emeritus Research Director
INSERM
Dr Bruno Sepodes
Chair of COMP
EMA
Sheela Upadhyaya
Assoc. Director Highly Specialised Technologies
National Institute For Health and Care Excellence
Alastair Kent
Former Director
Genetic Alliance UK
Dr Carlo Incerti
SVP, Head of Global Medical Affairs, CMO
Genzyme, A Sanofi Company
Dr Mathew Pletcher
Head of Rare Disease Discovery
Roche
M Ken Kengatharan
Managing Partner, Atheneos Ventures and CEO
Auxesia Orion
Birgitte Volck
President Research & Development
AVROBIO
Dr Pedro Franco
Former Scientific Administrator
EMA
Rick Thompson
CEO
Findacure
Dr Alexander Natz
Secretary General
EUCOPE
Anna Bucsics
Project Advisor
MoCA
Josie Godfrey
Former Associate Director
NICE
Dr Diego Ardigo
Chair, IRDiRCTherapies Scientific Committee & R&D Rare Diseases Unit Head at Chiesi Group
Steve Groft
Senior Advisor to Director
National Center for Advancing Translational Sciences (NCATS), NIH
Durhane Wong-Rieger
Chair of RDI and CEO, CORD
Dr Josep Torrent-Farnell
Head of the medicine division
CatSalut
"It is an important meeting that sheds light on the value patient advocates bring to the development process"
Global Medicines Development Lead - Rare Diseases, Pfizer
Who Attends
AANORA Actelion Pharma Ltd Action Duchenne Addmedica Adelphi Values AGSD (UK) AirLiquide
AKU Society Alcimed Alexion Pharmaceuticals Allaysis LLC Alliance Life Sciences ALS Liga Belgi
Alstrom Syndrome U.K. AMICULUM Anticancer Fund AOP Orphan Pharmaceuticals AG
ArmaGen Technologies, Inc. Atacsia a Fi / Ataxia and Me Ataxia UK aTyr aTyr Pharma
BioBlast Pharma Ltd Biopontis Alliance Blackswan Foundation Brace Pharma Capital
Caligor Rx, Inc. Calypso Biotech SA Capsugel Celgene Centogene AG
Charity Association Neurohereditary Diseases Chiesi Farmaceutici Spa Clear Pharma
Clinart MENA Clinerion Clinigen Global Access Programs Comradis Concenter BioPharma/Silkim Ltd.
Cote Orphan Coulter Partners Covance UK CRF Health CureDuchenne Cures Within Reach
Cydan Development Cytokinetics Daiichi Sankyo Europe GmbH Dipharma SA Diurnal Limited
Dravet Syndrome Foundation Durbin E.C.R.I.N. ECRIN-ERIC ELA Suisse
Emmaus Life Sciences, Inc Ergomed EspeRare Euromedica EuropaBio
European Huntington's Disease Network EURORDIS Euticals Spa EvaluatePharma Ltd
Evidera F.Hoffmann-La Roche Ltd. Facio Therapies BV Federal Joint Committee
F Hoffmann-La Roche French Association Against Friedreich Ataxia Gaucher Disease Russia
Genesis Pharma Genetic Alliance U.K. Genkyotex Innovation Sas Genpharm Genzyme Europe BV
Gerson Lehrman Group Giddi Pharma GlaxoSmithKline Greenovation Biotech GmbH
Grünenthal GmbH GSK Rare Diseases GW Pharmaceuticals Haute Autorite De Sante
Horizon Pharma Inc I.M.S. Health Idis Managed Access Idis Pharma
Imagine - Institut des Maladies génétiques IMS Health INC Research Index Ventures INSERM
Lysogene M3 Pharma S/A Mapi Consultancy Midas Pharma GmbH Minoryx Therapeutics
MPS Society N.O.R.D. National Institute for Health and Care Excellence
National Institutes of Biomedical Innovation, Health and Nutrition
National organisation for rare diseases of Serbia NephCure Kidney International Niemann-Pick UK Novartis
Generate new business
Get your brand, your message and your sales people in front of your customers.
The congress opens doors to fantastic opportunities to form lucrative partnerships and source new ground-breaking solutions.
Join us in Barcelona 12-14 November 2019
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