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    World Orphan Drug Congress

    Barcelona, 14-15 November, 2017
    Pre-Congress Workshops 13 November

    STRATEGY, ADVOCACY AND PARTNERING FOR THE ORPHAN DRUG INDUSTRY

    World Orphan Drug Congress

     

2017 PROSPECTUS

Get your brand, your message and your sales people in front of your customers.

The Congress opens doors to fantastic opportunities to form lucrative partnerships and source new ground-breaking solutions.

 

 

World Orphan Drug Congress 2017  sponsorship prospectus

OUR HISTORY

 

The 8th annual World Orphan Drug Congress is the marketplace for orphan drug professionals looking at the complete value chain of orphan drug development, from clinical development and R&D to corporate development and market access.

Being Europe’s largest Orphan Drug Congress, this event will provide a platform for you to showcase your thought leadership and expertise pharma, biotechs, payers, regulators and patient advocates.

 

 

ADVISORY BOARD

We thank our Advisory Board members for their contribution to the agenda this year:

 

Sven Kili, Vice President and Head of Gene Therapy Development, GlaxoSmithKlineSven Kili
Vice President and Head of Gene Therapy Development
GlaxoSmithKline

 

Prof Michael Linden, VP Gene Therapy & Head, GMI, PfizerProf Michael Linden
VP Gene Therapy & Head, GMI
Pfizer

Yann Le Cam, Chief Executive Officer, EURORDIS

Yann Le Cam
Chief Executive Officer

EURORDIS

Dr Ségolène Aymé, Founder of Orphanet, Emeritus Research Director, INSERM
Dr Ségolène Aymé
Founder of Orphanet, Emeritus Research Director
INSERM

Dr Bruno Sepodes, Chair of COMP, EMA

Dr Bruno Sepodes
Chair of COMP
EMA

Alastair Kent, Director, Genetic Alliance UK

Alastair Kent
Director

Genetic Alliance UK

Nicole Boice, Founder & CEO, Global Genes

Nicole Boice
Founder & CEO
Global Genes

Dr Carlo Incerti, SVP, Head of Global Medical Affairs, CMO, Genzyme, A Sanofi Company

Dr Carlo Incerti
SVP, Head of Global Medical Affairs, CMO
Genzyme, A Sanofi Company

 

 

 

 

DOWNLOAD THE BROCHURE

 

 
 

EUROPE’S MEETING PLACE FOR THE RARE DISEASE COMMUNITY

The Conference offers strategic keynote plenaries, themed tracks and dedicated networking sessions, you have the chance to really tailor the event to the needs of your day-to-day role. 

The Exhibitors  have a unique opportunity to put their business products and services in front of potential buyers looking to source the latest technologies in the orphan drugs industry. 

The pre-congress workshops will offer insights into Pricing, Reimbursement and Market Access Challenges and Accelerating Commercialization of Rare Disease Treatments in the afternoon.

Meet and listen to biotech start-ups and investors in our Pitch & Partner track where the most promising companies showcase their orphan drug technology and pipeline.

Enjoy discussions on: 

FUTURE OF ORPHAN DRUGS

PRICING & REIMBURSEMENT

APPROVAL & ACCESS

M&A AND COMMERCIALIZATION

PATIENT-CENTRIC RESEARCH

REAL-WORLD EVIDENCE

MARKETING & COMPETITIVENESS

GENE THERAPY

SCIENTIFIC INNOVATION

REGIONAL MARKET ANALYSIS

BIOSIMILARS

ROUNDTABLES

Colocated with:

Rare Disease Advocacy World Logo

Pitch and Partner Logo

 

2017 SPEAKERS

 

  • Ron Bartek at World Orphan Drug Congress
    Ron Bartek
    President/Co-Founder
    Friedreich's Ataxia Research Alliance
    David Dasberg at World Orphan Drug Congress
    David Dasberg
    Managing Director
    Facio Therapies BV
    Jim Green at World Orphan Drug Congress
    Jim Green
    President
    International Niemann-Pick Disease Aliance
  • Wills Hughes-Wilson at World Orphan Drug Congress
    Wills Hughes-Wilson
    Senior Vice President, Chief Patient Access Officer
    Sobi
    Pierre Laurin at World Orphan Drug Congress
    Pierre Laurin
    Chief Executive Officer
    ProMetic Life Sciences Inc.
    Prof Michael Linden at World Orphan Drug Congress
    Prof Michael Linden
    VP Gene Therapy & Head, GMI
    Pfizer
  • Dr Will Maier at World Orphan Drug Congress
    Dr Will Maier
    Chief Scientific Officer
    Mapi Group
    Diana Ribeiro at World Orphan Drug Congress
    Diana Ribeiro
    Director of Research
    Action Duchenne
    Dr Paul Robinson at World Orphan Drug Congress
    Dr Paul Robinson
    Executive Director, Patient Perspective
    Merck Sharp and Dohme
  • Sheela Upadhyaya at World Orphan Drug Congress
    Sheela Upadhyaya
    Assoc. Director Highly Specialised Technologies
    National Institute For Health and Care Excellence
    Stephen Yoo at World Orphan Drug Congress
    Stephen Yoo
    Chief Medical Officer
    ReGenXBio
    Dr Omar Khwaja at World Orphan Drug Congress
    Dr Omar Khwaja
    Global Head of Rare Diseases
    F. Hoffmann-La Roche AG
  • Dr Bruno Sepodes at World Orphan Drug Congress
    Dr Bruno Sepodes
    Chair, Committee for Orphan Medicinal Products (COMP)
    European Medicines Agency
    Julie Walters at World Orphan Drug Congress
    Julie Walters
    Founder
    Raremark
    Christina Waters at World Orphan Drug Congress
    Christina Waters
    CEO and Founder
    RARE Science

 

SEE MORE

"It is an important meeting that sheds light on the value patient advocates bring to the development process!"

Global Medicines Development Lead - Rare Diseases, Pfizer

 

OUR SPONSORS & EXHIBITORS

 

  • Supporting Partner

    EURORDIS at World Orphan Drug Congress

    Supporting Partner

    The National Organization for Rare Disorders at World Orphan Drug Congress
  • Platinum Sponsor

    Mapi Group at World Orphan Drug Congress

    Gold Sponsor

    INC Research at World Orphan Drug Congress
  • Gold Sponsor

    PRA Health Sciences at World Orphan Drug Congress

    Gold Sponsor

    Premier Research at World Orphan Drug Congress
  • Gold Sponsor

    QuintilesIMS at World Orphan Drug Congress

    Silver Sponsor

    Clinigen Group at World Orphan Drug Congress
  • Silver Sponsor

    Medical Marketing Economics at World Orphan Drug Congress

    Silver Sponsor

    Partners4Access at World Orphan Drug Congress
  • Bronze Sponsor

    Cello Health at World Orphan Drug Congress

    Bronze Sponsor

    Dolon at World Orphan Drug Congress
  • Bronze Sponsor

    Komtur Polska sp. z.o.o at World Orphan Drug Congress

    Bronze Sponsor

    Raremark at World Orphan Drug Congress
  • Bronze Sponsor

    SKC Beratungsgesellschaft at World Orphan Drug Congress

    Bronze Sponsor

    Worldwide Clinical Trials at World Orphan Drug Congress
  • Pitch & Partner Sponsor

    Braincures at World Orphan Drug Congress

    Pitch & Partner Sponsor

    Facio Therapies BV at World Orphan Drug Congress
  • Pitch & Partner Sponsor

    SOM Biotech at World Orphan Drug Congress

 

"The information provided was really helpful, I will use it in my daily work. The networking was also great!" 

 

Director, Value Evidence Lead Rare Diseases, GSK

PAST ATTENDEES

 

AANORA Actelion Pharma Ltd Action Duchenne Addmedica Adelphi Values AGSD (UK) AirLiquide

AKU Society Alcimed Alexion Pharmaceuticals Allaysis LLC Alliance Life Sciences ALS Liga Belgi

Alstrom Syndrome U.K. AMICULUM Anticancer Fund AOP Orphan Pharmaceuticals AG

ArmaGen Technologies, Inc. Atacsia a Fi / Ataxia and Me Ataxia UK aTyr aTyr Pharma

BioBlast Pharma Ltd Biopontis Alliance Blackswan Foundation Brace Pharma Capital

Caligor Rx, Inc. Calypso Biotech SA  Capsugel Celgene Centogene AG

Charity Association Neurohereditary Diseases Chiesi Farmaceutici Spa Clear Pharma

Clinart MENA Clinerion Clinigen Global Access Programs Comradis Concenter BioPharma/Silkim Ltd.

Cote Orphan Coulter Partners   Covance UK CRF Health CureDuchenne Cures Within Reach

Cydan Development  Cytokinetics Daiichi Sankyo Europe GmbH Dipharma SA Diurnal Limited

Dravet Syndrome Foundation Durbin E.C.R.I.N. ECRIN-ERIC ELA Suisse

Emmaus Life Sciences, Inc Ergomed EspeRare Euromedica EuropaBio

European Huntington's Disease Network EURORDIS  Euticals Spa EvaluatePharma Ltd

Evidera F.Hoffmann-La Roche Ltd. Facio Therapies BV Federal Joint Committee

F Hoffmann-La Roche French Association Against Friedreich Ataxia Gaucher Disease Russia

Genesis Pharma Genetic Alliance U.K. Genkyotex Innovation Sas Genpharm Genzyme Europe BV

Gerson Lehrman Group Giddi Pharma GlaxoSmithKline  Greenovation Biotech GmbH

Grünenthal GmbH GSK Rare Diseases GW Pharmaceuticals   Haute Autorite De Sante

Horizon Pharma Inc I.M.S. Health Idis Managed Access Idis Pharma

Imagine - Institut des Maladies génétiques IMS Health INC Research Index Ventures INSERM

 Lysogene M3 Pharma S/A Mapi Consultancy Midas Pharma GmbH Minoryx Therapeutics

MPS Society N.O.R.D. National Institute for Health and Care Excellence

National Institutes of Biomedical Innovation, Health and Nutrition

National organisation for rare diseases of Serbia  NephCure Kidney International Niemann-Pick UK Novartis

 

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