World Orphan Drug Congress


12 - 14 November 2019 | Barcelona


Strategy, advocacy and partnering for the orphan drug industry




What is The World Orphan Drug Congress?

World Orphan Drug Congress is Europe's meeting place for the rare disease community. The Conference offers strategic keynote plenaries, themed tracks and dedicated networking sessions, you have the chance to really tailor the event to the needs of your day-to-day role.

Exhibitors have a unique opportunity to put their business products and services in front of potential buyers looking to source the latest technologies in the orphan drugs industry.

Meet and listen to biotech start-ups and investors in our Pitch & Partner track where the most promising companies showcase their orphan drug technology and pipeline.

Enjoy discussions on: 

Cell & Gene Therapies

Genetic Testing

Gene Editing

Partnering & Investment 

Global Market Access

Expanded Access Programs

Real World Evidence

Global Patient Advocacy

Value based pricing & reimbursement

Epidemiology & forecasting

Orphan Drugs Policy

Gene Therapy Development 

Together with:


Supported by:














Advisory Board

Wills Hughes-Wilson, Former Senior Vice President, Chief Patient Access Officer, Sobi

Wills Hughes-Wilson
Head of Patient Access & Commercial Planning 
Mereo Biopharma

Professor Michael Linden, Former VP Gene Therapy & Head, GMI, Pfizer

Professor Michael Linden
Former VP Gene Therapy & Head, GMI

Yann Le Cam, Chief Executive Officer, EURORDIS

Yann Le Cam
Chief Executive Officer  

Dr Ségolène Aymé, Founder of Orphanet, Emeritus Research Director, INSERM

Dr Ségolène Aymé
Founder of Orphanet, Emeritus Research Director

Dr Bruno Sepodes, Chair of COMP, EMA

Dr Bruno Sepodes
Chair of COMP

Sheela Upadhyaya, Assoc. Director Highly Specialised Technologies, National Institute For Health and Care Excellence

Sheela Upadhyaya
Assoc. Director Highly Specialised Technologies
National Institute For Health and Care Excellence

Alastair Kent, Director, Genetic Alliance UK

Alastair Kent
Former Director
Genetic Alliance UK

Dr Carlo Incerti, SVP, Head of Global Medical Affairs, CMO, Genzyme, A Sanofi Company

Dr Carlo Incerti
SVP, Head of Global Medical Affairs, CMO
Genzyme, A Sanofi Company

Dr Mathew Pletcher, Head of Rare Disease Discovery, Roche

Dr Mathew Pletcher
Head of Rare Disease Discovery

Dr M Ken Kengatharan, Managing Director, Atheneos Capital

M Ken Kengatharan
Managing Partner, Atheneos Ventures and CEO
Auxesia Orion

Birgitte Volck, President Research & Development, AVROBIO

Birgitte Volck
President Research & Development

Dr Pedro Franco, Former Scientific Administrator, EMA

Dr Pedro Franco 
Former Scientific Administrator 

Rick Thompson, CEO, Findacure

Rick Thompson 

Dr Alexander Natz, Secretary General, EUCOPE

Dr Alexander Natz
Secretary General

Anna Bucsics, Project Advisor, MoCA

Anna Bucsics
Project Advisor

Josie Godfrey, Former Associate Director, NICE

Josie Godfrey
Former Associate Director

Dr Diego Ardigo, Chair, IRDiRC Therapies Scientific Committee & R&D Rare Diseases Unit Head at Chiesi Group

Dr Diego Ardigo
Chair, IRDiRCTherapies Scientific Committee & R&D Rare Diseases Unit Head at Chiesi Group

Steve Groft, Senior Advisor to Director, National Center for Advancing Translational Sciences (NCATS), NIH

Steve Groft
Senior Advisor to Director
National Center for Advancing Translational Sciences (NCATS), NIH

Durhane Wong-Rieger, Chair of RDI and CEO, CORD

Durhane Wong-Rieger
Chair of RDI and CEO,  CORD

Dr Josep Torrent-Farnell, Head of the medicine division, CatSalut

Dr Josep Torrent-Farnell
Head of the medicine division



Who Attends


AANORA Actelion Pharma Ltd Action Duchenne Addmedica Adelphi Values AGSD (UK) AirLiquide

AKU Society Alcimed Alexion Pharmaceuticals Allaysis LLC Alliance Life Sciences ALS Liga Belgi

Alstrom Syndrome U.K. AMICULUM Anticancer Fund AOP Orphan Pharmaceuticals AG

ArmaGen Technologies, Inc. Atacsia a Fi / Ataxia and Me Ataxia UK aTyr aTyr Pharma

BioBlast Pharma Ltd Biopontis Alliance Blackswan Foundation Brace Pharma Capital

Caligor Rx, Inc. Calypso Biotech SA  Capsugel Celgene Centogene AG

Charity Association Neurohereditary Diseases Chiesi Farmaceutici Spa Clear Pharma

Clinart MENA Clinerion Clinigen Global Access Programs Comradis Concenter BioPharma/Silkim Ltd.

Cote Orphan Coulter Partners   Covance UK CRF Health CureDuchenne Cures Within Reach

Cydan Development  Cytokinetics Daiichi Sankyo Europe GmbH Dipharma SA Diurnal Limited

Dravet Syndrome Foundation Durbin E.C.R.I.N. ECRIN-ERIC ELA Suisse

Emmaus Life Sciences, Inc Ergomed EspeRare Euromedica EuropaBio

European Huntington's Disease Network EURORDIS  Euticals Spa EvaluatePharma Ltd

Evidera F.Hoffmann-La Roche Ltd. Facio Therapies BV Federal Joint Committee

F Hoffmann-La Roche French Association Against Friedreich Ataxia Gaucher Disease Russia

Genesis Pharma Genetic Alliance U.K. Genkyotex Innovation Sas Genpharm Genzyme Europe BV

Gerson Lehrman Group Giddi Pharma GlaxoSmithKline  Greenovation Biotech GmbH

Grünenthal GmbH GSK Rare Diseases GW Pharmaceuticals   Haute Autorite De Sante

Horizon Pharma Inc I.M.S. Health Idis Managed Access Idis Pharma

Imagine - Institut des Maladies génétiques IMS Health INC Research Index Ventures INSERM

 Lysogene M3 Pharma S/A Mapi Consultancy Midas Pharma GmbH Minoryx Therapeutics

MPS Society N.O.R.D. National Institute for Health and Care Excellence

National Institutes of Biomedical Innovation, Health and Nutrition

National organisation for rare diseases of Serbia  NephCure Kidney International Niemann-Pick UK Novartis



2018 Sponsors


  • Platinum Sponsor

    Gold Sponsor

    Gold Sponsor

  • Gold Sponsor

    Gold Sponsor

    Gold Sponsor

  • Gold Sponsor

    Gold Sponsor

    Silver Sponsor

  • Silver Sponsor

    Silver Sponsor

    Silver Sponsor

  • Silver Sponsor

    Bronze Sponsor

    Bronze Sponsor

  • Bronze Sponsor

    Bronze Sponsor

    Bronze Sponsor

  • Bronze Sponsor

    Showcase Sponsor

    Showcase Sponsor

  • Showcase Sponsor

    Showcase Sponsor

Generate new business

Get your brand, your message and your sales people in front of your customers.

The congress opens doors to fantastic opportunities to form lucrative partnerships and source new ground-breaking solutions.



World Orphan Drug Congress 2019 sponsorship prospectus


Join us in Barcelona 12-14 November 2019



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To Sponsor Or Exhibit


Michael Hodge
t/ +44 20 7092 1091


To Speak


Wing-Yun Cheung
t/ +44 20 7092 1172


To Register


Issa Mauthoor
t/ +44 20 7092 1257