World Orphan Drug Congress 2018


Strategy, advocacy and partnering for the orphan drug industry



Generate new business

Get your brand, your message and your sales people in front of your customers.

The congress opens doors to fantastic opportunities to form lucrative partnerships and source new ground-breaking solutions.



World Orphan Drug Congress 2018  sponsorship prospectus

"It is an important meeting that sheds light on the value patient advocates bring to the development process"

Global Medicines Development Lead - Rare Diseases, Pfizer

What is World Orphan Drug Congress?


World Orphan Drug Congress is Europe's meeting place for the rare disease community. The Conference offers strategic keynote plenaries, themed tracks and dedicated networking sessions, you have the chance to really tailor the event to the needs of your day-to-day role.

Exhibitors have a unique opportunity to put their business products and services in front of potential buyers looking to source the latest technologies in the orphan drugs industry. Meet and listen to biotech start-ups and investors in our Pitch & Partner track where the most promising companies showcase their orphan drug technology and pipeline.

Enjoy discussions on: 

Cell & Gene Therapies

Genetic Testing

Gene Editing

Partnering & Investment 

Global Market Access

Expanded Access Programs

Real World Evidence

Global Patient Advocacy

Value based pricing & reimbursement

Epidemiology & forecasting

Orphan Drugs Policy

Gene Therapy Development 


Together with: 

Rare Disease Advocacy World 2018

Pitch & Partner 2018

Meet key orphan drug & rare disease decision makers

Speakers from 2017 included:



  • David Dasberg at World Orphan Drug Congress
    David Dasberg
    Managing Director
    Facio Therapies BV
    Jim Green at World Orphan Drug Congress
    Jim Green
    International Niemann-Pick Disease Aliance
  • Wills Hughes-Wilson at World Orphan Drug Congress
    Wills Hughes-Wilson
    Senior Vice President, Chief Patient Access Officer
    Dr Will Maier at World Orphan Drug Congress
    Dr Will Maier
    Chief Scientific Officer
    Mapi Group
  • Diana Ribeiro at World Orphan Drug Congress
    Diana Ribeiro
    Director of Research
    Action Duchenne
    Dr Paul Robinson at World Orphan Drug Congress
    Dr Paul Robinson
    Executive Director, Patient Perspective
    Merck Sharp and Dohme
  • Sheela Upadhyaya at World Orphan Drug Congress
    Sheela Upadhyaya
    Assoc. Director Highly Specialised Technologies
    National Institute For Health and Care Excellence
    Stephen Yoo at World Orphan Drug Congress
    Stephen Yoo
    Chief Medical Officer
  • Dr Bruno Sepodes at World Orphan Drug Congress
    Dr Bruno Sepodes
    Chair, Committee for Orphan Medicinal Products (COMP)
    European Medicines Agency
    Julie Walters at World Orphan Drug Congress
    Julie Walters
  • Christina Waters at World Orphan Drug Congress
    Christina Waters
    CEO and Founder
    RARE Science
    Scott L Pescatore at World Orphan Drug Congress
    Scott L Pescatore
    Oncology General Manager. Rare Diseases
  • Edmund Jessop at World Orphan Drug Congress
    Edmund Jessop
    Medical Adviser
    National Health Service
    Marco Petschulies at World Orphan Drug Congress
    Marco Petschulies
    Scientific Advisor




Who Attends


AANORA Actelion Pharma Ltd Action Duchenne Addmedica Adelphi Values AGSD (UK) AirLiquide

AKU Society Alcimed Alexion Pharmaceuticals Allaysis LLC Alliance Life Sciences ALS Liga Belgi

Alstrom Syndrome U.K. AMICULUM Anticancer Fund AOP Orphan Pharmaceuticals AG

ArmaGen Technologies, Inc. Atacsia a Fi / Ataxia and Me Ataxia UK aTyr aTyr Pharma

BioBlast Pharma Ltd Biopontis Alliance Blackswan Foundation Brace Pharma Capital

Caligor Rx, Inc. Calypso Biotech SA  Capsugel Celgene Centogene AG

Charity Association Neurohereditary Diseases Chiesi Farmaceutici Spa Clear Pharma

Clinart MENA Clinerion Clinigen Global Access Programs Comradis Concenter BioPharma/Silkim Ltd.

Cote Orphan Coulter Partners   Covance UK CRF Health CureDuchenne Cures Within Reach

Cydan Development  Cytokinetics Daiichi Sankyo Europe GmbH Dipharma SA Diurnal Limited

Dravet Syndrome Foundation Durbin E.C.R.I.N. ECRIN-ERIC ELA Suisse

Emmaus Life Sciences, Inc Ergomed EspeRare Euromedica EuropaBio

European Huntington's Disease Network EURORDIS  Euticals Spa EvaluatePharma Ltd

Evidera F.Hoffmann-La Roche Ltd. Facio Therapies BV Federal Joint Committee

F Hoffmann-La Roche French Association Against Friedreich Ataxia Gaucher Disease Russia

Genesis Pharma Genetic Alliance U.K. Genkyotex Innovation Sas Genpharm Genzyme Europe BV

Gerson Lehrman Group Giddi Pharma GlaxoSmithKline  Greenovation Biotech GmbH

Grünenthal GmbH GSK Rare Diseases GW Pharmaceuticals   Haute Autorite De Sante

Horizon Pharma Inc I.M.S. Health Idis Managed Access Idis Pharma

Imagine - Institut des Maladies génétiques IMS Health INC Research Index Ventures INSERM

 Lysogene M3 Pharma S/A Mapi Consultancy Midas Pharma GmbH Minoryx Therapeutics

MPS Society N.O.R.D. National Institute for Health and Care Excellence

National Institutes of Biomedical Innovation, Health and Nutrition

National organisation for rare diseases of Serbia  NephCure Kidney International Niemann-Pick UK Novartis



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Get Involved At World Orphan Drug Congress 2018


To Sponsor Or Exhibit


Andrew Mears
t/ +44 20 7092 1228




To Speak


Wing-Yun Cheung
t/ +44 20 7092 1172




To Register


Issa Mauthoor
t/ +44 20 7092 1257