2018 Speakers

 

Annemieke Aartsma Rus, Professor of Translational Genetics, Department of Human Genetics, Leiden University Medical Center

Annemieke Aartsma Rus | Professor of Translational Genetics, Department of Human Genetics | Leiden University Medical Center » speaking at Orphan Drug Congress

Karen Aiach, Chief Executive Officer, Lysogene

Karen Aiach | Chief Executive Officer | Lysogene » speaking at Orphan Drug Congress

Dennis Akkaya, Corporate Development, myTomorrows

Dennis Akkaya | Corporate Development | myTomorrows » speaking at Orphan Drug Congress

Luca Alberici, Chief Business Officer, MolMed

Luca Alberici | Chief Business Officer | MolMed » speaking at Orphan Drug Congress

Sofie Alverlind, Project Manager, Swedish Association of Local Authorities and Regions

Sofie Alverlind | Project Manager | Swedish Association of Local Authorities and Regions » speaking at Orphan Drug Congress

Einar Andreassen, Senior Adviser, Norwegian Medicines Agency

Einar Andreassen | Senior Adviser | Norwegian Medicines Agency » speaking at Orphan Drug Congress

Aris Angelis, Research Officer, Medical Technology Research Group, London School of Economics and Political Science

Aris Angelis | Research Officer, Medical Technology Research Group | London School of Economics and Political Science » speaking at Orphan Drug Congress

Diego Ardigo, R&D Rare Diseases Unit Head, CHIESI Farmaceutici Spa

Diego Ardigo | R&D Rare Diseases Unit Head | CHIESI Farmaceutici Spa » speaking at Orphan Drug Congress

Francis Arickx, Head of the Directorate Reimbursement of Medicines and Pharmaceutical Policy,, National Institute for Health and Disability Insurance RIZIV-INAMI

Francis Arickx | Head of the Directorate Reimbursement of Medicines and Pharmaceutical Policy, | National Institute for Health and Disability Insurance RIZIV-INAMI » speaking at Orphan Drug Congress

Dr Segolene Ayme, Founder of Orphanet & Rare Disease Expert in Residence, Inserm

Dr Segolene Ayme | Founder of Orphanet & Rare Disease Expert in Residence | Inserm » speaking at Orphan Drug Congress

Jasmin Barman, Scientific Advisor, SGP

Jasmin Barman | Scientific Advisor | SGP » speaking at Orphan Drug Congress

Denis Belyakov, Executive Director, Union of Patients? And Patients? Organizations With Rare Diseases

Denis Belyakov | Executive Director | Union of Patients? And Patients? Organizations With Rare Diseases » speaking at Orphan Drug Congress

Marian Bendik, Head of Gene Therapy, Process Development, Shire

Marian Bendik | Head of Gene Therapy, Process Development | Shire » speaking at Orphan Drug Congress

Annika Bergman, Pricing and Market Access Europe, Sarepta International Holdings GmbH

Annika Bergman | Pricing and Market Access Europe | Sarepta International Holdings GmbH » speaking at Orphan Drug Congress

Dr Michael Binks, VP, Rare Disease Clinical Research, Pfizer

Dr Michael Binks | VP, Rare Disease Clinical Research | Pfizer » speaking at Orphan Drug Congress

Catalin Bobirca, Medical Franchise Head, Rare Diseases, Oncology Region Europe, Novartis

Catalin Bobirca | Medical Franchise Head, Rare Diseases, Oncology Region Europe | Novartis » speaking at Orphan Drug Congress

Mathieu Boudes, Coordinator of PARADIGM, European Patients' Forum

Mathieu Boudes | Coordinator of PARADIGM | European Patients' Forum » speaking at Orphan Drug Congress

Dr Meriem Bouslouk, Orphan drug policy adviser for Germany

Dr Meriem Bouslouk |  | Orphan drug policy adviser for Germany » speaking at Orphan Drug Congress

Meriem Bouslouk, Orphan drug policy adviser for Germany

Meriem Bouslouk |  | Orphan drug policy adviser for Germany » speaking at Orphan Drug Congress

Jacoline Bouvy, Senior Scientific Adviser, National Insitute for Health and Care Excellence

Jacoline Bouvy | Senior Scientific Adviser | National Insitute for Health and Care Excellence » speaking at Orphan Drug Congress

Sophia Brodin, Deputy Head of Department, Department of Value Based Pricing, The Dental and Pharmaceutical Benefits Agency T.L.V.

Sophia Brodin | Deputy Head of Department, Department of Value Based Pricing | The Dental and Pharmaceutical Benefits Agency T.L.V. » speaking at Orphan Drug Congress

Nicholas Brooke, Executive Director, Patient Focused Medicines Development

Nicholas Brooke | Executive Director | Patient Focused Medicines Development » speaking at Orphan Drug Congress

Virginie Bros-Facer, Scientific Director, EURORDIS

Virginie Bros-Facer | Scientific Director | EURORDIS » speaking at Orphan Drug Congress

Anna Bucsics, Project Advisor, Mechanism of Coordinated Access to orphan medicinal products (MoCA)

Anna Bucsics | Project Advisor | Mechanism of Coordinated Access to orphan medicinal products (MoCA) » speaking at Orphan Drug Congress

Dr Andreas Busch, Chief Scientific Officer, Head of Research and Development, Shire Pharmaceuticals

Dr Andreas Busch | Chief Scientific Officer, Head of Research and Development | Shire Pharmaceuticals » speaking at Orphan Drug Congress

Clara Campàs, Partner, Asabys Partners

Clara Campàs | Partner | Asabys Partners » speaking at Orphan Drug Congress

Agnese Cangini, Health Economist, AIFA

Agnese Cangini | Health Economist | AIFA » speaking at Orphan Drug Congress

Nathalie Cartier, Director, Institut National De La sante Et De La Recherche Medicale

Nathalie Cartier | Director | Institut National De La sante Et De La Recherche Medicale » speaking at Orphan Drug Congress

Fleur Chandler, Therapy Area Head of Respiratory Value Evidence and Outcomes, GlaxoSmithKline Biologicals

Fleur Chandler | Therapy Area Head of Respiratory Value Evidence and Outcomes | GlaxoSmithKline Biologicals » speaking at Orphan Drug Congress

Maria Chatzou, Co-founder & Senior Advisor, Innovation Forum

Maria Chatzou | Co-founder & Senior Advisor | Innovation Forum » speaking at Orphan Drug Congress

James Christie, SVP Manufacturing and Supply Chain, MeiraGTx

James Christie | SVP Manufacturing and Supply Chain | MeiraGTx » speaking at Orphan Drug Congress

Gabriel Cohn, Vice President Of Clinical Development Lead, Avrobio

Gabriel Cohn | Vice President Of Clinical Development Lead | Avrobio » speaking at Orphan Drug Congress

Laura Cox, UK Country Lead and Business Development, myTomorrows

Laura Cox | UK Country Lead and Business Development | myTomorrows » speaking at Orphan Drug Congress

Emily Crossley, Co-founder, Duchenne U.K.

Emily Crossley | Co-founder | Duchenne U.K. » speaking at Orphan Drug Congress

Avril Daly, CEO, Retina International

Avril Daly | CEO | Retina International » speaking at Orphan Drug Congress

Tagle Danilo, Associate Director for Special Initiatives, National Center for Advancing Translational Sciences

Tagle Danilo | Associate Director for Special Initiatives | National Center for Advancing Translational Sciences » speaking at Orphan Drug Congress

Cecile De Coster, Director Regulatory Science, Bluebird Bio

Cecile De Coster | Director Regulatory Science | Bluebird Bio » speaking at Orphan Drug Congress

Dr Sjef De Kimpe, Co-founder and SVP R&D, Auxesia Orion

Dr Sjef De Kimpe | Co-founder and SVP R&D | Auxesia Orion » speaking at Orphan Drug Congress

Professor Michele De Luca, Scientist, Professor, University of Modena e Reggio Emilia

Professor Michele De Luca | Scientist, Professor | University of Modena e Reggio Emilia » speaking at Orphan Drug Congress

Laura De Rosa, Collaborator & Co-author, University of Modena e Reggio Emilia

Laura De Rosa | Collaborator & Co-author | University of Modena e Reggio Emilia » speaking at Orphan Drug Congress

Dr Renato Dellamano, President, Medical Marketing Economics

Dr Renato Dellamano | President | Medical Marketing Economics » speaking at Orphan Drug Congress

Lisa Dilworth, Vice President Rare and Orphan Diseases, Synteract

Lisa Dilworth | Vice President Rare and Orphan Diseases | Synteract » speaking at Orphan Drug Congress

Scott Dorfman, President & CEO, Odylia Therapeutics

Scott Dorfman | President & CEO | Odylia Therapeutics » speaking at Orphan Drug Congress

Cinzia Dorigo, Executive Director Clinical Development, Syneos Health

Cinzia Dorigo | Executive Director Clinical Development | Syneos Health » speaking at Orphan Drug Congress

Dr Cynthia Dukes, Vice President, Drug Development, Rare Disease, ICON plc

Dr Cynthia Dukes | Vice President, Drug Development, Rare Disease | ICON plc » speaking at Orphan Drug Congress

Rudy Dupree, Senior Project Manager, EUnetHTA WP4, EUnetHTA

Rudy Dupree | Senior Project Manager, EUnetHTA WP4 | EUnetHTA » speaking at Orphan Drug Congress

Jami Ellis, Executive Director of Commercial Development, Horizon Pharma

Jami Ellis | Executive Director of Commercial Development | Horizon Pharma » speaking at Orphan Drug Congress

Erik Emerson, Executive Vice President, Commercial Operations, Mezzion Pharma

Erik Emerson | Executive Vice President, Commercial Operations | Mezzion Pharma » speaking at Orphan Drug Congress

Van Zyl Engelbrecht, Clinical Project Director EU, UBC

Van Zyl Engelbrecht | Clinical Project Director EU | UBC » speaking at Orphan Drug Congress

Karen Facey, Senior Research Fellow, University of Edinburgh

Karen Facey | Senior Research Fellow | University of Edinburgh » speaking at Orphan Drug Congress

Kelly Franchetti, RN, CCRN, CEN VP, Global Patient Insights & Engagement, Commercialisation & Outcomes, ICON plc

Kelly Franchetti | RN, CCRN, CEN VP, Global Patient Insights & Engagement, Commercialisation & Outcomes | ICON plc » speaking at Orphan Drug Congress

Pedro Franco, Director for Europe for Global Regulatory and Scientific Policy, Merck Serono

Pedro Franco | Director for Europe for Global Regulatory and Scientific Policy | Merck Serono » speaking at Orphan Drug Congress

Michela Gabaldo, Head of Alliance Management, Fondazione Telethon

Michela Gabaldo | Head of Alliance Management | Fondazione Telethon » speaking at Orphan Drug Congress

Benjamin Gannon, Head of International Government Affairs, Public Policy & Patient Engagement, Vertex Pharmaceuticals

Benjamin Gannon | Head of International Government Affairs, Public Policy & Patient Engagement | Vertex Pharmaceuticals » speaking at Orphan Drug Congress

Dr Caridad Pontes García, Pharmacotherapeutic Harmonization, Catalan Health Service

Dr Caridad Pontes García | Pharmacotherapeutic Harmonization | Catalan Health Service » speaking at Orphan Drug Congress

Pamela Gavin, Chief Strategy Officer, National Organization for Rare Disorders

Pamela Gavin | Chief Strategy Officer | National Organization for Rare Disorders » speaking at Orphan Drug Congress

Josie Godfrey, Director, JG Zebra Consulting

Josie Godfrey | Director | JG Zebra Consulting » speaking at Orphan Drug Congress

Rory Graham, BPharm, MBA Senior Director, Regulatory Affairs, Europe & International Region, ICON plc

Rory Graham | BPharm, MBA Senior Director, Regulatory Affairs, Europe & International Region | ICON plc » speaking at Orphan Drug Congress

Dr Tim Guilliams, CEO, Healx

Dr Tim Guilliams | CEO | Healx » speaking at Orphan Drug Congress

Dr Femida Gwadry-Sridhar, Founder and CEO, Pulse Infoframe Inc

Dr Femida Gwadry-Sridhar | Founder and CEO | Pulse Infoframe Inc » speaking at Orphan Drug Congress

Denis Horgan, Executive Director, EAPM (European Alliance for Personalised Medicine)

Denis Horgan | Executive Director | EAPM (European Alliance for Personalised Medicine) » speaking at Orphan Drug Congress

Annie Hubert, Director, European Public Policy, Alliance for Regenerative Medicine

Annie Hubert | Director, European Public Policy | Alliance for Regenerative Medicine » speaking at Orphan Drug Congress

Lynne Hughes, Vice President & Head, Centre of Excellence, Neurology, Therapeutic & Speciality Business Development, IQVIA

Lynne Hughes | Vice President & Head, Centre of Excellence, Neurology, Therapeutic & Speciality Business Development | IQVIA » speaking at Orphan Drug Congress

Wills Hughes-Wilson, Head of Patient Access & Commercial Planning, Mereo BioPharma

Wills Hughes-Wilson | Head of Patient Access  & Commercial Planning | Mereo BioPharma » speaking at Orphan Drug Congress

Adam Hutchings, Managing Director, Dolon

Adam Hutchings | Managing Director | Dolon » speaking at Orphan Drug Congress

Dr Carlo Incerti, SVP, Head of Global Medical Affairs, CMO, Genzyme, A Sanofi Company

Dr Carlo Incerti | SVP, Head of Global Medical Affairs, CMO | Genzyme, A Sanofi Company » speaking at Orphan Drug Congress

Edmund Jessop, Medical Adviser, National Health Service

Edmund Jessop | Medical Adviser | National Health Service » speaking at Orphan Drug Congress

Bodil Jonason, Vice President, Marketing and Sales, Inceptua

Bodil Jonason | Vice President, Marketing and Sales | Inceptua » speaking at Orphan Drug Congress

M Ken Kengatharan, Managing Partner, Atheneos Ventures and CEO, Auxesia Orion

M Ken Kengatharan | Managing Partner, Atheneos Ventures and CEO | Auxesia Orion » speaking at Orphan Drug Congress

Alastair Kent Obe, Former Director, Genetic Alliance UK, Retired

Alastair Kent Obe | Former Director, Genetic Alliance UK | Retired » speaking at Orphan Drug Congress

Diane Kleinermans, Advisor to the Ministry of Health and Social Affairs, Belgian Federal Government

Diane Kleinermans | Advisor to the Ministry of Health and Social Affairs | Belgian Federal Government » speaking at Orphan Drug Congress

Nicolas Koebel, Head of Program & Portfolio Management, Orchard Therapeutics

Nicolas Koebel | Head of Program & Portfolio Management | Orchard Therapeutics » speaking at Orphan Drug Congress

Maryna Kolochavina, Project Director, Real World & Late Phase, Syneos Health

Maryna Kolochavina | Project Director, Real World & Late Phase | Syneos Health » speaking at Orphan Drug Congress

Daan Kranenburg, VP Commercial Operations Europe, bluebird bio

Daan Kranenburg | VP Commercial Operations Europe | bluebird bio » speaking at Orphan Drug Congress

Jennifer Lambe, Senior Project Manager, ICON plc

Jennifer Lambe | Senior Project Manager | ICON plc » speaking at Orphan Drug Congress

Dr Greg Larosa, Senior Vice President & Head of Scientific Strategy, Rare Disease RU, Pfizer

Dr Greg Larosa | Senior Vice President & Head of Scientific Strategy, Rare Disease RU | Pfizer » speaking at Orphan Drug Congress

Yann Le Cam, Chief Executive Officer, EURORDIS

Yann Le Cam | Chief Executive Officer | EURORDIS » speaking at Orphan Drug Congress

Bastiaan Leewis, MSAT Manager Industrialization, MeiraGTx

Bastiaan Leewis | MSAT Manager Industrialization | MeiraGTx » speaking at Orphan Drug Congress

Sune Lindgaard, Chief of Business Intelligence, Amgros, Denmark

Sune Lindgaard | Chief of Business Intelligence | Amgros, Denmark » speaking at Orphan Drug Congress

Yolanda Ludena, Foundation twenty-nine

Yolanda Ludena |  | Foundation twenty-nine » speaking at Orphan Drug Congress

Alastair Mackinnon, CMO, Mereo BioPharma

Alastair Mackinnon | CMO | Mereo BioPharma » speaking at Orphan Drug Congress

Dr William Maier, PhD, MPH Chief Scientific Officer & Head, Rare Disease Research, Commercialisation and Outcomes, ICON plc

Dr William Maier | PhD, MPH Chief Scientific Officer & Head, Rare Disease Research, Commercialisation and Outcomes | ICON plc » speaking at Orphan Drug Congress

Marc Martinell, CEO, Minoryx Therapeutics

Marc Martinell | CEO | Minoryx Therapeutics » speaking at Orphan Drug Congress

Camille Metais, Senior Regulatory Affairs Director, Alexion Pharma LLC

Camille Metais | Senior Regulatory Affairs Director | Alexion Pharma LLC » speaking at Orphan Drug Congress

Ana Mingorance, Chief Development Officer, Loulou Foundation

Ana Mingorance | Chief Development Officer | Loulou Foundation » speaking at Orphan Drug Congress

Eva Molero, CEO, Synapse Research Management Partners

Eva Molero | CEO | Synapse Research Management Partners » speaking at Orphan Drug Congress

Nathalie Moll, Director General, EFPIA

Nathalie Moll | Director General | EFPIA » speaking at Orphan Drug Congress

Arlete Monteiro, IT Director, Ministry Of Health Of Portugal

Arlete Monteiro | IT Director | Ministry Of Health Of Portugal » speaking at Orphan Drug Congress

Dr Marisol Montolio Del Olmo, Scientific Director, Duchenne Parent Project Spain

Dr Marisol Montolio Del Olmo | Scientific Director | Duchenne Parent Project Spain » speaking at Orphan Drug Congress

Dmitry Mordvintsev, Head of Specialty Care BU, Genzyme

Dmitry Mordvintsev | Head of Specialty Care BU | Genzyme » speaking at Orphan Drug Congress

Dirk Moritz, Principal, Blue Matter Consulting

Dirk Moritz | Principal | Blue Matter Consulting » speaking at Orphan Drug Congress

Dr William Motel, Regulatory Affairs Director, IQVIA

Dr William Motel | Regulatory Affairs Director | IQVIA » speaking at Orphan Drug Congress

Karl-Johan Myren, Head of Patient Access, Alexion Pharmaceuticals

Karl-Johan Myren | Head of Patient Access | Alexion Pharmaceuticals » speaking at Orphan Drug Congress

Dr Alexander Natz, Secretary General, EUCOPE

Dr Alexander Natz | Secretary General | EUCOPE » speaking at Orphan Drug Congress

Daniel O'Connor, Medical Assessor, Medicines and Healthcare Products Regulatory Agency

Daniel O'Connor | Medical Assessor | Medicines and Healthcare Products Regulatory Agency » speaking at Orphan Drug Congress

Sam Oliver, Joint Managing Director, pH Associates

Sam Oliver | Joint Managing Director | pH Associates » speaking at Orphan Drug Congress

Tuyen Ong, Chief Development Officer, Nightstar Therapeutics

Tuyen Ong | Chief Development Officer | Nightstar Therapeutics » speaking at Orphan Drug Congress

Dr Emanuele Ostuni, Head of Europe, Cell and Gene Therapy, Novartis

Dr Emanuele Ostuni | Head of Europe, Cell and Gene Therapy | Novartis » speaking at Orphan Drug Congress

Romina Oxborough, Director of Clinigen Consulting, Clinigen Group

Romina Oxborough | Director of Clinigen Consulting | Clinigen Group » speaking at Orphan Drug Congress

Dr Pan Pantziarka, Program Director, Anticancer Fund

Dr Pan Pantziarka | Program Director | Anticancer Fund » speaking at Orphan Drug Congress

Samantha Parker, Chief Patient Access Officer, Lysogene

Samantha Parker | Chief Patient Access Officer | Lysogene » speaking at Orphan Drug Congress

Andrew Parker, Executive Vice President and Chief Science Officer, Zealand Pharma

Andrew Parker | Executive Vice President and Chief Science Officer | Zealand Pharma » speaking at Orphan Drug Congress

Doug Paul, partner, Medical Marketing Economics

Doug Paul | partner | Medical Marketing Economics » speaking at Orphan Drug Congress

Tapani Piha, Head Of Unit, European Commission

Tapani Piha | Head Of Unit | European Commission » speaking at Orphan Drug Congress

Sarah Pitluck, Head, Global Pricing & Reimbursement, Spark Therapeutics

Sarah Pitluck | Head, Global Pricing & Reimbursement | Spark Therapeutics » speaking at Orphan Drug Congress

Silvia Ragno, Senior Director External Asset Lead, Takeda

Silvia Ragno | Senior Director External Asset Lead | Takeda » speaking at Orphan Drug Congress

Dr Sam Rasty, Chief Operating Officer, Homology Medicines

Dr Sam Rasty | Chief Operating Officer | Homology Medicines » speaking at Orphan Drug Congress

Kirsty Reid, Senior Manager Science Policy and Animal Welfare, EFPIA

Kirsty Reid | Senior Manager Science Policy and Animal Welfare | EFPIA » speaking at Orphan Drug Congress

Owen Roberts, Chief Executive Officer, M4K Pharma

Owen Roberts | Chief Executive Officer | M4K Pharma » speaking at Orphan Drug Congress

Dr Paul Robinson, Patient Engagement Lead, Europe, Merck Sharp and Dohme

Dr Paul Robinson | Patient Engagement Lead, Europe | Merck Sharp and Dohme » speaking at Orphan Drug Congress

Angi Robinson, Executive Director, Strategic Development, Rare Disease & Pediatrics, Premier Research

Angi Robinson | Executive Director, Strategic Development, Rare Disease & Pediatrics | Premier Research » speaking at Orphan Drug Congress

Gregory Robinson, Chief Scientific Officer, Nightstar Therapeutics

Gregory Robinson | Chief Scientific Officer | Nightstar Therapeutics » speaking at Orphan Drug Congress

Dr Jerome Rossert, Vice President, General Medicine, Global Clinical Development, Vertex Pharmaceuticals

Dr Jerome Rossert | Vice President, General Medicine, Global Clinical Development | Vertex Pharmaceuticals » speaking at Orphan Drug Congress

Delphine Roulland, Senior Manager Public Affairs chez, EUCOPE

Delphine Roulland | Senior Manager Public Affairs chez | EUCOPE » speaking at Orphan Drug Congress

Jude Samulski, Director, Professor of Pharmacology, University of North Carolina at Chapel Hill, Gene Therapy Center

Jude Samulski | Director, Professor of Pharmacology | University of North Carolina at Chapel Hill, Gene Therapy Center » speaking at Orphan Drug Congress

Luca Sangiori, Head of Medical Genetics and Rare Orthopedic Diseases, Rizzoli Orthopaedic Institute

Luca Sangiori | Head of Medical Genetics and Rare Orthopedic Diseases | Rizzoli Orthopaedic Institute » speaking at Orphan Drug Congress

Reto Schaberl, Head Business Development, Ewopharma AG

Reto Schaberl | Head Business Development | Ewopharma AG » speaking at Orphan Drug Congress

Scott Schliebner, Vice President, Scientific Affairs, Rare Diseases, PRA Health Sciences

Scott Schliebner | Vice President, Scientific Affairs, Rare Diseases | PRA Health Sciences » speaking at Orphan Drug Congress

Gabriele Schlosser-Weber, Clinical assessor, Bfarm

Gabriele Schlosser-Weber | Clinical assessor | Bfarm » speaking at Orphan Drug Congress

Dr Yvonne Schmidt, Scientific Advisor, Pharmaceuticals Department, G-BA

Dr Yvonne Schmidt | Scientific Advisor, Pharmaceuticals Department | G-BA » speaking at Orphan Drug Congress

Sophie Schmitz, Managing Partner, Partners4Access

Sophie Schmitz | Managing Partner | Partners4Access » speaking at Orphan Drug Congress

Ad Schuurman, Senior Advisor International Affairs, National Health Care Institute (ZIN), the Netherlands

Ad Schuurman | Senior Advisor International Affairs | National Health Care Institute (ZIN), the Netherlands » speaking at Orphan Drug Congress

Raghuram Selvaraju, Managing Director, Senior Analyst, Healthcare, Rodman & Renshaw

Raghuram Selvaraju | Managing Director, Senior Analyst, Healthcare | Rodman & Renshaw » speaking at Orphan Drug Congress

Daniela Settesoldi, Pharmaceutical Expenditure, Expenditure monitoring, AIFA

Daniela Settesoldi | Pharmaceutical Expenditure, Expenditure monitoring | AIFA » speaking at Orphan Drug Congress

Nick Sireau, Chairman, AKU Society

Nick Sireau | Chairman | AKU Society » speaking at Orphan Drug Congress

David Sourdive, Executive Vice President Technical Operations, Cellectis

David Sourdive | Executive Vice President Technical Operations | Cellectis » speaking at Orphan Drug Congress

Marcio Souza, Chief Operating Officer, PTC Therapeutics

Marcio Souza | Chief Operating Officer | PTC Therapeutics » speaking at Orphan Drug Congress

Leo Strican, Head of Access Value & Evidence Strategy, Europe, Bluebird Bio

Leo Strican | Head of Access Value & Evidence Strategy, Europe | Bluebird Bio » speaking at Orphan Drug Congress

Rick Thompson, CEO, Findacure

Rick Thompson | CEO | Findacure » speaking at Orphan Drug Congress

Dr Josep Torrent-Farnell, Medicines Department, Catalan Health Service

Dr Josep Torrent-Farnell | Medicines Department | Catalan Health Service » speaking at Orphan Drug Congress

Marie Trad, Executive Medical Director, IQVIA

Marie Trad | Executive Medical Director | IQVIA » speaking at Orphan Drug Congress

Dr Giuliana Vallanti, Director Of Development, Quality Control And Qualified Person, Molmed SpA

Dr Giuliana Vallanti | Director Of Development, Quality Control And Qualified Person | Molmed SpA » speaking at Orphan Drug Congress

Inneke Van De Vijver, Advisor, N.I.H.D.I.

Inneke Van De Vijver | Advisor | N.I.H.D.I. » speaking at Orphan Drug Congress

Dr Sander Van Deventer, Chief Scientific Officer And General Manager, uniQure

Dr Sander Van Deventer | Chief Scientific Officer And General Manager | uniQure » speaking at Orphan Drug Congress

Dr Andreas Vogel, Head of European Regulatory, Bluebird Bio

Dr Andreas Vogel | Head of European Regulatory | Bluebird Bio » speaking at Orphan Drug Congress

Till Voigtlander, Vice-President of the Board of Members States on ERNs, Medical University of Vienna

Till Voigtlander | Vice-President of the Board of Members States on ERNs | Medical University of Vienna » speaking at Orphan Drug Congress

Dr Birgitte Volck, Senior Vice President, Head of R&D Rare Diseases, GlaxoSmithKline

Dr Birgitte Volck | Senior Vice President, Head of R&D Rare Diseases | GlaxoSmithKline » speaking at Orphan Drug Congress

Lucia Von Bredow, Public Affairs & Patient Policy Manager, Clinigen Group

Lucia Von Bredow | Public Affairs & Patient Policy Manager | Clinigen Group » speaking at Orphan Drug Congress

Misha Votruba, Director, Gradus R.S.J. Life Sciences

Misha Votruba | Director | Gradus R.S.J. Life Sciences » speaking at Orphan Drug Congress

Darren Walsh, Senior Director - Market Access & Govt. Affairs – EU, Orchard Therapeutics

Darren Walsh | Senior Director - Market Access & Govt. Affairs – EU | Orchard Therapeutics » speaking at Orphan Drug Congress

Dr Mary Wang, Global Partnerships & Project Manager, Fondazione Telethon

Dr Mary Wang | Global Partnerships & Project Manager | Fondazione Telethon » speaking at Orphan Drug Congress

Dr Richard Wenzel, Principal, Charles River Associates

Dr Richard Wenzel | Principal | Charles River Associates » speaking at Orphan Drug Congress

Magdalena Wladysiuk, Owner And Vice President, HTA Consulting

Magdalena Wladysiuk | Owner And Vice President | HTA Consulting » speaking at Orphan Drug Congress

Pawel Wozniak, Managing Director, Komtur Polska

Pawel Wozniak | Managing Director | Komtur Polska » speaking at Orphan Drug Congress

Entela Xoxi, Former AIFA, Universita Cattolica Del Sacro Cuore

Entela Xoxi | Former AIFA | Universita Cattolica Del Sacro Cuore » speaking at Orphan Drug Congress

Stefano Zancan, Head Clinical Development and Operations, Fondazione Telethon

Stefano Zancan | Head Clinical Development and Operations | Fondazione Telethon » speaking at Orphan Drug Congress

Martine Zimmermann, Senior Vice President, Head of Global Regulatory Affairs, Alexion Pharmaceuticals

Martine Zimmermann | Senior Vice President, Head of Global Regulatory Affairs | Alexion Pharmaceuticals » speaking at Orphan Drug Congress

 

 

 

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