Gold Sponsor

GSK Rare Diseases Unit

GSK Rare Diseases Unit is a leading provider of transformational solutions for people affected by rare diseases. We currently have an innovative portfolio of development programmes focusing on amyloidosis, pulmonary arterial hypertension and gene therapy for lysosomal storage disorders and primary immune deficiencies. Collaboration with other institutions, scientific and patient experts will enable us to continue our goal of making positive differences to the lives of rare disease patients and their families.